Study of Picoplatin Efficacy After Relapse

NCT ID: NCT00465491

Last Updated: 2009-04-14

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

UNKNOWN

Clinical Phase

PHASE3

Total Enrollment

399 participants

Study Classification

INTERVENTIONAL

Study Start Date

2007-04-30

Brief Summary

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Picoplatin is a new type of platinum drug that has been investigated in several clinical trials, and may provide an improved safety profile over current treatment options. This study is designed to compare the efficacy and safety of picoplatin plus Best Supportive Care (BSC) with BSC alone. Best Supportive Care includes care and treatment to optimize the comfort of patients and their ability to function, as well as to minimize the side-effects of anti-cancer treatments.

Detailed Description

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This Phase 3 study will enroll subjects with Small Cell Lung Cancer (SCLC) who are refractory or progressive within 6 months of completing first-line, platinum-containing chemotherapy. Subjects will be centrally randomized 2:1 to receive picoplatin plus BSC every 3 weeks, or BSC alone. After discontinuation of picoplatin, all subjects will continue to receive BSC and will continue to be evaluated every 3 weeks until discontinuation from the study, death, or the end of the study. After discontinuation of picoplatin, subjects may be treated with another chemotherapy at their physician's discretion and then will be followed for survival.

Conditions

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Small Cell Lung Cancer

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

NONE

Study Groups

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1

Picoplatin

Group Type EXPERIMENTAL

picoplatin

Intervention Type DRUG

IV picoplatin 150mg/m2 q3wk

2

BSC

Group Type OTHER

best supportive care

Intervention Type OTHER

best supportive care

Interventions

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picoplatin

IV picoplatin 150mg/m2 q3wk

Intervention Type DRUG

best supportive care

best supportive care

Intervention Type OTHER

Eligibility Criteria

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Inclusion Criteria

* Histological or cytological diagnosis of SCLC or combined SCLC/non-small cell lung cancer (NSCLC) defined as SCLC mixed with squamous cell carcinoma, adenocarcinoma, or large cell carcinoma.
* One and only 1 prior cisplatin or carboplatin-containing chemotherapy regimen for SCLC within the scope of the National Comprehensive Cancer Network (NCCN) Guidelines (Section 5.4.1).
* Radiological evidence of SCLC that never responded or progressed within 90 days after completion of first-line therapy (refractory); or responded initially to first-line therapy but progressed between 91 and 180 days after treatment was completed (progressed within 91 to 180 days).
* CT scans of head, chest and abdomen (including adrenal and full extent of liver) with contrast, preferably within 14 days prior to randomization (up to 21 days is allowed if necessary). MRI is acceptable in the case of allergy to contrast agents. The presence or absence of measurable disease gy RECIST must be documented from the baseline CT or MRI scan.
* Patients with brain metastases must have been treated with brain irradiation. Only patients wtih asymptomatic brain metastases are eligible for this study.
* ECOG PS 0, 1 or 2 within 3 days prior to randomization (Appendix II).
* Life expectancy of at least 8 weeks within 3 days prior to randomization.
* At least 21 days must have elapsed since the most recent prior chemotherapy dose, with evidence of hematological recovery.
* At least 14 days must have elapsed since the most recent prior radiotherapy dose.
* At least 14 days must have elapsed since prior surgery except for the placement of venous access device or bronchoscopy.
* Subject must be recovered to ≤ Grade 1 toxicity from all non-hematological adverse effects of prior therapies (excluding alopecia).
* Age 18 years or over.
* ANC ≥ 1.5 x 109/L.
* Platelet count ≥ 100 x 109/L.
* Hemoglobin of ≥ 90 g/L (transfusion permitted to achieve this hemoglobin).
* Aspartate aminotransferase, alanine aminotransferase, and lactate dehydrogenase levels ≤ 2.5 times upper limit of normal (ULN) or ≤ 5 times ULN if liver involvement is present.
* Bilirubin of ≤ 1.5 times upper limit of normal (ULN).
* Blood urea nitrogen ≤ 1.5 times ULN (hypovolemic subjects may be hydrated to achieve this BUN).
* Creatinine clearance of ≥ 50 mL/min, as calculated by the Cockcroft-Gault formula (Appendix III).
* Women of childbearing potential must have a negative pregnancy test (serum or urine). Sexually active couples of child-bearing potential must agree to use appropriate birth control methods during chemotherapy and for 3 months after chemotherapy.
* Signed informed consent.

