Trial Outcomes & Findings for Saizen® E-Device User Trial (NCT NCT00450190)

NCT ID: NCT00450190

Last Updated: 2018-07-23

Results Overview

Subjects' overall impression after using E-Device was measured on a scale ranging from 1 to 3, where 1 = bad, 2 = good, and 3 = very good. Number of subjects with response based on overall impression scale were presented.

Recruitment status

COMPLETED

Study phase

PHASE3

Target enrollment

20 participants

Primary outcome timeframe

2 Weeks

Results posted on

2018-07-23

Participant Flow

Participant milestones

Participant milestones
Measure
Saizen® E-Device
Saizen® (recombinant human growth hormone \[r-hGH\]) injection 8 milligram (mg) per 137 milliliter (mL) was administered using an electronic auto-injector (E-Device) subcutaneously (SC) in the evening as per local Summary of Product Characteristics (SmPC) for 60 days.
Overall Study
STARTED
20
Overall Study
COMPLETED
18
Overall Study
NOT COMPLETED
2

Reasons for withdrawal

Reasons for withdrawal
Measure
Saizen® E-Device
Saizen® (recombinant human growth hormone \[r-hGH\]) injection 8 milligram (mg) per 137 milliliter (mL) was administered using an electronic auto-injector (E-Device) subcutaneously (SC) in the evening as per local Summary of Product Characteristics (SmPC) for 60 days.
Overall Study
Withdrawal by Subject
2

Baseline Characteristics

Saizen® E-Device User Trial

Baseline characteristics by cohort

Baseline characteristics by cohort
Measure
Saizen® E-Device
n=20 Participants
Saizen® (recombinant human growth hormone \[r-hGH\]) injection 8 milligram (mg) per 137 milliliter (mL) was administered using an electronic auto-injector (E-Device) subcutaneously (SC) in the evening as per local Summary of Product Characteristics (SmPC) for 60 days.
Age, Continuous
11.30 years
STANDARD_DEVIATION 2.66 • n=5 Participants
Sex: Female, Male
Female
10 Participants
n=5 Participants
Sex: Female, Male
Male
10 Participants
n=5 Participants

PRIMARY outcome

Timeframe: 2 Weeks

Population: All subjects who were administered with at least 1 dose of study medication with E-Device.

Subjects' overall impression after using E-Device was measured on a scale ranging from 1 to 3, where 1 = bad, 2 = good, and 3 = very good. Number of subjects with response based on overall impression scale were presented.

Outcome measures

Outcome measures
Measure
Saizen® E-Device
n=20 Participants
Saizen® (recombinant human growth hormone \[r-hGH\]) injection 8 milligram (mg) per 137 milliliter (mL) was administered using an electronic auto-injector (E-Device) subcutaneously (SC) in the evening as per local Summary of Product Characteristics (SmPC) for 60 days.
Subjects' Overall Impression After Using E-Device
Good
7 subjects
Subjects' Overall Impression After Using E-Device
Bad
0 subjects
Subjects' Overall Impression After Using E-Device
Very Good
13 subjects

PRIMARY outcome

Timeframe: 2 Weeks

Population: All subjects who were administered with at least 1 dose of study medication with E-Device.

Following functions were assessed: Display of remaining dose in cartridge, Display of last injection date and time, Automatic needle attachment, Audible and visual signals, Dose injected confirmation, Dose history, Customizable needle insertion speed, Customizable drug insertion speed, Customizable insertion depth, Teach me menu, On screen instructions, Customizable name and picture, Pre-programmed dose and Skin sensor. Usefulness and reliability of each of the E-Device functions was measured on a scale ranging from 1 to 3, where 1 = not useful, 2 = useful, and 3 = very useful. Number of subjects with response based on usefulness and reliability scale were presented.

