Trial Outcomes & Findings for Aspirin in Preventing Colorectal Cancer in Patients at Increased Risk of Colorectal Cancer (NCT NCT00468910)

NCT ID: NCT00468910

Last Updated: 2017-05-31

Results Overview

Spectral marker assessment was performed via LEBS analysis (low-coherence enhanced backscattering spectroscopy) on the uninvolved mucosal biopsies of subjects taken at baseline and after 3 months of treatment with either aspirin or placebo. SPEC characterizes the size distribution of macromolecular complexes and other intracellular structures, with a decrease of the spectral slope implying a shift of the size distribution of intracellular structures toward smaller sizes. Spectral markers SPEC and FRAC provide a measure of the fundamental characteristics of the tissue nanoscale architecture.

Recruitment status

COMPLETED

Study phase

PHASE2

Target enrollment

79 participants

Primary outcome timeframe

3 months from baseline colonoscopy to end of intervention.

Results posted on

2017-05-31

Participant Flow

The study opened to accrual 02/22/2007 and closed to accrual 08/10/2009. Subjects were recruited at Northwestern University and University of Chicago.

A total of 110 subjects met the clinical definition of high risk for colorectal cancer, were entered onto the trial, and underwent initial spectral analysis. Of these, 81 had a cancer-associated spectral signature in histologically normal colonic mucosa.79 of these 81 subjects were randomized and began the study intervention

Participant milestones

Participant milestones
Measure
Acetylsalicylic Acid
Patients receive oral acetylsalicylic acid (aspirin) once daily.
Placebo
Patients receive oral placebo once daily.
Overall Study
STARTED
40
39
Overall Study
Randomization
40
39
Overall Study
Treatment
36
36
Overall Study
Post-Treatment Biopsy
36
36
Overall Study
Follow-up
36
36
Overall Study
COMPLETED
36
36
Overall Study
NOT COMPLETED
4
3

Reasons for withdrawal

Reasons for withdrawal
Measure
Acetylsalicylic Acid
Patients receive oral acetylsalicylic acid (aspirin) once daily.
Placebo
Patients receive oral placebo once daily.
Overall Study
Lost to Follow-up
2
1
Overall Study
Withdrawal by Subject
2
1
Overall Study
Medical Contraindication
0
1

Baseline Characteristics

Aspirin in Preventing Colorectal Cancer in Patients at Increased Risk of Colorectal Cancer

Baseline characteristics by cohort

Baseline characteristics by cohort
Measure
Acetylsalicylic Acid
n=40 Participants
Patients receive oral acetylsalicylic acid (aspirin) once daily.
Placebo
n=39 Participants
Patients receive oral placebo once daily.
Total
n=79 Participants
Total of all reporting groups
Age, Categorical
<=18 years
0 Participants
n=5 Participants
0 Participants
n=7 Participants
0 Participants
n=5 Participants
Age, Categorical
Between 18 and 65 years
33 Participants
n=5 Participants
34 Participants
n=7 Participants
67 Participants
n=5 Participants
Age, Categorical
>=65 years
7 Participants
n=5 Participants
5 Participants
n=7 Participants
12 Participants
n=5 Participants
Sex: Female, Male
Female
15 Participants
n=5 Participants
16 Participants
n=7 Participants
31 Participants
n=5 Participants
Sex: Female, Male
Male
25 Participants
n=5 Participants
23 Participants
n=7 Participants
48 Participants
n=5 Participants
Ethnicity (NIH/OMB)
Hispanic or Latino
3 Participants
n=5 Participants
0 Participants
n=7 Participants
3 Participants
n=5 Participants
Ethnicity (NIH/OMB)
Not Hispanic or Latino
37 Participants
n=5 Participants
39 Participants
n=7 Participants
76 Participants
n=5 Participants
Ethnicity (NIH/OMB)
Unknown or Not Reported
0 Participants
n=5 Participants
0 Participants
n=7 Participants
0 Participants
n=5 Participants
Race (NIH/OMB)
American Indian or Alaska Native
0 Participants
n=5 Participants
0 Participants
n=7 Participants
0 Participants
n=5 Participants
Race (NIH/OMB)
Asian
0 Participants
n=5 Participants
2 Participants
n=7 Participants
2 Participants
n=5 Participants
Race (NIH/OMB)
Native Hawaiian or Other Pacific Islander
0 Participants
n=5 Participants
0 Participants
n=7 Participants
0 Participants
n=5 Participants
Race (NIH/OMB)
Black or African American
2 Participants
n=5 Participants
1 Participants
n=7 Participants
3 Participants
n=5 Participants
Race (NIH/OMB)
White
37 Participants
n=5 Participants
36 Participants
n=7 Participants
73 Participants
n=5 Participants
Race (NIH/OMB)
More than one race
1 Participants
n=5 Participants
0 Participants
n=7 Participants
1 Participants
n=5 Participants
Race (NIH/OMB)
Unknown or Not Reported
0 Participants
n=5 Participants
0 Participants
n=7 Participants
0 Participants
n=5 Participants

