Trial Outcomes & Findings for Dasatinib as Therapy for Myeloproliferative Disorders (MPDs) (NCT NCT00255346)

NCT ID: NCT00255346

Last Updated: 2025-12-30

Results Overview

Response Rate is complete response plus partial response (CR+PR) for each disease category. Response Evaluation Criteria are as follows: Systemic Mastocytosis (SM): CR is the improvement of C-Findings, Tryptase \<20, and no organomegaly. PR is the improvement of C-Findings. Acute Myeloid Leukemia (AML)/MDS and CMML: CR is bone marrow blasts \</= 5%, absolute neutrophil count (ANC) \>/= 1000 and platelets \>/= 100. PR is bone marrow blasts 6-25% but decreased by \> 50% and absolute neutrophil count, absolute neutrophil count (ANC) \>/= 1000 and platelets \>/= 100. Primary Myelofibrosis (PMF): CR is bone marrow blasts \</= 5%, absolute neutrophil count (ANC) \>/= 1000 and platelets \>/= 100. CR is PR plus one or more of the following: ANC \>/= 1000, decreased platelets by 50%, hemoglobin increase of 2g/dl or reduction splenomegaly and/or hepatomegaly by 50%. HES/CEL: CR is disappearance of eosinophilia \</= 10%, PR is reduction of eosinophilia by \>/= 50%

Recruitment status

COMPLETED

Study phase

PHASE2

Target enrollment

68 participants

Primary outcome timeframe

Baseline to completion of 4 week cycle or until disease progression

Results posted on

2025-12-30

Participant Flow

Sixty-Seven participants were registered and received the study medication for this study.

Participant milestones

Participant milestones
Measure
Acute Myeloid Leukemia (AML)
Dasatinib 70 mg orally twice daily. Dasatinib (BMS-354825): 70 mg orally twice daily
MDS/CMML
Dasatinib 70 mg orally twice daily. Dasatinib (BMS-354825): 70 mg orally twice daily
HES/CEL
Dasatinib 70 mg orally twice daily. Dasatinib (BMS-354825): 70 mg orally twice daily
Primary Myelofibrosis (PMF)
Dasatinib 70 mg orally twice daily. Dasatinib (BMS-354825): 70 mg orally twice daily
Systemic Mastocytosis (SM)
Dasatinib 70 mg orally twice daily. Dasatinib (BMS-354825): 70 mg orally twice daily
Overall Study
STARTED
10
6
8
11
33
Overall Study
COMPLETED
9
6
8
11
33
Overall Study
NOT COMPLETED
1
0
0
0
0

Reasons for withdrawal

Reasons for withdrawal
Measure
Acute Myeloid Leukemia (AML)
Dasatinib 70 mg orally twice daily. Dasatinib (BMS-354825): 70 mg orally twice daily
MDS/CMML
Dasatinib 70 mg orally twice daily. Dasatinib (BMS-354825): 70 mg orally twice daily
HES/CEL
Dasatinib 70 mg orally twice daily. Dasatinib (BMS-354825): 70 mg orally twice daily
Primary Myelofibrosis (PMF)
Dasatinib 70 mg orally twice daily. Dasatinib (BMS-354825): 70 mg orally twice daily
Systemic Mastocytosis (SM)
Dasatinib 70 mg orally twice daily. Dasatinib (BMS-354825): 70 mg orally twice daily
Overall Study
Adverse Event
1
0
0
0
0

Baseline Characteristics

Dasatinib as Therapy for Myeloproliferative Disorders (MPDs)

