Trial Outcomes & Findings for Cytarabine in Treating Young Patients With Recurrent or Refractory Ewing's Sarcoma (NCT NCT00470275)

NCT ID: NCT00470275

Last Updated: 2014-10-20

Results Overview

Any patient who is enrolled and receives at least one dose of cytarabine will be considered evaluable for response if (1) the patient demonstrates progressive disease while on protocol therapy or (2) the patient is observed on protocol therapy for at least one cycle. Patients who achieve a complete or partial response according to the RECIST (Response Evaluation Criteria In Solid Tumors) criteria will be considered responders for the study design. All other patients who are evaluable for response will be considered non-responders for the study.

Recruitment status

COMPLETED

Study phase

PHASE2

Target enrollment

10 participants

Primary outcome timeframe

the first six cycles of study chemotherapy (126 days)

Results posted on

2014-10-20

Participant Flow

Participant milestones

Participant milestones
Measure
Cytarbine
Cytarabine IV every 12 hours days 1-5 of 21 day cycle. Response evaluation after 6 cycles of therapy.
Overall Study
STARTED
10
Overall Study
COMPLETED
0
Overall Study
NOT COMPLETED
10

Reasons for withdrawal

Reasons for withdrawal
Measure
Cytarbine
Cytarabine IV every 12 hours days 1-5 of 21 day cycle. Response evaluation after 6 cycles of therapy.
Overall Study
Death
1
Overall Study
Lack of Efficacy
7
Overall Study
Withdrawal by Subject
2

Baseline Characteristics

Cytarabine in Treating Young Patients With Recurrent or Refractory Ewing's Sarcoma

Baseline characteristics by cohort

Baseline characteristics by cohort
Measure
Cytarbine
n=10 Participants
Cytarabine IV every 12 hours days 1-5 of 21 day cycle. Response evaluation after 6 cycles of therapy.
Age, Categorical
<=18 years
4 Participants
n=5 Participants
Age, Categorical
Between 18 and 65 years
6 Participants
n=5 Participants
Age, Categorical
>=65 years
0 Participants
n=5 Participants
Sex: Female, Male
Female
3 Participants
n=5 Participants
Sex: Female, Male
Male
7 Participants
n=5 Participants
Ethnicity (NIH/OMB)
Hispanic or Latino
2 Participants
n=5 Participants
Ethnicity (NIH/OMB)
Not Hispanic or Latino
7 Participants
n=5 Participants
Ethnicity (NIH/OMB)
Unknown or Not Reported
1 Participants
n=5 Participants
Race (NIH/OMB)
American Indian or Alaska Native
0 Participants
n=5 Participants
Race (NIH/OMB)
Asian
0 Participants
n=5 Participants
Race (NIH/OMB)
Native Hawaiian or Other Pacific Islander
0 Participants
n=5 Participants
Race (NIH/OMB)
Black or African American
0 Participants
n=5 Participants
Race (NIH/OMB)
White
8 Participants
n=5 Participants
Race (NIH/OMB)
More than one race
0 Participants
n=5 Participants
Race (NIH/OMB)
Unknown or Not Reported
2 Participants
n=5 Participants
Region of Enrollment
United States
8 participants
n=5 Participants
Region of Enrollment
Canada
2 participants
n=5 Participants

PRIMARY outcome

Timeframe: the first six cycles of study chemotherapy (126 days)

Any patient who is enrolled and receives at least one dose of cytarabine will be considered evaluable for response if (1) the patient demonstrates progressive disease while on protocol therapy or (2) the patient is observed on protocol therapy for at least one cycle. Patients who achieve a complete or partial response according to the RECIST (Response Evaluation Criteria In Solid Tumors) criteria will be considered responders for the study design. All other patients who are evaluable for response will be considered non-responders for the study.

