Fludarabine With or Without Cyclophosphamide in Treating Patients With Advanced Chronic Lymphocytic Leukemia

NCT ID: NCT00276848

Last Updated: 2019-05-23

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE3

Total Enrollment

375 participants

Study Classification

INTERVENTIONAL

Study Start Date

1999-07-31

Study Completion Date

2007-07-31

Brief Summary

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RATIONALE: Drugs used in chemotherapy, such as fludarabine and cyclophosphamide, work in different ways to stop the growth of cancer cells, either by killing the cells or by stopping them from dividing. It is not yet known whether giving fludarabine together with cyclophosphamide is more effective than fludarabine alone in treating chronic lymphocytic leukemia.

PURPOSE: This randomized phase III trial is studying giving fludarabine together with cyclophosphamide to see how well it works compared to fludarabine alone in treating patients with advanced chronic lymphocytic leukemia.

Detailed Description

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OBJECTIVES:

Primary

* Compare the progression-free survival, as well the overall survival and duration of remission in patients with previously untreated, advanced chronic lymphocytic leukemia treated with fludarabine with versus without cyclophosphamide.

Secondary

* Compare the incidence of side effects and quality of life of patients treated with these drugs.

OUTLINE: This is a multicenter, randomized study. Patients are randomized to 1 of 2 treatment arms

* Arm I: Patients receive fludarabine IV on days 1-5.
* Arm II: Patients receive fludarabine IV and cyclophosphamide IV on days 1-3. In both arms, treatment repeats every 28 days for up to 6 courses in the absence of disease progression or unacceptable toxicity.

PROJECTED ACCRUAL: A total of 375 patients will be accrued for this study.

Conditions

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Chronic Lymphocytic Leukemia

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

NONE

Study Groups

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Fludarabine plus Cyclophosphamide

Group Type ACTIVE_COMPARATOR

Fludarabine plus Cyclophosphamide

Intervention Type DRUG

fludarabine at a dose of 25 mg/m2, administered intravenously daily over 30 minutes for 5 days, or fludarabine dosed at 30 mg/m2, administered intravenously daily over 30 minutes for 3 days, plus cyclophosphamide dosed at 250 mg/m2, administered intravenously daily over 30 minutes for 3 days, repeated every 28 days for a maximum of 6 courses

Fludarabine

Group Type ACTIVE_COMPARATOR

Fludarabine

Intervention Type DRUG

fludarabine at a dose of 25 mg/m2, administered intravenously daily over 30 minutes for 5 days, or fludarabine dosed at 30 mg/m2, administered intravenously daily over 30 minutes for 3 days, , repeated every 28 days for a maximum of 6 courses

Interventions

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Fludarabine plus Cyclophosphamide

fludarabine at a dose of 25 mg/m2, administered intravenously daily over 30 minutes for 5 days, or fludarabine dosed at 30 mg/m2, administered intravenously daily over 30 minutes for 3 days, plus cyclophosphamide dosed at 250 mg/m2, administered intravenously daily over 30 minutes for 3 days, repeated every 28 days for a maximum of 6 courses

Intervention Type DRUG

Fludarabine

fludarabine at a dose of 25 mg/m2, administered intravenously daily over 30 minutes for 5 days, or fludarabine dosed at 30 mg/m2, administered intravenously daily over 30 minutes for 3 days, , repeated every 28 days for a maximum of 6 courses

Intervention Type DRUG

Eligibility Criteria

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Inclusion Criteria

DISEASE CHARACTERISTICS:

* Confirmed diagnosis of previously untreated chronic lymphocytic leukemia (CLL)

* Binet stage C and stage B are acceptable if there is rapid disease progression, symptoms of enlarged lymph nodes and organs, or severe B-symptoms
* Binet stage A is acceptable, if there are B-symptoms

PATIENT CHARACTERISTICS:

* ECOG performance status 0-2
* Life expectancy \> 6 months
* No severe organ dysfunction
* No other previous or concurrent neoplasms, autoimmune hemolytic anemia, or thrombocytopenia

PRIOR CONCURRENT THERAPY:

* No prior or concurrent chemotherapy
Minimum Eligible Age

18 Years

Maximum Eligible Age

65 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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German CLL Study Group

OTHER

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Michael Hallek, MD

Role: STUDY_CHAIR

Medizinische Universitaetsklinik I at the University of Cologne

Locations

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Allgemeines Krankenhaus - Universitatskliniken

Vienna, , Austria

Site Status

Hanuschkrankenhaus

Vienna, , Austria

Site Status

Gemeinschaftspraxis Fuer Innere Medizin, Haematologie Und Internistische Onkologie

Ansbach, , Germany

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Internistische Praxis - Arnstadt

Arnstadt, , Germany

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Specialist Practice for Oncology

Aschaffenburg, , Germany

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Klinikum Augsburg

Augsburg, , Germany

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Kreiskrankenhaus Aurich

Aurich, , Germany

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Kreiskrankenhaus

Bad Hersfeld, , Germany

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Caritas-Krankenhaus Bad Mergentheim

Bad Mergentheim, , Germany

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Humaine - Clinic

Bad Saarow, , Germany

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Internistische Praxis - Bad Salzuflen

Bad Salzuflen, , Germany

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Internistische Praxis - Bayreuth

Bayreuth, , Germany

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Internistische Gemeinschaftspraxis - Bergisch Gladbach

Bergisch Gladbach, , Germany

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Charite - Campus Charite Mitte

Berlin, , Germany

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Onkolog - Haematolog Schwerpunktpraxis

Berlin, , Germany

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Charite - Universitaetsmedizin Berlin - Campus Benjamin Franklin

Berlin, , Germany

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Onkologische Gemeinschaftspraxis - Berlin

Berlin, , Germany

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Robert Roessle Comprehensive Cancer Center at University of Berlin - Charite Campus Buch

Berlin, , Germany

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Internistische Gemeinschaftspraxis - Berlin

Berlin, , Germany

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Charite - Campus Virchow Klinikum

Berlin, , Germany

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Evang. Waldkrankenhaus Spandau

Berlin, , Germany

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Internistische Praxis - Berlin

Berlin, , Germany

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Internistische Gemeinschaftspraxis - Berlin

Berlin, , Germany

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Krankenhaus Bietigheim

Bietigheim, , Germany

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DIAKO Ev. Diakonie Krankenhaus gGmbH

Bremen, , Germany

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Internistische Praxis - Chemnitz

Chemnitz, , Germany

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Praxis Fuer Haematologie Internistische Onkologie

Cologne, , Germany

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Medizinische Universitaetsklinik I at the University of Cologne

Cologne, , Germany

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Onkologische Schwerpunktpraxis

Cottbus, , Germany

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Onkologische Gemeinschaftspraxis - Dresden

Dresden, , Germany

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Krankenhaus Benrath

Düsseldorf, , Germany

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St. Georg Klinikum Eisenach GmbH

Eisenach, , Germany

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Hans - Susemihl - Krankenhaus

Emden, , Germany

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Internistische/Onkologische Praxis - Erfurt

Erfurt, , Germany

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Praxis DR. J. Weniger

Erfurt, , Germany

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Klinikum Erfurt

Erfurt, , Germany

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Praxis fuer Haematologie/Onkologie - Erfurt

Erfurt, , Germany

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Onkologische Schwerpunkt Praxis

Erlangen, , Germany

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St. Antonius Hospital

Eschweiler, , Germany

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Universitaetsklinikum Essen

Essen, , Germany

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Onkologische Praxis - Essen

Essen, , Germany

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Evangelisches Krankenhaus Essen Werden

Essen, , Germany

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Staedtische Kliniken Esslingen

Esslingen am Neckar, , Germany

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Internistische Gemeinschaftspraxis - Forchheim

Forchheim, , Germany

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Klinikum Frankfurt (Oder) GmbH

Frankfurt, , Germany

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Gemeinschaftspraxis - Freiburg

Freiburg im Breisgau, , Germany

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Klinikum Garmisch - Partenkirchen GmbH

Garmisch-Partenkirchen, , Germany

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Internistische Praxis - Gerlingen

Gerlingen, , Germany

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Internistische Praxisgemeinschaft

