Trial Outcomes & Findings for Study of Decitabine for Treatment of Older Patients With Acute Myeloid Leukemia (AML) (NCT NCT00358644)

NCT ID: NCT00358644

Last Updated: 2013-05-20

Results Overview

Recruitment status

COMPLETED

Study phase

PHASE2

Target enrollment

55 participants

Primary outcome timeframe

1 year

Results posted on

2013-05-20

Participant Flow

Participant milestones

Participant milestones
Measure
Decitabine 20 mg/m2 Intravenous
Decitabine 20 mg/m2 Intravenous on Days 1-5 of each 28 day cycle
Overall Study
STARTED
55
Overall Study
COMPLETED
5
Overall Study
NOT COMPLETED
50

Reasons for withdrawal

Reasons for withdrawal
Measure
Decitabine 20 mg/m2 Intravenous
Decitabine 20 mg/m2 Intravenous on Days 1-5 of each 28 day cycle
Overall Study
Progressive Disease
21
Overall Study
Adverse Event
7
Overall Study
Death
11
Overall Study
Withdrawal by Subject
4
Overall Study
Physician Decision
6
Overall Study
Patient not eligible for study
1

Baseline Characteristics

Study of Decitabine for Treatment of Older Patients With Acute Myeloid Leukemia (AML)

Baseline characteristics by cohort

Baseline characteristics by cohort
Measure
Decitabine 20 mg/m2 Intravenous
n=55 Participants
Decitabine 20 mg/m2 Intravenous on Days 1-5 of each 28 day cycle
Age, Categorical
<=18 years
0 Participants
n=5 Participants
Age, Categorical
Between 18 and 65 years
7 Participants
n=5 Participants
Age, Categorical
>=65 years
48 Participants
n=5 Participants
Age Continuous
73.0 years
STANDARD_DEVIATION 6.84 • n=5 Participants
Sex: Female, Male
Female
28 Participants
n=5 Participants
Sex: Female, Male
Male
27 Participants
n=5 Participants
Race (NIH/OMB)
American Indian or Alaska Native
0 Participants
n=5 Participants
Race (NIH/OMB)
Asian
0 Participants
n=5 Participants
Race (NIH/OMB)
Native Hawaiian or Other Pacific Islander
0 Participants
n=5 Participants
Race (NIH/OMB)
Black or African American
5 Participants
n=5 Participants
Race (NIH/OMB)
White
50 Participants
n=5 Participants
Race (NIH/OMB)
More than one race
0 Participants
n=5 Participants
Race (NIH/OMB)
Unknown or Not Reported
0 Participants
n=5 Participants
Region of Enrollment
United States
55 participants
n=5 Participants

PRIMARY outcome

Timeframe: 1 year

Population: Intent-to-Treat (ITT)

Outcome measures

Outcome measures
Measure
Decitabine 20 mg/m2 Intravenous
n=55 Participants
Decitabine 20 mg/m2 Intravenous on Days 1-5 of each 28 day cycle
Complete Response = Morphologic Complete Remission (mCR)
13 Participants

