Trial Outcomes & Findings for Paclitaxel/Carboplatin Plus Bevacizumab/Erlotinib in the First Line Treatment of Carcinoma of Unknown Primary Site (NCT NCT00360360)

NCT ID: NCT00360360

Last Updated: 2013-12-04

Results Overview

Recruitment status

COMPLETED

Study phase

PHASE2

Target enrollment

60 participants

Primary outcome timeframe

18 months

Results posted on

2013-12-04

Participant Flow

Participant milestones

Participant milestones
Measure
Bevacizumab/Paclitaxel/Carboplatin/Erlotinib
Bevacizumab 15mg/kg IV infusion,Day 1 Paclitaxel 175mg/m2, 1-3 hour IV infusion,Day 1 Carboplatin AUC 6.0 IV Day 1 Erlotinib 150 mg by mouth daily
Overall Study
STARTED
60
Overall Study
COMPLETED
54
Overall Study
NOT COMPLETED
6

Reasons for withdrawal

Withdrawal data not reported

Baseline Characteristics

Paclitaxel/Carboplatin Plus Bevacizumab/Erlotinib in the First Line Treatment of Carcinoma of Unknown Primary Site

Baseline characteristics by cohort

Baseline characteristics by cohort
Measure
Bevacizumab/Paclitaxel/Carboplatin/Erlotinib
n=60 Participants
Bevacizumab 15mg/kg IV infusion,Day 1 Paclitaxel 175mg/m2, 1-3 hour IV infusion,Day 1 Carboplatin AUC 6.0 IV Day 1 Erlotinib 150 mg by mouth daily
Age Continuous
50 years
n=5 Participants
Sex: Female, Male
Female
31 Participants
n=5 Participants
Sex: Female, Male
Male
29 Participants
n=5 Participants
Region of Enrollment
United States
60 participants
n=5 Participants

PRIMARY outcome

Timeframe: 18 months

Outcome measures

Outcome measures
Measure
Bevacizumab/Paclitaxel/Carboplatin/Erlotinib
n=54 Participants
Bevacizumab 15mg/kg IV infusion,Day 1 Paclitaxel 175mg/m2, 1-3 hour IV infusion,Day 1 Carboplatin AUC 6.0 IV Day 1 Erlotinib 150 mg by mouth daily
Overall Survival (OS), the Length of Time, in Months, That Patients Were Alive From Their First Date of Protocol Treatment Until Death
12.6 months
Interval 9.7 to 18.5

SECONDARY outcome

Timeframe: 18 months

Progression is defined using Response Evaluation Criteria In Solid Tumors Criteria (RECIST v1.0), as a 20% increase in the sum of the longest diameter of target lesions, or a measurable increase in a non-target lesion, or the appearance of new lesions.

Outcome measures

Outcome measures
Measure
Bevacizumab/Paclitaxel/Carboplatin/Erlotinib
n=54 Participants
Bevacizumab 15mg/kg IV infusion,Day 1 Paclitaxel 175mg/m2, 1-3 hour IV infusion,Day 1 Carboplatin AUC 6.0 IV Day 1 Erlotinib 150 mg by mouth daily
Progression-free Survival
8 months
Interval 6.4 to 13.8

