Trial Outcomes & Findings for A Study of Enzastaurin in Participants With Follicular Lymphoma (NCT NCT00475644)

NCT ID: NCT00475644

Last Updated: 2018-11-05

Results Overview

Tumor response rate is defined as the number of responders divided by the number of treated patients. A responder is a patient who exhibits a complete response (CR), complete response unconfirmed (CRu), or partial response (PR) as defined by Cheson et al. CR, the disappearance of target lesions and any pathological lymph nodes \[target or non-target\] taking as reference the baseline sum of diameters in response to treatment; CRu, complete disappearance of all detectable clinical and radiographic evidence of disease, return of spleen to non-palpable if involved, residual lymph node mass greater than 1.5 centimeters (cm) has regressed by more than 75%; PR, 50% decrease in the sum of the products of the greatest diameter (SPD) of the 6 largest dominant masses, no increase of other nodes, liver or spleen and no new sites of disease.

Recruitment status

COMPLETED

Study phase

PHASE2

Target enrollment

66 participants

Primary outcome timeframe

Baseline to Measured Progressive Disease (up to 1559 Days)

Results posted on

2018-11-05

Participant Flow

Participants who were considered to have completed the study who received at least 1 dose of study drug, did not have any protocol violations, and from whom a valid assay result was obtained.

Participant milestones

Participant milestones
Measure
Enzastaurin
Enzastaurin 500 milligram (mg) administered orally (PO) each day (QD) after an initial loading dose of 1125 mg on Day 1.
Overall Study
STARTED
66
Overall Study
Received at Least One Dose of Study Drug
66
Overall Study
COMPLETED
53
Overall Study
NOT COMPLETED
13

Reasons for withdrawal

Reasons for withdrawal
Measure
Enzastaurin
Enzastaurin 500 milligram (mg) administered orally (PO) each day (QD) after an initial loading dose of 1125 mg on Day 1.
Overall Study
Protocol Violation
13

Baseline Characteristics

A Study of Enzastaurin in Participants With Follicular Lymphoma

Baseline characteristics by cohort

Baseline characteristics by cohort
Measure
Enzastaurin
n=66 Participants
Enzastaurin 500 milligram (mg) administered orally (PO) each day (QD) after an initial loading dose of 1125 mg on Day 1.
Age, Continuous
60.55 years
STANDARD_DEVIATION 11.851 • n=5 Participants
Sex: Female, Male
Female
43 Participants
n=5 Participants
Sex: Female, Male
Male
23 Participants
n=5 Participants
Ethnicity (NIH/OMB)
Hispanic or Latino
3 Participants
n=5 Participants
Ethnicity (NIH/OMB)
Not Hispanic or Latino
63 Participants
n=5 Participants
Ethnicity (NIH/OMB)
Unknown or Not Reported
0 Participants
n=5 Participants
Race (NIH/OMB)
American Indian or Alaska Native
0 Participants
n=5 Participants
Race (NIH/OMB)
Asian
0 Participants
n=5 Participants
Race (NIH/OMB)
Native Hawaiian or Other Pacific Islander
0 Participants
n=5 Participants
Race (NIH/OMB)
Black or African American
2 Participants
n=5 Participants
Race (NIH/OMB)
White
61 Participants
n=5 Participants
Race (NIH/OMB)
More than one race
0 Participants
n=5 Participants
Race (NIH/OMB)
Unknown or Not Reported
3 Participants
n=5 Participants

PRIMARY outcome

Timeframe: Baseline to Measured Progressive Disease (up to 1559 Days)

Population: Participants who received at least 1 dose of study drug and did not violate any study criteria.

Tumor response rate is defined as the number of responders divided by the number of treated patients. A responder is a patient who exhibits a complete response (CR), complete response unconfirmed (CRu), or partial response (PR) as defined by Cheson et al. CR, the disappearance of target lesions and any pathological lymph nodes \[target or non-target\] taking as reference the baseline sum of diameters in response to treatment; CRu, complete disappearance of all detectable clinical and radiographic evidence of disease, return of spleen to non-palpable if involved, residual lymph node mass greater than 1.5 centimeters (cm) has regressed by more than 75%; PR, 50% decrease in the sum of the products of the greatest diameter (SPD) of the 6 largest dominant masses, no increase of other nodes, liver or spleen and no new sites of disease.

