Comparison of Tendon Transfer, Botox Injections and Ongoing Treatment in Hemiplegic Cerebral Palsy

NCT ID: NCT00250081

Last Updated: 2014-11-19

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

TERMINATED

Clinical Phase

NA

Total Enrollment

38 participants

Study Classification

INTERVENTIONAL

Study Start Date

2005-02-28

Study Completion Date

2013-05-31

Brief Summary

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Doctors use different treatments for people with Cerebral Palsy. Surgery is one option. Botulinum toxin injections are another option; these are given directly into spastic muscles to weaken them temporarily. Regular ongoing treatment (splinting, stretching and exercises) is another option. The investigators want to find out if surgery works better than Botulinum Toxin (Botox) injections or regular ongoing treatment (therapy), and if the effects of Botulinum Toxin injections last for longer than six months.

Detailed Description

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The specific aims of this study and the methodology for achieving them are:

1. To determine if tendon surgery for the forearm, wrist and thumb deformities of UECP is more effective than Botulinum toxin injections or regular ongoing treatment at improving function and quality of life for children with UECP. Children who are candidates for tendon surgery will be prospectively randomized to one of three treatment groups: standard tendon surgery, a series of three Botulinum toxin injections over a period of 12 months, and regular ongoing treatment. Validated tests of cognition, function and quality of life with tests of stereognosis and range of motion will be administered before, during and after treatment in order to compare outcomes of the three treatment groups.
2. To determine if serial Botulinum toxin injections have long-term beneficial effects on upper extremity function which outlast their paralytic effects.

Botulinum toxin has been shown to have beneficial effects on UE function while the muscles injected remain weakened by the toxin. Clinicians have theorized that improvements in UE function are maintained after the toxin wears off, but this has not been proven. Children randomized to the Botulinum toxin injection group will receive 3 injections. Their function will be tested before the first injection, while the paralytic results of the second injection are still in effect, and after the paralytic effects of the third injection have worn off, and the results compared in order to determine if functional improvements outlast the medicinal effects.

Conditions

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Cerebral Palsy

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Blinding Strategy

NONE

Study Groups

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Therapy Group

Therapy only

Group Type ACTIVE_COMPARATOR

Regularly ongoing therapy

Intervention Type PROCEDURE

Surgery Group

surgical intervention

Group Type ACTIVE_COMPARATOR

Upper Extremity Tendon transfer

Intervention Type PROCEDURE

Botox Injections

botulinum toxin

Group Type ACTIVE_COMPARATOR

Botulinum Toxin injections in Upper Extremity

Intervention Type PROCEDURE

Interventions

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Upper Extremity Tendon transfer

Intervention Type PROCEDURE

Botulinum Toxin injections in Upper Extremity

Intervention Type PROCEDURE

Regularly ongoing therapy

Intervention Type PROCEDURE

Eligibility Criteria

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Inclusion Criteria

* diagnosis of UECP
* aged four to 17 years
* candidate for standard surgical management (tendon transfer)

Exclusion Criteria

* subject could benefit from procedures in addition to standard surgical management and releases, and these procedures could be performed at the same anesthetic (for example, elbow flexor release)
* previous Botulinum toxin injection session in the affected UE in \< 1 year
* previous ipsilateral UE surgery
* primary language other than English or Spanish
* subject and/or parent unwilling to attend eight therapy sessions and perform home exercise protocol
Minimum Eligible Age

4 Years

Maximum Eligible Age

17 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Shriners Hospitals for Children

OTHER

Sponsor Role lead

Responsible Party

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Michelle James

Chief of Orthopaedics

Responsibility Role PRINCIPAL_INVESTIGATOR

Principal Investigators

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Michelle James, MD

Role: PRINCIPAL_INVESTIGATOR

Shriners Hospitals for Children, Northern Calfiornia

Ann Van Heest, MD

Role: PRINCIPAL_INVESTIGATOR

Shriners Hospitals for Children, Twin Cities

Anita Bagley, PhD

Role: PRINCIPAL_INVESTIGATOR

Shriners Hospitals for Children, Northern California

Locations

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Shriners Hospitals for Children Northern California

Sacramento, California, United States

Site Status

Alfred I duPont Childrens Hospital

Wilmington, Delaware, United States

Site Status

Children's National Medical Center

Washington D.C., District of Columbia, United States

Site Status

Shriners Hosptials for Children

Tampa, Florida, United States

Site Status

Shriners Hospitals for Children Chicago

Chicago, Illinois, United States

Site Status

Shriners Hospitals for Children

Shreveport, Louisiana, United States

Site Status

Shriners Hospitals for Children, Twin Cities

Minneapolis, Minnesota, United States

Site Status

Children's Mercy Hospital

Kansas City, Missouri, United States

Site Status

Shriners Hospitals for Children

Greenville, South Carolina, United States

Site Status

Shriners Hosptials for Children, Intermountain

Salt Lake City, Utah, United States

Site Status

Countries

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United States

References

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Related Links

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http://www.shrinershq.org/Hospitals/Main

Official website for Shriners Hospitals for Children, a network of 22 hospitals that provide expert, no-cost orthopaedic and burn care to children under 18

Other Identifiers

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83004-278826

Identifier Type: -

Identifier Source: org_study_id