Adverse Events

Decitabine 20 mg/m2 Intravenous

Serious events: 40 serious events
Other events: 55 other events
Deaths: 0 deaths

Serious adverse events

Serious adverse events
Measure
Decitabine 20 mg/m2 Intravenous
n=55 participants at risk
Decitabine 20 mg/m2 Intravenous on Days 1-5 of each 28 day cycle
Blood and lymphatic system disorders
Anemia
1.8%
1/55
Blood and lymphatic system disorders
Febrile Neutropenia
23.6%
13/55
Blood and lymphatic system disorders
Neutropenia
7.3%
4/55
Cardiac disorders
Angina Pectoris
1.8%
1/55
Blood and lymphatic system disorders
Atrial Fibrillation
3.6%
2/55
Cardiac disorders
Myocardial Infarction
1.8%
1/55
Gastrointestinal disorders
Caecitis
1.8%
1/55
Gastrointestinal disorders
Diarrhea
5.5%
3/55
Gastrointestinal disorders
Gastrointestinal Haemorrhage
1.8%
1/55
Gastrointestinal disorders
Nausea
1.8%
1/55
Gastrointestinal disorders
Toothache
1.8%
1/55
Gastrointestinal disorders
Upper Gastrointestinal Haemorrhage
1.8%
1/55
Gastrointestinal disorders
Vomiting
1.8%
1/55
General disorders
Catheter Thrombosis
1.8%
1/55
General disorders
Chest Pain
1.8%
1/55
General disorders
Disease Progression
16.4%
9/55
General disorders
Mucosal Inflammation
1.8%
1/55
General disorders
Performance Status Decreased
5.5%
3/55
General disorders
Pyrexia
7.3%
4/55
Hepatobiliary disorders
Cholecystitis Acute
1.8%
1/55
Hepatobiliary disorders
Hyperbilirubinaemia
1.8%
1/55
Infections and infestations
Alpha Haemolytic Streptococcal Infection
1.8%
1/55
Infections and infestations
Bacteraemia
10.9%
6/55
Infections and infestations
Catheter Site Infection
1.8%
1/55
Infections and infestations
Cellulitis
1.8%
1/55
Infections and infestations
Clostridium Difficile Colitis
7.3%
4/55
Infections and infestations
Enterocolitis Infectious
1.8%
1/55
Infections and infestations
Fungaemia
1.8%
1/55
Infections and infestations
Fungal Sepsis
1.8%
1/55
Infections and infestations
Gingival Infection
1.8%
1/55
Infections and infestations
Groin Abscess
1.8%
1/55
Infections and infestations
Lobar Pneumonia
1.8%
1/55
Infections and infestations
Pneumonia
12.7%
7/55
Infections and infestations
Pneumonia Fungal
1.8%
1/55
Infections and infestations
Pneumonia Klebsiella
1.8%
1/55
Infections and infestations
Pneumonia Primary Atypical
1.8%
1/55
Infections and infestations
Pseudomonal Bacteraemia
1.8%
1/55
Infections and infestations
Sepsis
14.5%
8/55
Infections and infestations
Staphylococcal Bacteraemia
5.5%
3/55
Infections and infestations
Staphylococcal Infection
1.8%
1/55
Infections and infestations
Staphylococcal Sepsis
1.8%
1/55
Infections and infestations
Streptococcal Bacteraemia
1.8%
1/55
Infections and infestations
Tonsillitis
1.8%
1/55
Infections and infestations
Tooth Abscess
1.8%
1/55
Infections and infestations
Urinary Tract Infection
7.3%
4/55
Infections and infestations
Urosepsis
1.8%
1/55
Injury, poisoning and procedural complications
Haemolytic Transfusion Reaction
1.8%
1/55
Injury, poisoning and procedural complications
Subdural Haemorrhage
1.8%
1/55
Investigations
Blood Creatinine Increased
1.8%
1/55
Metabolism and nutrition disorders
Acidosis
1.8%
1/55
Metabolism and nutrition disorders
Dehydration
1.8%
1/55
Metabolism and nutrition disorders
Hypokalaemia
1.8%
1/55
Metabolism and nutrition disorders
Malnutrition
1.8%
1/55
Musculoskeletal and connective tissue disorders
Pain in Extremity
1.8%
1/55
Neoplasms benign, malignant and unspecified (incl cysts and polyps)
Acute Myeloid Leukaemia
1.8%
1/55
Nervous system disorders
Haemorrhage Intracranial
1.8%
1/55
Psychiatric disorders
Mental Status Changes
3.6%
2/55
Renal and urinary disorders
Renal Failure
3.6%
2/55
Respiratory, thoracic and mediastinal disorders
Acute Respiratory Distress Syndrome
1.8%
1/55
Respiratory, thoracic and mediastinal disorders
Dyspnoea
3.6%
2/55
Respiratory, thoracic and mediastinal disorders
Hypoxia
1.8%
1/55
Respiratory, thoracic and mediastinal disorders
Pulmonary Haemorrhage
1.8%
1/55
Respiratory, thoracic and mediastinal disorders
Respiratory Distress
1.8%
1/55
Respiratory, thoracic and mediastinal disorders
Respiratory Failure
5.5%
3/55
Skin and subcutaneous tissue disorders
Dermatitis Allergic
1.8%
1/55
Vascular disorders
Embolism
1.8%
1/55
Vascular disorders
Hypotension
3.6%
2/55