Exclusion Criteria

* Prior radiotherapy that included ≥ 30% of the bone marrow (Appendix IV).
* Pleural effusion as the only radiological evidence of SCLC.
* Untreated or symptomatic brain or central nervous system (CNS) metastases.
* Grade 2 or higher peripheral neuropathy.
* Significant cardiac disease, defined as myocardial infarction within 3 months prior to randomization, congestive heart failure classified by the New York Heart Association as Class III or IV (Appendix V), uncontrolled cardiac arrhythmias, poorly controlled or unstable angina, or electrocardiographic evidence of acute ischemia.
* Serious medical or psychiatric illness that could potentially interfere with the completion of study treatment according to this protocol, e.g., active infection, Crohn's disease, ulcerative colitis, etc.
* Use of other investigational drugs within 30 days prior to randomization.
* Breast-feeding.
* History of any other malignancy within 5 years, with the exception of treated non-melanoma skin cancer or carcinoma in situ of the cervix.
Minimum Eligible Age

18 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Poniard Pharmaceuticals

INDUSTRY

Sponsor Role lead

Responsible Party

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Poniard Pharmaceuticals, Inc.

Principal Investigators

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Dr. Hazel Breitz, M.D.

Role: STUDY_DIRECTOR

Poniard Pharmaceuticals

Locations

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Consultorios Privados

Buenos Aires, , Argentina

Site Status

Clinica Constituyentes

Buenos Aires, , Argentina

Site Status

CETEN Centro de Estudio y Tratamiento de Enfermedades Neoplasicas

Buenos Aires, , Argentina

Site Status

IADT (Insttituto Argentino de Diagnostico y Tratamiento S.A.)

Buenos Aires, , Argentina

Site Status

Centro Oncologico

Buenos Aires, , Argentina

Site Status

Instituto Alexander Fleming

Buenos Aires, , Argentina

Site Status

PALIAR

Buenos Aires, , Argentina

Site Status

IONC

Córdoba, , Argentina

Site Status

Centro Medico San Roque

San Miguel de Tucumán, , Argentina

Site Status

Centro Oncologico de Rosario

Santa Fe, , Argentina

Site Status

ISIS Clinica Especializada

Santa Fe, , Argentina

Site Status

Institution of Healthcare "Grodno Regional Clinical Hospital

Grodno, , Belarus

Site Status

Gomel Regional Oncological Dispensary

Homyel, , Belarus

Site Status

Minsk City Clinical Oncology Dispensary

Minsk, , Belarus

Site Status

Research Institute of Oncology and Medical Radiology named by N.N. Aleksandrov

Minsk, , Belarus

Site Status

Vitebsk Regional Oncology Dispensary

Vitebsk, , Belarus

Site Status

Clinic for Lung Diseases, Clinical Center, Banja Luka

Banja Luka, , Bosnia and Herzegovina

Site Status

Clinic of Pulmonary Diseases Podhrastovi

Sarajevo, , Bosnia and Herzegovina

Site Status

Multiprofile Hospital for Active Treatment, Dr. Tota Venkova

Gabrovo, , Bulgaria

Site Status

University Multifunctional Hospital for Active Treatment "Dr. Georgi Stranski"