Adverse Events

Bevacizumab/Paclitaxel/Carboplatin/Erlotinib

Serious events: 29 serious events
Other events: 60 other events
Deaths: 0 deaths

Serious adverse events

Serious adverse events
Measure
Bevacizumab/Paclitaxel/Carboplatin/Erlotinib
n=60 participants at risk
Bevacizumab 15mg/kg IV infusion,Day 1 Paclitaxel 175mg/m2, 1-3 hour IV infusion,Day 1 Carboplatin AUC 6.0 IV Day 1 Erlotinib 150 mg by mouth daily
Metabolism and nutrition disorders
Acidosis
1.7%
1/60 • Number of events 1
Gastrointestinal disorders
Dehydration
11.7%
7/60 • Number of events 11
Infections and infestations
Febrile neutropenia
8.3%
5/60 • Number of events 5
Gastrointestinal disorders
Cholecystitis
1.7%
1/60 • Number of events 1
Metabolism and nutrition disorders
Bilirubin (hyperbilirubinemia)
1.7%
1/60 • Number of events 1
Gastrointestinal disorders
Vomiting
1.7%
1/60 • Number of events 2
Endocrine disorders
Neuroendocrine: ADH secretion abnormality
1.7%
1/60 • Number of events 1
Musculoskeletal and connective tissue disorders
Musculoskeletal/Soft Tissue - Other
1.7%
1/60 • Number of events 1
Cardiac disorders
Cardiac General
1.7%
1/60 • Number of events 1
Musculoskeletal and connective tissue disorders
Pain
1.7%
1/60 • Number of events 1
Infections and infestations
Infection
1.7%
1/60 • Number of events 1
Respiratory, thoracic and mediastinal disorders
Pneumothorax
1.7%
1/60 • Number of events 1
Cardiac disorders
Hypotension
1.7%
1/60 • Number of events 1
Gastrointestinal disorders
Perforation
1.7%
1/60 • Number of events 1
Cardiac disorders
Pain
1.7%
1/60 • Number of events 1
Gastrointestinal disorders
Ascites
3.3%
2/60 • Number of events 3
Gastrointestinal disorders
Obstruction, GI
1.7%
1/60 • Number of events 1
Cardiac disorders
Pericardial tumor constriction
1.7%
1/60 • Number of events 1
Gastrointestinal disorders
Pain
5.0%
3/60 • Number of events 3
Blood and lymphatic system disorders
Pancytopenia
1.7%
1/60 • Number of events 1
Respiratory, thoracic and mediastinal disorders
Aspiration
1.7%
1/60 • Number of events 1
Gastrointestinal disorders
Hemorrhage
1.7%
1/60 • Number of events 1
Cardiac disorders
Supraventricular and nodal arrhythmia
1.7%
1/60 • Number of events 1
Vascular disorders
CNS cerebrovascular ischemia
1.7%
1/60 • Number of events 1
General disorders
Generalized weakness
1.7%
1/60 • Number of events 1
Neoplasms benign, malignant and unspecified (incl cysts and polyps)
disease progression
10.0%
6/60 • Number of events 6