Outcome measures

Outcome measures
Measure
Enzastaurin
n=53 Participants
Enzastaurin 500 milligram (mg) administered orally (PO) each day (QD) after an initial loading dose of 1125 mg on Day 1.
Tumor Response Rate (RR) (Percentage of Participants Exhibiting Complete Response [CR] or Complete Response Unconfirmed [CRu] or Partial Response [PR])
26.4 percentage of participants
Interval 15.3 to 40.3

SECONDARY outcome

Timeframe: Baseline to Measured Progressive Disease or Death from Any Cause (Up to 1559 Days)

Population: Participants who received at least 1 dose of study drug and who did not violate any study entry criteria. There were 18 censored participants.

PFS is defined as the time from the date of study enrollment to the first date of measured progressive disease or death from any cause. For patients not known to have died as of the data cut-off date and who do not have objective progressive disease, PFS will be censored at the date of the last objective progression-free assessment. For patients who receive subsequent anticancer therapy (after discontinuation from the study treatment) prior to objective disease progression or death, PFS will be censored at the date of last objective progression-free assessment prior to the initiation of postdiscontinuation anticancer therapy. For reference, PFS will also be calculated and analyzed based on an alternative definition of censoring: for each patient who is not known to have died or to have had objective progression of disease as of the data cut-off date, PFS will be censored for that analysis at the date of last prior contact.

Outcome measures

Outcome measures
Measure
Enzastaurin
n=53 Participants
Enzastaurin 500 milligram (mg) administered orally (PO) each day (QD) after an initial loading dose of 1125 mg on Day 1.
Progression-Free Survival (PFS)
551.0 Days
Interval 350.0 to 863.0

SECONDARY outcome

Timeframe: Baseline to Date of Confirmed Response (Up to 890 Days)

Population: Participants who received at least 1 dose of study drug and did not violate any study entry criteria and who had baseline and post-baseline response data.

TtR is defined as the time from the date of study enrollment to the date of response (CR, CRu, or PR) for patients who have responded prior to receiving any subsequent anticancer therapy.CR, the disappearance of target lesions and any pathological lymph nodes \[target or non-target\] taking as reference the baseline sum of diameters in response to treatment; CRu, complete disappearance of all detectable clinical and radiographic evidence of disease, return of spleen to non-palpable if involved, residual lymph node mass greater than 1.5 centimeters (cm) has regressed by more than 75%; PR, 50% decrease in the sum of the products of the greatest diameter (SPD) of the 6 largest dominant masses, no increase of other nodes, liver or spleen and no new sites of disease.

Outcome measures

Outcome measures
Measure
Enzastaurin
n=14 Participants
Enzastaurin 500 milligram (mg) administered orally (PO) each day (QD) after an initial loading dose of 1125 mg on Day 1.
Time to Response (TtR)
148.0 Days
Interval 84.0 to 246.0

SECONDARY outcome

Timeframe: Time of Response to Measured Progressive Disease (Up to 1415 Days)

Population: Participants who received at least 1 dose of study drug, did not violate any study entry criteria and had baseline and post-baseline response data. There were 4 censored participants.

DoR is defined as the time from the date when the measurement criteria are met for CR, CRu, or PR (whichever status is recorded first) until the date of first observation of measured progressive disease. For responding participants who die without progressive disease (including death from study disease), DoR will be censored at the date of death. For responding participants not known to have died as of the data cut-off date and who do not have progressive disease, DoR will be censored at the last objective progression-free assessment date prior to the data cut-off date. For responding participants who receive subsequent anticancer therapy (after discontinuation from the study treatment) prior to disease progression, DoR will be censored at the date of last objective progression-free assessment prior to the initiation of postdiscontinuation anticancer therapy.