Pleven, , Bulgaria

Site Status

District Dispensary for Cancer Diseases with Inpatient Hospital Plovdiv

Plovdiv, , Bulgaria

Site Status

Regional Oncodispensary with Inpatient Sector

Rousse, , Bulgaria

Site Status

Inter-district Dispensary for Cancer Diseases w/Inpatient Hospital

Shumen, , Bulgaria

Site Status

Regional Oncodispensary with Inpatient Sector-Sofia District

Sofia, , Bulgaria

Site Status

Inter-district Dispensary for Cancer Disease w/Inpatient Hospital "Dr. Marko Markov", Varna

Varna, , Bulgaria

Site Status

Multiprofile Hospital for Active Treatment "St. Marina"

Varna, , Bulgaria

Site Status

Instituto Nacional de Cancer

Santiago, , Chile

Site Status

Clinical Hospital

Dubrovnik, , Croatia

Site Status

Clinical Hospital

Osijek, , Croatia

Site Status

Clinical Hospital Split

Split, , Croatia

Site Status

Clinic for Pulmonary Diseses "Jordanovac"

Zagreb, , Croatia

Site Status

St. George County Hospital

Fejer County, , Hungary

Site Status

University of Szeged

Szeged, , Hungary

Site Status

General Rehablitation and Medicinal Bath Hospital

Szombathely, , Hungary

Site Status

Gujrat Cancer Research Institute

Asarwa, Ahmadabad, India

Site Status

Kidwai Memorial Institute of Oncology

Bangalore, Karnataka, India

Site Status

Lakeshore Hospital and Research Center

Kochi, Kerala, India

Site Status

Shatabdi Superspeciality Hospital

Nashik, Maharashtra, India

Site Status

Curie Centre of Oncology

Bangalore, , India

Site Status

Jawaharlal Nehru Cancer Hospital and Research Centre

Bhopal, , India

Site Status

Apollo Speciality Hospital

Chennai, , India

Site Status

MNJ Institute of Oncology

Hyderabaad, , India

Site Status

Indo American Institute of Oncology

Hyderabaad, , India

Site Status

Yashoda Group of Hospitals

Hyderabad, , India

Site Status

SEAROC Cancer Center

Jaipur, , India

Site Status

Institute of Post Graduate Medical Education and Research

Kolkata, , India

Site Status

Orchid Nursing Home

Kolkata, , India

Site Status

King George Medical University

Lucknow, , India

Site Status

KMC (Karturba Medical College) Hospital

Manipal, , India

Site Status

Jaslok Hospital and Research Centre

Mumbai, , India

Site Status

Tata Memorial Centre

Mumbai, , India

Site Status

Sir Ganga Ram Hospital

New Delhi, , India

Site Status

Rajiv Gandhi Cancer Institute, Delhi

New Delhi, , India

Site Status

Mahaveer Cancer Sansthan

Patna, , India

Site Status

Jahangir Hospital and Research Centre

Pune, , India

Site Status

Smt. Vasantben R. Desai Cancer Research Center

Rajkot, , India

Site Status

Regional Cancer Centre

Trivandrum, , India

Site Status

King George Hospital

Visakhapatnam, , India

Site Status

Daugavas Hospital

Daugavpils, , Latvia

Site Status

Paul Stradins Clincial University Hospital

Riga, , Latvia

Site Status

Special Hospital for Pulmonary Diseases

Nikšić, , Montenegro

Site Status

Silesian Medical University in Katowice

Zabrze, Dolny Slask, Poland

Site Status

Dolnoslaskie Centre of Lung Diseases

Wroclaw, Lower Silesian Voivodeship, Poland

Site Status

Kujawsko-Pomorski Centre of Pulmonology

Bydgoszcz, , Poland

Site Status

NMP, Memorial Voyvodship Hospital

Częstochowa, , Poland

Site Status

Dr. Bieganski Memorial Regional Specialsitic Hospital

Grudziądz, , Poland

Site Status

Regional Hospital, Department of Pulmonary Diseases and Chemotherapy

Krakow, , Poland

Site Status

Independent Public Group for Tuberculosis and Lung Disease in Olsztyn

Olsztyn, , Poland

Site Status

Department of Clinical Oncology, Wielkopolskie Centre of Lung Diseases and Tuberculosis

