Trial Outcomes & Findings for Phase II Trial of SAHA & Tamoxifen for Patients With Breast Cancer (NCT NCT00365599)

NCT ID: NCT00365599

Last Updated: 2014-11-21

Results Overview

The Objective Response Rate. Response and progression were evaluated in this study using the new international criteria proposed by the Response Evaluation Criteria in Solid Tumors (RECIST). Changes in only the largest diameter (unidimensional measurement) of the tumor lesions are used in the RECIST criteria. For the purposes of this study, patients were evaluated for response every 8 weeks. In addition to a baseline scan, confirmatory scans were also obtained ≥ 4 weeks following initial documentation of objective response.

Recruitment status

COMPLETED

Study phase

PHASE2

Target enrollment

43 participants

Primary outcome timeframe

24 weeks

Results posted on

2014-11-21

Participant Flow

Estrogen or progesterone receptor positive advanced breast cancer: Postmenopausal, failed first-line therapy with aromatase inhibitor or recurred within 12 months of adjuvant treatments with aromatase inhibitors; Premenopausal, recurred \>12 months after adjuvant tamoxifen or never treated with tamoxifen; Not candidate for aromatase inhibitor

Participant milestones

Participant milestones
Measure
Vorinostat and Tamoxifen
Vorinostat and Tamoxifen as outlined in Intervention Descriptions
Overall Study
STARTED
43
Overall Study
COMPLETED
43
Overall Study
NOT COMPLETED
0

Reasons for withdrawal

Withdrawal data not reported

Baseline Characteristics

Phase II Trial of SAHA & Tamoxifen for Patients With Breast Cancer

Baseline characteristics by cohort

Baseline characteristics by cohort
Measure
Vorinostat and Tamoxifen
n=43 Participants
Vorinostat and Tamoxifen as outlined in Intervention Descriptions
Age, Categorical
<=18 years
0 Participants
n=5 Participants
Age, Categorical
Between 18 and 65 years
37 Participants
n=5 Participants
Age, Categorical
>=65 years
6 Participants
n=5 Participants
Age, Customized
56 years
n=5 Participants
Sex: Female, Male
Female
43 Participants
n=5 Participants
Sex: Female, Male
Male
0 Participants
n=5 Participants
Region of Enrollment
United States
43 participants
n=5 Participants

PRIMARY outcome

Timeframe: 24 weeks

Population: All participants

The Objective Response Rate. Response and progression were evaluated in this study using the new international criteria proposed by the Response Evaluation Criteria in Solid Tumors (RECIST). Changes in only the largest diameter (unidimensional measurement) of the tumor lesions are used in the RECIST criteria. For the purposes of this study, patients were evaluated for response every 8 weeks. In addition to a baseline scan, confirmatory scans were also obtained ≥ 4 weeks following initial documentation of objective response.

Outcome measures

Outcome measures
Measure
Vorinostat and Tamoxifen
n=43 Participants
Vorinostat and Tamoxifen as outlined in Intervention Descriptions
Number of Participants With Objective Response (OR)
8 participants

SECONDARY outcome

Timeframe: Up to 30 months

Population: All participants

The median response duration in months. Response and progression were evaluated in this study using the new international criteria proposed by the Response Evaluation Criteria in Solid Tumors (RECIST).

Outcome measures

Outcome measures
Measure
Vorinostat and Tamoxifen
n=43 Participants
Vorinostat and Tamoxifen as outlined in Intervention Descriptions
Time to Progression (TTP)
10.3 months
Interval 8.1 to 12.4

SECONDARY outcome

Timeframe: 4 years, 7 months

Population: All participants

Safety evaluation according to descriptions and grading scales found in the revised NCI Common Terminology Criteria for Adverse Events (CTCAE) version 3.0.

