Trastuzumab for 6 Months or 1 Year in Treating Women With Nonmetastatic Breast Cancer That Can Be Removed By Surgery

NCT ID: NCT00381901

Last Updated: 2011-05-13

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE3

Total Enrollment

3400 participants

Study Classification

INTERVENTIONAL

Study Start Date

2006-05-31

Brief Summary

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RATIONALE: Monoclonal antibodies, such as trastuzumab, can block tumor growth in different ways. Some block the ability of tumor cells to grow and spread. Others find tumor cells and help kill them or carry tumor-killing substances to them. It is not yet known whether giving trastuzumab for 6 months is as effective as giving trastuzumab for 1 year in treating patients with breast cancer.

PURPOSE: This randomized phase III trial is studying trastuzumab to see how well it works when given for 6 months compared to 12 months in treating women with nonmetastatic breast cancer that can be removed by surgery.

Detailed Description

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OBJECTIVES:

Primary

* Compare the disease-free survival of women with nonmetastatic, resectable breast cancer treated with adjuvant trastuzumab (Herceptin®) for 6 months vs 12 months.

Secondary

* Compare cardiotoxicity in patients receiving these regimens.
* Compare the cardiotoxicity and disease-free survival of patients receiving concurrent trastuzumab and chemotherapy vs sequential administration.
* Correlate HER-2 polymorphism with disease-free survival/cardiotoxicity in these patients.

OUTLINE: This is a randomized, controlled, multicenter study. Patients are stratified according to participating center, modality of adjuvant chemotherapy (concurrent vs sequential), and adjuvant hormonal therapy (yes vs no). Patients are randomized to 1 of 2 treatment arms.

* Arm I (control arm, 12-month therapy): Patients continue to receive trastuzumab (Herceptin®) IV until a total of 12 months of therapy is completed in the absence of disease progression or unacceptable toxicity.
* Arm II (experimental arm, 6-month therapy): Patients continue to receive trastuzumab\* IV until a total of 6 months of therapy is completed in the absence of disease progression or unacceptable toxicity.

NOTE: \*Patients who have already finished 6 months of trastuzumab at randomization do not receive further trastuzumab.

Some patients undergo blood collection for HER-2 polymorphism analysis.

After completion of study therapy, patients are followed periodically for approximately 5 years.

PROJECTED ACCRUAL: A total of 7,000 patients will be accrued for this study.

Conditions

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Breast Cancer

Study Design

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Allocation Method

RANDOMIZED

Primary Study Purpose

TREATMENT

Interventions

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trastuzumab

Intervention Type BIOLOGICAL

polymorphism analysis

Intervention Type GENETIC

adjuvant therapy

Intervention Type PROCEDURE

Eligibility Criteria

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Inclusion Criteria

DISEASE CHARACTERISTICS:

* Histologically confirmed adenocarcinoma of the breast
* Nonmetastatic disease

* Positive or negative axillary nodes
* Tumor size ≥ 10 mm
* Resectable disease
* Must have received ≥ 4 courses of chemotherapy for this disease
* A 12-month adjuvant treatment with trastuzumab (Herceptin®) has been initiated

* Informed consent form must be signed between the third and sixth months of trastuzumab therapy
* Overexpression of HER-2 in the invasive component of the primary tumor as indicated by 1 of the following:

* 3+ by immunohistochemistry (IHC)
* 2+ by IHC and confirmation by fluorescent in situ hybridization (FISH) or chromogenic in situ hybridization (CISH)
* Hormone receptor status not specified

PATIENT CHARACTERISTICS:

* Female
* Menopausal status not specified
* LVEF considered favorable for continuing trastuzumab treatment as measured by echocardiography or MUGA at 2-4 months after beginning adjuvant trastuzumab
* No serious cardiac illness or medical condition precluding trastuzumab treatment, including any of the following:

* History of documented congestive heart failure
* High-risk uncontrolled arrhythmias
* Angina pectoris requiring antianginal medication
* Severe dyspnea at rest or oxygen-dependent
* No known hypersensitivity to trastuzumab, murine proteins, or any of the excipients
* Not pregnant or nursing
* No social, geographical, or psychological condition that would preclude study participation