Poznan, , Poland

Site Status

Conservative Outpatient Oncology Department, Voyevodship Hospital in Plock

Płock, , Poland

Site Status

Department of Pulmonology, Voyvodship Specialsitic Hospital in Radom

Radom, , Poland

Site Status

SP ZOZ Voyevodship Specialistic Hospital #3

Rybnik, , Poland

Site Status

Department of Chemotherapy, Prof. A. Sokolowski Memorial Specialistic Hospital in Szczecin

Szczecin, , Poland

Site Status

Department of Clinical Oncology, SP ZOZ, Yoyvodship Specialistic Hospital

Torun, , Poland

Site Status

Prof. Dr. Ion Chiricuta, Institute of Oncology Cluj-Napoca

Cluj-Napoca, Cluj, Romania

Site Status

Baia Mare "Constantin Opris" County Emergency Hospital

Baia Mare, Maramureş, Romania

Site Status

IANULI Medconsult SRL

Bucharest, , Romania

Site Status

Bucharest Institute of Oncology

Bucharest, , Romania

Site Status

Prof. Dr. Ion Chircuta, Oncology Institute

Cluj-Napoca, , Romania

Site Status

Clinical Emergency County Hospital Constanta

Constanța, , Romania

Site Status

Medical Oncology Center Iasi

Iași, , Romania

Site Status

Schuller Municipal Hospital Ploiesti-Medical Oncology Department

Ploieşti, , Romania

Site Status

Clinical County Hospital

Sibiu, , Romania

Site Status

Sf. loan cel Nou, Emergency County Hospital

Suceava, , Romania

Site Status

OncoMed

Timișoara, , Romania

Site Status

Buryatia Republican Oncology Center

Ulan-Ude, Buryatiya Republic, Russia

Site Status

Regional Oncology Center

Birobidzhan, Jewish Republic, Russia

Site Status

Republican Oncology Center of the Ministry of Healthcare of Karelia Republic

Petrozavodsk, Karelia Republic, Russia

Site Status

Komi Republican Oncology Center

Syktyvkar, Komi, Russia

Site Status

Clinical Oncology Center

Kazan', Tatarstan Republic, Russia

Site Status

Kazan Oncology Center

Kazan', Tatarstan Republic, Russia

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Arkhangelsk Regional Clinical Oncology Center

Arkhangelsk, , Russia

Site Status

Altai Regional Oncology Center

Barnaul, , Russia

Site Status

Chelyabinsk Regional Oncology Center

Chelyabinsk, , Russia

Site Status

City Hospital #1

Cherepovets, , Russia

Site Status

Chita Regional Oncology Center

Chita, , Russia

Site Status

Regional Oncology Center

Engel's, , Russia

Site Status

Regional Oncology Center

Irkutsk, , Russia

Site Status

Ivanovo Regional Oncology Center

Ivanovo, , Russia

Site Status

Republican Clinical Oncology Center of the Republic of Udmurtia

Izhevsk, , Russia

Site Status

Kaluga Regional Oncology Center

Kaluga, , Russia

Site Status

Regional Clinical Oncology Center

Khabarovsk, , Russia

Site Status

Regional Clinical Oncology Center

Kirov, , Russia

Site Status

City Oncology Center

Komsomolsk-on-Amur, , Russia

Site Status

Krasnodar Clinical Oncology

Krasnodar, , Russia

Site Status

Regional Clinical Hospital #1

Krasnodar, , Russia

Site Status

Kurst Regional Oncology Center

Kurst, , Russia

Site Status

Lipetsk Regional Oncology Center

Lipetsk, , Russia

Site Status

Magnitogorsk Clinical Oncology Hospital

Magnitogorsk, , Russia

Site Status

Blokhin Russian Oncology Research Center

Moscow, , Russia

Site Status

Central Clinical Hospital and Outpatient Unit of the Medical Center under the Russian Presidential Administration

