Trial Outcomes & Findings for The Effect of Hormonal Add-Back Therapy in Adolescents Treated With a GnRH Agonist for Endometriosis: A Randomized Trial (NCT NCT00474851)

NCT ID: NCT00474851

Last Updated: 2015-03-30

Results Overview

Adjusted mean change in total body areal bone mineral density (aBMD) over the 12 month trial

Recruitment status

COMPLETED

Study phase

PHASE2

Target enrollment

53 participants

Primary outcome timeframe

Baseline to 12 months

Results posted on

2015-03-30

Participant Flow

Participant milestones

Participant milestones
Measure
Intervention Group
Conjugated equine estrogens: Conjugated estrogens 0.625 mg PO daily Norethindrone acetate: Norethindrone acetate 5 mg PO daily
Placebo Group
Placebo group Placebo: Placebo capsule 1 pill PO daily Norethindrone acetate: Norethindrone acetate 5 mg PO daily
Overall Study
STARTED
26
27
Overall Study
Completed Baseline
25
26
Overall Study
COMPLETED
18
16
Overall Study
NOT COMPLETED
8
11

Reasons for withdrawal

Withdrawal data not reported

Baseline Characteristics

The Effect of Hormonal Add-Back Therapy in Adolescents Treated With a GnRH Agonist for Endometriosis: A Randomized Trial

Baseline characteristics by cohort

Baseline characteristics by cohort
Measure
Intervention Group
n=25 Participants
Conjugated equine estrogens: Conjugated estrogens 0.625 mg PO daily Norethindrone acetate: Norethindrone acetate 5 mg PO daily
Placebo Group
n=26 Participants
Placebo: Placebo capsule 1 pill PO daily Norethindrone acetate: Norethindrone acetate 5 mg PO daily
Total
n=51 Participants
Total of all reporting groups
Age, Continuous
17.7 years
STANDARD_DEVIATION 1.4 • n=5 Participants
18.1 years
STANDARD_DEVIATION 1.9 • n=7 Participants
17.9 years
STANDARD_DEVIATION 1.7 • n=5 Participants
Sex: Female, Male
Female
25 Participants
n=5 Participants
26 Participants
n=7 Participants
51 Participants
n=5 Participants
Sex: Female, Male
Male
0 Participants
n=5 Participants
0 Participants
n=7 Participants
0 Participants
n=5 Participants
Ethnicity (NIH/OMB)
Hispanic or Latino
0 Participants
n=5 Participants
0 Participants
n=7 Participants
0 Participants
n=5 Participants
Ethnicity (NIH/OMB)
Not Hispanic or Latino
25 Participants
n=5 Participants
26 Participants
n=7 Participants
51 Participants
n=5 Participants
Ethnicity (NIH/OMB)
Unknown or Not Reported
0 Participants
n=5 Participants
0 Participants
n=7 Participants
0 Participants
n=5 Participants
Race (NIH/OMB)
American Indian or Alaska Native
0 Participants
n=5 Participants
0 Participants
n=7 Participants
0 Participants
n=5 Participants
Race (NIH/OMB)
Asian
1 Participants
n=5 Participants
0 Participants
n=7 Participants
1 Participants
n=5 Participants
Race (NIH/OMB)
Native Hawaiian or Other Pacific Islander
0 Participants
n=5 Participants
0 Participants
n=7 Participants
0 Participants
n=5 Participants
Race (NIH/OMB)
Black or African American
1 Participants
n=5 Participants
0 Participants
n=7 Participants
1 Participants
n=5 Participants
Race (NIH/OMB)
White
23 Participants
n=5 Participants
26 Participants
n=7 Participants
49 Participants
n=5 Participants
Race (NIH/OMB)
More than one race
0 Participants
n=5 Participants
0 Participants
n=7 Participants
0 Participants
n=5 Participants
Race (NIH/OMB)
Unknown or Not Reported
0 Participants
n=5 Participants
0 Participants
n=7 Participants
0 Participants
n=5 Participants
Region of Enrollment
United States
25 participants
n=5 Participants
26 participants
n=7 Participants
51 participants
n=5 Participants

PRIMARY outcome

Timeframe: Baseline to 12 months

Adjusted mean change in total body areal bone mineral density (aBMD) over the 12 month trial

Outcome measures

Outcome measures
Measure
Intervention Group
n=25 Participants
Conjugated equine estrogens: Conjugated estrogens 0.625 mg PO daily Norethindrone acetate: Norethindrone acetate 5 mg PO daily
Placebo Group
n=26 Participants
Placebo group Placebo: Placebo capsule 1 pill PO daily Norethindrone acetate: Norethindrone acetate 5 mg PO daily
Bone Mineral Density
0.01 g/cm^2
Standard Error 0.006
-0.11 g/cm^2
Standard Error 0.006