Germering, , Germany

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Gemeinschaftspraxis Fuer Innere Medizin, Hematologie Und Onkologie

Giessen, , Germany

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Klinik fuer Radioonkologie und Strahlentherapie

Göppingen, , Germany

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Universitaetsklinikum Goettingen

Göttingen, , Germany

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Klinik Fuer Innere Medizin, Hematology/Oncology, Ernst Moritz Armdt Universitaet

Greifswald, , Germany

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Praxis fuer Haematologie und Internistische Onkologie - Greifswald

Greifswald, , Germany

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Internistisch-Haematologische Gemeinschaftspraxis - Gustrow

Güstrow, , Germany

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St. Marien Hospital - Katholisches Krankenhaus Hagen gGmbH

Hagen, , Germany

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Internistische Praxis - Halle

Halle, , Germany

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Internistische Gemeinschaftspraxis - Halle

Halle, , Germany

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Asklepios Klinik St. Georg

Hamburg, , Germany

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Universitaetsklinikum Hamburg-Eppendorf

Hamburg, , Germany

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Evangelische Krankenhaus Hamm

Hamm, , Germany

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St. Marien-Hospital Hamm - Klinik Knappenstrasse

Hamm, , Germany

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Schwerpunktpraxis Haematologie/Onkologie - Hannover

Hanover, , Germany

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Universitaets-Kinderklinik Heidelberg

Heidelberg, , Germany

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SLK - Kliniken Heilbronn GmbH - Klinikum am Gesundbrunnen

Heilbronn, , Germany

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Privatklinik Dr. R. Schindlbeck GmbH & Co. KG

Herrsching am Ammersee, , Germany

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Onkologische Schwerpunktpraxis

Hildesheim, , Germany

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Evang. Hospital

Holzminden, , Germany

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Universitaetsklinikum des Saarlandes

Homburg, , Germany

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Onkologische Gemeinschaftspraxis - Hoevelhof

Hövelhof, , Germany

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Clinic for Bone Marrow Transplantation and Hematology and Oncology

Idar-Oberstein, , Germany

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Internistische Praxis - Ingolstadt

Ingolstadt, , Germany

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Internistische Gemeinschaftspraxis - Jena

Jena, , Germany

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Westpfalz-Klinikum GmbH

Kaiserslautern, , Germany

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Onkologische Gemeinschaftspraxis - Kaiserslautern

Kaiserslautern, , Germany

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Staedtisches Klinikum Karlsruhe gGmbH

Karlsruhe, , Germany

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St. Vincentius-Kliniken

Karlsruhe, , Germany

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Internistische Gemeinschaftspraxis - Kassel

Kassel, , Germany

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Klinikum Kempten Oberallgaeu

Kempten, , Germany

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University Hospital Schleswig-Holstein - Kiel Campus

Kiel, , Germany

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Internistische Onkologische Praxis - Kronach

Kronach, , Germany

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Internistische Praxis - Landshut

Landshut, , Germany

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Onkologische Schwerpunktpraxis - Leer

Leer, , Germany

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Klinikum Lippe - Lemgo

Lemgo, , Germany

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Internistische Praxis - Ludwigsburg

Ludwigsburg, , Germany

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Staedtisches Klinikum Magdeburg - Altstadt

Magdeburg, , Germany

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Universitaetsklinkum Magdeburg der Otto-von-Guericke-Universitaet Magdeburg

Magdeburg, , Germany

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III Medizinische Klinik Mannheim

Mannheim, , Germany

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Haematologische Praxis - Moenchengladbach

Mönchengladbach, , Germany

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Internistische Praxis - Muhr am See

Muhr am See, , Germany

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Klinikum der Universitaet Muenchen - Innenstadt Campus

Munich, , Germany

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Munich Oncologic Practice at Elisenhof

Munich, , Germany

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Krankenhaus Muenchen Schwabing

Munich, , Germany

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Klinikum der Universitaet Muenchen - Grosshadern Campus

Munich, , Germany

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Klinikum Rechts Der Isar - Technische Universitaet Muenchen

