Isavuconazole (BAL8557) for Primary Treatment of Invasive Aspergillosis

NCT ID: NCT00412893

Last Updated: 2024-12-10

Study Results

Results available

Outcome measurements, participant flow, baseline characteristics, and adverse events have been published for this study.

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Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE3

Total Enrollment

527 participants

Study Classification

INTERVENTIONAL

Study Start Date

2007-03-07

Study Completion Date

2013-03-28

Brief Summary

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The purpose of this study is to compare the efficacy and safety of isavuconazole versus voriconazole in the treatment of patients with invasive aspergillosis.

Detailed Description

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Acute invasive fungal infections caused by aspergillus, zygomycetes and other filamentous fungi remain life threatening diseases. Early treatment with highly effective anti-fungals reduces mortality. This study investigates the efficacy and safety of isavuconazole in the treatment of invasive fungal diseases, caused by Aspergillus or other filamentous fungi.

Conditions

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Aspergillosis Invasive Fungal Infection

Keywords

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Invasive fungal disease BAL8557 Isavuconazole ASP9766 Filamentous fungi Phase III Aspergillus species

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

DOUBLE

Participants Investigators

Study Groups

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Isavuconazole

Participants received a loading dose of isavuconazole, 200 mg three times a day by intravenous infusion (IV) for the first 2 days followed by a maintenance dose from Day 3 of 200 mg once daily either IV or orally until they reached a treatment endpoint or for a maximum of 84 days.

Group Type EXPERIMENTAL

Isavuconazole

Intervention Type DRUG

Loading doses were administered as IV infusion and maintenance doses were administered as IV infusion or oral (capsules).

Voriconazole

Participants received a loading dose of voriconazole, 6 mg/kg every 12 hours IV for the first 24 hours, followed by a maintenance dose of 4 mg/kg every 12 hours by IV on Day 2. Beginning on Day 3, participants received 4 mg/kg every 12 hours by IV or 200 mg every 12 hours orally, until they reached a treatment endpoint or for a maximum of 84 days.

Group Type ACTIVE_COMPARATOR

Voriconazole

Intervention Type DRUG

Loading doses were administered as IV infusion and maintenance doses were administered as IV infusion or oral (capsules).

Interventions

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Isavuconazole

Loading doses were administered as IV infusion and maintenance doses were administered as IV infusion or oral (capsules).

Intervention Type DRUG

Voriconazole

Loading doses were administered as IV infusion and maintenance doses were administered as IV infusion or oral (capsules).

Intervention Type DRUG

Other Intervention Names

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ASP9766 BAL8557 VFend

Eligibility Criteria

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Inclusion Criteria

* Patients must have proven, probable or possible invasive fungal disease caused by Aspergillus species or other filamentous fungi
* Female patients must be non-lactating and at no risk for pregnancy

Exclusion Criteria

* Patients with invasive fungal infections other than Aspergillus species or other filamentous fungi
* Evidence of hepatic dysfunction at Baseline or moderate to severe renal dysfunction
* Patients with chronic aspergillosis, or aspergilloma or allergic bronchopulmonary aspergillosis
* Patients who have received more than 4 days of systemic antifungal therapy other than fluconazole within the 7 days prior to the first administration of study medication
* Patients previously enrolled in a Phase III study with isavuconazole
* Patients with a body weight \</= 40 kg
Minimum Eligible Age

18 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Basilea Pharmaceutica International Ltd

INDUSTRY

Sponsor Role collaborator

Astellas Pharma Inc

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Medical Director

Role: STUDY_DIRECTOR

Astellas Pharma Global Development

Locations

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University of Alabama

Birmingham, Alabama, United States

Site Status

University of California at San Francisco

San Francisco, California, United States

Site Status

University of Chicago, Division of Infectious Diseases

Chicago, Illinois, United States

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Indiana BMT

Springfield, Illinois, United States

Site Status

Springfield Clinic LLP

Springfield, Illinois, United States

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Infectious Disease of Indiana

Indianapolis, Indiana, United States

Site Status

Brigham & Womens Hospital

Boston, Massachusetts, United States

Site Status

Worcester, Massachusetts, United States

Site Status

Upstate Infectious Diseases Association LLP

Albany, New York, United States

Site Status

Regional Infection Diseases Infusion Center Inc.