SECONDARY outcome

Timeframe: Baseline to 12 months

Outcome measures

Outcome measures
Measure
Intervention Group
n=25 Participants
Conjugated equine estrogens: Conjugated estrogens 0.625 mg PO daily Norethindrone acetate: Norethindrone acetate 5 mg PO daily
Placebo Group
n=26 Participants
Placebo group Placebo: Placebo capsule 1 pill PO daily Norethindrone acetate: Norethindrone acetate 5 mg PO daily
Total Body Bone Mineral Content (BMC)
37 g
Standard Error 10
15 g
Standard Error 11

Adverse Events

Intervention Group

Serious events: 8 serious events
Other events: 15 other events
Deaths: 0 deaths

Placebo Group

Serious events: 5 serious events
Other events: 13 other events
Deaths: 0 deaths

Serious adverse events

Serious adverse events
Measure
Intervention Group
n=25 participants at risk
Conjugated equine estrogens: Conjugated estrogens 0.625 mg PO daily Norethindrone acetate: Norethindrone acetate 5 mg PO daily
Placebo Group
n=26 participants at risk
Placebo group Placebo: Placebo capsule 1 pill PO daily Norethindrone acetate: Norethindrone acetate 5 mg PO daily
Reproductive system and breast disorders
Hospitalization for pelvic/abdominal pain
12.0%
3/25 • Number of events 4 • Adverse events were evaluated every 3 months (at every research visit) for a total of 12 months (the duration of study participation).
0.00%
0/26 • Adverse events were evaluated every 3 months (at every research visit) for a total of 12 months (the duration of study participation).
Gastrointestinal disorders
Rectal bleeding
4.0%
1/25 • Number of events 1 • Adverse events were evaluated every 3 months (at every research visit) for a total of 12 months (the duration of study participation).
0.00%
0/26 • Adverse events were evaluated every 3 months (at every research visit) for a total of 12 months (the duration of study participation).
Psychiatric disorders
Depression
4.0%
1/25 • Number of events 1 • Adverse events were evaluated every 3 months (at every research visit) for a total of 12 months (the duration of study participation).
19.2%
5/26 • Number of events 7 • Adverse events were evaluated every 3 months (at every research visit) for a total of 12 months (the duration of study participation).
Musculoskeletal and connective tissue disorders
Fracture
12.0%
3/25 • Number of events 3 • Adverse events were evaluated every 3 months (at every research visit) for a total of 12 months (the duration of study participation).
0.00%
0/26 • Adverse events were evaluated every 3 months (at every research visit) for a total of 12 months (the duration of study participation).

Other adverse events

Other adverse events
Measure
Intervention Group
n=25 participants at risk
Conjugated equine estrogens: Conjugated estrogens 0.625 mg PO daily Norethindrone acetate: Norethindrone acetate 5 mg PO daily
Placebo Group
n=26 participants at risk
Placebo group Placebo: Placebo capsule 1 pill PO daily Norethindrone acetate: Norethindrone acetate 5 mg PO daily
Musculoskeletal and connective tissue disorders
Myalgias/arthralgias
8.0%
2/25 • Number of events 2 • Adverse events were evaluated every 3 months (at every research visit) for a total of 12 months (the duration of study participation).
7.7%
2/26 • Number of events 2 • Adverse events were evaluated every 3 months (at every research visit) for a total of 12 months (the duration of study participation).
Reproductive system and breast disorders
Pelvic pain
32.0%
8/25 • Number of events 11 • Adverse events were evaluated every 3 months (at every research visit) for a total of 12 months (the duration of study participation).
30.8%
8/26 • Number of events 8 • Adverse events were evaluated every 3 months (at every research visit) for a total of 12 months (the duration of study participation).
Reproductive system and breast disorders
Vaginal bleeding
12.0%
3/25 • Number of events 3 • Adverse events were evaluated every 3 months (at every research visit) for a total of 12 months (the duration of study participation).
7.7%
2/26 • Number of events 2 • Adverse events were evaluated every 3 months (at every research visit) for a total of 12 months (the duration of study participation).
Psychiatric disorders
Mood swings
8.0%
2/25 • Number of events 2 • Adverse events were evaluated every 3 months (at every research visit) for a total of 12 months (the duration of study participation).
3.8%
1/26 • Number of events 1 • Adverse events were evaluated every 3 months (at every research visit) for a total of 12 months (the duration of study participation).

Additional Information

Dr. Amy D. DiVasta

Boston Children's Hospital

Phone: 617-355-3792

Results disclosure agreements

  • Principal investigator is a sponsor employee
  • Publication restrictions are in place