Safety and Efficacy of Orally Administered Laquinimod Versus Placebo for Treatment of Relapsing Remitting Multiple Sclerosis (RRMS)

NCT ID: NCT00509145

Last Updated: 2021-11-02

Study Results

Results available

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Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE3

Total Enrollment

1106 participants

Study Classification

INTERVENTIONAL

Study Start Date

2007-11-13

Study Completion Date

2010-11-08

Brief Summary

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Determination the efficacy of daily oral treatment with laquinimod 0.6 mg capsules as compared to placebo in subjects with Relapsing Remitting Multiple Sclerosis (RRMS).

Detailed Description

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Conditions

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Multiple Sclerosis

Keywords

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Relapsing Remitting

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

QUADRUPLE

Participants Caregivers Investigators Outcome Assessors

Study Groups

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Laquinimod

Laquinimod 0.6 mg, oral

Group Type EXPERIMENTAL

Laquinimod

Intervention Type DRUG

Laquinimod 0.6 mg capsule, oral, once daily

Placebo

Matching placebo

Group Type PLACEBO_COMPARATOR

Placebo

Intervention Type OTHER

oral, once daily, capsule

Interventions

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Laquinimod

Laquinimod 0.6 mg capsule, oral, once daily

Intervention Type DRUG

Placebo

oral, once daily, capsule

Intervention Type OTHER

Other Intervention Names

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TV-5600

Eligibility Criteria

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Inclusion Criteria

1. Subjects must have a confirmed and documented MS diagnosis as defined by the Revised McDonald criteria \[Ann Neurol 2005: 58:840-846\], with a relapsing-remitting disease course.
2. Subjects must be ambulatory with converted Kurtzke EDSS score of 0-5.5.
3. Subjects must be in a stable neurological condition and free of corticosteroid treatment \[intravenous (iv), intramuscular (im) and/or per os (po)\] 30 days prior to screening (month -1).
4. Subjects must have had experienced one of the following:

* At least one documented relapse in the 12 months prior to screening
* At least two documented relapses in the 24 months prior to screening
* One documented relapse between 12 and 24 months prior to screening with at least one documented T1-Gd enhancing lesion in an MRI performed within 12 months prior to screening.
5. Subjects must be between 18 and 55 years of age, inclusive.
6. Subjects must have disease duration of at least 6 months (from the first symptom) prior to screening.
7. Women of child-bearing potential must practice an acceptable method of birth control \[acceptable methods of birth control in this study include: surgical sterilization, intrauterine devices, oral contraceptive, contraceptive patch, long-acting injectable contraceptive, partner's vasectomy or double-barrier method (condom or diaphragm with spermicide).
8. Subjects must be able to sign and date a written informed consent prior to entering the study
9. Subjects must be willing and able to comply with the protocol requirements for the duration of the study.

Exclusion Criteria

1. Subjects with progressive forms of MS
2. An onset of relapse, unstable neurological condition or any treatment with corticosteroids \[intravenous (iv), intramuscular (im) and/or per os (po)\] or ACTH between month -1 (screening) and 0 (baseline).
3. Use of experimental or investigational drugs, and/or participation in drug clinical studies within the 6 months prior to screening.
4. Use of immunosuppressive including Mitoxantrone (Novantrone®) or cytotoxic agents within 6 months prior to the screening visit.
5. Previous use of either of the following: natalizumab (Tysabri®), cladribine, laquinimod.
6. Previous treatment with glatiramer acetate (Copaxone®) Interferon-β (either 1a or 1b) or IVIG within 2 months prior to screening visit.
7. Systemic corticosteroid treatment of ≥30 consecutive days duration within 2 months prior to screening visit.
8. Previous total body irradiation or total lymphoid irradiation.
9. Previous stem cell treatment, autologous bone marrow transplantation or allogenic bone marrow transplantation.
10. A known history of tuberculosis.
11. Acute infection two weeks prior to baseline visit.
12. Major trauma or surgery two weeks prior to baseline
13. A history of vascular thrombosis (excluding catheter-site superficial venous thrombophlebitis).
14. A carrier state of factor V Leiden mutation (either homo- or heterozygous) as disclosed at screening.
15. Positive screening test for Hepatitis B surface antigen, Hepatitis C antibody, or HIV antibody as disclosed at screening visit.
16. Use of potent inhibitors of CYP3A4 within 2 weeks prior to baseline visit (1 month for fluoxetine) see detailed list in Appendix 5
17. Use of amiodarone within 2 years prior to screening visit.
18. Pregnancy or breastfeeding.
19. Subjects with a clinically significant or unstable medical or surgical condition that would preclude safe and complete study participation, as determined by medical history, physical examinations, ECG, laboratory tests or chest X-ray. Such conditions may include:

* A cardiovascular or pulmonary disorder that cannot be well-controlled by standard treatment permitted by the study protocol.
* A gastrointestinal disorder that may affect the absorption of study medication.
* Renal or metabolic diseases.
* Any form of chronic liver disease, including known non-alcoholic steatohepatitis.
* A ≥2xULN serum elevation of either of the following at screening: ALT, AST or direct bilirubin
* A QTC interval (obtained from either 2 ECG recordings at screening or from the mean value calculated from 3 measurements at baseline visit) which is \>450msec.
* A family history of Long- QT syndrome.
* A history of drug and/or alcohol abuse.
* Major psychiatric disorder.
20. A known history of sensitivity to Gd.
21. Inability to successfully undergo MRI scanning.
22. Known drug hypersensitivity that would preclude administration of laquinimod, such as hypersensitivity to: mannitol, meglumine or sodium stearyl fumarate.


1. Subjects who suffer from any form of progressive MS.
2. Any condition which the investigator feels may interfere with participation in the study.
3. Subjects with a clinically significant or unstable medical or surgical condition that would preclude safe and complete study participation,
4. Subjects who received any investigational medication, immunosuppressives or cytotoxic agents within 6 months prior to screening
5. Previous treatment with immunomodulators within two months prior to screening
6. Pregnancy or breastfeeding.
Minimum Eligible Age

18 Years

Maximum Eligible Age

55 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Teva Branded Pharmaceutical Products R&D, Inc.

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Giancarlo Comi

Role: PRINCIPAL_INVESTIGATOR

U.O.Neurology-Neurorehabilitation and Clinical Neurophysiology

Locations

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Teva Investigational Site 1076

Phoenix, Arizona, United States

Site Status

Teva Investigational Site 1090

Centennial, Colorado, United States

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Teva Investigational Site 1088

Fort Collins, Colorado, United States

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Teva Investigational Site 1094

New Haven, Connecticut, United States

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Teva Investigational Site 1102

Northbrook, Illinois, United States

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Teva Investigational Site 1081

Fort Wayne, Indiana, United States

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Teva Investigational Site 1083

Des Moines, Iowa, United States

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Teva Investigational Site 1086

Kansas City, Kansas, United States

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Teva Investigational Site 1101

Lexington, Kentucky, United States

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Teva Investigational Site 1096

Farmington Hills, Michigan, United States

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Teva Investigational Site 1093

Minneapolis, Minnesota, United States

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Teva Investigational Site 1098

St Louis, Missouri, United States

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Teva Investigational Site 1082

New York, New York, United States

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Teva Investigational Site 1079

Rochester, New York, United States

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Teva Investigational Site 1073

Winston-Salem, North Carolina, United States

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Teva Investigational Site 1097

Fargo, North Dakota, United States

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Teva Investigational Site 1084

Dayton, Ohio, United States

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Teva Investigational Site 1092

Oklahoma City, Oklahoma, United States

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Teva Investigational Site 1100

Hershey, Pennsylvania, United States

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Teva Investigational Site 1087

Philadelphia, Pennsylvania, United States

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Teva Investigational Site 1075

Lubbock, Texas, United States

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Teva Investigational Site 1078

San Antonio, Texas, United States

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Teva Investigational Site 1085

Milwaukee, Wisconsin, United States

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Teva Investigational Site 3300

Klagenfurt, , Austria

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Teva Investigational Site 3303

Linz, , Austria

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Teva Investigational Site 3302

Sankt Pölten, , Austria

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Teva Investigational Site 3301

Villach, , Austria

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Teva Investigational Site 5901

Pleven, , Bulgaria

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Teva Investigational Site 5904

Sofia, , Bulgaria

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Teva Investigational Site 5903

Sofia, , Bulgaria

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Teva Investigational Site 5900

Sofia, , Bulgaria

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Teva Investigational Site 5905

Sofia, , Bulgaria

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Teva Investigational Site 5902

Varna, , Bulgaria

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Teva Investigational Site 1132

Halifax, Nova Scotia, Canada

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Teva Investigational Site 1126

London, Ontario, Canada

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Teva Investigational Site 1128