Munich, , Germany

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Hamatologie/Onkologie Praxisgemeinschaft - Muenchen

München, , Germany

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University of Muenster

Münster, , Germany

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Onkologische Schwerpunktpraxis Dr. Schmidt

Neunkirchen, , Germany

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Praxis fuer Haematologie und Interne Onkologie

Norderstedt, , Germany

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Sudharz-Krankenhaus Nordhausen gGmbH

Nordhausen, , Germany

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Klinikum Nuernberg - Klinikum Nord

Nuremberg, , Germany

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Internistische Gemeinschaftspraxis - Offenbach

Offenbach, , Germany

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Internistische Gemeinschaftspraxis - Oldenburg

Oldenburg, , Germany

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Paracelsus Karankenhaus Ruit

Ostfildern, , Germany

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Asklepios Klinik Pasewalk

Pasewalk, , Germany

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Vogtland - Klinikum Plauen GMBH

Plauen, , Germany

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Klinikum Ernst Von Bergmann

Postdam, , Germany

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Internistische Gemeinschaftspraxis - Potsdam

Potsdam, , Germany

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Krankenhaus Barmherzige Brueder Regensburg

Regensburg, , Germany

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Staedtische Klinikum-Kinderklinik

Rosenheim, , Germany

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Haematologische/Onkologische Schwerpunktpraxis - Rostock

Rostock, , Germany

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Klinik und Poliklinik fuer Innere Medizin - Universitaet Rostock

Rostock, , Germany

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Schwerpunktpraxis fuer Haematologie und Onkologie

Saarbruecke, , Germany

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Caritasklinik St. Theresia

Saarbrücken, , Germany

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Klinikum Schwerin

Schwerin, , Germany

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St. Marien - Krankenhaus Siegen GMBH

Siegen, , Germany

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Haematologische Praxis

Stuttgart, , Germany

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Klinik fuer Onkologie - Katharinenhospital Stuttgart

Stuttgart, , Germany

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Diakonie Klinikum Stuttgart

Stuttgart, , Germany

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Internistische Gemeinschaftspraxis - Stuttgart

Stuttgart, , Germany

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Marienhospital Stuttgart

Stuttgart, , Germany

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Robert-Bosch-Krankenhaus

Stuttgart, , Germany

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Krankenanstalt Mutterhaus der Borromaerinnen

Trier, , Germany

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Onkologische Gemeinschaftspraxis - Trier

Trier, , Germany

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Schwerpunktpraxis für Rheumatologie und Haematologie/Internistische Onkologie

Tübingen, , Germany

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Southwest German Cancer Center at Eberhard-Karls-University

Tübingen, , Germany

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Comprehensive Cancer Center Ulm at Universitaetsklinikum Ulm

Ulm, , Germany

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St. Marienhospital - Vechta

Vechta, , Germany

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Haematologisch-Onkologische Schwerpunktpraxis - Weilheim

Weilheim, , Germany

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Internistische Praxis - Wendlingen

Wendlingen, , Germany

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Gemeinschaftspraxis

Worms, , Germany

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Kliniken St. Antonius

Wuppertal, , Germany

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Hamatologisch - Onkologische Praxis Wurzburg

Würzburg, , Germany

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Medizinische Klinik und Poliklinik II - Universitaetsklinikum Wuerzburg

Würzburg, , Germany

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Internistische Praxis - Zittau

Zittau, , Germany

Site Status

Countries

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Austria Germany

References

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Eichhorst BF, Fischer K, Fink AM, Elter T, Wendtner CM, Goede V, Bergmann M, Stilgenbauer S, Hopfinger G, Ritgen M, Bahlo J, Busch R, Hallek M; German CLL Study Group (GCLLSG). Limited clinical relevance of imaging techniques in the follow-up of patients with advanced chronic lymphocytic leukemia: results of a meta-analysis. Blood. 2011 Feb 10;117(6):1817-21. doi: 10.1182/blood-2010-04-282228. Epub 2010 Dec 7.

