Trial Outcomes & Findings for Gel-200 Versus Placebo in Osteoarthritis of the Knee (NCT NCT00449696)

NCT ID: NCT00449696

Last Updated: 2011-10-07

Results Overview

Observed WOMAC pain subscore on VAS of 100 mm; 0 mm meaning no pain; 100 mm meaning extreme pain. Change in score from baseline to week 13 was calculated as baseline minus week 13. Primary endpoint was the model estimated difference between Gel-200 and PBS placebo.

Recruitment status

COMPLETED

Study phase

PHASE3

Target enrollment

379 participants

Primary outcome timeframe

Baseline and Week 13

Results posted on

2011-10-07

Participant Flow

A total of 598 patients were screened.

Participant milestones

Participant milestones
Measure
Gel-200
Patients received 1 single dose of Gel-200 (3mL) intra-articular injection into knee joint.
PBS Placebo
Patients received 1 single dose of Phosphate Buffered Saline (PBS) placebo (3mL) intra-articular injection into knee joint.
Overall Study
STARTED
251
128
Overall Study
Received Injection
249
128
Overall Study
Analyzed Participants
247
128
Overall Study
COMPLETED
231
119
Overall Study
NOT COMPLETED
20
9

Reasons for withdrawal

Reasons for withdrawal
Measure
Gel-200
Patients received 1 single dose of Gel-200 (3mL) intra-articular injection into knee joint.
PBS Placebo
Patients received 1 single dose of Phosphate Buffered Saline (PBS) placebo (3mL) intra-articular injection into knee joint.
Overall Study
Other Treatment Required
6
1
Overall Study
Withdrawal by Subject
5
5
Overall Study
Lost to Follow-up
2
3
Overall Study
Others
7
0

Baseline Characteristics

Gel-200 Versus Placebo in Osteoarthritis of the Knee

Baseline characteristics by cohort

Baseline characteristics by cohort
Measure
Gel-200
n=247 Participants
Patients received 1 single dose of Gel-200 (3mL) intra-articular injection into knee joint.
PBS Placebo
n=128 Participants
Patients received 1 single dose of Phosphate Buffered Saline (PBS) placebo (3mL) intra-articular injection into knee joint.
Total
n=375 Participants
Total of all reporting groups
Age Continuous
60.9 years
STANDARD_DEVIATION 10.24 • n=5 Participants
60.3 years
STANDARD_DEVIATION 9.97 • n=7 Participants
60.7 years
STANDARD_DEVIATION 10.14 • n=5 Participants
Sex: Female, Male
Female
147 Participants
n=5 Participants
77 Participants
n=7 Participants
224 Participants
n=5 Participants
Sex: Female, Male
Male
100 Participants
n=5 Participants
51 Participants
n=7 Participants
151 Participants
n=5 Participants
Region of Enrollment
United States
247 participants
n=5 Participants
128 participants
n=7 Participants
375 participants
n=5 Participants
Body Mass Index (BMI)
28.3 kilograms/meters square
STANDARD_DEVIATION 4.14 • n=5 Participants
28.7 kilograms/meters square
STANDARD_DEVIATION 3.83 • n=7 Participants
28.5 kilograms/meters square
STANDARD_DEVIATION 4.04 • n=5 Participants
WOMAC VAS Pain Subscore
70.7 scores on a scale
STANDARD_DEVIATION 14.42 • n=5 Participants
68.0 scores on a scale
STANDARD_DEVIATION 13.05 • n=7 Participants
69.8 scores on a scale
STANDARD_DEVIATION 14.01 • n=5 Participants
WOMAC VAS Stiffness Subscore
71.6 scores on a scale
STANDARD_DEVIATION 17.48 • n=5 Participants
69.3 scores on a scale
STANDARD_DEVIATION 17.31 • n=7 Participants
70.8 scores on a scale
STANDARD_DEVIATION 17.43 • n=5 Participants
WOMAC VAS Physical Function Subcore
68.9 scores on a scale
STANDARD_DEVIATION 17.41 • n=5 Participants
67.6 scores on a scale
STANDARD_DEVIATION 15.80 • n=7 Participants
68.5 scores on a scale
STANDARD_DEVIATION 16.87 • n=5 Participants
WOMAC VAS Total Score
69.5 scores on a scale
STANDARD_DEVIATION 15.99 • n=5 Participants
67.8 scores on a scale
STANDARD_DEVIATION 14.68 • n=7 Participants
68.9 scores on a scale
STANDARD_DEVIATION 15.56 • n=5 Participants
Subject Global Evaluations
64.7 scores on a scale
STANDARD_DEVIATION 21.83 • n=5 Participants
66.5 scores on a scale
STANDARD_DEVIATION 21.21 • n=7 Participants
65.3 scores on a scale
STANDARD_DEVIATION 21.61 • n=5 Participants
Physician Global Evaluations
61.5 scores on a scale
STANDARD_DEVIATION 14.79 • n=5 Participants
64.2 scores on a scale
STANDARD_DEVIATION 14.25 • n=7 Participants
62.4 scores on a scale
STANDARD_DEVIATION 14.65 • n=5 Participants

PRIMARY outcome

Timeframe: Baseline and Week 13

Population: ITT population was used for analysis. 2 patients with Gel-200 were removed from ITT population analysis and baseline because of no post treatment data according to a pre-specified rule. These data were submitted to FDA.

