Trial Outcomes & Findings for Whole-Brain Radiation Therapy and Pemetrexed in Treating Patients With Brain Metastases From Non-Small Cell Lung Cancer (NCT NCT00280748)

NCT ID: NCT00280748

Last Updated: 2017-06-23

Results Overview

Radiographic response will be measured by RECIST, Response Evaluation Criteria In Solid Tumors Criteria, indicating if subject experienced a Complete Response (CR), disappearance of all target lesions; Partial Response (PR), \>=30% decrease in the sum of the longest diameter of target lesions; Stable Disease (SD), no response or less response than Partial or Progressive; or Progressive Disease (PD), as a 20% increase in the sum of the longest diameter of target lesions, or a measurable increase in a non-target lesion, or the appearance of new lesions.

Recruitment status

TERMINATED

Study phase

PHASE2

Target enrollment

10 participants

Primary outcome timeframe

126 days

Results posted on

2017-06-23

Participant Flow

Subjects were recruited from 2 institutions between May 2005 and April 2008.

Participant milestones

Participant milestones
Measure
Single Arm Study
Single Arm Study pemetrexed disodium: 500 mg/m2 once every 21 days up to 126 days radiation therapy: Patients will receive cranial irradiation at 2.5 Gy per fraction, 5 days a week, for 3 weeks to a total dose of 37.5 Gy
Overall Study
STARTED
10
Overall Study
COMPLETED
6
Overall Study
NOT COMPLETED
4

Reasons for withdrawal

Reasons for withdrawal
Measure
Single Arm Study
Single Arm Study pemetrexed disodium: 500 mg/m2 once every 21 days up to 126 days radiation therapy: Patients will receive cranial irradiation at 2.5 Gy per fraction, 5 days a week, for 3 weeks to a total dose of 37.5 Gy
Overall Study
Decline in performance
3
Overall Study
Extra-cranial disease progression
1

Baseline Characteristics

Whole-Brain Radiation Therapy and Pemetrexed in Treating Patients With Brain Metastases From Non-Small Cell Lung Cancer

Baseline characteristics by cohort

Baseline characteristics by cohort
Measure
Single Arm Study
n=10 Participants
Single Arm Study pemetrexed disodium: 500 mg/m2 once every 21 days up to 126 days radiation therapy: Patients will receive cranial irradiation at 2.5 Gy per fraction, 5 days a week, for 3 weeks to a total dose of 37.5 Gy
Age, Continuous
62.5 years
n=5 Participants
Sex: Female, Male
Female
4 Participants
n=5 Participants
Sex: Female, Male
Male
6 Participants
n=5 Participants
Race (NIH/OMB)
American Indian or Alaska Native
1 Participants
n=5 Participants
Race (NIH/OMB)
Asian
0 Participants
n=5 Participants
Race (NIH/OMB)
Native Hawaiian or Other Pacific Islander
0 Participants
n=5 Participants
Race (NIH/OMB)
Black or African American
1 Participants
n=5 Participants
Race (NIH/OMB)
White
8 Participants
n=5 Participants
Race (NIH/OMB)
More than one race
0 Participants
n=5 Participants
Race (NIH/OMB)
Unknown or Not Reported
0 Participants
n=5 Participants
Region of Enrollment
United States
10 participants
n=5 Participants
Karnofsky Performance Status
KPS 90-100; minor symptoms of disease
3 Participants
n=5 Participants
Karnofsky Performance Status
KPS 80-90; some symptoms of disease
0 Participants
n=5 Participants
Karnofsky Performance Status
KPS 70-80; unable to carry on all normal activity
6 Participants
n=5 Participants
Karnofsky Performance Status
KPS unknown
1 Participants
n=5 Participants

PRIMARY outcome

Timeframe: 126 days

Population: Of the 10 patients, four patients were unevaluable due to extra-cranial disease progression or decline in performance status prevent re-evaluation.

Radiographic response will be measured by RECIST, Response Evaluation Criteria In Solid Tumors Criteria, indicating if subject experienced a Complete Response (CR), disappearance of all target lesions; Partial Response (PR), \>=30% decrease in the sum of the longest diameter of target lesions; Stable Disease (SD), no response or less response than Partial or Progressive; or Progressive Disease (PD), as a 20% increase in the sum of the longest diameter of target lesions, or a measurable increase in a non-target lesion, or the appearance of new lesions.