Other adverse events

Other adverse events
Measure
Bevacizumab/Paclitaxel/Carboplatin/Erlotinib
n=60 participants at risk
Bevacizumab 15mg/kg IV infusion,Day 1 Paclitaxel 175mg/m2, 1-3 hour IV infusion,Day 1 Carboplatin AUC 6.0 IV Day 1 Erlotinib 150 mg by mouth daily
Skin and subcutaneous tissue disorders
Rash (acneiform)
8.3%
5/60 • Number of events 7
Immune system disorders
Allergic Reaction/Hypersensitivity Grade
10.0%
6/60 • Number of events 8
Skin and subcutaneous tissue disorders
Alopecia
45.0%
27/60 • Number of events 94
Blood and lymphatic system disorders
Anemia
5.0%
3/60 • Number of events 5
Gastrointestinal disorders
Anorexia
51.7%
31/60 • Number of events 90
Gastrointestinal disorders
Bleeding (gums)
5.0%
3/60 • Number of events 3
Gastrointestinal disorders
Constipation
38.3%
23/60 • Number of events 45
Respiratory, thoracic and mediastinal disorders
Cough
21.7%
13/60 • Number of events 20
Gastrointestinal disorders
Dehydration
26.7%
16/60 • Number of events 34
Psychiatric disorders
Depression
6.7%
4/60 • Number of events 6
Gastrointestinal disorders
Diarrhea
66.7%
40/60 • Number of events 139
Nervous system disorders
Dizziness/Lightheadedness
8.3%
5/60 • Number of events 10
Gastrointestinal disorders
Dyspepsia
5.0%
3/60 • Number of events 8
Gastrointestinal disorders
Dysphagia
6.7%
4/60 • Number of events 7
Respiratory, thoracic and mediastinal disorders
Dyspnea
25.0%
15/60 • Number of events 42
Respiratory, thoracic and mediastinal disorders
Epistaxis
25.0%
15/60 • Number of events 28
General disorders
Fatigue
75.0%
45/60 • Number of events 237
General disorders
Fever
13.3%
8/60 • Number of events 8
Nervous system disorders
Headache
20.0%
12/60 • Number of events 31
Metabolism and nutrition disorders
Hemoglobin
56.7%
34/60 • Number of events 124
Respiratory, thoracic and mediastinal disorders
Hoarseness
6.7%
4/60 • Number of events 11
Metabolism and nutrition disorders
Hyperglycemia
13.3%
8/60 • Number of events 16
Metabolism and nutrition disorders
Hyperkalemia
10.0%
6/60 • Number of events 12
Cardiac disorders
Hypertension
6.7%
4/60 • Number of events 7
Metabolism and nutrition disorders
Hypoglycemia
5.0%
3/60 • Number of events 3
Metabolism and nutrition disorders
Hypokalemia
5.0%
3/60 • Number of events 3
Metabolism and nutrition disorders
Hyponatremia
8.3%
5/60 • Number of events 5
Cardiac disorders
Hypotension
28.3%
17/60 • Number of events 55
Gastrointestinal disorders
Indigestion
5.0%
3/60 • Number of events 15
General disorders
Insomnia
15.0%
9/60 • Number of events 24
Blood and lymphatic system disorders
Leukocytes (WBC)
46.7%
28/60 • Number of events 61
Psychiatric disorders
Mood alteration (anxiety)
11.7%
7/60 • Number of events 15
Psychiatric disorders
Mood alteration (confusion)
5.0%
3/60 • Number of events 4
Psychiatric disorders
Mood alteration (depression)
8.3%
5/60 • Number of events 6
Gastrointestinal disorders
Mouth (sore)
5.0%
3/60 • Number of events 3
Gastrointestinal disorders
Mucositis
13.3%
8/60 • Number of events 17
Musculoskeletal and connective tissue disorders
Myalgia
21.7%
13/60 • Number of events 34
Gastrointestinal disorders
Nausea
66.7%
40/60 • Number of events 125
Nervous system disorders
Neuropathy-sensory
31.7%
19/60 • Number of events 101
Blood and lymphatic system disorders
Neutropenia
5.0%
3/60 • Number of events 3
Infections and infestations
Neutropenic fever
5.0%
3/60 • Number of events 3
Blood and lymphatic system disorders
Neutrophils (ANC)
50.0%
30/60 • Number of events 53
General disorders
Night Sweats
5.0%
3/60 • Number of events 3
General disorders
Pain (NOS)
5.0%
3/60 • Number of events 5
Gastrointestinal disorders
Pain (abdominal)
16.7%
10/60 • Number of events 15
Musculoskeletal and connective tissue disorders
Pain (back)
8.3%
5/60 • Number of events 20
Musculoskeletal and connective tissue disorders
Pain (bone)
10.0%
6/60 • Number of events 8
Cardiac disorders
Pain (chest)
5.0%
3/60 • Number of events 3
Musculoskeletal and connective tissue disorders
Pain (legs)
5.0%
3/60 • Number of events 4
Blood and lymphatic system disorders
Platelets
51.7%
31/60 • Number of events 77
Metabolism and nutrition disorders
Proteinuria
20.0%
12/60 • Number of events 20
Skin and subcutaneous tissue disorders
Pruritis
26.7%
16/60 • Number of events 27
Skin and subcutaneous tissue disorders
Rash (facial)
5.0%
3/60 • Number of events 5
Skin and subcutaneous tissue disorders
Rash/Desquamation
75.0%
45/60 • Number of events 218
Respiratory, thoracic and mediastinal disorders
Sinus congestion
8.3%
5/60 • Number of events 7
Respiratory, thoracic and mediastinal disorders
Sinus drainage
5.0%
3/60 • Number of events 6
Skin and subcutaneous tissue disorders
Skin (dry)
11.7%
7/60 • Number of events 20
Gastrointestinal disorders
Taste alteration
10.0%
6/60 • Number of events 14
Respiratory, thoracic and mediastinal disorders
Throat (sore)
6.7%
4/60 • Number of events 6
Musculoskeletal and connective tissue disorders
Weakness
5.0%
3/60 • Number of events 3
General disorders
Weight Loss
15.0%
9/60 • Number of events 35

Additional Information

John D. Hainsworth, MD

Sarah Cannon Research Institute

Phone: 1-877-MY-1-SCRI

Results disclosure agreements

  • Principal investigator is a sponsor employee The sponsor can review/embargo results communications prior to public release for a period that is \>60 days but ≤180 days from date submitted to sponsor, who may require changes to the communication in order to remove specifically identified confidential information (other than study data) and/or delay the proposed publication to enable the sponsor to seek patent protection for inventions. The PI may not publish its results until 18 mos. after the trial has been completed at all sites.
  • Publication restrictions are in place

Restriction type: OTHER