Outcome measures

Outcome measures
Measure
Enzastaurin
n=14 Participants
Enzastaurin 500 milligram (mg) administered orally (PO) each day (QD) after an initial loading dose of 1125 mg on Day 1.
Duration of Response (DoR)
677.5 Days
Interval 269.0 to
Data is not available to be presented because endpoint was not reached.

SECONDARY outcome

Timeframe: Baseline

Population: The TR (Translational Research) population consisted of participants from whom tumor tissue was obtained.

Correlative analyses of tumor RR for PKC-β2 (protein kinase C-β) protein expression. Immunohistochemistry (IHC) staining was performed to assess protein expression of PKC-β2 in cytoplasm reported as H scores (logistic model of response rate), which was derived from a weighted average of staining intensity (scale 0 to 3, increasing intensity) and percentage of positive cells (0 to 100%) at each staining intensity. PKC-β2 expression was further classified into high vs. low expression using the cutpoint of the median of the distribution of PKC-β2 H scores.

Outcome measures

Outcome measures
Measure
Enzastaurin
n=12 Participants
Enzastaurin 500 milligram (mg) administered orally (PO) each day (QD) after an initial loading dose of 1125 mg on Day 1.
Number of Participants With Response With Expression of Protein Biomarkers
High Expression
1 participants
Number of Participants With Response With Expression of Protein Biomarkers
Low Expression
5 participants

Adverse Events

Enzastaurin

Serious events: 16 serious events
Other events: 58 other events
Deaths: 0 deaths

Serious adverse events

Serious adverse events
Measure
Enzastaurin
n=66 participants at risk
Enzastaurin 500 milligram (mg) administered orally (PO) each day (QD) after an initial loading dose of 1125 mg on Day 1.
Cardiac disorders
Angina pectoris
1.5%
1/66 • Number of events 1
Cardiac disorders
Palpitations
1.5%
1/66 • Number of events 1
Eye disorders
Visual acuity reduced
1.5%
1/66 • Number of events 1
Gastrointestinal disorders
Diarrhoea
1.5%
1/66 • Number of events 2
Gastrointestinal disorders
Gastrooesophageal reflux disease
1.5%
1/66 • Number of events 1
Gastrointestinal disorders
Pancreatitis
1.5%
1/66 • Number of events 1
Gastrointestinal disorders
Pancreatitis acute
1.5%
1/66 • Number of events 1
Hepatobiliary disorders
Cholecystitis
1.5%
1/66 • Number of events 1
Hepatobiliary disorders
Cholelithiasis
1.5%
1/66 • Number of events 2
Infections and infestations
Bronchitis
1.5%
1/66 • Number of events 1
Infections and infestations
Sepsis
1.5%
1/66 • Number of events 1
Injury, poisoning and procedural complications
Ankle fracture
1.5%
1/66 • Number of events 6
Injury, poisoning and procedural complications
Femur fracture
1.5%
1/66 • Number of events 1
Injury, poisoning and procedural complications
Fractured sacrum
1.5%
1/66 • Number of events 2
Injury, poisoning and procedural complications
Incisional hernia
1.5%
1/66 • Number of events 1
Metabolism and nutrition disorders
Dehydration
1.5%
1/66 • Number of events 1
Metabolism and nutrition disorders
Failure to thrive
1.5%
1/66 • Number of events 1
Metabolism and nutrition disorders
Hypertriglyceridaemia
1.5%
1/66 • Number of events 1
Metabolism and nutrition disorders
Hypokalaemia
1.5%
1/66 • Number of events 2
Neoplasms benign, malignant and unspecified (incl cysts and polyps)
Breast cancer
1.5%
1/66 • Number of events 2
Neoplasms benign, malignant and unspecified (incl cysts and polyps)
Prostate cancer
4.3%
1/23 • Number of events 3
Neoplasms benign, malignant and unspecified (incl cysts and polyps)
Rectal adenoma
1.5%
1/66 • Number of events 1
Psychiatric disorders
Mental status changes
1.5%
1/66 • Number of events 1
Renal and urinary disorders
Renal mass
1.5%
1/66 • Number of events 1
Respiratory, thoracic and mediastinal disorders
Dyspnoea
1.5%
1/66 • Number of events 1
Respiratory, thoracic and mediastinal disorders
Pulmonary embolism
1.5%
1/66 • Number of events 1
Vascular disorders
Deep vein thrombosis
1.5%
1/66 • Number of events 1