Observed WOMAC pain subscore on VAS of 100 mm; 0 mm meaning no pain; 100 mm meaning extreme pain. Change in score from baseline to week 13 was calculated as baseline minus week 13. Primary endpoint was the model estimated difference between Gel-200 and PBS placebo.

Outcome measures

Outcome measures
Measure
Gel-200
n=247 Participants
Patients received 1 single dose of Gel-200 (3mL) intra-articular injection into knee joint.
PBS Placebo
n=128 Participants
Patients received 1 single dose of Phosphate Buffered Saline (PBS) placebo (3mL) intra-articular injection into knee joint.
Change From Baseline in Western Ontario and McMaster Universities Osteoarthritis Index (WOMAC) Visual Analog Scale (VAS) Pain Subscore
27.8 scores on a scale
Standard Deviation 29.26
22.6 scores on a scale
Standard Deviation 29.31

SECONDARY outcome

Timeframe: Baseline and Week 13

Population: ITT population was used for analysis. 2 patients with Gel-200 were removed from ITT population analysis and baseline because of no post treatment data according to a pre-specified rule. These data were submitted to FDA.

Observed WOMAC stiffness subscore on Visual Analog Scale (VAS) of 100 mm; 0 mm meaning no stiffness; 100 mm meaning extreme stiffness. Change in score from baseline to week 13 was calculated as baseline minus week 13. Primary endpoint was the model estimated difference between Gel-200 and PBS placebo.

Outcome measures

Outcome measures
Measure
Gel-200
n=247 Participants
Patients received 1 single dose of Gel-200 (3mL) intra-articular injection into knee joint.
PBS Placebo
n=128 Participants
Patients received 1 single dose of Phosphate Buffered Saline (PBS) placebo (3mL) intra-articular injection into knee joint.
Change From Baseline in WOMAC VAS Stiffness Subscore
26.9 scores on a scale
Standard Deviation 30.46
22.5 scores on a scale
Standard Deviation 28.66

SECONDARY outcome

Timeframe: Baseline and Week 13

Population: ITT population was used for analysis. 2 patients with Gel-200 were removed from ITT population analysis and baseline because of no post treatment data according to a pre-specified rule. These data were submitted to FDA.

Observed WOMAC physical function subscore on Visual Analog Scale (VAS) of 100 mm; 0 mm meaning no difficulty; 100 mm meaning extreme difficulty. Change in score from baseline to week 13 was calculated as baseline minus week 13. Primary endpoint was the model estimated difference between Gel-200 and PBS placebo.

Outcome measures

Outcome measures
Measure
Gel-200
n=247 Participants
Patients received 1 single dose of Gel-200 (3mL) intra-articular injection into knee joint.
PBS Placebo
n=128 Participants
Patients received 1 single dose of Phosphate Buffered Saline (PBS) placebo (3mL) intra-articular injection into knee joint.
Change From Baseline in WOMAC VAS Physical Function Subscore
26.2 scores on a scale
Standard Deviation 28.81
21.0 scores on a scale
Standard Deviation 28.62

SECONDARY outcome

Timeframe: Baseline and Week 13

Population: ITT population was used for analysis. 2 patients with Gel-200 were removed from ITT population analysis and baseline because of no post treatment data according to a pre-specified rule. These data were submitted to FDA.

Mean of all WOMAC pain, stiffness and physical function subscores on Visual Analog Scale (VAS) of 100 mm; 0 mm meaning no pain, stiffness and difficulty; 100 mm meaning extreme pain, stiffness and difficulty. Change in score from baseline to week 13 was calculated as baseline minus week 13. Primary endpoint was the model estimated difference between Gel-200 and PBS placebo.

Outcome measures

Outcome measures
Measure
Gel-200
n=247 Participants
Patients received 1 single dose of Gel-200 (3mL) intra-articular injection into knee joint.
PBS Placebo
n=128 Participants
Patients received 1 single dose of Phosphate Buffered Saline (PBS) placebo (3mL) intra-articular injection into knee joint.
Change From Baseline in WOMAC VAS Total Score
26.6 scores on a scale
Standard Deviation 28.41
21.5 scores on a scale
Standard Deviation 28.37

SECONDARY outcome

Timeframe: Weeks 6 to 13

Population: ITT population was used for analysis. 2 patients with Gel-200 were removed from ITT population analysis and baseline because of no post treatment data according to a pre-specified rule. These data were submitted to FDA.