PRIMARY outcome

Timeframe: 3 months from baseline colonoscopy to end of intervention.

Population: Subjects at high risk for colorectal cancer (CRC) with a cancer-associated spectral marker signature in histologically normal colonic mucosa.

Spectral marker assessment was performed via LEBS analysis (low-coherence enhanced backscattering spectroscopy) on the uninvolved mucosal biopsies of subjects taken at baseline and after 3 months of treatment with either aspirin or placebo. SPEC characterizes the size distribution of macromolecular complexes and other intracellular structures, with a decrease of the spectral slope implying a shift of the size distribution of intracellular structures toward smaller sizes. Spectral markers SPEC and FRAC provide a measure of the fundamental characteristics of the tissue nanoscale architecture.

Outcome measures

Outcome measures
Measure
Acetylsalicylic Acid
n=36 Participants
Patients receive oral acetylsalicylic acid (aspirin) 325 mg once daily.
Placebo
n=36 Participants
Patients receive oral placebo once daily.
Change of a Spectral Biomarker for Colonic Carcinogenesis (Called Spectral Slope or SPEC) From Baseline to 3 Months.
Baseline
40.72 micron^-1
Standard Deviation 16.91
37.54 micron^-1
Standard Deviation 21.64
Change of a Spectral Biomarker for Colonic Carcinogenesis (Called Spectral Slope or SPEC) From Baseline to 3 Months.
Post Intervention
43.45 micron^-1
Standard Deviation 26.84
37.52 micron^-1
Standard Deviation 28.15

PRIMARY outcome

Timeframe: 3 months from baseline colonoscopy to end of intervention.

Population: Subjects at high risk for colorectal cancer (CRC) with a cancer-associated spectral marker signature in histologically normal colonic mucosa

Spectral marker assessment was performed via LEBS analysis (low-coherence enhanced backscattering spectroscopy) on the uninvolved mucosal biopsies of subjects taken at baseline and after 3 months of treatment with either aspirin or placebo. FRAC characterizes the spatial autocorrelation function of mass density distribution in tissue. SPEC and FRAC provide a measure of the fundamental characteristics of the tissue nanoscale architecture

Outcome measures

Outcome measures
Measure
Acetylsalicylic Acid
n=36 Participants
Patients receive oral acetylsalicylic acid (aspirin) 325 mg once daily.
Placebo
n=36 Participants
Patients receive oral placebo once daily.
Change of a Spectral Biomarker for Colonic Carcinogenesis (Called Fractal Dimension or FRAC) From Baseline to 3 Months.
Baseline
142.41 unitless
Standard Deviation 2570.86
23.28 unitless
Standard Deviation 2699.82
Change of a Spectral Biomarker for Colonic Carcinogenesis (Called Fractal Dimension or FRAC) From Baseline to 3 Months.
Post Intervention
-407.78 unitless
Standard Deviation 3470.69
650.97 unitless
Standard Deviation 3201.77

SECONDARY outcome

Timeframe: 3 months from baseline colonoscopy to end of intervention.

Population: Subjects at high risk for colorectal cancer (CRC) with a cancer-associated spectral marker signature in histologically normal colonic mucosa.

Evaluate the effect of aspirin on colonic epithelial apoptosis and cell proliferation as assessed by immunohistochemical detection of cleaved caspase 3 .These were performed on samples that had been previously analyzed for 4D-ELF.

