Trial Outcomes & Findings for Efficacy and Safety, Long-term Study of Zinc Acetate to Treat Wilson's Disease in Japan. (NCT NCT00212355)

NCT ID: NCT00212355

Last Updated: 2025-03-05

Results Overview

Number of patients who have at least one adverse events. ALT Change

Recruitment status

COMPLETED

Study phase

PHASE3

Target enrollment

37 participants

Primary outcome timeframe

During study period (up to 96W )

Results posted on

2025-03-05

Participant Flow

Participant milestones

Participant milestones
Measure
NPC-02
zinc acetate NPC-02: zinc acetate
Overall Study
STARTED
37
Overall Study
COMPLETED
34
Overall Study
NOT COMPLETED
3

Reasons for withdrawal

Reasons for withdrawal
Measure
NPC-02
zinc acetate NPC-02: zinc acetate
Overall Study
Adverse Event
1
Overall Study
Withdrawal by Subject
1
Overall Study
A change of address
1

Baseline Characteristics

Efficacy and Safety, Long-term Study of Zinc Acetate to Treat Wilson's Disease in Japan.

Baseline characteristics by cohort

Baseline characteristics by cohort
Measure
NPC-02
n=37 Participants
zinc acetate NPC-02: zinc acetate
Age, Customized
≥16
20 participants
n=5 Participants
Age, Customized
≥6 - <16
15 participants
n=5 Participants
Age, Customized
≥1 - <6
2 participants
n=5 Participants
Sex: Female, Male
Female
24 Participants
n=5 Participants
Sex: Female, Male
Male
13 Participants
n=5 Participants

PRIMARY outcome

Timeframe: During study period (up to 96W )

Population: The analysis was performed based on FAS population

Number of patients who have at least one adverse events. ALT Change

Outcome measures

Outcome measures
Measure
NPC-02
n=37 Participants
zinc acetate NPC-02: zinc acetate
Safety and Efficacy
37 participants

Adverse Events

NPC-02

Serious events: 4 serious events
Other events: 37 other events
Deaths: 0 deaths

Serious adverse events

Serious adverse events
Measure
NPC-02
n=37 participants at risk
zinc acetate NPC-02: zinc acetate
Psychiatric disorders
Depression
2.7%
1/37 • Number of events 1
Immune system disorders
Colitis ulcerative
2.7%
1/37 • Number of events 2
Infections and infestations
Varicella
2.7%
1/37 • Number of events 1
Congenital, familial and genetic disorders
Sebaceous naevus
2.7%
1/37 • Number of events 1

