Mannitol Dose Response Study in Cystic Fibrosis

NCT ID: NCT00251056

Last Updated: 2008-08-29

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE2

Total Enrollment

48 participants

Study Classification

INTERVENTIONAL

Study Start Date

2005-10-31

Study Completion Date

2008-08-31

Brief Summary

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Many cystic fibrosis patients die of lung failure caused by repeated lung infections from thick, sticky mucus. Past studies have shown Bronchitol inhalation may help to facilitate the clearance of mucus by altering its rheology and replenishing the airway surface liquid layer in these patients, thereby enhancing the shift of stagnant mucus from the lungs. The study aim is to determine the optimal dose of mannitol to generate clinical improvement in patients with cystic fibrosis.

Detailed Description

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Conditions

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Cystic Fibrosis

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

CROSSOVER

Primary Study Purpose

TREATMENT

Blinding Strategy

NONE

Study Groups

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1

Group Type ACTIVE_COMPARATOR

mannitol

Intervention Type DRUG

40 mg BD

2

Group Type ACTIVE_COMPARATOR

mannitol

Intervention Type DRUG

120mg BD

3

Group Type ACTIVE_COMPARATOR

mannitol

Intervention Type DRUG

240mg BD

4

Group Type ACTIVE_COMPARATOR

mannitol

Intervention Type DRUG

400mg BD

Interventions

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mannitol

120mg BD

Intervention Type DRUG

mannitol

40 mg BD

Intervention Type DRUG

mannitol

240mg BD

Intervention Type DRUG

mannitol

400mg BD

Intervention Type DRUG

Eligibility Criteria

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Inclusion Criteria

* Diagnosis of cystic fibrosis (sweat test/genotype)
* 7 years or older
* FEV1 between 40% and 90% of predicted for height, age and gender.
* Able to perform acceptable-quality spirometry
* Clinically stable in the week up to study entry
* No additional antibiotics or additional oral steroids for a period of 14 days before study entry (routine antibiotics permitted)

Exclusion Criteria

* Currently active asthma
* Subjects colonized with Burkholderia cepacia or MRSA
* Considered "terminally ill" or listed for transplantation
* Requiring home oxygen or assisted ventilation
* Concurrent illness that in the investigators opinion may contribute to an increased and unacceptable risk if the subject was enrolled in the study (e.g. significant varicies, portal hypertension, cor pulmonale)
* Significant episode of haemoptysis (\>60 mLs) in the previous 12 months
* Heart attack or stroke in last 3 months
* Known aortic or cerebral aneurysm
* Subjects who are breast feeding or pregnant.
* At risk females unwilling to use appropriate contraception to prevent pregnancy during the course of the study
* Subjects who have participated in another investigative drug study parallel to, or within 4 weeks of study entry.
* Known intolerance to mannitol or unable to take any form of bronchodilator medications.
* Uncontrolled hypertension, systolic BP \> 200 or diastolic BP\> than 100
* Concurrent use of beta blocker medication
* Concurrent use of hypertonic saline

Canada:

* Concurrent use of other pharmacological mucolytic agents other than Pulmozyme

Argentina:

* Concurrent use of other pharmacological mucolytic agents including Pulmozyme
Minimum Eligible Age

7 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Syntara

INDUSTRY

Sponsor Role lead

Responsible Party

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Pharmaxis Ltd

Principal Investigators

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Elizabeth Tullis, MD

Role: PRINCIPAL_INVESTIGATOR

St Michaels Hospital, Toronto, Ontario, Canada

Brett Charlton, MBBS PhD

Role: STUDY_DIRECTOR

Pharmaxis Ltd, Sydney, NSW, Australia

Locations

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Hospital de Niños Superiora Sor María Ludovica

La Plata, Buenos Aires, Argentina

Site Status

Hospital Pediatrico

Resistencia, Chaco Province, Argentina

Site Status

Hospital Interzonal Especializado Materno Infantil (HIEMI)

Buenos Aires, , Argentina

Site Status

Hospital General de Niños

CABA, , Argentina

Site Status

Hospital Pediatrico Dr Humberto J Notti

Mendoza, , Argentina

Site Status

BC Children's Hospital

Vancouver, British Columbia, Canada

Site Status

St Pauls Hospital

Vancouver, British Columbia, Canada

Site Status

Janeway Children's Health and Rehabilitation Center

St. John's, Newfoundland and Labrador, Canada

Site Status

Queen Elizabeth II Health Sciences Centre

Halifax, Nova Scotia, Canada

Site Status

Hamilton Health Sciences Corporation

Hamilton, Ontario, Canada

Site Status

The Hospital for Sick Children

Toronto, Ontario, Canada

Site Status

St Michaels Hospital

Toronto, Ontario, Canada

Site Status

Countries

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Argentina Canada

Other Identifiers

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DPM-CF-202

Identifier Type: -

Identifier Source: org_study_id