Baseline characteristics by cohort

Baseline characteristics by cohort
Measure
Primary Myelofibrosis (PMF)
n=11 Participants
Dasatinib 70 mg orally twice daily. Dasatinib (BMS-354825): 70 mg orally twice daily
Systemic Mastocytosis (SM)
n=33 Participants
Dasatinib 70 mg orally twice daily. Dasatinib (BMS-354825): 70 mg orally twice daily
Total
n=68 Participants
Total of all reporting groups
MDS/CMML
n=6 Participants
Dasatinib 70 mg orally twice daily. Dasatinib (BMS-354825): 70 mg orally twice daily
HES/CEL
n=8 Participants
Dasatinib 70 mg orally twice daily. Dasatinib (BMS-354825): 70 mg orally twice daily
Acute Myeloid Leukemia (AML)
n=10 Participants
Dasatinib 70 mg orally twice daily. Dasatinib (BMS-354825): 70 mg orally twice daily
Age, Categorical
<=18 years
0 Participants
n=164 Participants
0 Participants
n=671 Participants
0 Participants
n=77 Participants
0 Participants
n=166 Participants
0 Participants
n=167 Participants
0 Participants
n=174 Participants
Age, Categorical
Between 18 and 65 years
8 Participants
n=164 Participants
28 Participants
n=671 Participants
46 Participants
n=77 Participants
2 Participants
n=166 Participants
5 Participants
n=167 Participants
3 Participants
n=174 Participants
Age, Categorical
>=65 years
3 Participants
n=164 Participants
5 Participants
n=671 Participants
22 Participants
n=77 Participants
4 Participants
n=166 Participants
3 Participants
n=167 Participants
7 Participants
n=174 Participants
Age, Continuous
63 years
n=164 Participants
57 years
n=671 Participants
62 years
n=77 Participants
68 years
n=166 Participants
62 years
n=167 Participants
70 years
n=174 Participants
Sex: Female, Male
Female
1 Participants
n=164 Participants
19 Participants
n=671 Participants
28 Participants
n=77 Participants
2 Participants
n=166 Participants
3 Participants
n=167 Participants
3 Participants
n=174 Participants
Sex: Female, Male
Male
10 Participants
n=164 Participants
14 Participants
n=671 Participants
40 Participants
n=77 Participants
4 Participants
n=166 Participants
5 Participants
n=167 Participants
7 Participants
n=174 Participants
Race (NIH/OMB)
American Indian or Alaska Native
0 Participants
n=164 Participants
0 Participants
n=671 Participants
0 Participants
n=77 Participants
0 Participants
n=166 Participants
0 Participants
n=167 Participants
0 Participants
n=174 Participants
Race (NIH/OMB)
Asian
0 Participants
n=164 Participants
0 Participants
n=671 Participants
0 Participants
n=77 Participants
0 Participants
n=166 Participants
0 Participants
n=167 Participants
0 Participants
n=174 Participants
Race (NIH/OMB)
Native Hawaiian or Other Pacific Islander
0 Participants
n=164 Participants
0 Participants
n=671 Participants
0 Participants
n=77 Participants
0 Participants
n=166 Participants
0 Participants
n=167 Participants
0 Participants
n=174 Participants
Race (NIH/OMB)
Black or African American
0 Participants
n=164 Participants
1 Participants
n=671 Participants
1 Participants
n=77 Participants
0 Participants
n=166 Participants
0 Participants
n=167 Participants
0 Participants
n=174 Participants
Race (NIH/OMB)
White
11 Participants
n=164 Participants
31 Participants
n=671 Participants
66 Participants
n=77 Participants
6 Participants
n=166 Participants
8 Participants
n=167 Participants
10 Participants
n=174 Participants
Race (NIH/OMB)
More than one race
0 Participants
n=164 Participants
0 Participants
n=671 Participants
0 Participants
n=77 Participants
0 Participants
n=166 Participants
0 Participants
n=167 Participants
0 Participants
n=174 Participants
Race (NIH/OMB)
Unknown or Not Reported
0 Participants
n=164 Participants
1 Participants
n=671 Participants
1 Participants
n=77 Participants
0 Participants
n=166 Participants
0 Participants
n=167 Participants
0 Participants
n=174 Participants
Region of Enrollment
United States
11 participants
n=164 Participants
33 participants
n=671 Participants
67 participants
n=77 Participants
6 participants
n=166 Participants
8 participants
n=167 Participants
9 participants
n=174 Participants

PRIMARY outcome

Timeframe: Baseline to completion of 4 week cycle or until disease progression

Response Rate is complete response plus partial response (CR+PR) for each disease category. Response Evaluation Criteria are as follows: Systemic Mastocytosis (SM): CR is the improvement of C-Findings, Tryptase \<20, and no organomegaly. PR is the improvement of C-Findings. Acute Myeloid Leukemia (AML)/MDS and CMML: CR is bone marrow blasts \</= 5%, absolute neutrophil count (ANC) \>/= 1000 and platelets \>/= 100. PR is bone marrow blasts 6-25% but decreased by \> 50% and absolute neutrophil count, absolute neutrophil count (ANC) \>/= 1000 and platelets \>/= 100. Primary Myelofibrosis (PMF): CR is bone marrow blasts \</= 5%, absolute neutrophil count (ANC) \>/= 1000 and platelets \>/= 100. CR is PR plus one or more of the following: ANC \>/= 1000, decreased platelets by 50%, hemoglobin increase of 2g/dl or reduction splenomegaly and/or hepatomegaly by 50%. HES/CEL: CR is disappearance of eosinophilia \</= 10%, PR is reduction of eosinophilia by \>/= 50%