Other adverse events

Other adverse events
Measure
Enzastaurin
n=66 participants at risk
Enzastaurin 500 milligram (mg) administered orally (PO) each day (QD) after an initial loading dose of 1125 mg on Day 1.
Blood and lymphatic system disorders
Anaemia
13.6%
9/66 • Number of events 36
Cardiac disorders
Palpitations
6.1%
4/66 • Number of events 19
Gastrointestinal disorders
Abdominal distension
10.6%
7/66 • Number of events 29
Gastrointestinal disorders
Abdominal pain
12.1%
8/66 • Number of events 22
Gastrointestinal disorders
Abdominal pain upper
7.6%
5/66 • Number of events 22
Gastrointestinal disorders
Constipation
15.2%
10/66 • Number of events 53
Gastrointestinal disorders
Diarrhoea
30.3%
20/66 • Number of events 121
Gastrointestinal disorders
Dyspepsia
9.1%
6/66 • Number of events 38
Gastrointestinal disorders
Faeces discoloured
15.2%
10/66 • Number of events 91
Gastrointestinal disorders
Flatulence
7.6%
5/66 • Number of events 21
Gastrointestinal disorders
Nausea
28.8%
19/66 • Number of events 77
Gastrointestinal disorders
Stomatitis
7.6%
5/66 • Number of events 12
Gastrointestinal disorders
Vomiting
7.6%
5/66 • Number of events 5
General disorders
Fatigue
37.9%
25/66 • Number of events 139
General disorders
Oedema peripheral
9.1%
6/66 • Number of events 26
Infections and infestations
Nasopharyngitis
6.1%
4/66 • Number of events 12
Infections and infestations
Oral herpes
6.1%
4/66 • Number of events 13
Infections and infestations
Rhinitis
6.1%
4/66 • Number of events 5
Infections and infestations
Sinusitis
7.6%
5/66 • Number of events 11
Infections and infestations
Upper respiratory tract infection
7.6%
5/66 • Number of events 10
Infections and infestations
Urinary tract infection
7.6%
5/66 • Number of events 6
Metabolism and nutrition disorders
Decreased appetite
6.1%
4/66 • Number of events 10
Musculoskeletal and connective tissue disorders
Arthralgia
16.7%
11/66 • Number of events 56
Musculoskeletal and connective tissue disorders
Back pain
13.6%
9/66 • Number of events 44
Musculoskeletal and connective tissue disorders
Musculoskeletal pain
6.1%
4/66 • Number of events 22
Nervous system disorders
Dizziness
12.1%
8/66 • Number of events 50
Nervous system disorders
Headache
16.7%
11/66 • Number of events 69
Psychiatric disorders
Insomnia
7.6%
5/66 • Number of events 34
Renal and urinary disorders
Chromaturia
21.2%
14/66 • Number of events 114
Respiratory, thoracic and mediastinal disorders
Cough
19.7%
13/66 • Number of events 36
Respiratory, thoracic and mediastinal disorders
Dyspnoea
12.1%
8/66 • Number of events 43
Respiratory, thoracic and mediastinal disorders
Oropharyngeal pain
6.1%
4/66 • Number of events 6
Skin and subcutaneous tissue disorders
Dry skin
6.1%
4/66 • Number of events 26
Skin and subcutaneous tissue disorders
Hyperhidrosis
6.1%
4/66 • Number of events 21
Skin and subcutaneous tissue disorders
Night sweats
12.1%
8/66 • Number of events 36
Skin and subcutaneous tissue disorders
Rash
9.1%
6/66 • Number of events 27
Skin and subcutaneous tissue disorders
Rash pruritic
6.1%
4/66 • Number of events 10

Additional Information

Cheif Medical Officer

Eli Lilly and Company

Phone: 800-545-5979

Results disclosure agreements

  • Principal investigator is a sponsor employee
  • Publication restrictions are in place

Restriction type: GT60