Lima, Ohio, United States

Site Status

University of Texas MD Anderson Cancer Center

Houston, Texas, United States

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Buenos Aires, , Argentina

Site Status

Buenos Aires, , Argentina

Site Status

Buenos Aires, , Argentina

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Capital Federal, , Argentina

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Capital Federal, , Argentina

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Hospital Italiano de Buenos Aires

Ciudad Autonoma, , Argentina

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Instituto Medico Especializado Alexander Fleming

Ciudad Autonoma, , Argentina

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Perth, , Australia

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Mater Medical Centre

South Brisbane, , Australia

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Woolloongabba, , Australia

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AZ ST Jan

Bruges, , Belgium

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Institut Jules Bordet

Brussels, , Belgium

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ULB Hospital Erasme

Brussels, , Belgium

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Universitair Ziekenhuis Gent

Ghent, , Belgium

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Universitaire Ziekenhuizen Leuven

Leuven, , Belgium

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Felicio Rocho

Belo Horizonte, , Brazil

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Santa Casa de Misericordia de Belo Horizonte

Belo Horizonte, , Brazil

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Hospital das Clinicas da UFPR

Curitiba, , Brazil

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Hospital de Clinicas da FMUSP - Ribeirao Preto

Ribeirão Preto, , Brazil

Site Status

Hospital Universitario Clementino Fraga Filho

Rio de Janeiro, , Brazil

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The Ottawa Hospital - General Campus

Ottawa, Ontario, Canada

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Hamilton Health Sciences - Henderson Site

Hamilton, , Canada

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Santiago, , Chile

Site Status

Hospital Dr. Hernan Henriquez Aravena

Temuco, , Chile

Site Status

Valdivia, , Chile

Site Status

3rd Hospital, Peking University

Beijing, , China

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The 1st Hospital, Jilin University

Changchun, , China

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The Third Xiangya Hospital of Central South University

Changsha, , China

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West China Hospital of Sichuan University

Chengdu, , China

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The Affiliated Union Hospital of Fujian Medical University

Fuzhou, , China

Site Status

The First Affiliated Hospital, Med. School, Zhejiang Uni.

Hangzhou, , China

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The First Affiliated Hospital of Nanjing Medical University

Nanjing, , China

Site Status

The 1st Affiliated Hospital of Guangxi Medical University

Nanning, , China

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Huashan Hospital, Insitute of Antibiotics

Shanghai, , China

Site Status

No.6 Renmin Hosp. of Shanghai City

Shanghai, , China

Site Status

Chang Hai Hospital

Shanghai, , China

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Wuhan Union Hospital

Wuhan, , China

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Alexandria University Hospital

Alexandria, , Egypt

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National Cancer Institute

Cairo, , Egypt

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Nasser Institute

Cairo, , Egypt

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Dijon, , France

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CHU de Nantes - Hôpital Hôtel Dieu

Nantes, , France

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Hotel Dieu

Nantes, , France

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Hôpital Hautepierre

Strasbourg, , France

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Hôpital de brabois adultes

Vandœuvre-lès-Nancy, , France

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Universitaetsklinikum Aachen

Aachen, , Germany

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Charité Universitaetsmedizin Berlin- Campus Charité Mitte

Berlin, , Germany

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Universitaet Koeln

Cologne, , Germany

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Universitaetsklinik Leipzig

Leipzig, , Germany

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Lübeck, , Germany

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Klinikum Schwabing

München, , Germany

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Medizinische klinik und Polyklinik II

Würzburg, , Germany

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Budapest, , Hungary

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Petz Aladar Megyei Oktato Korhaz

Győr, , Hungary

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Szegedi Tudomanyegyetem

Szeged, , Hungary

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Apollo Hospitals

Hyderabad, Andh Prad, India

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Sterling Hospital

Ahmedabad, Gujarat, India

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Kasturba Medical College and Hospital

Mangalore, Karna, India

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Shirdi Sai Baba Cancer Hospital K. M. C. Hospital

Manipal, Karna, India

Site Status

Tata Memorial Hopital, Department of Anesthesia

Mumbai, Mahara, India

Site Status

Deenanath Mangeshkar Hospital & Research Centre

Pune, Mahara, India

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Sahyadri Hospital

Pune, Mahara, India

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Noida, Uttar Prad, India

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Rambam Health Care Campus

Haifa, , Israel

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Hadassah Universtiy Hospital - Ein Kerem

Jerusalem, , Israel

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Rabin MC

Petah Tikva, , Israel

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Chaim Sheba Medical Center

Ramat Gan, , Israel

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Sourasky MC Ichilov Hospital Tel Aviv