Outcome measures

Outcome measures
Measure
Vorinostat and Tamoxifen
n=43 Participants
Vorinostat and Tamoxifen as outlined in Intervention Descriptions
Number of Participants With Serious Adverse Events (SAEs)
4 participants

Adverse Events

Vorinostat and Tamoxifen

Serious events: 4 serious events
Other events: 33 other events
Deaths: 0 deaths

Serious adverse events

Serious adverse events
Measure
Vorinostat and Tamoxifen
n=43 participants at risk
Vorinostat and Tamoxifen as outlined in Intervention Descriptions
Gastrointestinal disorders
Anorexia
2.3%
1/43 • Number of events 1 • 4 years, 7 months
Blood and lymphatic system disorders
Hemoglobin
2.3%
1/43 • Number of events 1 • 4 years, 7 months
Blood and lymphatic system disorders
Hemorrhage/Bleeding
2.3%
1/43 • Number of events 1 • 4 years, 7 months
Blood and lymphatic system disorders
Neutrophils/granulocytes (ANC/AGC)
2.3%
1/43 • Number of events 1 • 4 years, 7 months
Blood and lymphatic system disorders
Platelets
2.3%
1/43 • Number of events 1 • 4 years, 7 months
Metabolism and nutrition disorders
Sodium, serum-low (hyponatremia)
2.3%
1/43 • Number of events 1 • 4 years, 7 months
Vascular disorders
Thrombosis/thrombus/embolism
4.7%
2/43 • Number of events 2 • 4 years, 7 months

Other adverse events

Other adverse events
Measure
Vorinostat and Tamoxifen
n=43 participants at risk
Vorinostat and Tamoxifen as outlined in Intervention Descriptions
Skin and subcutaneous tissue disorders
Alopecia - Grade 2
9.3%
4/43 • Number of events 4 • 4 years, 7 months
Gastrointestinal disorders
Anorexia/weight loss - Grade 2
16.3%
7/43 • Number of events 11 • 4 years, 7 months
Gastrointestinal disorders
Anorexia/weight loss - Grade 3
9.3%
4/43 • Number of events 4 • 4 years, 7 months
Respiratory, thoracic and mediastinal disorders
Deep vein thrombosis/pulmonary embolish (DVT/PE) - Grade 4
7.0%
3/43 • Number of events 3 • 4 years, 7 months
Gastrointestinal disorders
Diarrhea - Grade 2
16.3%
7/43 • Number of events 8 • 4 years, 7 months
General disorders
Fatigue - Grade 2
18.6%
8/43 • Number of events 16 • 4 years, 7 months
General disorders
Fatigue - Grade 3
16.3%
7/43 • Number of events 8 • 4 years, 7 months
Metabolism and nutrition disorders
Hepatic dysfunction (alanine aminotransferase/aspartate aminotransferase [ALT/AST]) - Grade 2
7.0%
3/43 • Number of events 8 • 4 years, 7 months
Metabolism and nutrition disorders
Hyperglycemia - Grade 2
11.6%
5/43 • Number of events 11 • 4 years, 7 months
Blood and lymphatic system disorders
Leukopenia - Grade 2
9.3%
4/43 • Number of events 9 • 4 years, 7 months
Blood and lymphatic system disorders
Lymphopenia - Grade 2
11.6%
5/43 • Number of events 16 • 4 years, 7 months
Blood and lymphatic system disorders
Lymphopenia - Grade 3
14.0%
6/43 • Number of events 6 • 4 years, 7 months
Gastrointestinal disorders
Nausea - Grade 2
18.6%
8/43 • Number of events 13 • 4 years, 7 months
Blood and lymphatic system disorders
Neutropenia - Grade 2
11.6%
5/43 • Number of events 5 • 4 years, 7 months
Blood and lymphatic system disorders
Neutropenia - Grade 3
16.3%
7/43 • Number of events 7 • 4 years, 7 months
Blood and lymphatic system disorders
Thrombocytopenia - Grade 2
9.3%
4/43 • Number of events 7 • 4 years, 7 months
Blood and lymphatic system disorders
Thrombocytopenia - Grade 3
7.0%
3/43 • Number of events 3 • 4 years, 7 months

Additional Information

Susan Minton, D.O.

H. Lee Moffitt Cancer Center and Research Institute

Phone: 813-745-3806

Results disclosure agreements

  • Principal investigator is a sponsor employee
  • Publication restrictions are in place