Outcome measures

Outcome measures
Measure
Single Arm Study
n=6 Participants
Single Arm Study pemetrexed disodium: 500 mg/m2 once every 21 days up to 126 days radiation therapy: Patients will receive cranial irradiation at 2.5 Gy per fraction, 5 days a week, for 3 weeks to a total dose of 37.5 Gy
Response of Intracranial Metastases (Complete and Partial Response)
partial response
1 Participants
Response of Intracranial Metastases (Complete and Partial Response)
stable disease
3 Participants
Response of Intracranial Metastases (Complete and Partial Response)
progressive disease
2 Participants

SECONDARY outcome

Timeframe: maximum 5 months

Population: All patients who received treatment were evaluated

Toxicities was assessed using Common Terminology Criteria for Adverse Events (CTCAE) grading scale. Only toxicities with attribution to chemotherapy of "definite" or "probable" are considered, as determined by treating physician.

Outcome measures

Outcome measures
Measure
Single Arm Study
n=10 Participants
Single Arm Study pemetrexed disodium: 500 mg/m2 once every 21 days up to 126 days radiation therapy: Patients will receive cranial irradiation at 2.5 Gy per fraction, 5 days a week, for 3 weeks to a total dose of 37.5 Gy
Number of Subjects Experiencing Adverse Events
Acute bronchitis
1 Participants
Number of Subjects Experiencing Adverse Events
Blurred vision
1 Participants
Number of Subjects Experiencing Adverse Events
Dry skin
1 Participants
Number of Subjects Experiencing Adverse Events
Fatigue
2 Participants
Number of Subjects Experiencing Adverse Events
Anemia
2 Participants
Number of Subjects Experiencing Adverse Events
Alpecia
2 Participants
Number of Subjects Experiencing Adverse Events
Nausea
6 Participants
Number of Subjects Experiencing Adverse Events
Anorexia
1 Participants
Number of Subjects Experiencing Adverse Events
Pruritic rash on head
1 Participants
Number of Subjects Experiencing Adverse Events
Cramps
1 Participants

SECONDARY outcome

Timeframe: 4 years

Population: Four patients were unevaluable due to extra-cranial disease progression or decline in performance status preventing re-evaluation.

Patients were followed for survival from start of treatment until death from any cause (up to 4 years)

Outcome measures

Outcome measures
Measure
Single Arm Study
n=6 Participants
Single Arm Study pemetrexed disodium: 500 mg/m2 once every 21 days up to 126 days radiation therapy: Patients will receive cranial irradiation at 2.5 Gy per fraction, 5 days a week, for 3 weeks to a total dose of 37.5 Gy
Estimate the Overall Survival of Patients Treated With This Regimen.
6.0 months
Interval 1.7 to 8.3

SECONDARY outcome

Timeframe: baseline functional status only

Functional status evaluated using the Karnofsky functional status scale. The Karnofsky Performance Scale (KPS) Index allows patients to be classified as to their functional impairment. This can be used to compare effectiveness of different therapies and to assess the prognosis in individual patients. The lower the Karnofsky score, the worse the survival for most serious illnesses. The Karnofsky score runs from 100 to 0, where 100 is "perfect" health and 0 is death.

Outcome measures

Outcome measures
Measure
Single Arm Study
n=10 Participants
Single Arm Study pemetrexed disodium: 500 mg/m2 once every 21 days up to 126 days radiation therapy: Patients will receive cranial irradiation at 2.5 Gy per fraction, 5 days a week, for 3 weeks to a total dose of 37.5 Gy
Evaluate the Functional Status of Patients Treated With This Regimen.
KPS 90-100; minor symptoms of disease
3 Participants
Evaluate the Functional Status of Patients Treated With This Regimen.
KPS 80-90; some symptoms of disease
0 Participants
Evaluate the Functional Status of Patients Treated With This Regimen.
KPS 70-80; unable to carry on all normal activity
6 Participants
Evaluate the Functional Status of Patients Treated With This Regimen.
KPS unknown
1 Participants

SECONDARY outcome

Timeframe: At Baseline, 30 days, and at end of treatment (maximum 5 months).

