Trial Outcomes & Findings for Anti-tumour Effects & Tolerability of Faslodex Alone or in Combination With Arimidex in Post Menopausal Women Prior to Surgery for Primary Breast Cancer (NCT NCT00259090)

NCT ID: NCT00259090

Last Updated: 2012-08-16

Results Overview

For each sample, the ER H-score is calculated from the percentage of cells staining very weak (+/-); weak (+); moderate (++); or strong (+++) as follows: H-score = \[(0.5 x percent +/-) + (1 x percent +) + (2 x percent ++) + (3 x percent +++)\]. Range 0-300. The greater the change from baseline (randomization) in ER H-score, the greater the blockage of ER expression and the greater the potential anti-tumour activity. Percentage change from baseline=\[(SRG - BL)/BL\]x100

Recruitment status

COMPLETED

Study phase

PHASE2

Target enrollment

120 participants

Primary outcome timeframe

Surgery (SRG) was to be performed between days 15 and 22 after baseline (BL)

Results posted on

2012-08-16

Participant Flow

Postmenopausal women with oestrogen receptor positive breast cancer, awaiting curative-intent surgery were recruited to 4 medical centres within the UK.

121 patients had baseline biopsy and were randomised 1:1:1. 120 patients received 14 to 21 days therapy. Surgery was actually performed between day 13 and 28 and a tumour sample was taken. Safety data is presented for all 120 patients who received therapy. The demography data are summarized for the population who had a usable tumour sample.

Participant milestones

Participant milestones
Measure
Fulvestrant
Fulvestrant 500 mg once monthly injection
Fulvestrant + Anastrozole
Fulvestrant 500 mg once monthly injection + Anastrozole 1 mg once daily tablet
Anastrozole
Anastrozole 1 mg once daily tablet
Overall Study
STARTED
35
31
37
Overall Study
COMPLETED
35
31
37
Overall Study
NOT COMPLETED
0
0
0

Reasons for withdrawal

Withdrawal data not reported

Baseline Characteristics

Anti-tumour Effects & Tolerability of Faslodex Alone or in Combination With Arimidex in Post Menopausal Women Prior to Surgery for Primary Breast Cancer

Baseline characteristics by cohort

Baseline characteristics by cohort
Measure
Fulvestrant
n=35 Participants
Fulvestrant 500 mg once monthly injection
Fulvestrant + Anastrozole
n=31 Participants
Fulvestrant 500 mg once monthly injection + Anastrozole 1 mg once daily tablet
Anastrozole
n=37 Participants
Anastrozole 1 mg once daily tablet
Total
n=103 Participants
Total of all reporting groups
Age, Customized
50 - 59 years
7 Participants
8.5 • n=5 Participants
13 Participants
10.5 • n=7 Participants
10 Participants
8.7 • n=5 Participants
30 Participants
9.0 • n=4 Participants
Age, Customized
60 - 69 years
13 Participants
n=5 Participants
7 Participants
n=7 Participants
14 Participants
n=5 Participants
34 Participants
n=4 Participants
Age, Customized
70 - 79 years
13 Participants
n=5 Participants
6 Participants
n=7 Participants
9 Participants
n=5 Participants
28 Participants
n=4 Participants
Age, Customized
80 - 89 years
2 Participants
n=5 Participants
3 Participants
n=7 Participants
2 Participants
n=5 Participants
7 Participants
n=4 Participants
Age, Customized
Not available
0 Participants
n=5 Participants
2 Participants
n=7 Participants
2 Participants
n=5 Participants
4 Participants
n=4 Participants
Sex: Female, Male
Female
35 Participants
n=5 Participants
31 Participants
n=7 Participants
37 Participants
n=5 Participants
103 Participants
n=4 Participants
Sex: Female, Male
Male
0 Participants
n=5 Participants
0 Participants
n=7 Participants
0 Participants
n=5 Participants
0 Participants
n=4 Participants

PRIMARY outcome

Timeframe: Surgery (SRG) was to be performed between days 15 and 22 after baseline (BL)

For each sample, the ER H-score is calculated from the percentage of cells staining very weak (+/-); weak (+); moderate (++); or strong (+++) as follows: H-score = \[(0.5 x percent +/-) + (1 x percent +) + (2 x percent ++) + (3 x percent +++)\]. Range 0-300. The greater the change from baseline (randomization) in ER H-score, the greater the blockage of ER expression and the greater the potential anti-tumour activity. Percentage change from baseline=\[(SRG - BL)/BL\]x100

Outcome measures

Outcome measures
Measure
Fulvestrant
n=35 Participants
Fulvestrant 500 mg once monthly injection
Fulvestrant + Anastrozole
n=31 Participants
Fulvestrant 500 mg once monthly injection + Anastrozole 1 mg once daily tablet
Anastrozole
n=37 Participants
Anastrozole 1 mg once daily tablet
Percentage Change From Baseline to Time of Surgery in Oestrogen Receptor (ER) H-score: Antitumour Effects of Fulvestrant, Anastrozole and a Combination of Both as Measured by the ER H-score.
-37 Percentage change from baseline
Standard Error 4
-38 Percentage change from baseline
Standard Error 5
-7 Percentage change from baseline
Standard Error 6

PRIMARY outcome

Timeframe: Surgery (SRG) was to be performed between days 15 and 22 after baseline (BL)

Population: nine patients with PgR=0 at baseline were excluded from analysis of PgR because the question of medical interest was the effect of treatment on PgR positive patients.

