US Biologic Lung Volume Reduction (BLVR) Phase 2 Emphysema Study

NCT ID: NCT00515164

Last Updated: 2011-10-24

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE2

Total Enrollment

22 participants

Study Classification

INTERVENTIONAL

Study Start Date

2007-08-31

Study Completion Date

2009-12-31

Brief Summary

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The purpose of this study it to evaluate the efficacy and safety of the 20 mL BLVR System in patients with advanced upper lobe predominant emphysema.

Detailed Description

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Background:

Patients with emphysema currently have limited treatment choices. Many patients are treated with steroids and inhaled medications, which often provide little or no benefit. In recent years, lung volume reduction surgery has become an accepted therapy for advanced emphysema. Lung volume reduction surgery involves the removal of diseased portions of the lung in order to enable the remaining, healthier portions of the lung to function better. This procedure, although effective for many patients, is complicated and is accompanied by substantial morbidity and mortality risk.

Aeris Therapeutics has developed the Biologic Lung Volume Reduction (BLVR) System which is intended to achieve lung volume reduction without surgery and its attendant risks. Patients are treated using a bronchoscope to direct treatment to the most damaged areas of the lung. The treatment delivers a precisely proportioned proprietary mixture of drugs and biologics which, when combined at the treatment site, form a biodegradable hydrogel. The hydrogel acts to reduce lung volume by permanently collapsing and sealing the diseased areas of the lung. This provides room within the chest to allow the remaining healthier portions of the lung to function better.

Aeris' BLVR development program has been granted Fast Track designation by the U.S. FDA, and is the subject of ongoing clinical trials designed to investigate the safety and efficacy of the BLVR System as a treatment for patients with advanced heterogeneous emphysema. Fast Track designation is reserved for drug and biologic development programs that are intended to treat serious or life-threatening conditions and that demonstrate the potential to address unmet medical needs.

Conditions

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Pulmonary Emphysema Chronic Obstructive Pulmonary Disease

Study Design

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Allocation Method

NON_RANDOMIZED

Intervention Model

SINGLE_GROUP

Primary Study Purpose

TREATMENT

Blinding Strategy

NONE

Study Groups

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Group 1

Treatment will be administered in 2 treatment sessions.

Group Type EXPERIMENTAL

Biologic Lung Volume Reduction (BLVR) - 20 mL Hydrogel

Intervention Type DRUG

20 mL Hydrogel

Group 2

Treatment will be administered in a single treatment session.

Group Type EXPERIMENTAL

Biologic Lung Volume Reduction (BLVR) - 20 mL Hydrogel

Intervention Type DRUG

20 mL Hydrogel

Interventions

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Biologic Lung Volume Reduction (BLVR) - 20 mL Hydrogel

20 mL Hydrogel

Intervention Type DRUG

Eligibility Criteria

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Inclusion Criteria

* clinical diagnosis of advanced upper lobe emphysema
* age \>/= 40 years
* clinically significant dyspnea
* failure of standard medical therapy to relieve symptoms (inhaled beta agonist \& inhaled anticholinergic)
* pulmonary function tests within protocol-specified ranges (post bronchodilator FEV1 \< 45% predicted \& experiencing \< 30% or 300 mL improvement using bronchodilator; total lung capacity \> 110% predicted; residual volume \> 150% predicted)
* 6 Minute Walk Distance \>/= 150 m

Exclusion Criteria

* alpha-1 protease inhibitor deficiency
* homogeneous emphysema
* tobacco use within 4 months of initial visit
* body mass index \< 15 kg/m2 or\> 35 kg/m2
* clinically significant asthma, chronic bronchitis or bronchiectasis
* allergy or sensitivity to procedural components
* pregnant, lactating or unwilling to use birth control if required
* prior lung volume reduction surgery, lobectomy, pneumonectomy, lung transplant, endotracheal valve placement, airway stent placement or pleurodesis
* comorbid condition that could adversely influence outcomes
* inability to tolerate bronchoscopy under conscious sedation (or anesthesia)
* history of renal infarction or renal failure
Minimum Eligible Age

40 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Aeris Therapeutics

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Geoffrey McLennan, MD

Role: PRINCIPAL_INVESTIGATOR

University of Iowa Hospitals & Clinics, Iowa City, IA

Charlie Strange, MD

Role: PRINCIPAL_INVESTIGATOR

Medical University of South Carolina

Mark Gotfried, MD

Role: PRINCIPAL_INVESTIGATOR

Pulmonary Associates, Phoenix, AZ

Mark Krasna, MD

Role: PRINCIPAL_INVESTIGATOR

St Joseph's Medical Center, Towson, MD

Sanjiv Tewari, MD

Role: PRINCIPAL_INVESTIGATOR

Akron Medical Center, Akron, OH

Gerard Criner, MD

Role: PRINCIPAL_INVESTIGATOR

Temple University Lung Center, Philadelphia, PA

William Leeds, DO

Role: PRINCIPAL_INVESTIGATOR

Veritas Clinical Specialties, Topeka, KS

Thomas Gildea, MD

Role: PRINCIPAL_INVESTIGATOR

Pulmonary, Allergy & Critical Care Medicine, Cleveland Clinic, Cleveland, OH

Locations

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Pulmonary Associates

Phoenix, Arizona, United States

Site Status

University of Iowa Hospitals & Clinics

Iowa City, Iowa, United States

Site Status

Veritas Clinical Specialties, Ltd

Topeka, Kansas, United States

Site Status

St Joseph's Medical Center

Towson, Maryland, United States

Site Status

Akron Medical Center

Akron, Ohio, United States

Site Status

Pulmonary, Allergy & Critical Care Medicine, Cleveland Clinic Foundation

Cleveland, Ohio, United States

Site Status

Temple University Lung Center

Philadelphia, Pennsylvania, United States

Site Status

Medical University of South Carolina

Charleston, South Carolina, United States

Site Status

Countries

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United States

References

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Ingenito EP, Berger RL, Henderson AC, Reilly JJ, Tsai L, Hoffman A. Bronchoscopic lung volume reduction using tissue engineering principles. Am J Respir Crit Care Med. 2003 Mar 1;167(5):771-8. doi: 10.1164/rccm.200208-842OC. Epub 2002 Oct 11.

Reference Type BACKGROUND
PMID: 12406835 (View on PubMed)

Reilly J, Washko G, Pinto-Plata V, Velez E, Kenney L, Berger R, Celli B. Biological lung volume reduction: a new bronchoscopic therapy for advanced emphysema. Chest. 2007 Apr;131(4):1108-13. doi: 10.1378/chest.06-1754.

Reference Type BACKGROUND
PMID: 17426216 (View on PubMed)

Criner GJ, Pinto-Plata V, Strange C, Dransfield M, Gotfried M, Leeds W, McLennan G, Refaely Y, Tewari S, Krasna M, Celli B. Biologic lung volume reduction in advanced upper lobe emphysema: phase 2 results. Am J Respir Crit Care Med. 2009 May 1;179(9):791-8. doi: 10.1164/rccm.200810-1639OC. Epub 2009 Jan 29.

Reference Type DERIVED
PMID: 19179484 (View on PubMed)

Other Identifiers

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01-C07-001

Identifier Type: -

Identifier Source: org_study_id