Trial Outcomes & Findings for Pyridoxine and Topical Urea/Lactic Acid-Based Cream in Preventing Hand-Foot Syndrome in Patients Receiving Capecitabine for Breast Cancer or Other Cancer (NCT NCT00296036)

NCT ID: NCT00296036

Last Updated: 2017-03-16

Results Overview

A patient self-reported hand-foot syndrome (HFSD), also known as palmar-plantar erythrodysesthesia, was completed daily while applying the cream. Patients rated skin severity symptoms individually in their hands and in their feet. Definitions of symptoms, which were based on Common Terminology Criteria for Adverse Events (CTCAE) v3.0, were provided to patients. The number of patients reporting moderate to severe symptoms in either hands or feet were tabulated and percentages are reported.

Recruitment status

COMPLETED

Study phase

PHASE3

Target enrollment

137 participants

Primary outcome timeframe

First 3 weeks of treatment

Results posted on

2017-03-16

Participant Flow

This trial was originally designed as a two-by-two factorial trial to test if urea/lactic acid-based cream and/or oral pyridoxine (B6) could decrease capecitabine-caused HFS. After results from another study found B6 and capecitabine combination ineffective in preventing HFS, the study was amended to a two-arm, randomized clinical trial.

Participant milestones

Participant milestones
Measure
Arm I: (Urea/Lactic Acid +Vit B6)
Patients receive topical urea/lactic acid-based cream applied to palms and soles twice daily and oral pyridoxine once daily on days 1-21.
Arm II: (Urea/Lactic Acid + Placebo)
Patients receive topical urea/lactic acid-based cream as in arm I (closed to accrual as of 10/24/2007) and oral placebo once daily on days 1-21.
Arm III: (Placebo +Vit B6)
Patients receive placebo cream applied to palms and soles twice daily and pyridoxine as in Arm I
Arm IV: (Placebo + Placebo)
Patients receive placebo cream and oral placebo.
Arm V: Urea/Lactic Acid
Patients receive topical urea/lactic acid-based cream applied to palms and soles twice daily on days 1-21.
Arm VI: (Placebo)
Patients receive placebo cream applied to palms and soles twice daily on days 1-21.
Overall Study
STARTED
19
18
18
17
33
32
Overall Study
COMPLETED
18
18
16
16
31
28
Overall Study
NOT COMPLETED
1
0
2
1
2
4

Reasons for withdrawal

Reasons for withdrawal
Measure
Arm I: (Urea/Lactic Acid +Vit B6)
Patients receive topical urea/lactic acid-based cream applied to palms and soles twice daily and oral pyridoxine once daily on days 1-21.
Arm II: (Urea/Lactic Acid + Placebo)
Patients receive topical urea/lactic acid-based cream as in arm I (closed to accrual as of 10/24/2007) and oral placebo once daily on days 1-21.
Arm III: (Placebo +Vit B6)
Patients receive placebo cream applied to palms and soles twice daily and pyridoxine as in Arm I
Arm IV: (Placebo + Placebo)
Patients receive placebo cream and oral placebo.
Arm V: Urea/Lactic Acid
Patients receive topical urea/lactic acid-based cream applied to palms and soles twice daily on days 1-21.
Arm VI: (Placebo)
Patients receive placebo cream applied to palms and soles twice daily on days 1-21.
Overall Study
Withdrawal by Subject
1
0
2
1
2
1
Overall Study
Protocol Violation
0
0
0
0
0
3

Baseline Characteristics

Pyridoxine and Topical Urea/Lactic Acid-Based Cream in Preventing Hand-Foot Syndrome in Patients Receiving Capecitabine for Breast Cancer or Other Cancer