For each sample, the PgR H-score is calculated from the percentage of cells staining very weak (+/-); weak (+); moderate (++); or strong (+++) as follows: H-score = \[(0.5 x percent+/-) + (1 x percent+) + (2 x percent++) + (3 x percent+++)\]. Range 0-300. The greater the change from baseline (randomization in PgR H-score, the greater the blockage of PgR expression and the greater the potential anti-tumour activity. Percentage change from baseline=\[(SRG - BL)/BL\]x100

Outcome measures

Outcome measures
Measure
Fulvestrant
n=33 Participants
Fulvestrant 500 mg once monthly injection
Fulvestrant + Anastrozole
n=28 Participants
Fulvestrant 500 mg once monthly injection + Anastrozole 1 mg once daily tablet
Anastrozole
n=33 Participants
Anastrozole 1 mg once daily tablet
Percentage Change From Baseline to Time of Surgery in Progesterone Receptor (PgR) H-score: Antitumour Effects of Fulvestrant, Anastrozole and a Combination of Both as Measured by the PgR H-score.
-31 Percentage change from baseline
Standard Error 8
-38 Percentage change from baseline
Standard Error 12
-38 Percentage change from baseline
Standard Error 7

PRIMARY outcome

Timeframe: Surgery (SRG) was to be performed between days 15 and 22 after baseline (BL)

For each sample, the Ki67 labelling index is calculated as the percentage of cells stained positive for Ki67. Range 0-100. The greater the change from baseline (randomization) in Ki67 labelling index, the greater the blockage of Ki67 expression and the greater the potential anti-tumour activity. Percentage change from baseline=\[(SRG - BL)/BL\]x100

Outcome measures

Outcome measures
Measure
Fulvestrant
n=35 Participants
Fulvestrant 500 mg once monthly injection
Fulvestrant + Anastrozole
n=31 Participants
Fulvestrant 500 mg once monthly injection + Anastrozole 1 mg once daily tablet
Anastrozole
n=37 Participants
Anastrozole 1 mg once daily tablet
Percentage Change From Baseline to Time of Surgery in Ki67 Labelling Index: Antitumour Effects of Fulvestrant, Anastrozole and a Combination of Both as Measured by the Ki67 Labelling Index.
-62 Percentage change from baseline
Standard Error 4
-68 Percentage change from baseline
Standard Error 6
-75 Percentage change from baseline
Standard Error 4

Adverse Events

Fulvestrant

Serious events: 0 serious events
Other events: 18 other events
Deaths: 0 deaths

Fulvestrant + Anastrozole

Serious events: 3 serious events
Other events: 13 other events
Deaths: 0 deaths

Anastrozole

Serious events: 2 serious events
Other events: 17 other events
Deaths: 0 deaths

Serious adverse events

Serious adverse events
Measure
Fulvestrant
n=40 participants at risk
Fulvestrant 500 mg once monthly injection
Fulvestrant + Anastrozole
n=40 participants at risk
Fulvestrant 500 mg once monthly injection + Anastrozole 1 mg once daily tablet
Anastrozole
n=40 participants at risk
Anastrozole 1 mg once daily tablet
Blood and lymphatic system disorders
Pancytopenia
0.00%
0/40
0.00%
0/40
2.5%
1/40
Cardiac disorders
Atrial Fibrillation
0.00%
0/40
2.5%
1/40
0.00%
0/40
General disorders
Unevaluable Event
0.00%
0/40
2.5%
1/40
0.00%
0/40
Infections and infestations
Subcutaneous Abscess
0.00%
0/40
0.00%
0/40
2.5%
1/40
Injury, poisoning and procedural complications
Procedural Complication
0.00%
0/40
2.5%
1/40
0.00%
0/40

Other adverse events

Other adverse events
Measure
Fulvestrant
n=40 participants at risk
Fulvestrant 500 mg once monthly injection
Fulvestrant + Anastrozole
n=40 participants at risk
Fulvestrant 500 mg once monthly injection + Anastrozole 1 mg once daily tablet
Anastrozole
n=40 participants at risk
Anastrozole 1 mg once daily tablet
Gastrointestinal disorders
Constipation
7.5%
3/40
2.5%
1/40
5.0%
2/40
Gastrointestinal disorders
Dyspepsia
7.5%
3/40
0.00%
0/40
2.5%
1/40
Gastrointestinal disorders
Nausea
0.00%
0/40
7.5%
3/40
5.0%
2/40
General disorders
Injection Site Rash
7.5%
3/40
0.00%
0/40
0.00%
0/40
General disorders
Unevaluable Event
7.5%
3/40
0.00%
0/40
7.5%
3/40
General disorders
Injection Site Pain
5.0%
2/40
2.5%
1/40
7.5%
3/40
Musculoskeletal and connective tissue disorders
Pain In Extremity
0.00%
0/40
10.0%
4/40
5.0%
2/40
Nervous system disorders
Headache
7.5%
3/40
10.0%
4/40
7.5%
3/40
Skin and subcutaneous tissue disorders
Rash
2.5%
1/40
7.5%
3/40
0.00%
0/40
Vascular disorders
Hot Flush
17.5%
7/40
7.5%
3/40
20.0%
8/40

Additional Information

Gerard Lynch

AstraZeneca

Results disclosure agreements

  • Principal investigator is a sponsor employee AZ shall have a period of 30 days from receipt of the proposed final manuscript for any publication or other disclosure to review it and may within such time request that submission for publication or disclosure of the manuscript be delayed for no more than an additional 45 days in order for AZ to file patent applications.
  • Publication restrictions are in place

Restriction type: OTHER