Tel Aviv, , Israel

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Unità Funzionale di Ematologia; Azienda Ospedaliera Universitaria Careggi

Florence, , Italy

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Azienda Ospedaliera Ospedale Niguarda Ca' Granda

Milan, , Italy

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Kuala Lumpur, , Malaysia

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Kuala Lumpur, , Malaysia

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México, , Mexico

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Hospital Universitario Dr Jose Eleuterio Gonzalez

Monterrey, , Mexico

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Nijmegen, , Netherlands

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Palmerston North, , New Zealand

Site Status

Samodzielny Publiczny Centralny Szpital Kliniczny

Warsaw, , Poland

Site Status

State Institution "Hematology Research Center" RAMS

Moscow, , Russia

Site Status

Republican Hospital named after V.A. Baranov

Petrozavodsk, , Russia

Site Status

Leningrad Regional Hospital

Saint Petersburg, , Russia

Site Status

St-Petersburg MA Postgraduate Education

Saint Petersburg, , Russia

Site Status

Saint Petersburg, , Russia

Site Status

Gachon University Gil Hospital

Incheon, , South Korea

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Seoul, , South Korea

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Samsung Medical Center

Seoul, , South Korea

Site Status

The Catholic University of Korea, St. Mary's Hospital

Seoul, , South Korea

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Asan Medical Center

Seoul, , South Korea

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Salamanca, , Spain

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Zurich, , Switzerland

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Songklanagarind Hospital

Hat Yai, , Thailand

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Khon Kaen, , Thailand

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Maharat Nakhon Ratchasima Hospital

Muang, , Thailand

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Srinagarind Hospital

Muang, , Thailand

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Maharaj Nakorn Chiang Mai Hospital

Muang, , Thailand

Site Status

Songkhla, , Thailand

Site Status

Istanbul, , Turkey (Türkiye)

Site Status

Countries

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Colombia Lebanon Peru Philippines Saudi Arabia Singapore South Africa United Kingdom United States Argentina Australia Belgium Brazil Canada Chile China Egypt France Germany Hungary India Israel Italy Malaysia Mexico Netherlands New Zealand Poland Russia South Korea Spain Switzerland Thailand Turkey (Türkiye)

References

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Hamed K, Engelhardt M, Kovanda LL, Huang JJ, Yan J, Aram JA. Post-hoc analysis of the safety and efficacy of isavuconazole in older patients with invasive fungal disease from the VITAL and SECURE studies. Sci Rep. 2023 Apr 25;13(1):6730. doi: 10.1038/s41598-023-31788-1.

Reference Type DERIVED
PMID: 37185921 (View on PubMed)

Kovanda LL, Kolamunnage-Dona R, Neely M, Maertens J, Lee M, Hope WW. Pharmacodynamics of Isavuconazole for Invasive Mold Disease: Role of Galactomannan for Real-Time Monitoring of Therapeutic Response. Clin Infect Dis. 2017 Jun 1;64(11):1557-1563. doi: 10.1093/cid/cix198.

Reference Type DERIVED
PMID: 28472247 (View on PubMed)

Maertens JA, Raad II, Marr KA, Patterson TF, Kontoyiannis DP, Cornely OA, Bow EJ, Rahav G, Neofytos D, Aoun M, Baddley JW, Giladi M, Heinz WJ, Herbrecht R, Hope W, Karthaus M, Lee DG, Lortholary O, Morrison VA, Oren I, Selleslag D, Shoham S, Thompson GR 3rd, Lee M, Maher RM, Schmitt-Hoffmann AH, Zeiher B, Ullmann AJ. Isavuconazole versus voriconazole for primary treatment of invasive mould disease caused by Aspergillus and other filamentous fungi (SECURE): a phase 3, randomised-controlled, non-inferiority trial. Lancet. 2016 Feb 20;387(10020):760-9. doi: 10.1016/S0140-6736(15)01159-9. Epub 2015 Dec 10.

Reference Type DERIVED
PMID: 26684607 (View on PubMed)

Related Links

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https://astellasclinicalstudyresults.com/study.aspx?ID=52

Link to results on Astellas Clinical Study Results website

Other Identifiers

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WSA-CS-004

Identifier Type: OTHER

Identifier Source: secondary_id

2006-003868-59

Identifier Type: EUDRACT_NUMBER

Identifier Source: secondary_id

9766-CL-0104

Identifier Type: -

Identifier Source: org_study_id