Baseline characteristics by cohort

Baseline characteristics by cohort
Measure
Urea/Lactic Acid Cream
n=67 Participants
Patients receive topical urea/lactic acid-based cream applied to palms and soles twice daily on days 1-21.
Placebo Cream
n=60 Participants
Patients receive placebo cream applied to palms and soles twice daily on days 1-21.
Total
n=127 Participants
Total of all reporting groups
Age, Customized
<50
11 participants
n=5 Participants
9 participants
n=7 Participants
20 participants
n=5 Participants
Age, Customized
50-60
19 participants
n=5 Participants
17 participants
n=7 Participants
36 participants
n=5 Participants
Age, Customized
> 60
37 participants
n=5 Participants
34 participants
n=7 Participants
71 participants
n=5 Participants
Sex: Female, Male
Female
52 Participants
n=5 Participants
49 Participants
n=7 Participants
101 Participants
n=5 Participants
Sex: Female, Male
Male
15 Participants
n=5 Participants
11 Participants
n=7 Participants
26 Participants
n=5 Participants
Region of Enrollment
United States
67 participants
n=5 Participants
60 participants
n=7 Participants
127 participants
n=5 Participants

PRIMARY outcome

Timeframe: First 3 weeks of treatment

Population: Eight patients from the Urea/Lactic Acid group were not included in the primary analysis (1 did not fill out the diary, 1 refused treatment, 3 had adverse events before completing the diary, and 3 for other reasons). For the placebo arm, 11 were excluded (2 refused further treatment, 2 had adverse events, and 7 went off for other reasons).

A patient self-reported hand-foot syndrome (HFSD), also known as palmar-plantar erythrodysesthesia, was completed daily while applying the cream. Patients rated skin severity symptoms individually in their hands and in their feet. Definitions of symptoms, which were based on Common Terminology Criteria for Adverse Events (CTCAE) v3.0, were provided to patients. The number of patients reporting moderate to severe symptoms in either hands or feet were tabulated and percentages are reported.

Outcome measures

Outcome measures
Measure
Urea/Lactic Acid Cream
n=59 Participants
Patients receive topical urea/lactic acid-based cream applied to palms and soles twice daily.
Placebo Cream
n=49 Participants
Patients receive placebo cream applied to palms and soles twice daily.
Arm III: (Placebo +Vit B6)
Patients receive placebo cream applied to palms and soles twice daily and pyridoxine as in Arm I
Arm IV: (Placebo + Placebo)
Patients receive placebo cream and oral placebo.
Arm V: Urea/Lactic Acid
Patients receive topical urea/lactic acid-based cream applied to palms and soles twice daily on days 1-21.
Arm VI: (Placebo)
Patients receive placebo cream applied to palms and soles twice daily on days 1-21.
To Determine Whether the Prophylactic Use of a Topical Urea/Lactic Acid Cream Can Decrease the Incidence/Severity of Capecitabine-caused Palmar-plantar Erythrodysesthesia
13.6 percentage of participants
10.2 percentage of participants

SECONDARY outcome

Timeframe: Up to 4, 21-day cycles

Population: All patients that were evaluated for adverse events were included in this analysis.

Frequency and severity of adverse events reported by patients in weekly diary and evaluated through clinical assessment by NCI CTCAE v3.0. The number of patients reporting grade 3 or higher events are reported in this outcome measure. For a full list of all events, please refer to the Adverse Events section of this report.

Outcome measures

Outcome measures
Measure
Urea/Lactic Acid Cream
n=67 Participants
Patients receive topical urea/lactic acid-based cream applied to palms and soles twice daily.
Placebo Cream
n=63 Participants
Patients receive placebo cream applied to palms and soles twice daily.
Arm III: (Placebo +Vit B6)
Patients receive placebo cream applied to palms and soles twice daily and pyridoxine as in Arm I
Arm IV: (Placebo + Placebo)
Patients receive placebo cream and oral placebo.
Arm V: Urea/Lactic Acid
Patients receive topical urea/lactic acid-based cream applied to palms and soles twice daily on days 1-21.
Arm VI: (Placebo)
Patients receive placebo cream applied to palms and soles twice daily on days 1-21.
To Evaluate the Potential Toxicity of Urea/Lactic Acid Cream
Grade 3+ Adverse Event
21 participants
18 participants
To Evaluate the Potential Toxicity of Urea/Lactic Acid Cream
Grade 4+ Adverse Event
3 participants
3 participants

SECONDARY outcome

Timeframe: First 3 weeks of treatment

Population: This endpoint is not analyzed due to the fact that Vitamin B6 had already been shown to be ineffective. Additionally, any insignificance may be due to lack of power from the smaller (Arms I, II, III and IV) than target sample size.

