A Study of Belimumab in Subjects With Systemic Lupus Erythematosus (SLE)

NCT ID: NCT00424476

Last Updated: 2016-12-12

Study Results

Results available

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Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE3

Total Enrollment

865 participants

Study Classification

INTERVENTIONAL

Study Start Date

2007-05-31

Study Completion Date

2010-03-31

Brief Summary

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The purpose of this study is to evaluate the efficacy, safety, tolerability, and impact on quality of life of two different doses of belimumab administered in addition to standard therapy in subjects with active, autoantibody-positive systemic lupus erythematosus (SLE) disease.

Detailed Description

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Conditions

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Systemic Lupus Erythematosus

Keywords

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Autoimmune Diseases Lupus SLE Systemic Lupus Erythematosus Belimumab Antibodies

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

DOUBLE

Participants Investigators

Study Groups

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Placebo

Placebo

Group Type PLACEBO_COMPARATOR

Placebo

Intervention Type DRUG

Placebo IV plus standard therapy; placebo administered on Days 0, 14, 28, and every 28 days thereafter through Week 48.

Belimumab 1 mg/kg

Belimumab 1 mg/kg

Group Type EXPERIMENTAL

Belimumab 1 mg/kg

Intervention Type DRUG

Belimumab 1 mg/kg IV plus standard therapy on Days 0, 14, 28, and every 28 days thereafter through Week 48.

Belimumab 10 mg/kg

Belimumab 10 mg/kg

Group Type EXPERIMENTAL

Belimumab 10 mg/kg

Intervention Type DRUG

Belimumab 10 mg/kg IV plus standard therapy on Days 0, 14, 28, and every 28 days thereafter through Week 48.

Interventions

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Placebo

Placebo IV plus standard therapy; placebo administered on Days 0, 14, 28, and every 28 days thereafter through Week 48.

Intervention Type DRUG

Belimumab 1 mg/kg

Belimumab 1 mg/kg IV plus standard therapy on Days 0, 14, 28, and every 28 days thereafter through Week 48.

Intervention Type DRUG

Belimumab 10 mg/kg

Belimumab 10 mg/kg IV plus standard therapy on Days 0, 14, 28, and every 28 days thereafter through Week 48.

Intervention Type DRUG

Other Intervention Names

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BENLYSTA™ (formerly LymphoStat-B™) BENLYSTA™ (formerly LymphoStat-B™)

Eligibility Criteria

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Inclusion Criteria

* Clinical diagnosis of SLE by ACR criteria.
* Active SLE disease.
* Autoantibody-positive.
* On stable SLE treatment regimen.

Exclusion Criteria

* Pregnant or nursing
* Have received treatment with any B cell targeted therapy.
* Have received treatment with a biological investigational agent in the past year.
* Have received IV cyclophosphamide within 180 days of Day 0.
* Have severe lupus kidney disease.
* Have active central nervous system (CNS) lupus.
* Have required management of acute or chronic infections within the past 60 days.
* Have current drug or alcohol abuse or dependence.
* Have a historically positive test or test positive at screening for HIV, hepatitis B, or hepatitis C.
Minimum Eligible Age

18 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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GlaxoSmithKline

INDUSTRY

Sponsor Role collaborator

Human Genome Sciences Inc.

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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GSK Clinical Trials

Role: STUDY_DIRECTOR

Human Genome Sciences Inc.

Locations

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OMI, Organización Médica de Investigación

