Trial Outcomes & Findings for Bortezomib and Pemetrexed Disodium in Treating Patients With Advanced Non-Small Cell Lung Cancer or Other Solid Tumors (NCT NCT00389805)

NCT ID: NCT00389805

Last Updated: 2018-10-31

Results Overview

Grade 4 thrombocytopenia or grade 3 thrombocytopenia associated with bleeding, requirement for transfusion or lasting \>7 days; febrile neutropenia; grade 3 neutropenia associated with infection; any other grade \>/=3 non-hematologic toxicity considered by the investigator to be related to study drug.

Recruitment status

COMPLETED

Study phase

PHASE1/PHASE2

Target enrollment

27 participants

Primary outcome timeframe

Up to 36 months

Results posted on

2018-10-31

Participant Flow

Participant milestones

Participant milestones
Measure
Arm A
Pemetrexed on day 1 (500 -600 mg/m2 IV) and bortezomib twice weekly (0.7-1.3mg/m3) on days 1, 4, 8, and 11 every 21 days
Arm B
Pemetrexed on day 1 (500 -600 mg/m2 IV) and bortezomib twice weekly (0.7-1.3mg/m2) on days 1 and 8 every 21 days
Phase I
STARTED
15
12
Phase I
COMPLETED
15
12
Phase I
NOT COMPLETED
0
0
Phase II
STARTED
0
0
Phase II
COMPLETED
0
0
Phase II
NOT COMPLETED
0
0

Reasons for withdrawal

Withdrawal data not reported

Baseline Characteristics

Bortezomib and Pemetrexed Disodium in Treating Patients With Advanced Non-Small Cell Lung Cancer or Other Solid Tumors

Baseline characteristics by cohort

Baseline characteristics by cohort
Measure
Arm A
n=15 Participants
Pemetrexed on day 1 and bortezomib days 1, 4, 8, and 11 every 21 days
Arm B
n=12 Participants
Pemetrexed on day 1 and bortezomib days 1 and 8 every 21 days
Total
n=27 Participants
Total of all reporting groups
Age, Continuous
62 years
n=5 Participants
59 years
n=7 Participants
60 years
n=5 Participants
Sex: Female, Male
Female
6 Participants
n=5 Participants
8 Participants
n=7 Participants
14 Participants
n=5 Participants
Sex: Female, Male
Male
9 Participants
n=5 Participants
4 Participants
n=7 Participants
13 Participants
n=5 Participants
Region of Enrollment
United States
15 participants
n=5 Participants
12 participants
n=7 Participants
27 participants
n=5 Participants

PRIMARY outcome

Timeframe: Up to 36 months

Grade 4 thrombocytopenia or grade 3 thrombocytopenia associated with bleeding, requirement for transfusion or lasting \>7 days; febrile neutropenia; grade 3 neutropenia associated with infection; any other grade \>/=3 non-hematologic toxicity considered by the investigator to be related to study drug.

Outcome measures

Outcome measures
Measure
Arm A
n=15 Participants
Pemetrexed on day 1 and bortezomib days 1, 4, 8, and 11 every 21 days
Arm B
n=12 Participants
Pemetrexed on day 1 and bortezomib days 1 and 8 every 21 days
Number of Patients Experiencing a Dose-limiting Toxicity (Phase I)
3 Participants
0 Participants

PRIMARY outcome

Timeframe: Throughout the entire study (up to 36 months).

Number of participants with treatment-related adverse events as assessed by CTCAE v3.0 (Phase I).

Outcome measures

Outcome measures
Measure
Arm A
n=15 Participants
Pemetrexed on day 1 and bortezomib days 1, 4, 8, and 11 every 21 days
Arm B
n=12 Participants
Pemetrexed on day 1 and bortezomib days 1 and 8 every 21 days
Number of Participants Who Experience Adverse Events (Phase I)
15 Participants
12 Participants

PRIMARY outcome

Timeframe: First cycle of treatment (3 weeks)

Grade 3/4 toxicity occurring in a patient within 1 cycle.