PRIOR CONCURRENT THERAPY:

* See Disease Characteristics
* Other prior anti-HER-2 therapy allowed
* No prior trastuzumab other than initiation of trastuzumab adjuvant therapy
Minimum Eligible Age

18 Years

Eligible Sex

FEMALE

Accepts Healthy Volunteers

No

Sponsors

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National Cancer Institute, France

OTHER_GOV

Sponsor Role lead

Principal Investigators

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Xavier Pivot, MD, PhD

Role: STUDY_CHAIR

Hopital Jean Minjoz

Locations

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Centre Paul Papin

Angers, , France

Site Status

Centre Hospitalier d'Annecy

Annecy, , France

Site Status

Centre Hospitalier La Fontonne

Antibes, , France

Site Status

Centre Hospitalier Victor Dupouy

Argenteuil, , France

Site Status

Centre Hospital General Robert Ballanger

Aulnay-sous-Bois, , France

Site Status

Institut Sainte Catherine

Avignon, , France

Site Status

C.H.G. Beauvais

Beauvais, , France

Site Status

Centre Hospitalier Regional de Besancon - Hopital Jean Minjoz

Besançon, , France

Site Status

Hopital Avicenne

Bobigny, , France

Site Status

Institut Bergonie

Bordeaux, , France

Site Status

Polyclinique Bordeaux Nord Aquitaine

Bordeaux, , France

Site Status

Clinique Tivoli

Bordeaux, , France

Site Status

Centre Hospitalier Docteur Duchenne

Boulogne-sur-Mer, , France

Site Status

C.H.U. de Brest

Brest, , France

Site Status

Centre Hospitalier General

Brivé, , France

Site Status

Centre Hospitalier William Morey

Chalon-sur-Saône, , France

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Clinique Notre Dame du Bon Secours

Chartres, , France

Site Status

Hopital Louis Pasteur

Chartres, , France

Site Status

Hopital Antoine Beclere

Clamart, , France

Site Status

Centre Jean Perrin

Clermont-Ferrand, , France

Site Status

Hopital Louis Pasteur

Colmar, , France

Site Status

Centre Hospitalier de Dax

Dax, , France

Site Status

Centre de Lutte Contre le Cancer Georges-Francois Leclerc

Dijon, , France

Site Status

Hopital Jean Monnet

Épinal, , France

Site Status

Hopital Clarac

Fort de France Cedex, , France

Site Status

Institut Prive de Cancerologie

Grenoble, , France

Site Status

Clinique Sainte-Marguerite

Hyères, , France

Site Status

Centre De Radiotherapie Charlebourg

La Garenne-Colombes, , France

Site Status

Centre Hospitalier Departemental

La Roche-sur-Yon, , France

Site Status

Centre Hospitalier de Lagny

Lagny-sur-Marne, , France

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Hopital Andre Mignot

Le Chesnay, , France

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Clinique Victor Hugo

Le Mans, , France

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Institut d'Oncologie Hartmann

Levallois-Perret, , France

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Hopital Robert Boulin

Libourne, , France

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Clinique Chenieux

Limoges, , France

Site Status

Centre Hospital Regional Universitaire de Limoges

Limoges, , France

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Centre Medical Parot

Lyon, , France

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Centre Leon Berard

Lyon, , France

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Hopital Edouard Herriot - Lyon

Lyon, , France

Site Status

Centre de Radiotherapie et Oncologie Saint-Faron

Mareuil-lès-Meaux, , France

Site Status

Marseille Institute of Cancer - Institut J. Paoli and I. Calmettes

Marseille, , France

Site Status

Hopital Clinique Claude Bernard

Metz, , France

Site Status

Centre de Radiologie et de Traitement des Tumeurs

Meudon-la-Forêt, , France

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CH Meulan

Meulan-en-Yvelines, , France

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Centre Hospitalier General de Mont de Marsan

