A Study of Trastuzumab Emtansine (Trastuzumab-MCC-DM1) Administered Intravenously to Patients With Human Epidermal Growth Factor Receptor 2 (HER2)-Positive Metastatic Breast Cancer

NCT ID: NCT00509769

Last Updated: 2013-04-02

Study Results

Results available

Outcome measurements, participant flow, baseline characteristics, and adverse events have been published for this study.

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Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE2

Total Enrollment

112 participants

Study Classification

INTERVENTIONAL

Study Start Date

2007-07-31

Study Completion Date

2009-06-30

Brief Summary

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This was a multi-institutional, open-label, single-arm, Phase II study of trastuzumab emtansine (T-DM1) administered by intravenous (IV) infusion to patients with human epidermal growth factor receptor 2 (HER2)-positive metastatic breast cancer (MBC).

Detailed Description

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Conditions

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Metastatic Breast Cancer

Study Design

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Allocation Method

NON_RANDOMIZED

Intervention Model

SINGLE_GROUP

Primary Study Purpose

TREATMENT

Blinding Strategy

NONE

Study Groups

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Trastuzumab emtansine 3.6 mg/kg

Patients received trastuzumab emtansine 3.6 mg/kg intravenously on Day 1 of each 21 day cycle for a maximum of 1 year. The total dose was dependent on the patient's weight on Day 1 of each cycle.

Group Type EXPERIMENTAL

Trastuzumab emtansine [Kadcyla]

Intervention Type DRUG

Trastuzumab emtansine was provided in either a liquid or a lyophilized formulation.

Interventions

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Trastuzumab emtansine [Kadcyla]

Trastuzumab emtansine was provided in either a liquid or a lyophilized formulation.

Intervention Type DRUG

Other Intervention Names

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trastuzumab-DM1 trastuzumab-MCC-DM1 T-DM1

Eligibility Criteria

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Inclusion Criteria

* Signed informed consent form.
* Human epidermal growth factor receptor 2 (HER2)-positive metastatic breast cancer (MBC); tissue (slides or blocks) available for HER2 confirmation.
* History of progression on HER2-directed therapy for the treatment of HER2-positive breast cancer.
* At least 1, and no more than 3, chemotherapy regimens for MBC.
* Granulocyte count ≥ 1500/μL, platelet count ≥ 100,000/μL, and hemoglobin ≥ 9 g/dL.
* Serum bilirubin ≤ 1.5 mg/dL, aspartate aminotransferase (AST), alanine aminotransferase (ALT), and alkaline phosphatase ≤ 2.5x the upper limit of normal (ULN).
* Serum creatinine ≤ 1.5 mg/dL or creatinine clearance ≥ 60 mL/min.
* Eastern Cooperative Oncology Group (ECOG) performance status of 0, 1, or 2.

Exclusion Criteria

* Any chemotherapy, hormonal therapy, radiotherapy, immunotherapy, or biological therapy for the treatment of breast cancer within 2 weeks of the first study treatment.
* Prior cumulative doxorubicin dose \> 360 mg/m\^2 or the equivalent.
* History of significant cardiac disease, unstable angina, congestive heart failure (CHF), myocardial infarction, or ventricular arrythmia requiring medication.
Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Genentech, Inc.

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Scott Holden, M.D.

Role: STUDY_DIRECTOR

Genentech, Inc.

Locations

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Little Rock Hem Onc Assoc

Little Rock, Arkansas, United States

Site Status

Rocky Mountain Cancer Center

Denver, Colorado, United States

Site Status

Washington Cancer Institute

Washington D.C., District of Columbia, United States

Site Status

Lynn Cancer Institute - West

Boca Raton, Florida, United States

Site Status

Florida Cancer Care

Davie, Florida, United States

Site Status

Mayo Clinic

Jacksonville, Florida, United States

Site Status

Hem/Onc Assoc - Treasure Coast

Port Saint Lucie, Florida, United States

Site Status

Gulfcoast Oncology Associates

St. Petersburg, Florida, United States

Site Status

Bay Area Oncology

Tampa, Florida, United States

Site Status

Northwest Georgia Onc Ctrs PC

Marietta, Georgia, United States

Site Status

John McClean, M.D. - Private P

Galesburg, Illinois, United States

Site Status

Cedar Valley Med Specialists

Waterloo, Iowa, United States

Site Status

Kentuckiana Cancer Institute

Louisville, Kentucky, United States

Site Status

Minnesota Oncology Hematology,

Minneapolis, Minnesota, United States

Site Status

Missouri Cancer Associates

Columbia, Missouri, United States

Site Status

Kansas City Cancer Center, LLC

Lee's Summit, Missouri, United States

Site Status

St. Louis Cancer & Breast Inst

St Louis, Missouri, United States

Site Status

St. Barnabas Health Care Sys

Livingston, New Jersey, United States

Site Status

New York Oncology Hematology

Albany, New York, United States

Site Status

Eastchester Center/Cancer Care

The Bronx, New York, United States

Site Status

Carolinas Hem-Oncology Assoc

Charlotte, North Carolina, United States

Site Status

Raleigh Hemotology & Oncology

Raleigh, North Carolina, United States

Site Status

Midwestern Regional Med Center

Eugene, Oregon, United States

Site Status

Texas Oncology Cancer Center

Austin, Texas, United States

Site Status

Texas Oncology, P.A.

Bedford, Texas, United States

Site Status

Cancer Specialists of South Te

Corpus Christi, Texas, United States

Site Status

US Oncology Research, Inc.

Dallas, Texas, United States

Site Status

USO

Dallas, Texas, United States

Site Status

Texas Oncology, P.A.

Dallas, Texas, United States

Site Status

Sammons Cancer Center

Dallas, Texas, United States

Site Status

El Paso Cancer Treatment Ctr

El Paso, Texas, United States

Site Status

Texas Oncology PA

Fort Worth, Texas, United States

Site Status

Texas Oncology, P.A.

Houston, Texas, United States

Site Status

US Oncology

Midland, Texas, United States

Site Status

USO - Tyler Cancer Ctr

Tyler, Texas, United States

Site Status

Waco Cancer Care & Research Ce

Waco, Texas, United States

Site Status

Northern Utah Associates

Ogden, Utah, United States

Site Status

Fairfax N Virginia Hem/Onc PC

Fairfax, Virginia, United States

Site Status

Northwest Medical Specialties

Tacoma, Washington, United States

Site Status

Northwest Cancer Specialists

Vancouver, Washington, United States

Site Status

Countries

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United States

Other Identifiers

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TDM4258g

Identifier Type: -

Identifier Source: org_study_id

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