2-Chlorodeoxyadenosine and Cytarabine in Patients With Idiopathic Hypereosinophilic Syndrome (HES)

NCT ID: NCT00483067

Last Updated: 2012-08-02

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE2

Total Enrollment

13 participants

Study Classification

INTERVENTIONAL

Study Start Date

1998-03-31

Study Completion Date

2008-07-31

Brief Summary

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Primary Objectives:

1. To determine the response rate, progression-free survival (PFS) and overall survival of patients who receive 2-CdA + Ara-C.
2. To examine if there is any clonality in the cytokine expression of helper T cells or cytokine receptor expression of eosinophils.
3. To determine the effect of 2-CdA on accumulation of Ara-C triphosphate in eosinophils.

Detailed Description

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Before the study begins, patients will have a physical exam, blood tests, and urine tests. Women will have a pregnancy test. A bone marrow sample will be taken. This is done with a large needle. Heart tests and an MRI scan of the brain will be done if there is a suspicion of disease in the heart or central nervous system.

Patients in this study must have a catheter (thin tube) placed in a vein in the arm or under the collarbone. This tube will be left in place throughout the study. 2-CdA (Cladribine) will be given through the catheter 24 hours a day on days 2 to 6. Ara-C (Cytarabine) will be given through the catheter over 2 hours on days 1, 3, 4, 5, and 6. Starting on day 9, patients will inject G-CSF under their skin once a day; G-CSF helps blood counts return to normal. Treatment will be given on an inpatient or outpatient basis. The first course is normally done inpatient.

During the study, patients will have blood tests daily during the first week and every other day after that. Bone marrow samples will be taken on days 14, 21, and 28. Further bone marrow samples may be necessary to evaluate response. Heart tests and MRI scans of the brain may be done.

This is an investigational study. G-CSF, 2-CdA, and Cytarabine are approved by the FDA for treatment of cancer. Up to 40 patients will take part in this study. Patients will be treated at M. D. Anderson or other centers. A total of 40 people will take part in this study. About 1 patient every 3 months will be enrolled at M. D. Anderson.

Conditions

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Leukemia

Keywords

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Idiopathic Hypereosinophilic Syndrome Leukemia 2-Chlorodeoxyadenosine Cladribine Cytarabine Ara-C 2-CdA G-CSF HES

Study Design

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Allocation Method

NON_RANDOMIZED

Intervention Model

SINGLE_GROUP

Primary Study Purpose

TREATMENT

Blinding Strategy

NONE

Study Groups

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2-CdA + Ara-C + G-CSF

2-CdA 12 mg/m\^2/day by vein (IV) Continuous Infusion and Ara-C 1 gm/m\^2/day IV for 5 Days with G-CSF 5 mcg/kg/day subcutaneously starting Day 9

Group Type EXPERIMENTAL

2-CdA

Intervention Type DRUG

12 mg/m\^2/day by vein (IV) Continuous Infusion x 5 Days

Ara-C

Intervention Type DRUG

1 gm/m\^2/day IV Over 2 Hours x 5 Days

G-CSF (Granulocyte colony-stimulating factor)

Intervention Type DRUG

5 mcg/kg/day given under the skin (subcutaneously) starting Day 9

Interventions

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2-CdA

12 mg/m\^2/day by vein (IV) Continuous Infusion x 5 Days

Intervention Type DRUG

Ara-C

1 gm/m\^2/day IV Over 2 Hours x 5 Days

Intervention Type DRUG

G-CSF (Granulocyte colony-stimulating factor)

5 mcg/kg/day given under the skin (subcutaneously) starting Day 9

Intervention Type DRUG

Other Intervention Names

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2-Chlorodeoxyadenosine Cladribine Cytarabine Filgrastim Neupogen Granulocyte colony-stimulating factor GCSF

Eligibility Criteria

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Inclusion Criteria

1. Patient must have diagnosis of idiopathic HES, defined as (1) no recent history of allergic reaction or parasitic infection; (2) sustained (\> 6 months) hypereosinophilia (1,500/mm\^3); and (3) signs or symptoms of organ involvement.
2. Age less than 76 years old.
3. Patient is not pregnant.
4. Zubrod performance status \< 3.
5. Life expectancy is not severely limited by concomitant illness.
6. Serum creatinine \< 2 mg/dL.
7. Serum bilirubin \< 2 times upper limit of normal (2 mg/dL).
8. Alanine aminotransferase (SGPT) \< 2 times upper limit of normal (112 IU/L).
9. Participant has completed the informed consent process, understands the investigational nature of the study, agrees to participate, and has signed the informed consent.

Exclusion Criteria

1. Evidence of chronic active hepatitis or cirrhosis, and \> 1 month from prior episode of hepatitis.
2. Presence of an active infection.
3. HIV positive.
4. Has eosinophilic leukemia (defined by presence of clonal cytogenetic abnormalities).
5. Recent history of parasite infection.
6. Recent history of allergic reaction.
Maximum Eligible Age

76 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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M.D. Anderson Cancer Center

OTHER

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Michael Andreeff, MD, PhD

Role: PRINCIPAL_INVESTIGATOR

M.D. Anderson Cancer Center

Locations

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U.T.M.D. Anderson Cancer Center

Houston, Texas, United States

Site Status

Countries

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United States

Related Links

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http://www.mdanderson.org

UT MD Anderson Cancer Center website

Other Identifiers

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DM97-232

Identifier Type: -

Identifier Source: org_study_id