Trial Outcomes & Findings for Sunitinib in Treating Patients With Idiopathic Myelofibrosis (NCT NCT00387426)

NCT ID: NCT00387426

Last Updated: 2014-05-28

Results Overview

Participant response assessed after two cycles of therapy according to categories: 1) complete response, 2) partial response, 3) clinical improvement, 4) stable disease 5) progressive disease, 6) early death from malignant disease, 7) early death from toxicity, 8) early death because of other cause, or 9) unknown (not assessable, insufficient data).

Recruitment status

TERMINATED

Study phase

PHASE2

Target enrollment

14 participants

Primary outcome timeframe

After two 6-week treatment courses (12 weeks)

Results posted on

2014-05-28

Participant Flow

Recruitment Period: September 14, 2006 to December 17, 2007. All recruitment done at UT MD Anderson Cancer Center.

Participant milestones

Participant milestones
Measure
Sunitinib
37.5 mg orally daily for 6-week cycle
Overall Study
STARTED
14
Overall Study
COMPLETED
0
Overall Study
NOT COMPLETED
14

Reasons for withdrawal

Reasons for withdrawal
Measure
Sunitinib
37.5 mg orally daily for 6-week cycle
Overall Study
Lack of Response
7
Overall Study
Toxicities
4
Overall Study
Disease Progression
3

Baseline Characteristics

Sunitinib in Treating Patients With Idiopathic Myelofibrosis

Baseline characteristics by cohort

Baseline characteristics by cohort
Measure
Sunitinib
n=14 Participants
37.5 mg orally daily for 6-week cycle
Age, Continuous
64 years
n=5 Participants
Sex: Female, Male
Female
7 Participants
n=5 Participants
Sex: Female, Male
Male
7 Participants
n=5 Participants
Region of Enrollment
United States
14 participants
n=5 Participants

PRIMARY outcome

Timeframe: After two 6-week treatment courses (12 weeks)

Population: All participants assessed for response.

Participant response assessed after two cycles of therapy according to categories: 1) complete response, 2) partial response, 3) clinical improvement, 4) stable disease 5) progressive disease, 6) early death from malignant disease, 7) early death from toxicity, 8) early death because of other cause, or 9) unknown (not assessable, insufficient data).

Outcome measures

Outcome measures
Measure
Sunitinib
n=14 Participants
37.5 mg orally daily for 6-week cycle
Number of Participants With Objective Clinical Response to Sunitinib Therapy
1 participants

Adverse Events

Sunitinib

Serious events: 7 serious events
Other events: 14 other events
Deaths: 0 deaths

Serious adverse events

Serious adverse events
Measure
Sunitinib
n=14 participants at risk
37.5 mg orally daily for 6-week cycle
Gastrointestinal disorders
Nausea
7.1%
1/14 • Number of events 2 • 2 years
Blood and lymphatic system disorders
Optic Disc Edema
7.1%
1/14 • Number of events 1 • 2 years
Infections and infestations
Pneumonia
7.1%
1/14 • Number of events 1 • 2 years
General disorders
Pain
7.1%
1/14 • Number of events 4 • 2 years
Blood and lymphatic system disorders
Thrombosis Embolism
7.1%
1/14 • Number of events 1 • 2 years
Blood and lymphatic system disorders
Hemorrhage
14.3%
2/14 • Number of events 2 • 2 years
Cardiac disorders
Left Ventricular Systolic Dysfunction
7.1%
1/14 • Number of events 1 • 2 years

Other adverse events

Other adverse events
Measure
Sunitinib
n=14 participants at risk
37.5 mg orally daily for 6-week cycle
Gastrointestinal disorders
Nausea
35.7%
5/14 • Number of events 5 • 2 years
General disorders
Fatigue
21.4%
3/14 • Number of events 3 • 2 years
Gastrointestinal disorders
Vomiting
28.6%
4/14 • Number of events 4 • 2 years
Cardiac disorders
High Blood Pressure
57.1%
8/14 • Number of events 8 • 2 years
Gastrointestinal disorders
Diarrhea
42.9%
6/14 • Number of events 6 • 2 years
Blood and lymphatic system disorders
Anemia
28.6%
4/14 • Number of events 4 • 2 years
Gastrointestinal disorders
Mucositis
7.1%
1/14 • Number of events 1 • 2 years
Metabolism and nutrition disorders
Elevated Liver Function Tests
14.3%
2/14 • Number of events 2 • 2 years
Gastrointestinal disorders
Constipation
7.1%
1/14 • Number of events 1 • 2 years
Blood and lymphatic system disorders
Leukopenia
64.3%
9/14 • Number of events 9 • 2 years
Musculoskeletal and connective tissue disorders
Muscle Weakness
7.1%
1/14 • Number of events 1 • 2 years
Blood and lymphatic system disorders
Neutropenia
85.7%
12/14 • Number of events 12 • 2 years
Blood and lymphatic system disorders
Thrombocytopenia
14.3%
2/14 • Number of events 2 • 2 years
Skin and subcutaneous tissue disorders
Pruritis
7.1%
1/14 • Number of events 1 • 2 years
Skin and subcutaneous tissue disorders
Rash
7.1%
1/14 • Number of events 1 • 2 years

Additional Information

Srdan Verstovsek, MD / Associate Professor

UT MD Anderson Cancer Center

Results disclosure agreements

  • Principal investigator is a sponsor employee
  • Publication restrictions are in place

Restriction type: LTE60