Trial Outcomes & Findings for A Study of MabThera (Rituximab) in Combination With Methotrexate in Patients With Rheumatoid Arthritis Who Have Had an Inadequate Response to Anti-TNF Agents. (NCT NCT00504777)

NCT ID: NCT00504777

Last Updated: 2014-08-04

Results Overview

DAS28 was calculated from the number of swollen joints, or swollen joint count (SJC) and tender joint count (TJC) using the 28 joints count, the erythrocyte sedimentation rate (ESR) (measured in millimeters per hour \[mm/hr\]), and Patient Global Assessment of Disease Activity (participant rated arthritis activity assessment) with transformed scores ranging 0 to 10; higher scores indicated greater affectation due to disease activity. A clinically significant improvement in DAS28 was a change of at least 1.2 units.

Recruitment status

COMPLETED

Study phase

PHASE4

Target enrollment

36 participants

Primary outcome timeframe

Week 24

Results posted on

2014-08-04

Participant Flow

Participant milestones

Participant milestones
Measure
Rituximab + Methotrexate (MTX)
Participants received rituximab 1000 milligrams (mg) intravenously (IV) and 100 mg methylprednisolone IV on Days 1 and 15. Participants were to be receiving background MTX (10-25 mg weekly, oral or parenteral dose).
Overall Study
STARTED
36
Overall Study
COMPLETED
35
Overall Study
NOT COMPLETED
1

Reasons for withdrawal

Reasons for withdrawal
Measure
Rituximab + Methotrexate (MTX)
Participants received rituximab 1000 milligrams (mg) intravenously (IV) and 100 mg methylprednisolone IV on Days 1 and 15. Participants were to be receiving background MTX (10-25 mg weekly, oral or parenteral dose).
Overall Study
Adverse Event
1

Baseline Characteristics

A Study of MabThera (Rituximab) in Combination With Methotrexate in Patients With Rheumatoid Arthritis Who Have Had an Inadequate Response to Anti-TNF Agents.

Baseline characteristics by cohort

Baseline characteristics by cohort
Measure
Rituximab + MTX
n=36 Participants
Participants received rituximab 1000 mg IV, and 100 mg methylprednisolone IV on Days 1 and 15. Participants were to be receiving background MTX (10-25 mg weekly, oral or parenteral dose).
Age, Continuous
50.72 years
STANDARD_DEVIATION 13.42 • n=5 Participants
Sex: Female, Male
Female
33 Participants
n=5 Participants
Sex: Female, Male
Male
3 Participants
n=5 Participants

PRIMARY outcome

Timeframe: Week 24

Population: ITT Population

DAS28 was calculated from the number of swollen joints, or swollen joint count (SJC) and tender joint count (TJC) using the 28 joints count, the erythrocyte sedimentation rate (ESR) (measured in millimeters per hour \[mm/hr\]), and Patient Global Assessment of Disease Activity (participant rated arthritis activity assessment) with transformed scores ranging 0 to 10; higher scores indicated greater affectation due to disease activity. A clinically significant improvement in DAS28 was a change of at least 1.2 units.

Outcome measures

Outcome measures
Measure
Rituximab + MTX
n=36 Participants
Participants received rituximab 1000 mg IV and 100 mg methylprednisolone IV on Days 1 and 15. Participants were to be receiving background MTX (10-25 mg weekly, oral or parenteral dose).
Change From Baseline in Disease Activity Score Based on 28-Joint Count (DAS28)
Baseline
5.51 scores on a scale
Standard Deviation 1.05
Change From Baseline in Disease Activity Score Based on 28-Joint Count (DAS28)
Week 24
4.39 scores on a scale
Standard Deviation 1.21
Change From Baseline in Disease Activity Score Based on 28-Joint Count (DAS28)
Change from Baseline to Week 24
-1.12 scores on a scale
Standard Deviation 1.19

SECONDARY outcome

Timeframe: Week 24

Population: ITT Population

ACR20/50/70 response defined as greater than or equal to (≥)20 percent (%), 50%, or 70% improvement, respectively, in TJC and SJC, and ≥20%/50%/70% improvement in at least 3 of 5 remaining ACR core measures: Patient Assessment of Pain, Patient Global Assessment of Disease Activity, Physician Global Assessment of Disease Activity, self-assessed disability based on the Health Assessment Questionnaire-Disability Index (HAQ-DI), and C-Reactive Protein (CRP).