A patient self-reported hand-foot syndrome diary (HFSD) was completed daily while applying the cream. Patients rated skin severity symptoms individually in their hands and in their feet. Definitions of symptoms, which were based on Common Terminology Criteria for Adverse Events (CTCAE) v3.0, were provided to patients. The number of patients reporting moderate to severe symptoms were tabulated and percentages are reported.

Outcome measures

Outcome data not reported

SECONDARY outcome

Timeframe: up to 4, 21-day cycles

Population: This endpoint is not analyzed due to the fact that Vitamin B6 had already been shown to be ineffective. Additionally, any insignificance may be due to lack of power from the smaller (Arms I, II, III and IV) than target sample size.

Frequency and severity of adverse events reported by patients in weekly diary and evaluated through clinical assessment by NCI CTCAE v3.0. The number of patients reporting grade 3 or higher events are reported in this outcome measure. For a full list of all events, please refer to the Adverse Events section of this report.

Outcome measures

Outcome data not reported

SECONDARY outcome

Timeframe: First 3 weeks of treatment

Population: This endpoint is not analyzed due to the fact that Vitamin B6 had already been shown to be ineffective. Additionally, any insignificance may be due to lack of power from the smaller (Arms I, II, III and IV) than target sample size.

A patient self-reported hand-foot syndrome diary (HFSD) was completed daily while applying the cream. Patients rated skin severity symptoms individually in their hands and in their feet. Definitions of symptoms, which were based on Common Terminology Criteria for Adverse Events (CTCAE) v3.0, were provided to patients. The number of patients reporting moderate to severe symptoms were tabulated.