Ottawa, Ontario, Canada

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Teva Investigational Site 1134

Toronto, Ontario, Canada

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Teva Investigational Site 1130

Greenfield Park, Quebec, Canada

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Teva Investigational Site 1129

Montreal, Quebec, Canada

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Teva Investigational Site 1131

Sherbrooke, Quebec, Canada

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Teva Investigational Site 5417

Olomouc, , Czechia

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Teva Investigational Site 5416

Ostrava - Poruba, , Czechia

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Teva Investigational Site 5504

Tallinn, , Estonia

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Teva Investigational Site 5505

Tartu, , Estonia

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Teva Investigational Site 3525

Besançon, , France

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Teva Investigational Site 3527

Bron, , France

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Teva Investigational Site 3526

Clermont-Ferrand, , France

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Teva Investigational Site 3524

Lille, , France

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Teva Investigational Site 3528

Marseille, , France

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Teva Investigational Site 3529

Rennes, , France

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Teva Investigational Site 8100

Tbilisi, , Georgia

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Teva Investigational Site 8101

Tbilisi, , Georgia

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Teva Investigational Site 3247

Bayreuth, , Germany

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Teva Investigational Site 3241

Berlin, , Germany

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Teva Investigational Site 3238

Berlin, , Germany

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Teva Investigational Site 3248

Bochum, , Germany

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Teva Investigational Site 3245

Dresden, , Germany

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Teva Investigational Site 3237

Emden, , Germany

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Teva Investigational Site 3242

Erbach im Odenwald, , Germany

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Teva Investigational Site 3240

Erfurt, , Germany

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Teva Investigational Site 3249

Freiburg im Breisgau, , Germany

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Teva Investigational Site 3236

Hamburg, , Germany

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Teva Investigational Site 3246

Hamburg, , Germany

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Teva Investigational Site 3239

Hanover, , Germany

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Teva Investigational Site 3243

Heidelberg, , Germany

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Teva Investigational Site 3251

Münster, , Germany

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Teva Investigational Site 3250

Trier, , Germany

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Teva Investigational Site 3244

Ulm, , Germany

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Teva Investigational Site 5115

Budapest, , Hungary

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Teva Investigational Site 5114

Debrecen, , Hungary

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Teva Investigational Site 5116

Miskolc, , Hungary

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Teva Investigational Site 5117

Veszprém, , Hungary

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Teva Investigational Site 8034

Haifa, , Israel

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Teva Investigational Site 8031

Haifa, , Israel

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Teva Investigational Site 8030

Jerusalem, , Israel

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Teva Investigational Site 8033

Ramat Gan, , Israel

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Teva Investigational Site 8032

Tel Aviv, , Israel

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Teva Investigational Site 3044

Catania, , Italy

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Teva Investigational Site 3045

Fidenza, , Italy

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Teva Investigational Site 3042

Gallarate, , Italy

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Teva Investigational Site 3046

Grosseto, , Italy

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Teva Investigational Site 3047

Milan, , Italy

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Teva Investigational Site 3038

Milan, , Italy

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Teva Investigational Site 555

Milan, , Italy

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Teva Investigational Site 3039

Milan, , Italy

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Teva Investigational Site 3041

Palermo, , Italy

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Teva Investigational Site 3040

Rome, , Italy

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Teva Investigational Site 5604

Riga, , Latvia

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Teva Investigational Site 5704

Kaunas, , Lithuania

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Teva Investigational Site 5705

Šiauliai, , Lithuania

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Teva Investigational Site 3809

Groesbeek, , Netherlands

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Teva Investigational Site 3810

Nieuwegein, , Netherlands

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Teva Investigational Site 3811

Tilburg, , Netherlands

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Teva Investigational Site 5322

Częstochowa, , Poland

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Teva Investigational Site 5319

Gmina Końskie, , Poland

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Teva Investigational Site 5320

Gorzów Wielkopolski, , Poland

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Teva Investigational Site 5316

Katowice, , Poland

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Teva Investigational Site 5318

Kielce, , Poland

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Teva Investigational Site 5317

Krakow, , Poland

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Teva Investigational Site 5315

Lodz, , Poland

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Teva Investigational Site 5325

Warsaw, , Poland

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Teva Investigational Site 5208

Bucharest, , Romania

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Teva Investigational Site 5210

Cluj-Napoca, , Romania

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Teva Investigational Site 5212

Constanța, , Romania

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Teva Investigational Site 5211