Outcome measures

Outcome measures
Measure
Acetylsalicylic Acid
n=36 Participants
Patients receive oral acetylsalicylic acid (aspirin) 325 mg once daily.
Placebo
n=36 Participants
Patients receive oral placebo once daily.
Colonic Epithelial Apoptosis as Measured by Immunohistochemical Detection of Cleaved Caspase 3
Baseline
4.56 Percentage of Total Cells
Standard Deviation 4.27
5.24 Percentage of Total Cells
Standard Deviation 3.69
Colonic Epithelial Apoptosis as Measured by Immunohistochemical Detection of Cleaved Caspase 3
At 3 Months
4.26 Percentage of Total Cells
Standard Deviation 4.44
7.26 Percentage of Total Cells
Standard Deviation 6.77

SECONDARY outcome

Timeframe: 3 months from baseline colonoscopy to end of intervention.

Population: Subjects at high risk for colorectal cancer (CRC) with a cancer-associated spectral marker signature in histologically normal colonic mucosa.

Evaluate the effect of aspirin on colonic epithelial apoptosis and cell proliferation as assessed by immunohistochemical detection of Ki-67. These were performed on samples that had been previously analyzed for 4D-ELF.

Outcome measures

Outcome measures
Measure
Acetylsalicylic Acid
n=36 Participants
Patients receive oral acetylsalicylic acid (aspirin) 325 mg once daily.
Placebo
n=36 Participants
Patients receive oral placebo once daily.
Changes in Colonic Cell Proliferation as Measured by Immunohistochemical Detection of Ki67
Baseline
38.07 Percentage of Total Cells
Standard Deviation 16.83
40.45 Percentage of Total Cells
Standard Deviation 12.26
Changes in Colonic Cell Proliferation as Measured by Immunohistochemical Detection of Ki67
3 Months Intervention
43.60 Percentage of Total Cells
Standard Deviation 14.77
37.74 Percentage of Total Cells
Standard Deviation 13.37

SECONDARY outcome

Timeframe: 3 months from baseline colonoscopy to end of intervention.

Population: Subjects at high risk for colorectal cancer (CRC) with a cancer-associated spectral marker signature in histologically normal colonic mucosa.

Evaluate the effect of aspirin on rectal prostaglandin levels.

Outcome measures

Outcome measures
Measure
Acetylsalicylic Acid
n=36 Participants
Patients receive oral acetylsalicylic acid (aspirin) 325 mg once daily.
Placebo
n=36 Participants
Patients receive oral placebo once daily.
Rectal Prostaglandin Levels as Measured by ELISA
Baseline
305.93 pg/ml
Standard Deviation 300.01
654.64 pg/ml
Standard Deviation 1536.52
Rectal Prostaglandin Levels as Measured by ELISA
Post Intervention
211.97 pg/ml
Standard Deviation 134.32
209.02 pg/ml
Standard Deviation 134.33

OTHER_PRE_SPECIFIED outcome

Timeframe: 3 months from baseline colonoscopy to end of intervention.

Population: Subjects at high risk for colorectal cancer (CRC) with a cancer-associated spectral marker signature in histologically normal colonic mucosa.

Evaluate the effect of aspirin on platelet COX activity as measured by a peroxidase-based Cox enzyme activity assay.

Outcome measures

Outcome measures
Measure
Acetylsalicylic Acid
n=36 Participants
Patients receive oral acetylsalicylic acid (aspirin) 325 mg once daily.
Placebo
n=36 Participants
Patients receive oral placebo once daily.
Platelet Cyclooxygenase (COX) Activity as Measured by a Peroxidase-based COX Enzyme Activity Assay
Baseline
712976.73 pg/ml
Standard Deviation 2082413.36
430109.56 pg/ml
Standard Deviation 798782.31
Platelet Cyclooxygenase (COX) Activity as Measured by a Peroxidase-based COX Enzyme Activity Assay
Post Intervention
6914.87 pg/ml
Standard Deviation 20891.41
200233.5 pg/ml
Standard Deviation 463029.1