Outcome measures

Outcome measures
Measure
Cytarabine
n=10 Participants
Cytarabine IV every 12 hours days 1-5 of 21 day cycle. Response evaluation after 6 cycles of therapy.
Response
Non Responder
10 participants
Response
Responder
0 participants

Adverse Events

Cytarabine

Serious events: 2 serious events
Other events: 10 other events
Deaths: 0 deaths

Serious adverse events

Serious adverse events
Measure
Cytarabine
n=10 participants at risk
Cytarabine IV every 12 hours days 1-5 of 21 day cycle. Response evaluation after 6 cycles of therapy.
Respiratory, thoracic and mediastinal disorders
Hypoxia
10.0%
1/10
Investigations
Neutrophil count decreased
10.0%
1/10
Investigations
Platelet count decreased
10.0%
1/10
Respiratory, thoracic and mediastinal disorders
Respiratory, thoracic and mediastinal disorders - Other, specify
10.0%
1/10

Other adverse events

Other adverse events
Measure
Cytarabine
n=10 participants at risk
Cytarabine IV every 12 hours days 1-5 of 21 day cycle. Response evaluation after 6 cycles of therapy.
Gastrointestinal disorders
Abdominal pain
10.0%
1/10
Investigations
Alanine aminotransferase increased
40.0%
4/10
Skin and subcutaneous tissue disorders
Alopecia
10.0%
1/10
Immune system disorders
Anaphylaxis
10.0%
1/10
Blood and lymphatic system disorders
Anemia
50.0%
5/10
Investigations
Aspartate aminotransferase increased
20.0%
2/10
Musculoskeletal and connective tissue disorders
Back pain
10.0%
1/10
Investigations
Blood bilirubin increased
10.0%
1/10
Musculoskeletal and connective tissue disorders
Chest wall pain
10.0%
1/10
General disorders
Chills
10.0%
1/10
Infections and infestations
Conjunctivitis infective
10.0%
1/10
Gastrointestinal disorders
Constipation
10.0%
1/10
Investigations
Creatinine increased
10.0%
1/10
Respiratory, thoracic and mediastinal disorders
Dyspnea
10.0%
1/10
Respiratory, thoracic and mediastinal disorders
Epistaxis
10.0%
1/10
Gastrointestinal disorders
Esophageal pain
10.0%
1/10
Gastrointestinal disorders
Esophagitis
10.0%
1/10
Eye disorders
Eye disorders - Other
10.0%
1/10
General disorders
Facial pain
10.0%
1/10
Blood and lymphatic system disorders
Febrile neutropenia
40.0%
4/10
General disorders
Fever
20.0%
2/10
Nervous system disorders
Headache
10.0%
1/10
Metabolism and nutrition disorders
Hyperglycemia
30.0%
3/10
Metabolism and nutrition disorders
Hypoalbuminemia
10.0%
1/10
Metabolism and nutrition disorders
Hypocalcemia
10.0%
1/10
Metabolism and nutrition disorders
Hypokalemia
10.0%
1/10
Metabolism and nutrition disorders
Hypomagnesemia
10.0%
1/10
Metabolism and nutrition disorders
Hyponatremia
20.0%
2/10
Infections and infestations
Infections and infestations - Other
50.0%
5/10
Investigations
Lymphocyte count decreased
30.0%
3/10
Gastrointestinal disorders
Nausea
10.0%
1/10
Nervous system disorders
Nervous system disorders - Other
10.0%
1/10
Investigations
Neutrophil count decreased
80.0%
8/10
General disorders
Non-cardiac chest pain
10.0%
1/10
Gastrointestinal disorders
Oral pain
10.0%
1/10
General disorders
Pain
10.0%
1/10
Eye disorders
Photophobia
10.0%
1/10
Investigations
Platelet count decreased
80.0%
8/10
Skin and subcutaneous tissue disorders
Rash maculo-papular
10.0%
1/10
Reproductive system and breast disorders
Uterine hemorrhage
10.0%
1/10
Gastrointestinal disorders
Vomiting
20.0%
2/10
Investigations
White blood cell decreased
40.0%
4/10

Additional Information

Results Reporting Coordinator

Children's Oncology Group

Phone: 626-447-0064

Results disclosure agreements

  • Principal investigator is a sponsor employee Must obtain prior Sponsor approval.
  • Publication restrictions are in place

Restriction type: OTHER