Outcome measures

Outcome measures
Measure
Rituximab + MTX
n=36 Participants
Participants received rituximab 1000 mg IV and 100 mg methylprednisolone IV on Days 1 and 15. Participants were to be receiving background MTX (10-25 mg weekly, oral or parenteral dose).
Percentage of Participants Achieving American College of Rheumatology (ACR) Response
ACR20
2.78 percentage of participants
Percentage of Participants Achieving American College of Rheumatology (ACR) Response
ACR50
0 percentage of participants
Percentage of Participants Achieving American College of Rheumatology (ACR) Response
ACR70
0 percentage of participants

SECONDARY outcome

Timeframe: Week 24

Population: ITT Population

Percentage of participants with a EULAR response at Week 24 based on a scale of good response, moderate response, or no response. The DAS28-based EULAR response criteria were used to measure individual response as none, good, and moderate, depending on the extent of change from baseline and the level of disease activity reached. Good responders have a change from baseline greater than (\>)1.2 with DAS28 less than or equal to (≤)3.2; moderate responders have a change from baseline \>1.2 with DAS28 \>3.2 to ≤5.1 or change from baseline \>0.6 to ≤1.2 with DAS28 ≤5.1; non-responders have a change from baseline ≤0.6 or change from baseline \>0.6 and ≤1.2 with DAS28 \>5.1.

Outcome measures

Outcome measures
Measure
Rituximab + MTX
n=36 Participants
Participants received rituximab 1000 mg IV and 100 mg methylprednisolone IV on Days 1 and 15. Participants were to be receiving background MTX (10-25 mg weekly, oral or parenteral dose).
Percentage of Participants Achieving a Response by European League Against Rheumatism (EULAR) Category
Good response
0 percentage of participants
Percentage of Participants Achieving a Response by European League Against Rheumatism (EULAR) Category
Moderate response
58.33 percentage of participants
Percentage of Participants Achieving a Response by European League Against Rheumatism (EULAR) Category
No response
41.67 percentage of participants

SECONDARY outcome

Timeframe: Week 24

Population: ITT Population

The Stanford HAQ-DI is a patient-reported questionnaire specific for rheumatoid arthritis. It consists of 20 questions referring to 8 component sets: dressing/grooming, arising, eating, walking, hygiene, reach, grip, and activities. Responses in each component set are scored from 0 (without any difficulty) to 3 (unable to do). The highest score recorded for any question in a category determines the score for the category, unless aids, devices, or help from another person is required. The HAQ-DI score is calculated as the sum of the category scores divided by the number of categories scored, giving a possible range of scores from 0 to 3. Scores of 0 to 1 are generally considered to represent "mild to moderate difficulty", 1 to 2 as "moderate to severe disability", and 2 to 3 as "severe to very severe disability".

Outcome measures

Outcome measures
Measure
Rituximab + MTX
n=36 Participants
Participants received rituximab 1000 mg IV and 100 mg methylprednisolone IV on Days 1 and 15. Participants were to be receiving background MTX (10-25 mg weekly, oral or parenteral dose).
Change From Baseline in HAQ-DI Score
Baseline
1.07 scores on a scale
Standard Deviation 0.69
Change From Baseline in HAQ-DI Score
Week 24
0.81 scores on a scale
Standard Deviation 0.65
Change From Baseline in HAQ-DI Score
Change from Baseline to Week 24
-0.26 scores on a scale
Standard Deviation 0.52

Adverse Events

Rituximab + MTX

Serious events: 3 serious events
Other events: 22 other events
Deaths: 0 deaths

Serious adverse events

Serious adverse events
Measure
Rituximab + MTX
n=36 participants at risk
Participants received rituximab 1000 mg IV and 100 mg methylprednisolone IV on Days 1 and 15. Participants were to be receiving background MTX (10-25 mg weekly, oral or parenteral dose).
Musculoskeletal and connective tissue disorders
Spinal column stenosis
2.8%
1/36 • 24 weeks
Hepatobiliary disorders
Cholelithiasis
2.8%
1/36 • 24 weeks
Musculoskeletal and connective tissue disorders
Back pain
2.8%
1/36 • 24 weeks