Adverse Events

Acetylsalicylic Acid

Serious events: 0 serious events
Other events: 17 other events
Deaths: 0 deaths

Placebo

Serious events: 0 serious events
Other events: 21 other events
Deaths: 0 deaths

Serious adverse events

Adverse event data not reported

Other adverse events

Other adverse events
Measure
Acetylsalicylic Acid
n=40 participants at risk
Patients receive oral acetylsalicylic acid (aspirin) once daily. acetylsalicylic acid: Given orally laboratory biomarker analysis: Correlative study
Placebo
n=39 participants at risk
Patients receive oral placebo once daily. placebo: Given orally laboratory biomarker analysis: Correlative study
Blood and lymphatic system disorders
Blood/Bone Marrow: Hemoglobin
2.5%
1/40 • Number of events 1 • 3 months from baseline colonoscopy to end of intervention and repeat colonoscopy.
2.6%
1/39 • Number of events 3 • 3 months from baseline colonoscopy to end of intervention and repeat colonoscopy.
Blood and lymphatic system disorders
Blood/Bone Marrow: Other
2.5%
1/40 • Number of events 2 • 3 months from baseline colonoscopy to end of intervention and repeat colonoscopy.
2.6%
1/39 • Number of events 1 • 3 months from baseline colonoscopy to end of intervention and repeat colonoscopy.
Blood and lymphatic system disorders
Hemorrhage with Surgery
0.00%
0/40 • 3 months from baseline colonoscopy to end of intervention and repeat colonoscopy.
2.6%
1/39 • Number of events 1 • 3 months from baseline colonoscopy to end of intervention and repeat colonoscopy.
Cardiac disorders
Hypertension
2.5%
1/40 • Number of events 1 • 3 months from baseline colonoscopy to end of intervention and repeat colonoscopy.
0.00%
0/39 • 3 months from baseline colonoscopy to end of intervention and repeat colonoscopy.
Gastrointestinal disorders
Diarrhea
2.5%
1/40 • Number of events 1 • 3 months from baseline colonoscopy to end of intervention and repeat colonoscopy.
0.00%
0/39 • 3 months from baseline colonoscopy to end of intervention and repeat colonoscopy.
Gastrointestinal disorders
Nausea
2.5%
1/40 • Number of events 1 • 3 months from baseline colonoscopy to end of intervention and repeat colonoscopy.
0.00%
0/39 • 3 months from baseline colonoscopy to end of intervention and repeat colonoscopy.
Gastrointestinal disorders
Heartburn
0.00%
0/40 • 3 months from baseline colonoscopy to end of intervention and repeat colonoscopy.
2.6%
1/39 • Number of events 1 • 3 months from baseline colonoscopy to end of intervention and repeat colonoscopy.
General disorders
Pain: Stomach
5.0%
2/40 • Number of events 2 • 3 months from baseline colonoscopy to end of intervention and repeat colonoscopy.
5.1%
2/39 • Number of events 2 • 3 months from baseline colonoscopy to end of intervention and repeat colonoscopy.
General disorders
Pain: Abdomen Nos
5.0%
2/40 • Number of events 2 • 3 months from baseline colonoscopy to end of intervention and repeat colonoscopy.
2.6%
1/39 • Number of events 2 • 3 months from baseline colonoscopy to end of intervention and repeat colonoscopy.
General disorders
Pain: Head/Headache
2.5%
1/40 • Number of events 1 • 3 months from baseline colonoscopy to end of intervention and repeat colonoscopy.
10.3%
4/39 • Number of events 4 • 3 months from baseline colonoscopy to end of intervention and repeat colonoscopy.
General disorders
Pain: Other
2.5%
1/40 • Number of events 1 • 3 months from baseline colonoscopy to end of intervention and repeat colonoscopy.
2.6%
1/39 • Number of events 1 • 3 months from baseline colonoscopy to end of intervention and repeat colonoscopy.
General disorders
Pain: Joint
0.00%
0/40 • 3 months from baseline colonoscopy to end of intervention and repeat colonoscopy.
2.6%
1/39 • Number of events 1 • 3 months from baseline colonoscopy to end of intervention and repeat colonoscopy.
General disorders
Pain: Extremity - Limb
0.00%
0/40 • 3 months from baseline colonoscopy to end of intervention and repeat colonoscopy.
2.6%
1/39 • Number of events 1 • 3 months from baseline colonoscopy to end of intervention and repeat colonoscopy.
General disorders
Pain: Uterus
0.00%
0/40 • 3 months from baseline colonoscopy to end of intervention and repeat colonoscopy.
2.6%
1/39 • Number of events 1 • 3 months from baseline colonoscopy to end of intervention and repeat colonoscopy.
General disorders
Constitutional Symptoms: Fever
0.00%