Reference Type BACKGROUND
PMID: 21139079 (View on PubMed)

Cramer P, Bahlo J, Eichhorst B, Fischer K, Hallek M. Extramedullary manifestations of chronic lymphocytic leukaemia are not unusual. Leuk Res. 2014 Mar;38(3):284-5. doi: 10.1016/j.leukres.2013.11.015. Epub 2013 Dec 1. No abstract available.

Reference Type BACKGROUND
PMID: 24412156 (View on PubMed)

Goede V, Cramer P, Busch R, Bergmann M, Stauch M, Hopfinger G, Stilgenbauer S, Dohner H, Westermann A, Wendtner CM, Eichhorst B, Hallek M; German CLL Study Group. Interactions between comorbidity and treatment of chronic lymphocytic leukemia: results of German Chronic Lymphocytic Leukemia Study Group trials. Haematologica. 2014 Jun;99(6):1095-100. doi: 10.3324/haematol.2013.096792. Epub 2014 Feb 28.

Reference Type BACKGROUND
PMID: 24584349 (View on PubMed)

Jebaraj BMC, Tausch E, Landau DA, Bahlo J, Robrecht S, Taylor-Weiner AN, Bloehdorn J, Scheffold A, Mertens D, Bottcher S, Kneba M, Jager U, Zenz T, Wenger MK, Fingerle-Rowson G, Wendtner C, Fink AM, Wu CJ, Eichhorst B, Fischer K, Hallek M, Dohner H, Stilgenbauer S. Short telomeres are associated with inferior outcome, genomic complexity, and clonal evolution in chronic lymphocytic leukemia. Leukemia. 2019 Sep;33(9):2183-2194. doi: 10.1038/s41375-019-0446-4. Epub 2019 Mar 25.

Reference Type BACKGROUND
PMID: 30911113 (View on PubMed)

Sachanas S, Pangalis GA, Fink AM, Bahlo J, Fischer K, Levidou G, Kyrtsonis MC, Bartzi V, Vassilakopoulos TP, Kalpadakis C, Koulieris E, Moschogiannis M, Yiakoumis X, Tsirkinidis P, Angelopoulou MK, Eichhorst B, Hallek M. Small Lymphocytic Lymphoma: Analysis of Two Cohorts Including Patients in Clinical Trials of the German Chronic Lymphocytic Leukemia Study Group (GCLLSG) or in "Real-Life" Outside of Clinical Trials. Anticancer Res. 2019 May;39(5):2591-2598. doi: 10.21873/anticanres.13382.

Reference Type BACKGROUND
PMID: 31092457 (View on PubMed)

Eichhorst BF, Busch R, Obwandner T, Kuhn-Hallek I, Herschbach P, Hallek M; German CLL Study Group. Health-related quality of life in younger patients with chronic lymphocytic leukemia treated with fludarabine plus cyclophosphamide or fludarabine alone for first-line therapy: a study by the German CLL Study Group. J Clin Oncol. 2007 May 1;25(13):1722-31. doi: 10.1200/JCO.2006.05.6929. Epub 2007 Mar 26.

Reference Type RESULT
PMID: 17389338 (View on PubMed)

Eichhorst BF, Busch R, Hopfinger G, Pasold R, Hensel M, Steinbrecher C, Siehl S, Jager U, Bergmann M, Stilgenbauer S, Schweighofer C, Wendtner CM, Dohner H, Brittinger G, Emmerich B, Hallek M; German CLL Study Group. Fludarabine plus cyclophosphamide versus fludarabine alone in first-line therapy of younger patients with chronic lymphocytic leukemia. Blood. 2006 Feb 1;107(3):885-91. doi: 10.1182/blood-2005-06-2395. Epub 2005 Oct 11.

Reference Type RESULT
PMID: 16219797 (View on PubMed)

Other Identifiers

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EU-20538

Identifier Type: -

Identifier Source: secondary_id

GCLLSG-153

Identifier Type: -

Identifier Source: secondary_id

ISRCTN75653261

Identifier Type: -

Identifier Source: secondary_id

MEDAC-GCLLSG-CLL4

Identifier Type: -

Identifier Source: secondary_id

CDR0000455094

Identifier Type: OTHER

Identifier Source: secondary_id

CLL4

Identifier Type: -

Identifier Source: org_study_id

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