Other adverse events

Other adverse events
Measure
NPC-02
n=37 participants at risk
zinc acetate NPC-02: zinc acetate
Eye disorders
Conjunctivitis allergic
5.4%
2/37 • Number of events 2
Eye disorders
Myopia
5.4%
2/37 • Number of events 2
Gastrointestinal disorders
Abdominal pain
8.1%
3/37 • Number of events 4
Gastrointestinal disorders
Abdominal pain upper
16.2%
6/37 • Number of events 7
Gastrointestinal disorders
Constipation
5.4%
2/37 • Number of events 2
Gastrointestinal disorders
Diarrhoea
16.2%
6/37 • Number of events 6
Gastrointestinal disorders
Nausea
16.2%
6/37 • Number of events 6
Gastrointestinal disorders
Stomach discomfort
18.9%
7/37 • Number of events 9
Gastrointestinal disorders
Stomatitis
5.4%
2/37 • Number of events 2
General disorders
Pain chest
5.4%
2/37 • Number of events 2
General disorders
Edema peripheral
5.4%
2/37 • Number of events 2
General disorders
Fever
13.5%
5/37 • Number of events 5
Immune system disorders
Seasonal allergy
5.4%
2/37 • Number of events 2
Infections and infestations
Acute bronchitis
10.8%
4/37 • Number of events 5
Infections and infestations
Gastroenteritis
10.8%
4/37 • Number of events 5
Infections and infestations
Hordeolum
5.4%
2/37 • Number of events 2
Infections and infestations
Influenza
24.3%
9/37 • Number of events 9
Infections and infestations
Molluscum contagious
5.4%
2/37 • Number of events 2
Infections and infestations
Nasopharyngitis
64.9%
24/37 • Number of events 43
Infections and infestations
Otitis meda
5.4%
2/37 • Number of events 2
Infections and infestations
Pharyngitis
18.9%
7/37 • Number of events 7
Infections and infestations
Rhinitis
8.1%
3/37 • Number of events 4
Infections and infestations
Sinusitis
8.1%
3/37 • Number of events 3
Infections and infestations
Varicella
5.4%
2/37 • Number of events 2
Injury, poisoning and procedural complications
Joint sprain
5.4%
2/37 • Number of events 2
Injury, poisoning and procedural complications
Bruise
5.4%
2/37 • Number of events 2
Investigations
ALT increased
16.2%
6/37 • Number of events 6
Investigations
AST increased
8.1%
3/37 • Number of events 3
Investigations
Blood alubumin decreased
5.4%
2/37 • Number of events 2
Investigations
Blood amylase increased
56.8%
21/37 • Number of events 23
Investigations
Blood bilirubin increased
10.8%
4/37 • Number of events 4
Investigations
Cholesterol blood decreased
16.2%
6/37 • Number of events 6
Investigations
Blood iron decreased
59.5%
22/37 • Number of events 25
Investigations
Blood triglycerides increased
32.4%
12/37 • Number of events 14
Investigations
Haematocrit decreased
8.1%
3/37 • Number of events 3
Investigations
Blood urine present
37.8%
14/37 • Number of events 15
Investigations
Hemoglobin decreased
10.8%
4/37 • Number of events 4
Investigations
Lipase increased
75.7%
28/37 • Number of events 29
Investigations
Mean cell haemoglobin concentration decreased
10.8%
4/37 • Number of events 4
Investigations
Mean corpuscular volume decreased
8.1%
3/37 • Number of events 3
Investigations
Platelet count decreased
5.4%
2/37 • Number of events 3
Investigations
Protein total decreased
5.4%
2/37 • Number of events 2
Investigations
White blood cell count decreased
18.9%
7/37 • Number of events 7
Investigations
White blood cell count increased
13.5%
5/37 • Number of events 5
Investigations
Platelet count increased
8.1%
3/37 • Number of events 3
Investigations
Protein urine present
35.1%
13/37 • Number of events 16
Investigations
Urobilin urine present
5.4%
2/37 • Number of events 2
Investigations
ALP increased
10.8%
4/37 • Number of events 4
Musculoskeletal and connective tissue disorders
Joint pain
5.4%
2/37 • Number of events 3
Musculoskeletal and connective tissue disorders
Back pain
16.2%
6/37 • Number of events 6
Musculoskeletal and connective tissue disorders
Pain in extremity
5.4%
2/37 • Number of events 2
Nervous system disorders
Headache
10.8%
4/37 • Number of events 4
Nervous system disorders
Hypoaesthesia
5.4%
2/37 • Number of events 2
Respiratory, thoracic and mediastinal disorders
Cough
5.4%
2/37 • Number of events 2
Respiratory, thoracic and mediastinal disorders
Rhinitis allergic
5.4%
2/37 • Number of events 2
Respiratory, thoracic and mediastinal disorders
Upper respiratory tract inflammation
35.1%
13/37 • Number of events 19
Skin and subcutaneous tissue disorders
Dermatitis atopic
8.1%
3/37 • Number of events 3
Skin and subcutaneous tissue disorders
Rash
8.1%
3/37 • Number of events 3
Skin and subcutaneous tissue disorders
Urticaria
5.4%
2/37 • Number of events 2
Vascular disorders
Orthostatic hypotension
8.1%
3/37 • Number of events 3
Skin and subcutaneous tissue disorders
Eczema
8.1%
3/37 • Number of events 3

Additional Information

Department director of clinical development department 1

Nobelpharama

Phone: +81-3-5651-1177

Results disclosure agreements

  • Principal investigator is a sponsor employee There is an agreement between the sponsor and PI that no restricts the PI's right but need to discuss the timing of publish date of trial results after the trial is completed.
  • Publication restrictions are in place

Restriction type: OTHER