Târgu Mureş, , Romania

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Teva Investigational Site 5209

Timișoara, , Romania

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Teva Investigational Site 5031

Kemerovo, , Russia

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Teva Investigational Site 5021

Moscow, , Russia

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Teva Investigational Site 5028

Nizhny Novgorod, , Russia

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Teva Investigational Site 5027

Novosibirsk, , Russia

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Teva Investigational Site 5030

Perm, , Russia

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Teva Investigational Site 5026

Saint Petersburg, , Russia

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Teva Investigational Site 5025

Saint Petersburg, , Russia

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Teva Investigational Site 5024

Saint Petersburg, , Russia

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Teva Investigational Site 5022

Saint Petersburg, , Russia

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Teva Investigational Site 5023

Saint Petersburg, , Russia

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Teva Investigational Site 5029

Yekaterinburg, , Russia

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Teva Investigational Site 6100

Belgrade, , Serbia

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Teva Investigational Site 6102

Niš, , Serbia

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Teva Investigational Site 3132

Barcelona, , Spain

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Teva Investigational Site 3134

Barcelona, , Spain

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Teva Investigational Site 3144

Barcelona, , Spain

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Teva Investigational Site 3140

Beade-Vigo, , Spain

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Teva Investigational Site 3142

Getafe, , Spain

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Teva Investigational Site 3136

Girona, , Spain

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Teva Investigational Site 3135

Lleida, , Spain

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Teva Investigational Site 3133

Madrid, , Spain

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Teva Investigational Site 3146

Madrid, , Spain

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Teva Investigational Site 3137

Murcia, , Spain

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Teva Investigational Site 3138

Pontevedra, , Spain

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Teva Investigational Site 3139

Santiago de Compostela, , Spain

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Teva Investigational Site 3143

Valencia, , Spain

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Teva Investigational Site 4204

Stockholm, , Sweden

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Teva Investigational Site 4205

Stockholm, , Sweden

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Teva Investigational Site 4206

Stockholm, , Sweden

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Teva Investigational Site 8201

Izmir, , Turkey (Türkiye)

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Teva Investigational Site 5803

Dnipropetrovsk, , Ukraine

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Teva Investigational Site 5802

Kyiv, , Ukraine

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Teva Investigational Site 5804

Kyiv, , Ukraine

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Teva Investigational Site 5800

Lviv, , Ukraine

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Teva Investigational Site 5801

Vinnytsia, , Ukraine

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Teva Investigational Site 3425

Liverpool, , United Kingdom

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Teva Investigational Site 3424

London, , United Kingdom

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Teva Investigational Site 3422

Sheffield, , United Kingdom

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Countries

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Portugal Serbia and Montenegro United States Austria Bulgaria Canada Czechia Estonia France Georgia Germany Hungary Israel Italy Latvia Lithuania Netherlands Poland Romania Russia Serbia Spain Sweden Turkey (Türkiye) Ukraine United Kingdom

References

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Kolb-Sobieraj C, Gupta S, Weinstock-Guttman B. Laquinimod therapy in multiple sclerosis: a comprehensive review. Neurol Ther. 2014 May 6;3(1):29-39. doi: 10.1007/s40120-014-0017-6. eCollection 2014 Jun.

Reference Type DERIVED
PMID: 26000222 (View on PubMed)

Filippi M, Rocca MA, Pagani E, De Stefano N, Jeffery D, Kappos L, Montalban X, Boyko AN, Comi G; ALLEGRO Study Group. Placebo-controlled trial of oral laquinimod in multiple sclerosis: MRI evidence of an effect on brain tissue damage. J Neurol Neurosurg Psychiatry. 2014 Aug;85(8):851-8. doi: 10.1136/jnnp-2013-306132. Epub 2013 Sep 12.

Reference Type DERIVED
PMID: 24029546 (View on PubMed)

Comi G, Jeffery D, Kappos L, Montalban X, Boyko A, Rocca MA, Filippi M; ALLEGRO Study Group. Placebo-controlled trial of oral laquinimod for multiple sclerosis. N Engl J Med. 2012 Mar 15;366(11):1000-9. doi: 10.1056/NEJMoa1104318.

Reference Type DERIVED
PMID: 22417253 (View on PubMed)

Other Identifiers

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EUDRACT 2007-003226-19

Identifier Type: -

Identifier Source: secondary_id

MS-LAQ-301

Identifier Type: -

Identifier Source: org_study_id