0/40 • 3 months from baseline colonoscopy to end of intervention and repeat colonoscopy.
2.6%
1/39 • Number of events 1 • 3 months from baseline colonoscopy to end of intervention and repeat colonoscopy.
General disorders
Constitutional Symptoms: Insomnia
0.00%
0/40 • 3 months from baseline colonoscopy to end of intervention and repeat colonoscopy.
2.6%
1/39 • Number of events 1 • 3 months from baseline colonoscopy to end of intervention and repeat colonoscopy.
Gastrointestinal disorders
Constitutional Symptoms: Weight Gain
0.00%
0/40 • 3 months from baseline colonoscopy to end of intervention and repeat colonoscopy.
2.6%
1/39 • Number of events 2 • 3 months from baseline colonoscopy to end of intervention and repeat colonoscopy.
General disorders
Constitutional Symptoms: Other
0.00%
0/40 • 3 months from baseline colonoscopy to end of intervention and repeat colonoscopy.
2.6%
1/39 • Number of events 1 • 3 months from baseline colonoscopy to end of intervention and repeat colonoscopy.
Immune system disorders
Rhinitis
2.5%
1/40 • Number of events 1 • 3 months from baseline colonoscopy to end of intervention and repeat colonoscopy.
0.00%
0/39 • 3 months from baseline colonoscopy to end of intervention and repeat colonoscopy.
Infections and infestations
Upper Airway Nos
2.5%
1/40 • Number of events 1 • 3 months from baseline colonoscopy to end of intervention and repeat colonoscopy.
5.1%
2/39 • Number of events 2 • 3 months from baseline colonoscopy to end of intervention and repeat colonoscopy.
Infections and infestations
Infection - Other
0.00%
0/40 • 3 months from baseline colonoscopy to end of intervention and repeat colonoscopy.
5.1%
2/39 • Number of events 2 • 3 months from baseline colonoscopy to end of intervention and repeat colonoscopy.
Metabolism and nutrition disorders
Metabolic/Lab - Other
2.5%
1/40 • Number of events 1 • 3 months from baseline colonoscopy to end of intervention and repeat colonoscopy.
2.6%
1/39 • Number of events 1 • 3 months from baseline colonoscopy to end of intervention and repeat colonoscopy.
Metabolism and nutrition disorders
AST
2.5%
1/40 • Number of events 1 • 3 months from baseline colonoscopy to end of intervention and repeat colonoscopy.
0.00%
0/39 • 3 months from baseline colonoscopy to end of intervention and repeat colonoscopy.
Metabolism and nutrition disorders
ALT
2.5%
1/40 • Number of events 1 • 3 months from baseline colonoscopy to end of intervention and repeat colonoscopy.
0.00%
0/39 • 3 months from baseline colonoscopy to end of intervention and repeat colonoscopy.
Metabolism and nutrition disorders
Hypoglycemia
0.00%
0/40 • 3 months from baseline colonoscopy to end of intervention and repeat colonoscopy.
2.6%
1/39 • Number of events 1 • 3 months from baseline colonoscopy to end of intervention and repeat colonoscopy.
Metabolism and nutrition disorders
Hyperkalemia
0.00%
0/40 • 3 months from baseline colonoscopy to end of intervention and repeat colonoscopy.
2.6%
1/39 • Number of events 1 • 3 months from baseline colonoscopy to end of intervention and repeat colonoscopy.
Nervous system disorders
Dizziness
0.00%
0/40 • 3 months from baseline colonoscopy to end of intervention and repeat colonoscopy.
5.1%
2/39 • Number of events 2 • 3 months from baseline colonoscopy to end of intervention and repeat colonoscopy.
Renal and urinary disorders
Cystitis
0.00%
0/40 • 3 months from baseline colonoscopy to end of intervention and repeat colonoscopy.
2.6%
1/39 • Number of events 2 • 3 months from baseline colonoscopy to end of intervention and repeat colonoscopy.
Reproductive system and breast disorders
Sexual - Other
0.00%
0/40 • 3 months from baseline colonoscopy to end of intervention and repeat colonoscopy.
2.6%
1/39 • Number of events 1 • 3 months from baseline colonoscopy to end of intervention and repeat colonoscopy.
Respiratory, thoracic and mediastinal disorders
Cough
2.5%
1/40 • Number of events 1 • 3 months from baseline colonoscopy to end of intervention and repeat colonoscopy.
2.6%
1/39 • Number of events 1 • 3 months from baseline colonoscopy to end of intervention and repeat colonoscopy.

Additional Information

Dr. Seema Khan

Northwestern University

Phone: 312-503- 4236

Results disclosure agreements

  • Principal investigator is a sponsor employee
  • Publication restrictions are in place

Restriction type: LTE60