Trial Outcomes & Findings for Synthetic Vaccine in Patients With Chronic Myeloid Leukemia and Minimal Residual Disease (NCT NCT00267085)

NCT ID: NCT00267085

Last Updated: 2012-08-07

Results Overview

Molecular response defined as reduction by one log of the circulating peripheral blood for reverse transcription polymerase chain reaction (RT-PCR) transcripts of BCR-ABL (tumor-specific oncogenic fusion protein) after two consecutive measurements. RT-PCR performed at 3 month intervals. Response categorized as either 'No Decrease' or 'Decrease' if one log reduction in BCR-ABL detected.

Recruitment status

COMPLETED

Study phase

PHASE2

Target enrollment

11 participants

Primary outcome timeframe

12 months

Results posted on

2012-08-07

Participant Flow

Recruitment Period 12/2/05 to 7/1/08. All participants registered at The University of Texas M.D. Anderson Cancer Center.

Eleven participants were registered, one was excluded from study enrollment and did not receive the Chronic Myeloid Leukemia (CML) Vaccine.

Participant milestones

Participant milestones
Measure
CML Vaccine
Imatinib mesylate subcutaneously every 2 weeks x 4 weeks, then every three weeks x 1 week, followed by monthly for 10 months
Overall Study
STARTED
10
Overall Study
COMPLETED
10
Overall Study
NOT COMPLETED
0

Reasons for withdrawal

Withdrawal data not reported

Baseline Characteristics

Synthetic Vaccine in Patients With Chronic Myeloid Leukemia and Minimal Residual Disease

Baseline characteristics by cohort

Baseline characteristics by cohort
Measure
CML Vaccine
n=10 Participants
Imatinib mesylate subcutaneously every 2 weeks x 4 weeks, then every three weeks x 1 week, followed by monthly for 10 months
Age, Categorical
<=18 years
0 Participants
n=5 Participants
Age, Categorical
Between 18 and 65 years
10 Participants
n=5 Participants
Age, Categorical
>=65 years
0 Participants
n=5 Participants
Age Continuous
45 years
n=5 Participants
Sex: Female, Male
Female
4 Participants
n=5 Participants
Sex: Female, Male
Male
6 Participants
n=5 Participants
Region of Enrollment
United States
10 participants
n=5 Participants

PRIMARY outcome

Timeframe: 12 months

Population: All 10 participants on study received treatment and were included in analysis.

Molecular response defined as reduction by one log of the circulating peripheral blood for reverse transcription polymerase chain reaction (RT-PCR) transcripts of BCR-ABL (tumor-specific oncogenic fusion protein) after two consecutive measurements. RT-PCR performed at 3 month intervals. Response categorized as either 'No Decrease' or 'Decrease' if one log reduction in BCR-ABL detected.

Outcome measures

Outcome measures
Measure
CML Vaccine
n=10 Participants
Imatinib mesylate subcutaneously every 2 weeks x 4 weeks, then every three weeks x 1 week, followed by monthly for 10 months
Response: One Log Decrease in BCR-ABL
Decrease
3 Participants
Response: One Log Decrease in BCR-ABL
No Decrease
7 Participants

Adverse Events

CML Vaccine

Serious events: 1 serious events
Other events: 10 other events
Deaths: 0 deaths

Serious adverse events

Serious adverse events
Measure
CML Vaccine
n=10 participants at risk
Imatinib mesylate subcutaneously every 2 weeks x 4 weeks, then every three weeks x 1 week, followed by monthly for 10 months
General disorders
Neck Pain
10.0%
1/10 • Number of events 1 • 2 years 3 months
General disorders
Back Pain
10.0%
1/10 • Number of events 1 • 2 years 3 months
Gastrointestinal disorders
Nausea
10.0%
1/10 • Number of events 1 • 2 years 3 months

Other adverse events

Other adverse events
Measure
CML Vaccine
n=10 participants at risk
Imatinib mesylate subcutaneously every 2 weeks x 4 weeks, then every three weeks x 1 week, followed by monthly for 10 months
Respiratory, thoracic and mediastinal disorders
Allergic Rhinitis
10.0%
1/10 • Number of events 1 • 2 years 3 months
Skin and subcutaneous tissue disorders
Bruising
20.0%
2/10 • Number of events 2 • 2 years 3 months
Skin and subcutaneous tissue disorders
Dermatology/skin (other)
10.0%
1/10 • Number of events 2 • 2 years 3 months
Gastrointestinal disorders
Diarrhea
40.0%
4/10 • Number of events 4 • 2 years 3 months
Skin and subcutaneous tissue disorders
Erythema multiforme
10.0%
1/10 • Number of events 1 • 2 years 3 months
General disorders
Fatigue
50.0%
5/10 • Number of events 9 • 2 years 3 months
General disorders
Fever without neutropenia
10.0%
1/10 • Number of events 1 • 2 years 3 months
Skin and subcutaneous tissue disorders
Injection site reaction
100.0%
10/10 • Number of events 31 • 2 years 3 months
Respiratory, thoracic and mediastinal disorders
Nasal/paranasal reactions
10.0%
1/10 • Number of events 1 • 2 years 3 months
Gastrointestinal disorders
Nausea
20.0%
2/10 • Number of events 2 • 2 years 3 months
General disorders
Pain (joint)
20.0%
2/10 • Number of events 2 • 2 years 3 months
General disorders
Pain (muscle)
30.0%
3/10 • Number of events 4 • 2 years 3 months
General disorders
Pain (NOS)
10.0%
1/10 • Number of events 1 • 2 years 3 months
General disorders
Pain (Other)
20.0%
2/10 • Number of events 2 • 2 years 3 months
Skin and subcutaneous tissue disorders
Pruitis
50.0%
5/10 • Number of events 8 • 2 years 3 months
Skin and subcutaneous tissue disorders
rash/desquamation
20.0%
2/10 • Number of events 3 • 2 years 3 months
General disorders
Sweating
10.0%
1/10 • Number of events 1 • 2 years 3 months

Additional Information

Jorge Cortes M.D./Professor

The University of Texas M. D. Anderson Cancer Center

Phone: 713/794-5783

Results disclosure agreements

  • Principal investigator is a sponsor employee
  • Publication restrictions are in place