Population: This study was terminated due to slow enrollment and the planned statistical analyses could not be performed due to limit sample size. The data represents the results of patients enrolled and treated on the trial.

A classification score defined as follows: 1. Able to work or to perform normal activities: neurological findings minor or absent 2. Able to carry out normal activities with minimal difficulties. Neurological impairment does not require nursing care or hospitalization 3. Seriously limited in performing normal activities. Requiring nursing care or hospitalization. Patients confined to bed or wheelchair or have significant intellectual impairment 4. Unable to perform even minimal normal activities. Requiring hospitalization and constant nursing care and feeding. Patients unable to communicate or in coma.A higher score indicates worse function.

Outcome measures

Outcome measures
Measure
Single Arm Study
n=10 Participants
Single Arm Study pemetrexed disodium: 500 mg/m2 once every 21 days up to 126 days radiation therapy: Patients will receive cranial irradiation at 2.5 Gy per fraction, 5 days a week, for 3 weeks to a total dose of 37.5 Gy
Neurological Function by Radiation Oncology Group (RTOG) Neurological Function Classification
Pre-Treatment
1.6 scores on a scale
Interval 1.0 to 2.0
Neurological Function by Radiation Oncology Group (RTOG) Neurological Function Classification
Cycle 2
1.9 scores on a scale
Interval 1.0 to 3.0
Neurological Function by Radiation Oncology Group (RTOG) Neurological Function Classification
End of Treatment
2.2 scores on a scale
Interval 1.0 to 3.0

SECONDARY outcome

Timeframe: Baseline (pre-treatment), 30 days (Cycle 2 Day 1), and maximum 5 months (end of treatment).

Population: This study was terminated due to slow enrollment and the planned statistical analyses could not be performed due to limited sample size. The data represents the results of patients enrolled and treated on the trial.

The Mini Mental State Examination is a 30-point questionnaire that is used to measure cognitive impairment. Score totals range from normal cognition (24-30 points), mild impairment (19-23 points), moderate impairment (10-18 points), to severe impairment (≤9 points).

Outcome measures

Outcome measures
Measure
Single Arm Study
n=10 Participants
Single Arm Study pemetrexed disodium: 500 mg/m2 once every 21 days up to 126 days radiation therapy: Patients will receive cranial irradiation at 2.5 Gy per fraction, 5 days a week, for 3 weeks to a total dose of 37.5 Gy
Neurological Function by Mini Mental State Examination
Pre-Treatment
28 score on the scale
Interval 24.0 to 30.0
Neurological Function by Mini Mental State Examination
Cycle 2 Day 1
28.2 score on the scale
Interval 25.0 to 30.0
Neurological Function by Mini Mental State Examination
End of treatment
27.7 score on the scale
Interval 21.0 to 30.0

SECONDARY outcome

Timeframe: maximum 5 months

Population: This study was terminated due to slow enrollment and the planned statistical analyses could not be performed due to limit sample size. The data represents the results of patients enrolled and treated on the trial.

Response was measured by Response Evaluation Criteria In Solid Tumors RECIST criteria v1.0. Complete Response (CR) - Disappearance of all lesions Partial Response (PR) - at least a 30% decrease in the sum of the longest diameter of target lesions, taking as reference the baseline sum longest diameter. Stable Disease (SD) - neither sufficient shrinkage to qualify for partial response nor sufficient increase to qualify for progressive disease, taking as reference the smallest sum longest diameter since the treatment started. Progressive Disease (PD) - at least a 20% increase in the sum of the longest diameter of target lesions, taking as reference the smallest sum longest diameter recorded since the treatment started or the appearance of one or more new lesions or unequivocal progression of existing nontarget lesions.