Outcome measures

Outcome measures
Measure
Saizen® E-Device
n=20 Participants
Saizen® (recombinant human growth hormone \[r-hGH\]) injection 8 milligram (mg) per 137 milliliter (mL) was administered using an electronic auto-injector (E-Device) subcutaneously (SC) in the evening as per local Summary of Product Characteristics (SmPC) for 60 days.
Usefulness and Reliability of E-Device Functions
Display of remaining dose in cartridge: Not Useful
0 subjects
Usefulness and Reliability of E-Device Functions
Display of remaining dose in cartridge: Useful
8 subjects
Usefulness and Reliability of E-Device Functions
Display of remaining dose in cartridge:Very Useful
12 subjects
Usefulness and Reliability of E-Device Functions
Display of last injection date/time: Not Useful
3 subjects
Usefulness and Reliability of E-Device Functions
Display of last injection date/time: Useful
11 subjects
Usefulness and Reliability of E-Device Functions
Display of last injection date/time: Very Useful
6 subjects
Usefulness and Reliability of E-Device Functions
Automatic needle attachment: Not Useful
0 subjects
Usefulness and Reliability of E-Device Functions
Automatic needle attachment: Useful
9 subjects
Usefulness and Reliability of E-Device Functions
Automatic needle attachment: Very Useful
11 subjects
Usefulness and Reliability of E-Device Functions
Audible and visual signals: Not Useful
1 subjects
Usefulness and Reliability of E-Device Functions
Audible and visual signals: Useful
9 subjects
Usefulness and Reliability of E-Device Functions
Audible and visual signals: Very Useful
10 subjects
Usefulness and Reliability of E-Device Functions
Dose injected confirmation: Not Useful
2 subjects
Usefulness and Reliability of E-Device Functions
Dose injected confirmation: Useful
10 subjects
Usefulness and Reliability of E-Device Functions
Dose injected confirmation: Very Useful
8 subjects
Usefulness and Reliability of E-Device Functions
Dose history: Not Useful
5 subjects
Usefulness and Reliability of E-Device Functions
Dose history: Useful
10 subjects
Usefulness and Reliability of E-Device Functions
Dose history: Very Useful
5 subjects
Usefulness and Reliability of E-Device Functions
Customizable needle insertion speed: Not Useful
2 subjects
Usefulness and Reliability of E-Device Functions
Customizable needle insertion speed: Useful
9 subjects
Usefulness and Reliability of E-Device Functions
Customizable needle insertion speed: Very Useful
9 subjects
Usefulness and Reliability of E-Device Functions
Customizable drug insertion speed: Not Useful
1 subjects
Usefulness and Reliability of E-Device Functions
Customizable drug insertion speed: Useful
11 subjects
Usefulness and Reliability of E-Device Functions
Customizable drug insertion speed: Very Useful
8 subjects
Usefulness and Reliability of E-Device Functions
Customizable insertion depth: Not Useful
1 subjects
Usefulness and Reliability of E-Device Functions
Customizable insertion depth: Useful
9 subjects
Usefulness and Reliability of E-Device Functions
Customizable insertion depth: Very Useful
10 subjects
Usefulness and Reliability of E-Device Functions
Teach me menu: Not Useful
8 subjects
Usefulness and Reliability of E-Device Functions
Teach me menu: Useful
7 subjects
Usefulness and Reliability of E-Device Functions
Teach me menu: Very Useful
5 subjects
Usefulness and Reliability of E-Device Functions
On screen instructions: Not Useful
0 subjects
Usefulness and Reliability of E-Device Functions
On screen instructions: Useful
6 subjects
Usefulness and Reliability of E-Device Functions
On screen instructions: Very Useful
14 subjects
Usefulness and Reliability of E-Device Functions
Customizable name and picture: Not Useful
13 subjects
Usefulness and Reliability of E-Device Functions
Customizable name and picture: Useful
7 subjects
Usefulness and Reliability of E-Device Functions
Customizable name and picture: Very Useful
0 subjects
Usefulness and Reliability of E-Device Functions
Pre-programmed dose: Not Useful
0 subjects
Usefulness and Reliability of E-Device Functions
Pre-programmed dose: Useful
6 subjects
Usefulness and Reliability of E-Device Functions
Pre-programmed dose: Very Useful
14 subjects
Usefulness and Reliability of E-Device Functions
Skin sensor: Not Useful
2 subjects
Usefulness and Reliability of E-Device Functions
Skin sensor: Useful
8 subjects
Usefulness and Reliability of E-Device Functions
Skin sensor: Very Useful
10 subjects

SECONDARY outcome

Timeframe: Inclusion visit (Day 1)

Population: All subjects who were administered with at least 1 dose of study medication with E-Device.

Subjects' feedback immediately after initial training on the handling and use of E-Device was assessed on scale ranging from 1 to 3, where 1 = difficult, 2 = easy, and 3 = very easy. Subjects were provided training on the following aspects: Cartridge loading, Needle attachment, Needle detachment, Injection process, Navigation in the menu, and Handling of the device. Number of subjects with response based on their feedback were presented.