Outcome measures

Outcome measures
Measure
Arm A
n=15 Participants
Pemetrexed on day 1 and bortezomib days 1, 4, 8, and 11 every 21 days
Arm B
n=12 Participants
Pemetrexed on day 1 and bortezomib days 1 and 8 every 21 days
Number of Patients With Grade ≥ 3 Toxicity (Phase I)
Neutropenia
12 participants
1 participants
Number of Patients With Grade ≥ 3 Toxicity (Phase I)
Anemia
1 participants
0 participants
Number of Patients With Grade ≥ 3 Toxicity (Phase I)
Thrombocytopenia
0 participants
1 participants
Number of Patients With Grade ≥ 3 Toxicity (Phase I)
Increased transaminases
1 participants
0 participants
Number of Patients With Grade ≥ 3 Toxicity (Phase I)
Fatigue
2 participants
0 participants

PRIMARY outcome

Timeframe: From start of treatment until disease progression/recurrence.

Population: The Phase II study was not conducted.

To determine the response rate of bortezomib in combination with pemetrexed in patients with advanced NSCLC. Response rate was assessed by CT scan. CT scans was performed at baseline and every two cycles (prior to 3rd and 5th cycle). The evaluation of response was based on standard RECIST criteria.

Outcome measures

Outcome data not reported

SECONDARY outcome

Timeframe: Up to 36 months

Adverse events possibly related to treatment, graded according to the NCI CTCAE v3.0.

Outcome measures

Outcome measures
Measure
Arm A
n=15 Participants
Pemetrexed on day 1 and bortezomib days 1, 4, 8, and 11 every 21 days
Arm B
n=12 Participants
Pemetrexed on day 1 and bortezomib days 1 and 8 every 21 days
Number of Patients With Toxicity by NCI CTC v3.0 (Phase I)
Weakness
0 participants
2 participants
Number of Patients With Toxicity by NCI CTC v3.0 (Phase I)
Neutropenia
12 participants
1 participants
Number of Patients With Toxicity by NCI CTC v3.0 (Phase I)
Anemia
1 participants
0 participants
Number of Patients With Toxicity by NCI CTC v3.0 (Phase I)
Thrombocytopenia
0 participants
1 participants
Number of Patients With Toxicity by NCI CTC v3.0 (Phase I)
Increased transaminases
12 participants
5 participants
Number of Patients With Toxicity by NCI CTC v3.0 (Phase I)
Anorexia
4 participants
6 participants
Number of Patients With Toxicity by NCI CTC v3.0 (Phase I)
Constipation
5 participants
3 participants
Number of Patients With Toxicity by NCI CTC v3.0 (Phase I)
Cough
5 participants
4 participants
Number of Patients With Toxicity by NCI CTC v3.0 (Phase I)
Dehydration
4 participants
1 participants
Number of Patients With Toxicity by NCI CTC v3.0 (Phase I)
Diarrhea
2 participants
3 participants
Number of Patients With Toxicity by NCI CTC v3.0 (Phase I)
Dizziness
5 participants
4 participants
Number of Patients With Toxicity by NCI CTC v3.0 (Phase I)
Edema
4 participants
4 participants
Number of Patients With Toxicity by NCI CTC v3.0 (Phase I)
Fatigue
15 participants
11 participants
Number of Patients With Toxicity by NCI CTC v3.0 (Phase I)
Fever
3 participants
3 participants
Number of Patients With Toxicity by NCI CTC v3.0 (Phase I)
Infection
6 participants
4 participants
Number of Patients With Toxicity by NCI CTC v3.0 (Phase I)
Nausea +/- vomiting
10 participants
6 participants
Number of Patients With Toxicity by NCI CTC v3.0 (Phase I)
Neuropathy
4 participants
6 participants
Number of Patients With Toxicity by NCI CTC v3.0 (Phase I)
Rash
6 participants
5 participants
Number of Patients With Toxicity by NCI CTC v3.0 (Phase I)
Renal impairment
5 participants
1 participants

SECONDARY outcome

Timeframe: Up to 36 months

Outcome measures

Outcome measures
Measure
Arm A
n=15 Participants
Pemetrexed on day 1 and bortezomib days 1, 4, 8, and 11 every 21 days
Arm B
n=12 Participants
Pemetrexed on day 1 and bortezomib days 1 and 8 every 21 days
Maximum Tolerated Dose of Bortezomib in Combination With Pemetrexel (Phase I)
1.3 Mg/m^2
1.6 Mg/m^2

SECONDARY outcome

Timeframe: Up to 36 months

Population: All patients for whom response evaluation measurements were recorded at baseline and after 2 cycles.

Per Response Evaluation Criteria In Solid Tumors Criteria (RECIST) for target lesions and assessed by CT: Complete Response (CR), Disappearance of all target lesions; Partial Response (PR), \>=30% decrease in the sum of the longest diameter of target lesions; Best overall response is the best response recorded from the start of the treatment until disease progression/recurrence.