Outcome measures

Outcome measures
Measure
Single Arm Study
n=10 Participants
Single Arm Study pemetrexed disodium: 500 mg/m2 once every 21 days up to 126 days radiation therapy: Patients will receive cranial irradiation at 2.5 Gy per fraction, 5 days a week, for 3 weeks to a total dose of 37.5 Gy
Response of Patients With Extracranial Disease Treated With Pemetrexed
partial response
2 Participants
Response of Patients With Extracranial Disease Treated With Pemetrexed
stable disease
3 Participants
Response of Patients With Extracranial Disease Treated With Pemetrexed
progressive disease
1 Participants
Response of Patients With Extracranial Disease Treated With Pemetrexed
missing data
4 Participants

Adverse Events

Single Arm Study

Serious events: 1 serious events
Other events: 10 other events
Deaths: 10 deaths

Serious adverse events

Serious adverse events
Measure
Single Arm Study
n=10 participants at risk
Single Arm Study pemetrexed disodium: 500 mg/m2 once every 21 days up to 126 days radiation therapy: Patients will receive cranial irradiation at 2.5 Gy per fraction, 5 days a week, for 3 weeks to a total dose of 37.5 Gy
Vascular disorders
pulmonary embolus
10.0%
1/10 • Number of events 1 • Adverse events were monitored up to 30 days after end of treatment
Nervous system disorders
Dizziness
10.0%
1/10 • Number of events 1 • Adverse events were monitored up to 30 days after end of treatment
Nervous system disorders
hallucinations
10.0%
1/10 • Number of events 1 • Adverse events were monitored up to 30 days after end of treatment