Buenos Aires, , Argentina

Site Status

CIER, Centro de Investigaciones en Enfermedades Reumáticas

Buenos Aires, , Argentina

Site Status

Hospital Britanico de Buenos Aires

Buenos Aires, , Argentina

Site Status

Hospital General de Agudos Carlos G. Durand

Buenos Aires, , Argentina

Site Status

Centro Privado de Medicina Familiar

Buenos Aires, , Argentina

Site Status

Hospital Sirio Libanes

Buenos Aires, , Argentina

Site Status

Atencion Integral en Reumatologia

Buenos Aires, , Argentina

Site Status

Instituto de Investigaciones Medicas

Buenos Aires, , Argentina

Site Status

Hospital Interzonal General San Martín

La Plata, , Argentina

Site Status

CAICI, Instituto Centralizado de Asistencia e Investigación Clínica Integral

Rosario, , Argentina

Site Status

Centro Medico Privado de Reumatologia

San Miguel de Tucumán, , Argentina

Site Status

Repatriation Hospital

Daw Park, , Australia

Site Status

Emeritus Research, Cabrini Hospital

Melbourne, , Australia

Site Status

Monash Medical Centre

Melbourne, , Australia

Site Status

Royal Perth Hospital

Shenton Park, , Australia

Site Status

Hospital de Clínicas - UNICAMP

Campinas, , Brazil

Site Status

Hospital das Clínicas - Universidade do Paraná

Curitiba, , Brazil

Site Status

Hospital de Clínicas - Universidade Federal de Pernambuco

Fortaleza, , Brazil

Site Status

Hospital Geral de Goiânia

Goiânia, , Brazil

Site Status

Hospital Universitário - Universidade Federal de Juiz de Fora

Juiz de Fora, , Brazil

Site Status

Hospital São Lucas da PUC-RS

Porto Alegre, , Brazil

Site Status

Hospital Universitário Pedro Ernesto - UERJ

Rio de Janeiro, , Brazil

Site Status

Hospital Unversitario Clementino Fraga Filho UFRJ

Rio de Janeiro, , Brazil

Site Status

Hospital Santa Izabel

Salvador, , Brazil

Site Status

Hospital Abreu Sodré

São Paulo, , Brazil

Site Status

Hospital do Servidor Público Estadual de São Paulo - Francisco Morato de Oliveira

São Paulo, , Brazil

Site Status

Hospital Heliópolis

São Paulo, , Brazil

Site Status

Hospital Dr. Sotero del Rio

Santiago, , Chile

Site Status

Pontificia Universidad Católica de Chile

Santiago, , Chile

Site Status

Clínica Dávila

Santiago, , Chile

Site Status

Hospital Dr. Gustavo Fricke

Viña del Mar, , Chile

Site Status

Office of Dr. Guzman

Bogota, Cundinamarca, Colombia

Site Status

Fundación Oftalmologica de Santander Clinica Carlos Ardila Lulle

Bucaramanga, Santander Department, Colombia

Site Status

Centro de Reumatologia y Ortopedia

Barranquilla, , Colombia

Site Status

Centrode de Investigaciones en Reumatologia Especialidades Medicas (CIREEH)

Bogotá, , Colombia

Site Status

Fundación Instituto de Reumatología Fernando Chalem

Bogotá, , Colombia

Site Status

Riesgo de Fracturas

Bogotá, , Colombia

Site Status

SERVIMED

Bucaramanga, , Colombia

Site Status

Corporación para Investigaciones Biológicas (CIB)

Medellín, , Colombia

Site Status

Office of Dr. Jose Molina

Medellín, , Colombia

Site Status

Pamela Youde Nethersole Eastern Hospital

Chai Wan, , Hong Kong

Site Status

Rheumatology Assessment and Treatment Center, Pok Oi Hospital

Shatin, , Hong Kong

Site Status

Tuen Mun Hospital

Tuenmen, , Hong Kong

Site Status

St. John's Medical College Hospital

Bangalore, , India

Site Status

Krishna Institute of Medical Sciences

Hyderabaad, , India

Site Status

Nizam's Institute of Medical Sciences

Hyderabaad, , India

Site Status

Apollo Hospitals

Hyderabad, , India

Site Status

Chhatrapati Shahuji Maharaj Medical University

Lucknow, , India

Site Status

King Edward Memorial (K.E.M.) Hospital

Mumbai, , India

Site Status

Kerala Institute of Medical Sciences

Trivandrum, , India

Site Status

Hospital Nacional Alberto Sabogal Sologuren ESSALUD

Lima, , Peru

Site Status

Hospital Nacional Guillermo Almenara Irigoyen ESSALUD

Lima, , Peru

Site Status

Clinica Ricardo Palma Anexo 9 - Javier Prado Este

Lima, , Peru

Site Status

Instituto de Ginecología y Reproducción

Lima, , Peru

Site Status

Chong Hua Hospital

Cebu City, , Philippines

Site Status

Davao Medical Center

Davao City, , Philippines

Site Status

University of Perpetual Help -Rizal

Las Piñas, , Philippines

Site Status

Philippine General Hospital

Manila, , Philippines

Site Status

University of Santo Tomas Hospital

Manila, , Philippines

Site Status

St. Luke's Medical Center

Quezon City, , Philippines

Site Status

Spitalul Clinic Sf Maria

Bucharest, , Romania

Site Status

Spitalul Clinic Colentina

Bucharest, , Romania

Site Status

Spitalul de Urgenta al Ministerului Administratiei si Internelor Prof. Dr. Dimitrie Gerota