Moscow, , Russia

Site Status

Semashko Central Clinical Hospital #2 under Russian Railways

Moscow, , Russia

Site Status

Novorossiysk Oncology Center

Novorossiysk, , Russia

Site Status

City Clinical Hospital #1

Novosibirsk, , Russia

Site Status

Medical Radiology Research Center under RAMS

Obnninsk, , Russia

Site Status

Orenburg Regional Clinical Oncology Center

Orenburg, , Russia

Site Status

Orel Oncology Center

Oryol, , Russia

Site Status

Regional Oncology Center

Penza, , Russia

Site Status

Pyatigorsk Affiliate of Stavropol Regional Clinical Oncology Center

Pyatigorsk, , Russia

Site Status

St. Petersburg City Multifield Hospital #2

Saint Petersburg, , Russia

Site Status

St. Petersburg Pavlov State Medical University

Saint Petersburg, , Russia

Site Status

Pavlov St. Petersburg State Medical University, Pulmonology Research Institute

Saint Petersburg, , Russia

Site Status

City Clinical Oncology Center, Thoracic Oncology Department #6

Saint Petersburg, , Russia

Site Status

Ogarev Mordovian State University

Saransk, , Russia

Site Status

State Higher Education Institution Saratov State Medical University under the Federal Agency for Healthcare and Social Development

Saratov, , Russia

Site Status

Oncology Center

Sochi, , Russia

Site Status

Tambov Regional Oncology Center

Tambov, , Russia

Site Status

Tomsk Regional Oncology Center

Tomsk, , Russia

Site Status

Tula Regional Oncology Center

Tula, , Russia

Site Status

Ufa, Republican Oncology Center

Ufa, , Russia

Site Status

Primorsky Regional Oncology Center

Vladivostok, , Russia

Site Status

Volgograd Regional Clinical Oncology Center#1

Volograd, , Russia

Site Status

Voronezh Regional Clinical Oncology Center

Voronezh, , Russia

Site Status

Regional Clinical Oncology Hospital

Yaroslavl, , Russia

Site Status

Sverdlovsk Regional Oncology Center

Yekaterinburg, , Russia

Site Status

Republican of Clinical Hospital, Mariy-El Republican

Yoshkar-Ola, , Russia

Site Status

Clinic for Pulmonary Diseases and TBC

Knez-Selo, , Serbia

Site Status

Institute for Pulmonary Diseases of Vijvodina

Vijvodina, , Serbia

Site Status

Volyn Regional Oncology Center

Lutsk, , Ukraine

Site Status

Public Treatment and Prevention Institution Mariupol City Interdistrict Oncology Center

Mariupol, , Ukraine

Site Status

Sumy Regional Oncology Center

Sumy, , Ukraine

Site Status

Ternopol Regional Clinical Oncology Center

Ternopil, , Ukraine

Site Status

Zaporozhye Regional Clinical Oncology Center

Zaporizhzhya, , Ukraine

Site Status

Countries

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Argentina Belarus Bosnia and Herzegovina Bulgaria Chile Croatia Hungary India Latvia Montenegro Poland Romania Russia Serbia Ukraine

References

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Raynaud FI, Boxall FE, Goddard PM, Valenti M, Jones M, Murrer BA, Abrams M, Kelland LR. cis-Amminedichloro(2-methylpyridine) platinum(II) (AMD473), a novel sterically hindered platinum complex: in vivo activity, toxicology, and pharmacokinetics in mice. Clin Cancer Res. 1997 Nov;3(11):2063-74.