Other adverse events

Other adverse events
Measure
Decitabine 20 mg/m2 Intravenous
n=55 participants at risk
Decitabine 20 mg/m2 Intravenous on Days 1-5 of each 28 day cycle
Blood and lymphatic system disorders
Anaemia
25.5%
14/55
Blood and lymphatic system disorders
Febrile Neutropenia
30.9%
17/55
Blood and lymphatic system disorders
Leukopenia
12.7%
7/55
Blood and lymphatic system disorders
Lymphopenia
7.3%
4/55
Blood and lymphatic system disorders
Neutropenia
25.5%
14/55
Blood and lymphatic system disorders
Thrombocytopenia
21.8%
12/55
Cardiac disorders
Atrial Fibrillation
7.3%
4/55
Cardiac disorders
Sinus Tachycardia
5.5%
3/55
Cardiac disorders
Tachycardia
9.1%
5/55
Ear and labyrinth disorders
Ear Pain
5.5%
3/55
Eye disorders
Conjuntival Haemorrhage
5.5%
3/55
Gastrointestinal disorders
Abdominal Pain
14.5%
8/55
Gastrointestinal disorders
Constipation
41.8%
23/55
Gastrointestinal disorders
Diarrhea
40.0%
22/55
Gastrointestinal disorders
Gingival Bleeding
5.5%
3/55
Gastrointestinal disorders
Nausea
50.9%
28/55
Gastrointestinal disorders
Oral Pain
9.1%
5/55
Gastrointestinal disorders
Stomatitis
7.3%
4/55
Gastrointestinal disorders
Toothache
5.5%
3/55
Gastrointestinal disorders
Vomiting
29.1%
16/55
General disorders
Asthenia
30.9%
17/55
General disorders
Catheter Site Pain
5.5%
3/55
General disorders
Chills
23.6%
13/55
General disorders
Disease Progression
16.4%
9/55
General disorders
Fatigue
67.3%
37/55
General disorders
Mucosal Inflammation
20.0%
11/55
General disorders
Oedema
20.0%
11/55
General disorders
Oedema Peripheral
36.4%
20/55
General disorders
Pain
18.2%
10/55
General disorders
Performance Status Decreased
9.1%
5/55
General disorders
Pyrexia
43.6%
24/55
Hepatobiliary disorders
Hyperbilirubinemia
5.5%
3/55
Infections and infestations
Bacteraemia
12.7%
7/55
Infections and infestations
Candidiasis
5.5%
3/55
Infections and infestations
Cellulitis
5.5%
3/55
Infections and infestations
Clostridium Difficile Colitis
9.1%
5/55
Infections and infestations
Pneumonia
16.4%
9/55
Infections and infestations
Sepsis
14.5%
8/55
Infections and infestations
Staphylococcal Bacteraemia
5.5%
3/55
Infections and infestations
Urinary Tract Infection
12.7%
7/55
Injury, poisoning and procedural complications
Contusion
14.5%
8/55
Injury, poisoning and procedural complications
Procedural Pain
14.5%
8/55
Investigations
Alanine Aminotransferase Increased
7.3%
4/55
Investigations
Blood Alkaline Phosphatase Increased
7.3%
4/55
Investigations
Blood Creatinine Increased
10.9%
6/55
Investigations
International Normalised Ratio Increased
10.9%
6/55
Investigations
Weight Decreased
5.5%
3/55
Metabolism and nutrition disorders
Anorexia
16.4%
9/55
Metabolism and nutrition disorders
Decreased Appetite
16.4%
9/55
Metabolism and nutrition disorders
Fluid Overload
9.1%
5/55
Metabolism and nutrition disorders
Hyperglycaemia
9.1%
5/55