Outcome measures

Outcome measures
Measure
Arm A
n=15 Participants
Pemetrexed on day 1 and bortezomib days 1, 4, 8, and 11 every 21 days
Arm B
n=12 Participants
Pemetrexed on day 1 and bortezomib days 1 and 8 every 21 days
Number of Participants With Response to Therapy as Measured by RECIST (Phase I)
Stable Disease (SD)
7 Participants
6 Participants
Number of Participants With Response to Therapy as Measured by RECIST (Phase I)
Complete Response (CR)
0 Participants
0 Participants
Number of Participants With Response to Therapy as Measured by RECIST (Phase I)
Partial Response (PR)
1 Participants
1 Participants
Number of Participants With Response to Therapy as Measured by RECIST (Phase I)
Progressive Disease (PD)
7 Participants
5 Participants

SECONDARY outcome

Timeframe: Up to 36 months

Population: The Phase II study was not conducted.

Each adverse event will be determined by using the NCI CTCAE, Version 3.0.

Outcome measures

Outcome data not reported

SECONDARY outcome

Timeframe: Up to 36 months

Population: The Phase II study was not conducted.

Expression of relevant molecular targets of the proteasome, which is inhibited by bortezomib.

Outcome measures

Outcome data not reported

SECONDARY outcome

Timeframe: Up to 36 months

Population: The Phase II study was not conducted.

Overexpression of reduced folate carrier (RFC) protein is thought to contribute to decreased resistance to pemetrexed. Levels of expression will be studied by measuring mRNA transcripts using quantitative Reverse Transcriptase-Polymerase Chain Reaction in archival patient tumor specimens.

Outcome measures

Outcome data not reported

SECONDARY outcome

Timeframe: Up to 36 months

Population: The Phase II study was not conducted.

Tumor levels of BCL-2, BCL-xL and BAX will be assessed by immunohistochemistry (IHC).

Outcome measures

Outcome data not reported

Adverse Events

Arm A

Serious events: 0 serious events
Other events: 15 other events
Deaths: 0 deaths

Arm B

Serious events: 0 serious events
Other events: 12 other events
Deaths: 0 deaths

Serious adverse events

Adverse event data not reported

Other adverse events

Other adverse events
Measure
Arm A
n=15 participants at risk
Pemetrexed on day 1 and bortezomib days 1, 4, 8, and 11 every 21 days
Arm B
n=12 participants at risk
Pemetrexed on day 1 and bortezomib days 1 and 8 every 21 days
Hepatobiliary disorders
Increased transaminases
80.0%
12/15
41.7%
5/12
Metabolism and nutrition disorders
Anorexia
26.7%
4/15
50.0%
6/12
Gastrointestinal disorders
Constipation
33.3%
5/15
25.0%
3/12
Respiratory, thoracic and mediastinal disorders
Cough
33.3%
5/15
33.3%
4/12
Metabolism and nutrition disorders
Dehydration
26.7%
4/15
8.3%
1/12
Gastrointestinal disorders
Diarrhea
13.3%
2/15
25.0%
3/12
Nervous system disorders
Dizziness
33.3%
5/15
33.3%
4/12
General disorders
Edema
26.7%
4/15
33.3%
4/12
General disorders
Fatigue
100.0%
15/15
91.7%
11/12
General disorders
Fever
20.0%
3/15
25.0%
3/12
Infections and infestations
Infection
40.0%
6/15
33.3%
4/12
Gastrointestinal disorders
Nausea +/- vomiting
66.7%
10/15
50.0%
6/12
Nervous system disorders
Neuropathy
26.7%
4/15
50.0%
6/12
Skin and subcutaneous tissue disorders
Rash
40.0%
6/15
41.7%
5/12
Renal and urinary disorders
Renal impairment
33.3%
5/15
8.3%
1/12
Musculoskeletal and connective tissue disorders
Weakness
0.00%
0/15
16.7%
2/12
Blood and lymphatic system disorders
Neutropenia
80.0%
12/15
8.3%
1/12
Blood and lymphatic system disorders
Anemia
6.7%
1/15
0.00%
0/12
Blood and lymphatic system disorders
Thrombocytopenia
0.00%
0/15
8.3%
1/12

Additional Information

Analyst

University of California, Davis

Phone: 916-734-8053

Results disclosure agreements

  • Principal investigator is a sponsor employee
  • Publication restrictions are in place