Outcome Measures in Rheumatology Clinical Trials and Osteoarthritis Research Society International (OMERACT-OARSI) strict responses defined by changes from baseline in WOMAC pain or physical function subscore ≥50% with absolute changes ≥20 mm (termed strict responders), or ≥20% with absolute changes ≥10mm in 2 of 3 measures of WOMAC pain or physical function subscore or subject global evaluations (termed responders).

Outcome measures

Outcome measures
Measure
Gel-200
n=247 Participants
Patients received 1 single dose of Gel-200 (3mL) intra-articular injection into knee joint.
PBS Placebo
n=128 Participants
Patients received 1 single dose of Phosphate Buffered Saline (PBS) placebo (3mL) intra-articular injection into knee joint.
Outcome Measures in Rheumatology Arthritis Clinical Trials (OMERACT)- and the Osteoarthritis Research Society International (OARSI) Response
Participants who met strict responders at Week 13
45.9 Percentage
38.7 Percentage
Outcome Measures in Rheumatology Arthritis Clinical Trials (OMERACT)- and the Osteoarthritis Research Society International (OARSI) Response
Participants who met responders at Week 13
61.0 Percentage
54.6 Percentage

SECONDARY outcome

Timeframe: Baseline and Week 13

Population: ITT population was used for analysis. 2 patients with Gel-200 were removed from ITT population analysis and baseline because of no post treatment data according to a pre-specified rule. These data were submitted to FDA.

Scored on physical component scale from 0 (negative health) to 100 (positive health). Calculated norm based with a mean of 50 and a standard deviation of 10.

Outcome measures

Outcome measures
Measure
Gel-200
n=247 Participants
Patients received 1 single dose of Gel-200 (3mL) intra-articular injection into knee joint.
PBS Placebo
n=128 Participants
Patients received 1 single dose of Phosphate Buffered Saline (PBS) placebo (3mL) intra-articular injection into knee joint.
Change From Baseline in Short Form - 36 (SF-36)
4.6 scores
Standard Deviation 9.34
5.3 scores
Standard Deviation 9.04

SECONDARY outcome

Timeframe: Baseline and Week 13

Population: ITT population was used for analysis. 2 patients with Gel-200 were removed from ITT population analysis and baseline because of no post treatment data according to a pre-specified rule. These data were submitted to FDA.

Observed subject evaluations on Visual Analog Scale (VAS) of 100 mm; 0 mm meaning excellent feeling in knee joint; 100 mm meaning poor feeling in knee joint. Change in score from baseline to week 13 was calculated as baseline minus week 13. Primary endpoint was the model estimated difference between Gel-200 and PBS placebo.

Outcome measures

Outcome measures
Measure
Gel-200
n=247 Participants
Patients received 1 single dose of Gel-200 (3mL) intra-articular injection into knee joint.
PBS Placebo
n=128 Participants
Patients received 1 single dose of Phosphate Buffered Saline (PBS) placebo (3mL) intra-articular injection into knee joint.
Change From Baseline in Subject Global Evaluations
22.8 scores on a scale
Standard Deviation 33.08
22.0 scores on a scale
Standard Deviation 30.58

SECONDARY outcome

Timeframe: Baseline and Week 13

Population: ITT population was used for analysis. 2 patients with Gel-200 were removed from ITT population analysis and baseline because of no post treatment data according to a pre-specified rule.

Observed physician global evaluations on Visual Analog Scale (VAS) of 100 mm; 0 mm meaning excellent feeling in knee joint; 100 mm meaning poor feeling in knee joint. Change in score from baseline to week 13 was calculated as baseline minus week 13. Primary endpoint was the model estimated difference between Gel-200 and PBS placebo.

Outcome measures

Outcome measures
Measure
Gel-200
n=247 Participants
Patients received 1 single dose of Gel-200 (3mL) intra-articular injection into knee joint.
PBS Placebo
n=128 Participants
Patients received 1 single dose of Phosphate Buffered Saline (PBS) placebo (3mL) intra-articular injection into knee joint.
Change From Baseline in Physician Global Evaluations
21.3 scores on a scale
Standard Deviation 28.46
19.0 scores on a scale
Standard Deviation 26.97

SECONDARY outcome

Timeframe: Weeks 9 to 13 (5 weeks)

Population: ITT population was used for analysis. 2 patients with Gel-200 were removed from ITT population analysis and baseline because of no post treatment data according to a pre-specified rule. These data were submitted to FDA.