Metabolism and nutrition disorders
Hyperkalaemia
5.5%
3/55
Metabolism and nutrition disorders
Hypoalbuminaemia
16.4%
9/55
Metabolism and nutrition disorders
Hypocalcaemia
18.2%
10/55
Metabolism and nutrition disorders
Hypokalaemia
29.1%
16/55
Metabolism and nutrition disorders
Hypomagnesaemia
18.2%
10/55
Metabolism and nutrition disorders
Hyponatraemia
10.9%
6/55
Metabolism and nutrition disorders
Hypophosphataemia
10.9%
6/55
Musculoskeletal and connective tissue disorders
Arthralgia
12.7%
7/55
Musculoskeletal and connective tissue disorders
Back Pain
14.5%
8/55
Musculoskeletal and connective tissue disorders
Bone Pain
12.7%
7/55
Musculoskeletal and connective tissue disorders
Muscle Spasms
5.5%
3/55
Musculoskeletal and connective tissue disorders
Muscular Weakness
5.5%
3/55
Musculoskeletal and connective tissue disorders
Pain in Extremity
14.5%
8/55
Nervous system disorders
Dizziness
27.3%
15/55
Nervous system disorders
Headache
23.6%
13/55
Nervous system disorders
Hypoaesthesia
5.5%
3/55
Psychiatric disorders
Anxiety
9.1%
5/55
Psychiatric disorders
Depression
9.1%
5/55
Psychiatric disorders
Insomnia
18.2%
10/55
Renal and urinary disorders
Renal Failure
9.1%
5/55
Respiratory, thoracic and mediastinal disorders
Cough
29.1%
16/55
Respiratory, thoracic and mediastinal disorders
Dyspnoea
40.0%
22/55
Respiratory, thoracic and mediastinal disorders
Dyspnoea Exertional
7.3%
4/55
Respiratory, thoracic and mediastinal disorders
Epistaxis
5.5%
3/55
Respiratory, thoracic and mediastinal disorders
Hypoxia
7.3%
4/55
Respiratory, thoracic and mediastinal disorders
Nasal Congestion
7.3%
4/55
Respiratory, thoracic and mediastinal disorders
Paranasal Sinus Hypersecretion
7.3%
4/55
Respiratory, thoracic and mediastinal disorders
Pharyngolaryngeal Pain
18.2%
10/55
Respiratory, thoracic and mediastinal disorders
Pleural Effusion
5.5%
3/55
Respiratory, thoracic and mediastinal disorders
Respiratory Failure
7.3%
4/55
Respiratory, thoracic and mediastinal disorders
Sinus Congestion
7.3%
4/55
Respiratory, thoracic and mediastinal disorders
Wheezing
5.5%
3/55
Skin and subcutaneous tissue disorders
Ecchymosis
9.1%
5/55
Skin and subcutaneous tissue disorders
Erythema
5.5%
3/55
Skin and subcutaneous tissue disorders
Hyperhidrosis
7.3%
4/55
Skin and subcutaneous tissue disorders
Night Sweats
9.1%
5/55
Skin and subcutaneous tissue disorders
Petechiae
9.1%
5/55
Skin and subcutaneous tissue disorders
Pruritis
5.5%
3/55
Skin and subcutaneous tissue disorders
Rash
14.5%
8/55
Skin and subcutaneous tissue disorders
Skin Ulcer
5.5%
3/55
Skin and subcutaneous tissue disorders
Urticaria
7.3%
4/55
Vascular disorders
Hypertension
9.1%
5/55
Vascular disorders
Hypotension
16.4%
9/55

Additional Information

Eisai Call Center

Eisai Inc.

Phone: 888-422-4743

Results disclosure agreements

  • Principal investigator is a sponsor employee
  • Publication restrictions are in place