Bucharest, , Romania

Site Status

Spitalul Clinic Dr. Ion Cantacuzino

Bucharest, , Romania

Site Status

Spitalul Clinic Judetean de Urgenta Cluj-Napoca

Cluj-Napoca, , Romania

Site Status

State Institution Scientific Research Institute of Rheumatology

Moscow, , Russia

Site Status

St. Petersburg City Hospital (Rheumatology Center)

Saint Petersburg, , Russia

Site Status

Academy of Post-Graduated Education

Saint Petersburg, , Russia

Site Status

St.-Petersburg Region Clinical Hospital

Saint Petersburg, , Russia

Site Status

Soloviev's City Clinical Hospital,

Yaroslavl, , Russia

Site Status

City Healthcare Institution Municipal Hospital NPZ,

Yaroslavl, , Russia

Site Status

Kyungpook National Univesity Hospital

Daegu, , South Korea

Site Status

Eulji University Hospital

Daejeon, , South Korea

Site Status

Inha University Hospital

Inchon, , South Korea

Site Status

Dong-A University Hospital 3-1 (Dept. Rhuematology)

Pusan, , South Korea

Site Status

Pusan National University Hospital

Pusan, , South Korea

Site Status

Seoul National University Hospital

Seoul, , South Korea

Site Status

The Hospital for Rheumatic Diseases, Hanyang University Hospital

Seoul, , South Korea

Site Status

Catholic Universtigy of Korea, Kangnam St. Mary's Hospital

Seoul, , South Korea

Site Status

Catholic University, Yoido St. Mary's Hospital

Seoul, , South Korea

Site Status

Ajou University Hospital

Suwon, , South Korea

Site Status

Buddhist Tzu Chi General Hospital, Dalin

Chiayi City, , Taiwan

Site Status

Buddhist Tzu Chi General Hospital - Hualien

Haulien, , Taiwan

Site Status

Chung-Ho Memorial Hospital, Kaohsiung Medical University

Kaohsiung City, , Taiwan

Site Status

Kaohsiung Veterans General Hospital

Kaohsiung City, , Taiwan

Site Status

Chang Gung Memorial Hospital, Kaosiung

Kaosiung, , Taiwan

Site Status

Chang Gung Memorial Hospital-Keelung

Keelung, , Taiwan

Site Status

Chung Shan Medical University Hospital

Taichung, , Taiwan

Site Status

China Medical University Hospital

Taichung, , Taiwan

Site Status

Taichung Veterans General Hospital

Taichung, , Taiwan

Site Status

National Taiwan University Hospital

Taipei, , Taiwan

Site Status

Chang Gung Memorial Hospital, Linko

Tau-Yuan County, , Taiwan

Site Status

Countries

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Bulgaria China Argentina Australia Brazil Chile Colombia Hong Kong India Peru Philippines Romania Russia South Korea Taiwan

References

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Botto J, Cetrez N, Nikolopoulos D, Regardt M, Heintz E, Lindblom J, Parodis I. Predicting EQ-5D full health state in systemic lupus erythematosus using machine learning algorithms. Rheumatol Adv Pract. 2025 Apr 18;9(2):rkaf032. doi: 10.1093/rap/rkaf032. eCollection 2025.

Reference Type DERIVED
PMID: 40256631 (View on PubMed)

Nikolopoulos D, Cetrez N, Lindblom J, Parodis I. Neuropsychiatric involvement in systemic lupus erythematosus contributes to organ damage beyond the nervous system: a post-hoc analysis of 5 phase III randomized clinical trials. Rheumatol Int. 2024 Sep;44(9):1679-1689. doi: 10.1007/s00296-024-05667-5. Epub 2024 Aug 8.

Reference Type DERIVED
PMID: 39115551 (View on PubMed)

Jesus D, Henriques C, Matos A, Doria A, Ines LS. Systemic Lupus Erythematosus Disease Activity Score Remission and Low Disease Activity States Discriminate Drug From Placebo and Better Health-Related Quality of Life. Arthritis Care Res (Hoboken). 2024 Jun;76(6):788-795. doi: 10.1002/acr.25305. Epub 2024 Feb 29.