Reference Type BACKGROUND
PMID: 9815598 (View on PubMed)

Beale P, Judson I, O'Donnell A, Trigo J, Rees C, Raynaud F, Turner A, Simmons L, Etterley L. A Phase I clinical and pharmacological study of cis-diamminedichloro(2-methylpyridine) platinum II (AMD473). Br J Cancer. 2003 Apr 7;88(7):1128-34. doi: 10.1038/sj.bjc.6600854.

Reference Type BACKGROUND
PMID: 12671715 (View on PubMed)

Giaccone G, O'Brien ME, Byrne MJ, Bard M, Kaukel E, Smit B. Phase II trial of ZD0473 as second-line therapy in mesothelioma. Eur J Cancer. 2002 Dec;38 Suppl 8:S19-24. doi: 10.1016/s0959-8049(02)80018-1.

Reference Type BACKGROUND
PMID: 12647701 (View on PubMed)

Treat J, Schiller J, Quoix E, Mauer A, Edelman M, Modiano M, Bonomi P, Ramlau R, Lemarie E. ZD0473 treatment in lung cancer: an overview of the clinical trial results. Eur J Cancer. 2002 Dec;38 Suppl 8:S13-8. doi: 10.1016/s0959-8049(02)80016-8.

Reference Type BACKGROUND
PMID: 12645908 (View on PubMed)

Gore ME, Atkinson RJ, Thomas H, Cure H, Rischin D, Beale P, Bougnoux P, Dirix L, Smit WM. Results of ZD0473 in platinum-pretreated ovarian cancer: analysis according to platinum free interval. Eur J Cancer. 2002 Dec;38 Suppl 8:S7-12. doi: 10.1016/s0959-8049(02)80014-4.

Reference Type BACKGROUND
PMID: 12645907 (View on PubMed)

Holford J, Raynaud F, Murrer BA, Grimaldi K, Hartley JA, Abrams M, Kelland LR. Chemical, biochemical and pharmacological activity of the novel sterically hindered platinum co-ordination complex, cis-[amminedichloro(2-methylpyridine)] platinum(II) (AMD473). Anticancer Drug Des. 1998 Jan;13(1):1-18.

Reference Type BACKGROUND
PMID: 9474239 (View on PubMed)

Holford J, Sharp SY, Murrer BA, Abrams M, Kelland LR. In vitro circumvention of cisplatin resistance by the novel sterically hindered platinum complex AMD473. Br J Cancer. 1998;77(3):366-73. doi: 10.1038/bjc.1998.59.

Reference Type BACKGROUND
PMID: 9472630 (View on PubMed)

Rogers P, Boxall FE, Allott CP, Stephens TC, Kelland LR. Sequence-dependent synergism between the new generation platinum agent ZD0473 and paclitaxel in cisplatin-sensitive and -resistant human ovarian carcinoma cell lines. Eur J Cancer. 2002 Aug;38(12):1653-60. doi: 10.1016/s0959-8049(02)00107-7.

Reference Type BACKGROUND
PMID: 12142057 (View on PubMed)

Sharp SY, O'Neill CF, Rogers P, Boxall FE, Kelland LR. Retention of activity by the new generation platinum agent AMD0473 in four human tumour cell lines possessing acquired resistance to oxaliplatin. Eur J Cancer. 2002 Nov;38(17):2309-15. doi: 10.1016/s0959-8049(02)00244-7.

Reference Type BACKGROUND
PMID: 12441268 (View on PubMed)

Kawamura-Akiyama Y, Kusaba H, Kanzawa F, Tamura T, Saijo N, Nishio K. Non-cross resistance of ZD0473 in acquired cisplatin-resistant lung cancer cell lines. Lung Cancer. 2002 Oct;38(1):43-50. doi: 10.1016/s0169-5002(02)00175-7.

Reference Type BACKGROUND
PMID: 12367792 (View on PubMed)

Related Links

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http://www.poniard.com

Poniard Pharmaceuticals, Inc.

Other Identifiers

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0601

Identifier Type: -

Identifier Source: org_study_id

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