Outcome measures

Outcome measures
Measure
Acute Myeloid Leukemia (AML)
n=9 Participants
Dasatinib 70 mg orally twice daily. Dasatinib (BMS-354825): 70 mg orally twice daily
MDS/CMML
n=6 Participants
Dasatinib 70 mg orally twice daily. Dasatinib (BMS-354825): 70 mg orally twice daily
HES/CEL
n=8 Participants
Dasatinib 70 mg orally twice daily. Dasatinib (BMS-354825): 70 mg orally twice daily
Primary Myelofibrosis (PMF)
n=11 Participants
Dasatinib 70 mg orally twice daily. Dasatinib (BMS-354825): 70 mg orally twice daily
Systemic Mastocytosis (SM)
n=33 Participants
Dasatinib 70 mg orally twice daily. Dasatinib (BMS-354825): 70 mg orally twice daily
Participant Response Rate
1 Participants
0 Participants
1 Participants
0 Participants
2 Participants

SECONDARY outcome

Timeframe: Baseline, once a week for a month, thereafter monthly, up to 10 years

Population: The number of participants analyzed for duration of response reflects the number of participants with a response for each arm.

Response date to loss of response or last follow up.

Outcome measures

Outcome measures
Measure
Acute Myeloid Leukemia (AML)
n=1 Participants
Dasatinib 70 mg orally twice daily. Dasatinib (BMS-354825): 70 mg orally twice daily
MDS/CMML
Dasatinib 70 mg orally twice daily. Dasatinib (BMS-354825): 70 mg orally twice daily
HES/CEL
n=1 Participants
Dasatinib 70 mg orally twice daily. Dasatinib (BMS-354825): 70 mg orally twice daily
Primary Myelofibrosis (PMF)
Dasatinib 70 mg orally twice daily. Dasatinib (BMS-354825): 70 mg orally twice daily
Systemic Mastocytosis (SM)
n=2 Participants
Dasatinib 70 mg orally twice daily. Dasatinib (BMS-354825): 70 mg orally twice daily
Duration of Response (Survival)
NA Months
The duration of response cannot be reported for a single participant for privacy reasons
NA Months
The duration of response cannot be reported for a single participant for privacy reasons
13 Months
Interval 8.0 to 18.0

Adverse Events

Dasatinib All Patient Groups

Serious events: 2 serious events
Other events: 67 other events
Deaths: 2 deaths

Serious adverse events

Serious adverse events
Measure
Dasatinib All Patient Groups
n=68 participants at risk
Dasatinib 70 mg orally twice daily. Dasatinib (BMS-354825): 70 mg orally twice daily
Blood and lymphatic system disorders
Hemorrhage CNS
1.5%
1/68 • Number of events 1 • Through study completion, up to 10 years
Infections and infestations
Skin Infection
1.5%
1/68 • Number of events 1 • Through study completion, up to 10 years
Respiratory, thoracic and mediastinal disorders
Pleural Effusion
1.5%
1/68 • Number of events 1 • Through study completion, up to 10 years
Cardiac disorders
Pericardial Effusion
1.5%
1/68 • Number of events 1 • Through study completion, up to 10 years

Other adverse events

Other adverse events
Measure
Dasatinib All Patient Groups
n=68 participants at risk
Dasatinib 70 mg orally twice daily. Dasatinib (BMS-354825): 70 mg orally twice daily
Respiratory, thoracic and mediastinal disorders
Dyspnea
26.5%
18/68 • Number of events 18 • Through study completion, up to 10 years
Blood and lymphatic system disorders
Edema
7.4%
5/68 • Number of events 5 • Through study completion, up to 10 years
General disorders
Fatigue
11.8%
8/68 • Number of events 8 • Through study completion, up to 10 years
General disorders
Headache
17.6%
12/68 • Number of events 12 • Through study completion, up to 10 years
Gastrointestinal disorders
Nausea/Vomiting
30.9%
21/68 • Number of events 21 • Through study completion, up to 10 years
General disorders
Pain
10.3%
7/68 • Number of events 7 • Through study completion, up to 10 years
Blood and lymphatic system disorders
Platelets/Hemoglobin
8.8%
6/68 • Number of events 6 • Through study completion, up to 10 years
Respiratory, thoracic and mediastinal disorders
Pleural Effusion
20.6%
14/68 • Number of events 14 • Through study completion, up to 10 years
Skin and subcutaneous tissue disorders
Rash
5.9%
4/68 • Number of events 4 • Through study completion, up to 10 years
Gastrointestinal disorders
Diarrhea
7.4%
5/68 • Number of events 5 • Through study completion, up to 10 years

Additional Information

Hagop Kantarjian, MD/Department Chair

The University of Texas MD Anderson Cancer Center

Phone: 713-792-7026

Results disclosure agreements

  • Principal investigator is a sponsor employee
  • Publication restrictions are in place