Outcome measures

Outcome measures
Measure
Saizen® E-Device
n=20 Participants
Saizen® (recombinant human growth hormone \[r-hGH\]) injection 8 milligram (mg) per 137 milliliter (mL) was administered using an electronic auto-injector (E-Device) subcutaneously (SC) in the evening as per local Summary of Product Characteristics (SmPC) for 60 days.
Subjects' Feedback Immediately After Initial Training During Inclusion Visit
Cartridge loading: Difficult
1 subjects
Subjects' Feedback Immediately After Initial Training During Inclusion Visit
Cartridge loading: Easy
17 subjects
Subjects' Feedback Immediately After Initial Training During Inclusion Visit
Cartridge loading: Very Easy
2 subjects
Subjects' Feedback Immediately After Initial Training During Inclusion Visit
Needle attachment: Difficult
2 subjects
Subjects' Feedback Immediately After Initial Training During Inclusion Visit
Needle attachment: Easy
15 subjects
Subjects' Feedback Immediately After Initial Training During Inclusion Visit
Needle attachment: Very Easy
3 subjects
Subjects' Feedback Immediately After Initial Training During Inclusion Visit
Needle detachment: Difficult
7 subjects
Subjects' Feedback Immediately After Initial Training During Inclusion Visit
Needle detachment: Easy
12 subjects
Subjects' Feedback Immediately After Initial Training During Inclusion Visit
Needle detachment: Very Easy
1 subjects
Subjects' Feedback Immediately After Initial Training During Inclusion Visit
Injection process: Difficult
1 subjects
Subjects' Feedback Immediately After Initial Training During Inclusion Visit
Injection process: Easy
16 subjects
Subjects' Feedback Immediately After Initial Training During Inclusion Visit
Injection process: Very Easy
1 subjects
Subjects' Feedback Immediately After Initial Training During Inclusion Visit
Injection process: Missing data
2 subjects
Subjects' Feedback Immediately After Initial Training During Inclusion Visit
Navigation in the menu: Difficult
2 subjects
Subjects' Feedback Immediately After Initial Training During Inclusion Visit
Navigation in the menu: Easy
17 subjects
Subjects' Feedback Immediately After Initial Training During Inclusion Visit
Navigation in the menu: Very Easy
1 subjects
Subjects' Feedback Immediately After Initial Training During Inclusion Visit
Handling of the device: Difficult
1 subjects
Subjects' Feedback Immediately After Initial Training During Inclusion Visit
Handling of the device: Easy
15 subjects
Subjects' Feedback Immediately After Initial Training During Inclusion Visit
Handling of the device: Very Easy
0 subjects
Subjects' Feedback Immediately After Initial Training During Inclusion Visit
Handling of the device: Missing data
4 subjects

SECONDARY outcome

Timeframe: Inclusion visit (Day 1)

Population: All included subjects were analyzed who used at least 1 dose of study medication with E-Device.

Nurse/physician's feedback was assessed for E-Device setting up and Dose programming on inclusion visit using a scale ranging from 1 to 3, where 1 = difficult, 2 = easy, and 3 = very easy. Nurse/Physician's response for the number of subjects were presented.

Outcome measures

Outcome measures
Measure
Saizen® E-Device
n=20 Participants
Saizen® (recombinant human growth hormone \[r-hGH\]) injection 8 milligram (mg) per 137 milliliter (mL) was administered using an electronic auto-injector (E-Device) subcutaneously (SC) in the evening as per local Summary of Product Characteristics (SmPC) for 60 days.
Nurse/Physician's Feedback After E-Device Set up During Inclusion Visit
Dose programming: Missing data
1 subjects
Nurse/Physician's Feedback After E-Device Set up During Inclusion Visit
Device setting up: Difficult
1 subjects
Nurse/Physician's Feedback After E-Device Set up During Inclusion Visit
Device setting up: Easy
19 subjects
Nurse/Physician's Feedback After E-Device Set up During Inclusion Visit
Device setting up: Very Easy
0 subjects
Nurse/Physician's Feedback After E-Device Set up During Inclusion Visit
Dose programming: Difficult
0 subjects
Nurse/Physician's Feedback After E-Device Set up During Inclusion Visit
Dose programming: Easy
19 subjects
Nurse/Physician's Feedback After E-Device Set up During Inclusion Visit
Dose programming: Very Easy
0 subjects

SECONDARY outcome

Timeframe: Day 1 up to Day 90

Population: All subjects who were administered with at least 1 dose of study medication with E-Device.

An Adverse Event (AE) was defined as any new untoward medical occurrences/worsening of pre-existing medical condition without regard to possibility of causal relationship. A Serious AE was an AE that resulted in any of the following outcomes: death; life threatening; persistent/significant disability/incapacity; initial or prolonged inpatient hospitalization; congenital anomaly/birth defect, AEs leading to discontinuation and AEs leading to death.

Outcome measures

Outcome measures
Measure
Saizen® E-Device
n=20 Participants
Saizen® (recombinant human growth hormone \[r-hGH\]) injection 8 milligram (mg) per 137 milliliter (mL) was administered using an electronic auto-injector (E-Device) subcutaneously (SC) in the evening as per local Summary of Product Characteristics (SmPC) for 60 days.
Number of Subjects With Adverse Events (AEs) or Serious Adverse Events (SAEs)
AEs
0 subjects
Number of Subjects With Adverse Events (AEs) or Serious Adverse Events (SAEs)
SAEs
0 subjects

Adverse Events

Saizen® E-Device

Serious events: 0 serious events
Other events: 0 other events
Deaths: 0 deaths

Serious adverse events

Adverse event data not reported

Other adverse events

Adverse event data not reported

Additional Information

Merck KGaA Communication Center

Merck Healthcare, a business of Merck KGaA, Darmstadt, Germany

Phone: +49-6151-72-5200

Results disclosure agreements

  • Principal investigator is a sponsor employee
  • Publication restrictions are in place

Restriction type: OTHER