Mont-de-Marsan, , France

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Centre Hospitalier de Montelimar

Montélimar, , France

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Centre Hospitalier de Montlucon

Montluçon, , France

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Centre Regional de Lutte Contre le Cancer - Centre Val d'Aurelle

Montpellier, , France

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Clinique Clementville

Montpellier, , France

Site Status

Centre Azureen de Cancerologie

Mougins, , France

Site Status

Centre Catherine de Sienne

Nantes, , France

Site Status

Centre Regional Rene Gauducheau

Nantes-Saint-Herblain, , France

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Clinique Les Genets

Narbonne, , France

Site Status

Clinique Hartmann

Neuilly-sur-Seine, , France

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Clinique Belvedere

Nice, , France

Site Status

Clinique Saint George

Nice, , France

Site Status

Centre Antoine Lacassagne

Nice, , France

Site Status

C.H.U. de Nimes - Groupe Hospitals-Universitaire Caremeau

Nîmes, , France

Site Status

Clinique De Valdegour

Nîmes, , France

Site Status

Hopital Europeen Georges Pompidou

Paris, , France

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Institut Curie Hopital

Paris, , France

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Hopital Saint-Louis

Paris, , France

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CHU Pitie-Salpetriere

Paris, , France

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Centre Hospitalier - Pau

Pau, , France

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Clinique Saint - Pierre

Perpignan, , France

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Polyclinique Francheville

Périgueux, , France

Site Status

Centre Hospitalier Lyon Sud

Pierre-Bénite, , France

Site Status

Centre Hospitalier Intercommunal de Poissy

Poissy, , France

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Hopital Jean Bernard

Poitiers, , France

Site Status

Institut Jean Godinot

Reims, , France

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Centre Eugene Marquis

Rennes, , France

Site Status

CHG Roanne

Roanne, , France

Site Status

Centre Henri Becquerel

Rouen, , France

Site Status

Clinique Armoricaine De Radiologie

Saint-Brieuc, , France

Site Status

Centre Etienne Dolet

Saint-Nazaire, , France

Site Status

Institut de Cancerologie de la Loire

Saint-Priest-en-Jarez, , France

Site Status

Clinique Sainte Clotilde

Sainte Clotilde, , France

Site Status

Clinique de l'Orangerie

Strasbourg, , France

Site Status

Centre Paul Strauss

Strasbourg, , France

Site Status

Centre Hospitalier Intercommunal Toulon - La Seyne Sur Mer

Toulon, , France

Site Status

Institut Claudius Regaud

Toulouse, , France

Site Status

Centre Hospitalier Universitaire Bretonneau de Tours

Tours, , France

Site Status

Countries

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France

References

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Pivot X, Romieu G, Debled M, Pierga JY, Kerbrat P, Bachelot T, Lortholary A, Espie M, Fumoleau P, Serin D, Jacquin JP, Jouannaud C, Rios M, Abadie-Lacourtoisie S, Venat-Bouvet L, Cany L, Catala S, Khayat D, Gambotti L, Pauporte I, Faure-Mercier C, Paget-Bailly S, Henriques J, Grouin JM; PHARE trial investigators. 6 months versus 12 months of adjuvant trastuzumab in early breast cancer (PHARE): final analysis of a multicentre, open-label, phase 3 randomised trial. Lancet. 2019 Jun 29;393(10191):2591-2598. doi: 10.1016/S0140-6736(19)30653-1. Epub 2019 Jun 6.

Reference Type DERIVED
PMID: 31178155 (View on PubMed)

Jacquinot Q, Paget-Bailly S, Fumoleau P, Romieu G, Pierga JY, Espie M, Lortholary A, Nabholtz JM, Mercier CF, Pauporte I, Henriques J, Pivot X. Fluctuation of the left ventricular ejection fraction in patients with HER2-positive early breast cancer treated by 12 months of adjuvant trastuzumab. Breast. 2018 Oct;41:1-7. doi: 10.1016/j.breast.2018.06.001. Epub 2018 Jun 15.