Weekly mean acetaminophen consumption between weeks 9 and 13.

Outcome measures

Outcome measures
Measure
Gel-200
n=247 Participants
Patients received 1 single dose of Gel-200 (3mL) intra-articular injection into knee joint.
PBS Placebo
n=128 Participants
Patients received 1 single dose of Phosphate Buffered Saline (PBS) placebo (3mL) intra-articular injection into knee joint.
Acetaminophen Consumption
2007 milligrams
Standard Deviation 3687
2599 milligrams
Standard Deviation 3806

Adverse Events

Gel-200

Serious events: 8 serious events
Other events: 122 other events
Deaths: 0 deaths

PBS Placebo

Serious events: 0 serious events
Other events: 55 other events
Deaths: 0 deaths

Serious adverse events

Serious adverse events
Measure
Gel-200
n=249 participants at risk
Patients received 1 single dose of Gel-200 (3mL) intra-articular injection into knee joint.
PBS Placebo
n=128 participants at risk
Patients received 1 single dose of Phosphate Buffered Saline (PBS) placebo (3mL) intra-articular injection into knee joint.
Cardiac disorders
Cardiac arrest
0.40%
1/249 • Number of events 1
0.00%
0/128
Eye disorders
Vision blurred
0.40%
1/249 • Number of events 1
0.00%
0/128
Gastrointestinal disorders
Abdominal pain
0.40%
1/249 • Number of events 2
0.00%
0/128
Gastrointestinal disorders
Femoral hernia
0.40%
1/249 • Number of events 1
0.00%
0/128
Hepatobiliary disorders
Cryptogenic cirrhosis
0.40%
1/249 • Number of events 1
0.00%
0/128
Metabolism and nutrition disorders
Hypokalemia
0.40%
1/249 • Number of events 1
0.00%
0/128
Neoplasms benign, malignant and unspecified (incl cysts and polyps)
Basal cell carcinoma
0.40%
1/249 • Number of events 1
0.00%
0/128
Neoplasms benign, malignant and unspecified (incl cysts and polyps)
Breast cancer
0.40%
1/249 • Number of events 1
0.00%
0/128
Neoplasms benign, malignant and unspecified (incl cysts and polyps)
Malignant melanoma
0.40%
1/249 • Number of events 1
0.00%
0/128
Neoplasms benign, malignant and unspecified (incl cysts and polyps)
Prostate cancer
0.40%
1/249 • Number of events 1
0.00%
0/128
Neoplasms benign, malignant and unspecified (incl cysts and polyps)
Squamous cell carcinoma
0.40%
1/249 • Number of events 1
0.00%
0/128
Nervous system disorders
Dizziness
0.40%
1/249 • Number of events 1
0.00%
0/128
Nervous system disorders
Transient Ischemic attack
0.40%
1/249 • Number of events 1
0.00%
0/128
Renal and urinary disorders
Renal failure acute
0.40%
1/249 • Number of events 1
0.00%
0/128
Respiratory, thoracic and mediastinal disorders
Acute pulmonary oedema
0.40%
1/249 • Number of events 1
0.00%
0/128
Respiratory, thoracic and mediastinal disorders
Exertional Dyspnea
0.40%
1/249 • Number of events 1
0.00%
0/128
Respiratory, thoracic and mediastinal disorders
Respiratory arrest
0.40%
1/249 • Number of events 1
0.00%
0/128
Respiratory, thoracic and mediastinal disorders
Respiratory failure
0.40%
1/249 • Number of events 1
0.00%
0/128

Other adverse events

Other adverse events
Measure
Gel-200
n=249 participants at risk
Patients received 1 single dose of Gel-200 (3mL) intra-articular injection into knee joint.
PBS Placebo
n=128 participants at risk
Patients received 1 single dose of Phosphate Buffered Saline (PBS) placebo (3mL) intra-articular injection into knee joint.
Infections and infestations
Upper respiratory tract infections
6.4%
16/249 • Number of events 16
4.7%
6/128 • Number of events 6
Musculoskeletal and connective tissue disorders
Joint swelling
28.1%
70/249 • Number of events 91
28.1%
36/128 • Number of events 42
Musculoskeletal and connective tissue disorders
Joint effusion
23.3%
58/249 • Number of events 69
25.8%
33/128 • Number of events 40
Musculoskeletal and connective tissue disorders
Arthralgia
17.7%
44/249 • Number of events 55
11.7%
15/128 • Number of events 22

Additional Information

Clinical Development Dept.

Seikagaku Corporation

Phone: 81-3-5220-8950

Results disclosure agreements

  • Principal investigator is a sponsor employee SKK has the right to review the disclosures. Investigator shall not make any publication of study data, information, results or similar information without the express of permission of SKK.
  • Publication restrictions are in place

Restriction type: OTHER