Reference Type DERIVED
PMID: 38258369 (View on PubMed)

Jagerback S, Gomez A, Parodis I. Predictors of renal flares in systemic lupus erythematosus: a post-hoc analysis of four phase III clinical trials of belimumab. Rheumatology (Oxford). 2025 Feb 1;64(2):623-631. doi: 10.1093/rheumatology/keae023.

Reference Type DERIVED
PMID: 38216728 (View on PubMed)

Emamikia S, Oon S, Gomez A, Lindblom J, Borg A, Enman Y, Morand E, Grannas D, van Vollenhoven RF, Nikpour M, Parodis I. Impact of remission and low disease activity on health-related quality of life in patients with systemic lupus erythematosus. Rheumatology (Oxford). 2022 Nov 28;61(12):4752-4762. doi: 10.1093/rheumatology/keac185.

Reference Type DERIVED
PMID: 35302581 (View on PubMed)

Gupta SV, Fanget MC, MacLauchlin C, Clausen VA, Li J, Cloutier D, Shen L, Robbie GJ, Mogalian E. Clinical and Preclinical Single-Dose Pharmacokinetics of VIR-2218, an RNAi Therapeutic Targeting HBV Infection. Drugs R D. 2021 Dec;21(4):455-465. doi: 10.1007/s40268-021-00369-w. Epub 2021 Nov 6.

Reference Type DERIVED
PMID: 34741731 (View on PubMed)

Zhou X, Lee TI, Zhu M, Ma P. Prediction of Belimumab Pharmacokinetics in Chinese Pediatric Patients with Systemic Lupus Erythematosus. Drugs R D. 2021 Dec;21(4):407-417. doi: 10.1007/s40268-021-00363-2. Epub 2021 Oct 9.

Reference Type DERIVED
PMID: 34628605 (View on PubMed)

Brunner HI, Abud-Mendoza C, Mori M, Pilkington CA, Syed R, Takei S, Viola DO, Furie RA, Navarra S, Zhang F, Bass DL, Eriksson G, Hammer AE, Ji BN, Okily M, Roth DA, Quasny H, Ruperto N. Efficacy and safety of belimumab in paediatric and adult patients with systemic lupus erythematosus: an across-study comparison. RMD Open. 2021 Sep;7(3):e001747. doi: 10.1136/rmdopen-2021-001747.

Reference Type DERIVED
PMID: 34531304 (View on PubMed)

Rendas-Baum R, Baranwal N, Joshi AV, Park J, Kosinski M. Psychometric properties of FACIT-Fatigue in systemic lupus erythematosus: a pooled analysis of three phase 3 randomised, double-blind, parallel-group controlled studies (BLISS-SC, BLISS-52, BLISS-76). J Patient Rep Outcomes. 2021 Apr 8;5(1):33. doi: 10.1186/s41687-021-00298-x.

Reference Type DERIVED
PMID: 33830377 (View on PubMed)

Maslen T, Bruce IN, D'Cruz D, Ianosev M, Bass DL, Wilkinson C, Roth DA. Efficacy of belimumab in two serologically distinct high disease activity subgroups of patients with systemic lupus erythematosus: post-hoc analysis of data from the phase III programme. Lupus Sci Med. 2021 Feb;8(1):e000459. doi: 10.1136/lupus-2020-000459.

Reference Type DERIVED
PMID: 33568389 (View on PubMed)

Gomez A, Hani Butrus F, Johansson P, Akerstrom E, Soukka S, Emamikia S, Enman Y, Pettersson S, Parodis I. Impact of overweight and obesity on patient-reported health-related quality of life in systemic lupus erythematosus. Rheumatology (Oxford). 2021 Mar 2;60(3):1260-1272. doi: 10.1093/rheumatology/keaa453.

Reference Type DERIVED
PMID: 32918459 (View on PubMed)

van Vollenhoven RF, Navarra SV, Levy RA, Thomas M, Heath A, Lustine T, Adamkovic A, Fettiplace J, Wang ML, Ji B, Roth D. Long-term safety and limited organ damage in patients with systemic lupus erythematosus treated with belimumab: a Phase III study extension. Rheumatology (Oxford). 2020 Feb 1;59(2):281-291. doi: 10.1093/rheumatology/kez279.

Reference Type DERIVED
PMID: 31302695 (View on PubMed)

Furie R, Petri MA, Strand V, Gladman DD, Zhong ZJ, Freimuth WW; BLISS-52 and BLISS-76 Study Groups. Clinical, laboratory and health-related quality of life correlates of Systemic Lupus Erythematosus Responder Index response: a post hoc analysis of the phase 3 belimumab trials. Lupus Sci Med. 2014 Jun 26;1(1):e000031. doi: 10.1136/lupus-2014-000031. eCollection 2014.

