Evaluating the Safety of Long Term Dosing of Romiplostim (Formerly AMG 531) in Thrombocytopenic Subjects With Myelodysplastic Syndromes (MDS)

NCT ID: NCT00472290

Last Updated: 2017-12-29

Study Results

Results available

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Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

NA

Total Enrollment

72 participants

Study Classification

INTERVENTIONAL

Study Start Date

2007-04-01

Study Completion Date

2011-12-26

Brief Summary

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This is an open label extension study of romiplostim for treatment of thrombocytopenia (platelet count ≤ 50 x 10\^9/L) in MDS subjects. The study is designed to assess the long-term safety of treatment with romiplostim, as measured by incidence of overall adverse events, the incidence of bleeding events, the utilization of platelet transfusions, and the duration of platelet response. The study will further describe the time to disease progression to acute myeloid leukemia (AML) and survival.

Detailed Description

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Conditions

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Hematology MDS Myelodysplastic Syndromes Thrombocytopenia

Keywords

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Hematology MDS Myelodysplastic Syndromes Thrombocytopenia

Study Design

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Allocation Method

NON_RANDOMIZED

Intervention Model

SINGLE_GROUP

Primary Study Purpose

TREATMENT

Blinding Strategy

NONE

Study Groups

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Open Label Romiplostim (formerly AMG 531)

Group Type EXPERIMENTAL

Romiplostim (formerly AMG 531)

Intervention Type DRUG

Subjects will begin the study at an initial dose of 750 µg.

Except for:

* Subject whose doses were escalated to doses higher than 750 µg AMG 531 weekly, and maintained a response per IWG guidelines for platelet response.
* Subjects who were stable at a lower dose of AMG 531 on the previous study. Doses will be adjusted throughout the study based on individual subject's platelet count.

Interventions

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Romiplostim (formerly AMG 531)

Subjects will begin the study at an initial dose of 750 µg.

Except for:

* Subject whose doses were escalated to doses higher than 750 µg AMG 531 weekly, and maintained a response per IWG guidelines for platelet response.
* Subjects who were stable at a lower dose of AMG 531 on the previous study. Doses will be adjusted throughout the study based on individual subject's platelet count.

Intervention Type DRUG

Eligibility Criteria

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Inclusion Criteria

* Subject completed a romiplostim study for the treatment of thrombocytopenia in subjects with MDS
* Subject has an Eastern Cooperative Oncology (ECOG) performance status of 0 to 2
* Subject had a platelet count ≤ 50 x 10\^9/L since the final dose of investigational product in the parent study
* Subject or his/her legally acceptable representative provided written informed consent before any study-specific procedures were initiated

Exclusion Criteria

* Subject has been diagnosed with AML or has a blast count ≥ 10% by peripheral blood or bone marrow biopsy
* Subject has a prior history of leukemia
* Subject has a prior history of bone marrow or stem cell transplantation
* Subject has a prior malignancy (other than in situ cervical cancer, controlled prostate cancer, or basal cell cancer of the skin) unless treated with curative intent and without evidence of disease for ≥ 3 years before randomization
* Subject has active or uncontrolled infections
* Subject has unstable angina, congestive heart failure \[New York Heart Association (NYHA) \> class II\], uncontrolled hypertension (diastolic \> 100 mmHg), uncontrolled cardiac arrhythmia, or recent (within 1 year) myocardial infarction
* Subject has a history of arterial thrombosis (eg, stroke or transient ischemic attack) in the past year
* Subject has a history of venous thrombosis that currently requires anti-coagulation therapy
* Subject received interleukin (IL)-11 within 4 weeks of screening
* Subject previously received a thrombopoietic growth factor (other than romiplostim)
* Subject has a known hypersensitivity to any recombinant E coli-derived product (eg, Infergen®, Neupogen®, Somatropin, Actimmune)
* Subject is currently enrolled in investigational device or drug study(ies), has not yet completed at least 4 weeks since ending investigational device or drug study(ies) (other than parent romiplostim study), or subject is receiving other investigational agent(s)/device(s)
* Subject is of child-bearing potential and is evidently pregnant (eg, positive human chorionic gonadotropin \[HCG\] test) or is breast feeding
* Subject is not using adequate contraceptive precautions
* Subject has any kind of disorder that compromises his/her ability to give written informed consent (and does not have a legally acceptable representative) or is unable to comply with study procedures
Minimum Eligible Age

18 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Amgen

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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MD

Role: STUDY_DIRECTOR

Amgen

Countries

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Australia Austria Belgium Canada Czechia Denmark France Germany Hungary Italy Netherlands Poland Spain United Kingdom United States

References

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Fenaux P, Muus P, Kantarjian H, Lyons RM, Larson RA, Sekeres MA, Becker PS, Orejudos A, Franklin J. Romiplostim monotherapy in thrombocytopenic patients with myelodysplastic syndromes: long-term safety and efficacy. Br J Haematol. 2017 Sep;178(6):906-913. doi: 10.1111/bjh.14792. Epub 2017 Jun 14.

Reference Type DERIVED
PMID: 28616874 (View on PubMed)

Related Links

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http://www.amgentrials.com

AmgenTrials clinical trials website

Other Identifiers

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20060197

Identifier Type: -

Identifier Source: org_study_id