Other adverse events

Other adverse events
Measure
Single Arm Study
n=10 participants at risk
Single Arm Study pemetrexed disodium: 500 mg/m2 once every 21 days up to 126 days radiation therapy: Patients will receive cranial irradiation at 2.5 Gy per fraction, 5 days a week, for 3 weeks to a total dose of 37.5 Gy
General disorders
Right maxillary pain with drainage
10.0%
1/10 • Number of events 1 • Adverse events were monitored up to 30 days after end of treatment
Blood and lymphatic system disorders
Anemia
20.0%
2/10 • Number of events 2 • Adverse events were monitored up to 30 days after end of treatment
Blood and lymphatic system disorders
face/upper/lower extremity swelling
10.0%
1/10 • Number of events 1 • Adverse events were monitored up to 30 days after end of treatment
Blood and lymphatic system disorders
swelling-lower extremities
10.0%
1/10 • Number of events 1 • Adverse events were monitored up to 30 days after end of treatment
Eye disorders
Blurred vision
10.0%
1/10 • Number of events 1 • Adverse events were monitored up to 30 days after end of treatment
Eye disorders
Dry Eyes
10.0%
1/10 • Number of events 1 • Adverse events were monitored up to 30 days after end of treatment
Gastrointestinal disorders
Anorexia
40.0%
4/10 • Number of events 4 • Adverse events were monitored up to 30 days after end of treatment
Gastrointestinal disorders
Constipation
20.0%
2/10 • Number of events 2 • Adverse events were monitored up to 30 days after end of treatment
Gastrointestinal disorders
Diarrhea
10.0%
1/10 • Number of events 1 • Adverse events were monitored up to 30 days after end of treatment
Gastrointestinal disorders
Flatulence
10.0%
1/10 • Number of events 1 • Adverse events were monitored up to 30 days after end of treatment
Gastrointestinal disorders
Hemmorroids
10.0%
1/10 • Number of events 1 • Adverse events were monitored up to 30 days after end of treatment
Gastrointestinal disorders
Mucositis
10.0%
1/10 • Number of events 1 • Adverse events were monitored up to 30 days after end of treatment
Gastrointestinal disorders
Nausea
80.0%
8/10 • Number of events 8 • Adverse events were monitored up to 30 days after end of treatment
Gastrointestinal disorders
Vomiting
10.0%
1/10 • Number of events 1 • Adverse events were monitored up to 30 days after end of treatment
General disorders
abdominal pain
10.0%
1/10 • Number of events 1 • Adverse events were monitored up to 30 days after end of treatment
General disorders
chest pain
10.0%
1/10 • Number of events 1 • Adverse events were monitored up to 30 days after end of treatment
General disorders
Headache
20.0%
2/10 • Number of events 2 • Adverse events were monitored up to 30 days after end of treatment
General disorders
Hip pain
10.0%
1/10 • Number of events 1 • Adverse events were monitored up to 30 days after end of treatment
General disorders
left lower quadrant pain
10.0%
1/10 • Number of events 1 • Adverse events were monitored up to 30 days after end of treatment
General disorders
Pain
10.0%
1/10 • Number of events 1 • Adverse events were monitored up to 30 days after end of treatment
General disorders
rib cage pain
10.0%
1/10 • Number of events 1 • Adverse events were monitored up to 30 days after end of treatment
General disorders
right foot 4th toes numbness
10.0%
1/10 • Number of events 1 • Adverse events were monitored up to 30 days after end of treatment
Infections and infestations
Acute bronchitis
10.0%
1/10 • Number of events 1 • Adverse events were monitored up to 30 days after end of treatment
Infections and infestations
UTI
10.0%
1/10 • Number of events 2 • Adverse events were monitored up to 30 days after end of treatment
Metabolism and nutrition disorders
difficulty sleeping
10.0%
1/10 • Number of events 1 • Adverse events were monitored up to 30 days after end of treatment
Metabolism and nutrition disorders
fatigue
20.0%
2/10 • Number of events 2 • Adverse events were monitored up to 30 days after end of treatment
Metabolism and nutrition disorders
Hypokalemia
10.0%
1/10 • Number of events 1 • Adverse events were monitored up to 30 days after end of treatment
Metabolism and nutrition disorders
Hyponatremia
10.0%
1/10 • Number of events 1 • Adverse events were monitored up to 30 days after end of treatment
Metabolism and nutrition disorders
weakness
20.0%
2/10 • Number of events 2 • Adverse events were monitored up to 30 days after end of treatment
Metabolism and nutrition disorders
weight loss
20.0%
2/10 • Number of events 2 • Adverse events were monitored up to 30 days after end of treatment
Musculoskeletal and connective tissue disorders
Cramps
10.0%
1/10 • Number of events 1 • Adverse events were monitored up to 30 days after end of treatment
Nervous system disorders
Anxiety
20.0%
2/10 • Number of events 2 • Adverse events were monitored up to 30 days after end of treatment
Nervous system disorders
Confusion
30.0%
3/10 • Number of events 3 • Adverse events were monitored up to 30 days after end of treatment
Nervous system disorders
depression
20.0%
2/10 • Number of events 2 • Adverse events were monitored up to 30 days after end of treatment
Nervous system disorders
Left eye visual disturbance
10.0%
1/10 • Number of events 1 • Adverse events were monitored up to 30 days after end of treatment
Nervous system disorders
memory impairment
10.0%
1/10 • Number of events 1 • Adverse events were monitored up to 30 days after end of treatment
Nervous system disorders
Transient ischemic attack
10.0%
1/10 • Number of events 1 • Adverse events were monitored up to 30 days after end of treatment
Renal and urinary disorders
Dysuria
10.0%
1/10 • Number of events 1 • Adverse events were monitored up to 30 days after end of treatment
Respiratory, thoracic and mediastinal disorders
cough
10.0%
1/10 • Number of events 1 • Adverse events were monitored up to 30 days after end of treatment
Respiratory, thoracic and mediastinal disorders
dyspnea
30.0%
3/10 • Number of events 3 • Adverse events were monitored up to 30 days after end of treatment
Skin and subcutaneous tissue disorders
Alopecia
30.0%
3/10 • Number of events 3 • Adverse events were monitored up to 30 days after end of treatment
Skin and subcutaneous tissue disorders
dry skin
10.0%
1/10 • Number of events 1 • Adverse events were monitored up to 30 days after end of treatment
Skin and subcutaneous tissue disorders
Erythemic/vesicular papule-right temple
10.0%
1/10 • Number of events 1 • Adverse events were monitored up to 30 days after end of treatment
Skin and subcutaneous tissue disorders
insect bite
10.0%
1/10 • Number of events 1 • Adverse events were monitored up to 30 days after end of treatment
Skin and subcutaneous tissue disorders
pruritic rash on head
10.0%
1/10 • Number of events 1 • Adverse events were monitored up to 30 days after end of treatment
Vascular disorders
INR
10.0%
1/10 • Number of events 1 • Adverse events were monitored up to 30 days after end of treatment
Vascular disorders
Nosebleed
10.0%
1/10 • Number of events 1 • Adverse events were monitored up to 30 days after end of treatment

Additional Information

Robin V. Johnson

UNC Lineberger Comprehensive Cancer Center

Phone: 919-966-1125

Results disclosure agreements

  • Principal investigator is a sponsor employee
  • Publication restrictions are in place