Reference Type DERIVED
PMID: 25396065 (View on PubMed)

Petri MA, van Vollenhoven RF, Buyon J, Levy RA, Navarra SV, Cervera R, Zhong ZJ, Freimuth WW; BLISS-52 and BLISS-76 Study Groups. Baseline predictors of systemic lupus erythematosus flares: data from the combined placebo groups in the phase III belimumab trials. Arthritis Rheum. 2013 Aug;65(8):2143-53. doi: 10.1002/art.37995.

Reference Type DERIVED
PMID: 23754628 (View on PubMed)

Strand V, Levy RA, Cervera R, Petri MA, Birch H, Freimuth WW, Zhong ZJ, Clarke AE; BLISS-52 and -76 Study Groups. Improvements in health-related quality of life with belimumab, a B-lymphocyte stimulator-specific inhibitor, in patients with autoantibody-positive systemic lupus erythematosus from the randomised controlled BLISS trials. Ann Rheum Dis. 2014 May;73(5):838-44. doi: 10.1136/annrheumdis-2012-202865. Epub 2013 Mar 22.

Reference Type DERIVED
PMID: 23524886 (View on PubMed)

Wallace DJ, Navarra S, Petri MA, Gallacher A, Thomas M, Furie R, Levy RA, van Vollenhoven RF, Cooper S, Zhong ZJ, Freimuth W, Cervera R; BLISS-52 and -76, and LBSL02 Study Groups. Safety profile of belimumab: pooled data from placebo-controlled phase 2 and 3 studies in patients with systemic lupus erythematosus. Lupus. 2013 Feb;22(2):144-54. doi: 10.1177/0961203312469259. Epub 2012 Dec 4.

Reference Type DERIVED
PMID: 23213069 (View on PubMed)

van Vollenhoven RF, Petri MA, Cervera R, Roth DA, Ji BN, Kleoudis CS, Zhong ZJ, Freimuth W. Belimumab in the treatment of systemic lupus erythematosus: high disease activity predictors of response. Ann Rheum Dis. 2012 Aug;71(8):1343-9. doi: 10.1136/annrheumdis-2011-200937. Epub 2012 Feb 15.

Reference Type DERIVED
PMID: 22337213 (View on PubMed)

Stohl W, Hiepe F, Latinis KM, Thomas M, Scheinberg MA, Clarke A, Aranow C, Wellborne FR, Abud-Mendoza C, Hough DR, Pineda L, Migone TS, Zhong ZJ, Freimuth WW, Chatham WW; BLISS-52 Study Group; BLISS-76 Study Group. Belimumab reduces autoantibodies, normalizes low complement levels, and reduces select B cell populations in patients with systemic lupus erythematosus. Arthritis Rheum. 2012 Jul;64(7):2328-37. doi: 10.1002/art.34400.

Reference Type DERIVED
PMID: 22275291 (View on PubMed)

Navarra SV, Guzman RM, Gallacher AE, Hall S, Levy RA, Jimenez RE, Li EK, Thomas M, Kim HY, Leon MG, Tanasescu C, Nasonov E, Lan JL, Pineda L, Zhong ZJ, Freimuth W, Petri MA; BLISS-52 Study Group. Efficacy and safety of belimumab in patients with active systemic lupus erythematosus: a randomised, placebo-controlled, phase 3 trial. Lancet. 2011 Feb 26;377(9767):721-31. doi: 10.1016/S0140-6736(10)61354-2. Epub 2011 Feb 4.

Reference Type DERIVED
PMID: 21296403 (View on PubMed)

Study Documents

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Document Type: Informed Consent Form

View Document

Document Type: Clinical Study Report

View Document

Document Type: Study Protocol

View Document

Document Type: Annotated Case Report Form

View Document

Document Type: Dataset Specification

View Document

Document Type: Statistical Analysis Plan

View Document

Document Type: Individual Participant Data Set

View Document

Related Links

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https://www.clinicalstudydatarequest.com

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Other Identifiers

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BLISS-52

Identifier Type: OTHER

Identifier Source: secondary_id

110752

Identifier Type: OTHER

Identifier Source: secondary_id

HGS1006-C1057

Identifier Type: -

Identifier Source: org_study_id