Reference Type DERIVED
PMID: 29913374 (View on PubMed)

Curtit E, Pivot X, Henriques J, Paget-Bailly S, Fumoleau P, Rios M, Bonnefoi H, Bachelot T, Soulie P, Jouannaud C, Bourgeois H, Petit T, Tennevet I, Assouline D, Mathieu MC, Jacquin JP, Lavau-Denes S, Darut-Jouve A, Ferrero JM, Tarpin C, Levy C, Delecroix V, Trillet-Lenoir V, Cojocarasu O, Meunier J, Pierga JY, Kerbrat P, Faure-Mercier C, Blanche H, Sahbatou M, Boland A, Bacq D, Besse C, Thomas G, Deleuze JF, Pauporte I, Romieu G, Cox DG. Assessment of the prognostic role of a 94-single nucleotide polymorphisms risk score in early breast cancer in the SIGNAL/PHARE prospective cohort: no correlation with clinico-pathological characteristics and outcomes. Breast Cancer Res. 2017 Aug 22;19(1):98. doi: 10.1186/s13058-017-0888-4.

Reference Type DERIVED
PMID: 28830573 (View on PubMed)

Pivot X, Fumoleau P, Pierga JY, Delaloge S, Bonnefoi H, Bachelot T, Jouannaud C, Bourgeois H, Rios M, Soulie P, Jacquin JP, Lavau-Denes S, Kerbrat P, Cox D, Faure-Mercier C, Pauporte I, Gligorov J, Curtit E, Henriques J, Paget-Bailly S, Romieu G. Superimposable outcomes for sequential and concomitant administration of adjuvant trastuzumab in HER2-positive breast cancer: Results from the SIGNAL/PHARE prospective cohort. Eur J Cancer. 2017 Aug;81:151-160. doi: 10.1016/j.ejca.2017.05.020. Epub 2017 Jun 16.

Reference Type DERIVED
PMID: 28624696 (View on PubMed)

Pivot X, Suter T, Nabholtz JM, Pierga JY, Espie M, Lortholary A, Khayat D, Pauporte I, Romieu G, Kramar A, Fumoleau P. Cardiac toxicity events in the PHARE trial, an adjuvant trastuzumab randomised phase III study. Eur J Cancer. 2015 Sep;51(13):1660-6. doi: 10.1016/j.ejca.2015.05.028. Epub 2015 Jul 7.

Reference Type DERIVED
PMID: 26163096 (View on PubMed)

Kramar A, Bachelot T, Madrange N, Pierga JY, Kerbrat P, Espie M, Fumoleau P, Pauporte I, Khayat D, Romieu G, Pivot X. Trastuzumab duration effects within patient prognostic subgroups in the PHARE trial. Ann Oncol. 2014 Aug;25(8):1563-70. doi: 10.1093/annonc/mdu177. Epub 2014 May 14.

Reference Type DERIVED
PMID: 24827132 (View on PubMed)

Pivot X, Romieu G, Debled M, Pierga JY, Kerbrat P, Bachelot T, Lortholary A, Espie M, Fumoleau P, Serin D, Jacquin JP, Jouannaud C, Rios M, Abadie-Lacourtoisie S, Tubiana-Mathieu N, Cany L, Catala S, Khayat D, Pauporte I, Kramar A; PHARE trial investigators. 6 months versus 12 months of adjuvant trastuzumab for patients with HER2-positive early breast cancer (PHARE): a randomised phase 3 trial. Lancet Oncol. 2013 Jul;14(8):741-8. doi: 10.1016/S1470-2045(13)70225-0. Epub 2013 Jun 11.

Reference Type DERIVED
PMID: 23764181 (View on PubMed)

Other Identifiers

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INCA-PHARE

Identifier Type: -

Identifier Source: secondary_id

INCA-RECF0146

Identifier Type: -

Identifier Source: secondary_id

EUDRACT-2006-000070-67

Identifier Type: -

Identifier Source: secondary_id

CDR0000509793

Identifier Type: -

Identifier Source: org_study_id

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