Outcome measures

Outcome data not reported

Adverse Events

Urea/Lactic Acid Cream

Serious events: 0 serious events
Other events: 56 other events
Deaths: 0 deaths

Placebo Cream

Serious events: 0 serious events
Other events: 50 other events
Deaths: 0 deaths

Serious adverse events

Adverse event data not reported

Other adverse events

Other adverse events
Measure
Urea/Lactic Acid Cream
n=67 participants at risk
Patients receive topical urea/lactic acid-based cream applied to palms and soles twice daily on days 1-21.
Placebo Cream
n=63 participants at risk
Patients receive placebo cream applied to palms and soles twice daily on days 1-21.
Blood and lymphatic system disorders
Febrile neutropenia
0.00%
0/67
1.6%
1/63 • Number of events 1
Blood and lymphatic system disorders
Hemoglobin decreased
0.00%
0/67
1.6%
1/63 • Number of events 1
Cardiac disorders
Arrhythmia supraventricular
1.5%
1/67 • Number of events 1
0.00%
0/63
Cardiac disorders
Atrial fibrillation
1.5%
1/67 • Number of events 1
0.00%
0/63
Gastrointestinal disorders
Abdominal distension
0.00%
0/67
3.2%
2/63 • Number of events 2
Gastrointestinal disorders
Ascites
0.00%
0/67
3.2%
2/63 • Number of events 2
Gastrointestinal disorders
Constipation
1.5%
1/67 • Number of events 1
1.6%
1/63 • Number of events 1
Gastrointestinal disorders
Diarrhea
38.8%
26/67 • Number of events 39
42.9%
27/63 • Number of events 44
Gastrointestinal disorders
Ear, nose and throat examination abnormal
0.00%
0/67
1.6%
1/63 • Number of events 1
Gastrointestinal disorders
Lower gastrointestinal hemorrhage
0.00%
0/67
1.6%
1/63 • Number of events 1
Gastrointestinal disorders
Mucositis oral
1.5%
1/67 • Number of events 1
4.8%
3/63 • Number of events 3
Gastrointestinal disorders
Nausea
6.0%
4/67 • Number of events 4
3.2%
2/63 • Number of events 2
Gastrointestinal disorders
Vomiting
1.5%
1/67 • Number of events 1
6.3%
4/63 • Number of events 4
General disorders
Chest pain
0.00%
0/67
1.6%
1/63 • Number of events 1
General disorders
Death NOS
1.5%
1/67 • Number of events 1
1.6%
1/63 • Number of events 1
General disorders
Disease progression
1.5%
1/67 • Number of events 1
1.6%
1/63 • Number of events 1
General disorders
Fatigue
6.0%
4/67 • Number of events 7
7.9%
5/63 • Number of events 6
General disorders
Multi-organ failure
1.5%
1/67 • Number of events 1
0.00%
0/63
Infections and infestations
Pharyngitis
0.00%
0/67
1.6%
1/63 • Number of events 1
Investigations
Alanine aminotransferase increased
0.00%
0/67
1.6%
1/63 • Number of events 1
Investigations
Aspartate aminotransferase increased
0.00%
0/67
3.2%
2/63 • Number of events 2
Investigations
Coagulopathy
0.00%
0/67
1.6%
1/63 • Number of events 1
Investigations
Electrocardiogram QTc interval prolonged
0.00%
0/67
1.6%
1/63 • Number of events 1
Investigations
Leukocyte count decreased
1.5%
1/67 • Number of events 1
0.00%
0/63
Investigations
Neutrophil count decreased
1.5%
1/67 • Number of events 1
1.6%
1/63 • Number of events 1
Investigations
Platelet count decreased
1.5%
1/67 • Number of events 1
1.6%
1/63 • Number of events 1
Metabolism and nutrition disorders
Anorexia
0.00%
0/67
1.6%
1/63 • Number of events 1
Metabolism and nutrition disorders
Dehydration
9.0%
6/67 • Number of events 6
7.9%
5/63 • Number of events 6
Metabolism and nutrition disorders
Serum albumin decreased
0.00%
0/67
1.6%
1/63 • Number of events 1
Metabolism and nutrition disorders
Serum calcium decreased
0.00%
0/67
1.6%
1/63 • Number of events 1
Metabolism and nutrition disorders
Serum potassium decreased
0.00%
0/67
1.6%
1/63 • Number of events 1
Metabolism and nutrition disorders
Serum sodium decreased
1.5%
1/67 • Number of events 2
1.6%
1/63 • Number of events 1
Musculoskeletal and connective tissue disorders
Back pain
1.5%
1/67 • Number of events 3
1.6%
1/63 • Number of events 3
Musculoskeletal and connective tissue disorders
Bone pain
3.0%
2/67 • Number of events 2
0.00%
0/63
Musculoskeletal and connective tissue disorders
Muscle weakness
1.5%
1/67 • Number of events 1
0.00%
0/63
Musculoskeletal and connective tissue disorders
Muscle weakness lower limb
1.5%
1/67 • Number of events 1
0.00%
0/63
Musculoskeletal and connective tissue disorders
Muscle weakness upper limb
1.5%
1/67 • Number of events 1
0.00%
0/63
Nervous system disorders
Peripheral motor neuropathy
1.5%
1/67 • Number of events 1
1.6%
1/63 • Number of events 1
Nervous system disorders
Peripheral sensory neuropathy
0.00%
0/67
3.2%
2/63 • Number of events 2
Psychiatric disorders
Confusion
3.0%
2/67 • Number of events 2
0.00%
0/63
Renal and urinary disorders
Urinary incontinence
0.00%
0/67
1.6%
1/63 • Number of events 1
Respiratory, thoracic and mediastinal disorders
Dyspnea
1.5%
1/67 • Number of events 1
1.6%
1/63 • Number of events 2
Respiratory, thoracic and mediastinal disorders
Pleural effusion
1.5%
1/67 • Number of events 1
1.6%
1/63 • Number of events 1
Skin and subcutaneous tissue disorders
Alopecia
0.00%
0/67
1.6%
1/63 • Number of events 1
Skin and subcutaneous tissue disorders
Hand-and-foot syndrome
64.2%
43/67 • Number of events 91
54.0%
34/63 • Number of events 60

Additional Information

Charles Lawrence Loprinzi, M.D.

Mayo Clinic

Results disclosure agreements

  • Principal investigator is a sponsor employee
  • Publication restrictions are in place

Restriction type: LTE60