Other adverse events

Other adverse events
Measure
Rituximab + MTX
n=36 participants at risk
Participants received rituximab 1000 mg IV and 100 mg methylprednisolone IV on Days 1 and 15. Participants were to be receiving background MTX (10-25 mg weekly, oral or parenteral dose).
Blood and lymphatic system disorders
Leukocytosis
2.8%
1/36 • 24 weeks
Blood and lymphatic system disorders
Mononucleosis syndrome
2.8%
1/36 • 24 weeks
Cardiac disorders
Dizziness
5.6%
2/36 • 24 weeks
Gastrointestinal disorders
Abdominal pain upper
2.8%
1/36 • 24 weeks
Gastrointestinal disorders
Diarrhoea
2.8%
1/36 • 24 weeks
Gastrointestinal disorders
Gastritis
2.8%
1/36 • 24 weeks
Gastrointestinal disorders
Gingival bleeding
2.8%
1/36 • 24 weeks
Gastrointestinal disorders
Hiatus hernia
2.8%
1/36 • 24 weeks
Gastrointestinal disorders
Mouth ulceration
2.8%
1/36 • 24 weeks
Gastrointestinal disorders
Oesophageal candidiasis
2.8%
1/36 • 24 weeks
Gastrointestinal disorders
Peptic ulcer
2.8%
1/36 • 24 weeks
General disorders
Fatigue
5.6%
2/36 • 24 weeks
General disorders
Oedema peripheral
2.8%
1/36 • 24 weeks
Hepatobiliary disorders
Hepatic function abnormal
2.8%
1/36 • 24 weeks
Infections and infestations
Respiratory tract infection
2.8%
1/36 • 24 weeks
Infections and infestations
Upper respiratory tract infection
22.2%
8/36 • 24 weeks
Investigations
Alanine aminotransferase increased
2.8%
1/36 • 24 weeks
Investigations
Blood pressure decreased
2.8%
1/36 • 24 weeks
Investigations
Blood pressure increased
2.8%
1/36 • 24 weeks
Investigations
Weight increased
2.8%
1/36 • 24 weeks
Metabolism and nutrition disorders
Hyperlipidaemia
2.8%
1/36 • 24 weeks
Musculoskeletal and connective tissue disorders
Arthralgia
2.8%
1/36 • 24 weeks
Musculoskeletal and connective tissue disorders
Back pain
2.8%
1/36 • 24 weeks
Musculoskeletal and connective tissue disorders
Joint dislocation
2.8%
1/36 • 24 weeks
Musculoskeletal and connective tissue disorders
Myalgia
2.8%
1/36 • 24 weeks
Neoplasms benign, malignant and unspecified (incl cysts and polyps)
Adenoma benign
2.8%
1/36 • 24 weeks
Psychiatric disorders
Insomnia
2.8%
1/36 • 24 weeks
Reproductive system and breast disorders
Menorrhagia
2.8%
1/36 • 24 weeks
Respiratory, thoracic and mediastinal disorders
Chronic obstructive pulmonary disease
2.8%
1/36 • 24 weeks
Respiratory, thoracic and mediastinal disorders
Cough
13.9%
5/36 • 24 weeks
Respiratory, thoracic and mediastinal disorders
Nasal obstruction
2.8%
1/36 • 24 weeks
Respiratory, thoracic and mediastinal disorders
Nasopharyngitis
5.6%
2/36 • 24 weeks
Respiratory, thoracic and mediastinal disorders
Rhinitis allergic
2.8%
1/36 • 24 weeks
Respiratory, thoracic and mediastinal disorders
Wheezing
2.8%
1/36 • 24 weeks
Skin and subcutaneous tissue disorders
Acne
2.8%
1/36 • 24 weeks
Skin and subcutaneous tissue disorders
Eczema
2.8%
1/36 • 24 weeks
Skin and subcutaneous tissue disorders
Rash
5.6%
2/36 • 24 weeks
Skin and subcutaneous tissue disorders
Seborrhoeic dermatitis
2.8%
1/36 • 24 weeks
Vascular disorders
Hypertension
5.6%
2/36 • 24 weeks

Additional Information

Medical Communications

Hoffmann-LaRoche

Phone: 800-821-8590

Results disclosure agreements

  • Principal investigator is a sponsor employee The Study being conducted under this Agreement is part of the Overall Study. Investigator is free to publish in reputable journals or to present at professional conferences the results of the Study, but only after the first publication or presentation that involves the Overall Study. The Sponsor may request that Confidential Information be deleted and/or the publication be postponed in order to protect the Sponsor's intellectual property rights.
  • Publication restrictions are in place

Restriction type: OTHER