C1 Esterase Inhibitor in Hereditary Angioedema (HAE)(Extension Study)

NCT ID: NCT00292981

Last Updated: 2015-05-07

Study Results

Results available

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Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE3

Total Enrollment

57 participants

Study Classification

INTERVENTIONAL

Study Start Date

2005-08-31

Study Completion Date

2010-05-31

Brief Summary

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Hereditary angioedema (HAE) is a rare disorder characterized by congenital lack of functional C1 esterase inhibitor. If not treated adequately, the acute attacks of HAE can be life-threatening and may even result in fatalities, especially in case of involvement of the larynx.The planned extension study is designed to enrol subjects that participated in the pivotal study in order to provide them with C1-INH for treatment of acute HAE attacks for 24 months or until the licensing procedure for C1-INH is finalized, whatever comes first.

Detailed Description

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Conditions

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Hereditary Angioedema

Study Design

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Allocation Method

NON_RANDOMIZED

Intervention Model

SINGLE_GROUP

Primary Study Purpose

TREATMENT

Blinding Strategy

NONE

Study Groups

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C1 Esterase Inhibitor

Group Type EXPERIMENTAL

C1 Esterase Inhibitor

Intervention Type DRUG

Lyophilisate containing approximately 500 U C1-INH to be reconstituted with 10 mL water for injection; Single Dose: 20 U/kg b.w. iv

Interventions

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C1 Esterase Inhibitor

Lyophilisate containing approximately 500 U C1-INH to be reconstituted with 10 mL water for injection; Single Dose: 20 U/kg b.w. iv

Intervention Type DRUG

Other Intervention Names

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Berinert P

Eligibility Criteria

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Inclusion Criteria

* Documented congenital C1-INH deficiency
* Acute HAE attack
* Participation in base study CE1145\_3001 (NCT00168103)

Exclusion Criteria

* Acquired angioedema
* Treatment with any other investigational drug besides CE1145 in the last 30 days before study entry
Minimum Eligible Age

6 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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CSL Behring

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Program Director

Role: STUDY_DIRECTOR

CSL Behring

Locations

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Weston, Florida, United States

Site Status

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Atlanta, Georgia, United States

Site Status

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Idaho Falls, Idaho, United States

Site Status

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Chicago, Illinois, United States

Site Status

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Shreveport, Louisiana, United States

Site Status

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Boston, Massachusetts, United States

Site Status

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Plymouth, Minnesota, United States

Site Status

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Omaha, Nebraska, United States

Site Status

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Tulsa, Oklahoma, United States

Site Status

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Eugene, Oregon, United States

Site Status

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Hershey, Pennsylvania, United States

Site Status

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Rapid City, South Dakota, United States

Site Status

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Dallas, Texas, United States

Site Status

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Ottawa, Ontario, Canada

Site Status

Countries

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United States Canada

References

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Craig TJ, Wasserman RL, Levy RJ, Bewtra AK, Schneider L, Packer F, Yang WH, Keinecke HO, Kiessling PC. Prospective study of rapid relief provided by C1 esterase inhibitor in emergency treatment of acute laryngeal attacks in hereditary angioedema. J Clin Immunol. 2010 Nov;30(6):823-9. doi: 10.1007/s10875-010-9442-1. Epub 2010 Jul 16.

Reference Type BACKGROUND
PMID: 20635155 (View on PubMed)

Bernstein JA, Machnig T, Keinecke HO, Whelan GJ, Craig TJ. The effect of weight on the efficacy and safety of C1 esterase inhibitor concentrate for the treatment of acute hereditary angioedema. Clin Ther. 2014 Apr 1;36(4):518-25. doi: 10.1016/j.clinthera.2014.02.005. Epub 2014 Mar 21.

Reference Type BACKGROUND
PMID: 24661784 (View on PubMed)

Bork K, Craig TJ, Bernstein JA, Feuersenger H, Machnig T, Staubach P. Efficacy of C1 esterase inhibitor concentrate in treatment of cutaneous attacks of hereditary angioedema. Allergy Asthma Proc. 2015 May-Jun;36(3):218-24. doi: 10.2500/aap.2015.36.3844. Epub 2015 Mar 23.

Reference Type BACKGROUND
PMID: 25803207 (View on PubMed)

Wasserman RL, Levy RJ, Bewtra AK, Hurewitz D, Craig TJ, Kiessling PC, Keinecke HO, Bernstein JA. Prospective study of C1 esterase inhibitor in the treatment of successive acute abdominal and facial hereditary angioedema attacks. Ann Allergy Asthma Immunol. 2011 Jan;106(1):62-8. doi: 10.1016/j.anai.2010.10.012. Epub 2010 Nov 20.

Reference Type RESULT
PMID: 21195947 (View on PubMed)

Craig TJ, Bewtra AK, Bahna SL, Hurewitz D, Schneider LC, Levy RJ, Moy JN, Offenberger J, Jacobson KW, Yang WH, Eidelman F, Janss G, Packer FR, Rojavin MA, Machnig T, Keinecke HO, Wasserman RL. C1 esterase inhibitor concentrate in 1085 Hereditary Angioedema attacks--final results of the I.M.P.A.C.T.2 study. Allergy. 2011 Dec;66(12):1604-11. doi: 10.1111/j.1398-9995.2011.02702.x. Epub 2011 Sep 2.

Reference Type RESULT
PMID: 21884533 (View on PubMed)

Craig TJ, Rojavin MA, Machnig T, Keinecke HO, Bernstein JA. Effect of time to treatment on response to C1 esterase inhibitor concentrate for hereditary angioedema attacks. Ann Allergy Asthma Immunol. 2013 Sep;111(3):211-5. doi: 10.1016/j.anai.2013.06.021. Epub 2013 Jul 16.

Reference Type DERIVED
PMID: 23987198 (View on PubMed)

Craig TJ, Bewtra AK, Hurewitz D, Levy R, Janss G, Jacobson KW, Packer F, Bernstein JA, Rojavin MA, Machnig T, Keinecke HO, Wasserman RL. Treatment response after repeated administration of C1 esterase inhibitor for successive acute hereditary angioedema attacks. Allergy Asthma Proc. 2012 Jul-Aug;33(4):354-61. doi: 10.2500/aap.2012.33.3589.

Reference Type DERIVED
PMID: 22856636 (View on PubMed)

Related Links

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http://www.hereditaryangioedema.com

United States Hereditary Angioedema Association

Other Identifiers

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1453

Identifier Type: OTHER

Identifier Source: secondary_id

CE1145_3003

Identifier Type: -

Identifier Source: org_study_id

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