Trial Outcomes & Findings for Imatinib Mesylate and Zoledronic Acid in Patients With Chronic Myeloid Leukaemia in Cytogenetic Response Without Molecular Response (NCT NCT00210119)

NCT ID: NCT00210119

Last Updated: 2021-11-08

Results Overview

A patient is considered to be in molecular response if at least one of the following conditions is observed : \- a complete molecular response at 6 months defined by PCR negativation tested on twice OR \- reduction of BCR-ABL transcript level \> 2 Log from the start of from initiation of treatment

Recruitment status

TERMINATED

Study phase

PHASE2

Target enrollment

19 participants

Primary outcome timeframe

6 months

Results posted on

2021-11-08

Participant Flow

The AFR-22 trial was based on a two-stage Simon's design, which included 17 patients in the first stage, followed by an additional 20 patients. Analysis of the first 17 evaluable patients showed insufficient efficacy of the study treatment. In accordance with the principle of Simon's two-stage design, enrollment was stopped.

Participant milestones

Participant milestones
Measure
Imatinib Mesylate
Imatinib mesylate 600 or 800 mg/day PO + zoledronate 4 mg IV over 15 min every 3 weeks for 6 months. Glivec
Overall Study
STARTED
19
Overall Study
COMPLETED
17
Overall Study
NOT COMPLETED
2

Reasons for withdrawal

Reasons for withdrawal
Measure
Imatinib Mesylate
Imatinib mesylate 600 or 800 mg/day PO + zoledronate 4 mg IV over 15 min every 3 weeks for 6 months. Glivec
Overall Study
Protocol Violation
1
Overall Study
Withdrawal by Subject
1

Baseline Characteristics

Imatinib Mesylate and Zoledronic Acid in Patients With Chronic Myeloid Leukaemia in Cytogenetic Response Without Molecular Response

Baseline characteristics by cohort

Baseline characteristics by cohort
Measure
Imatinib Mesylate
n=19 Participants
Imatinib mesylate 600 or 800 mg/day PO + zoledronate 4 mg IV over 15 min every 3 weeks for 6 months. Glivec
Age, Continuous
58.4 years
n=5 Participants
Sex: Female, Male
Female
3 Participants
n=5 Participants
Sex: Female, Male
Male
16 Participants
n=5 Participants
Region of Enrollment
France
19 Participants
n=5 Participants

PRIMARY outcome

Timeframe: 6 months

Population: 2 patients were not assessable for the primary outcome measure : 1 not eligible and 1 not treated because of withdrawal

A patient is considered to be in molecular response if at least one of the following conditions is observed : \- a complete molecular response at 6 months defined by PCR negativation tested on twice OR \- reduction of BCR-ABL transcript level \> 2 Log from the start of from initiation of treatment

Outcome measures

Outcome measures
Measure
Imatinib Mesylate
n=17 Participants
Imatinib mesylate 600 or 800 mg/day PO + zoledronate 4 mg IV over 15 min every 3 weeks for 6 months. Glivec
Percentage of Participants With Molecular Response
0 percentage of participants
Interval 0.0 to 0.0

SECONDARY outcome

Timeframe: 6 months

Population: 2 patients were not assessable for secondary outcome measures

reduction of BCR-ABL transcript level \> 4.5 Log from the start of from initiation of treatment

Outcome measures

Outcome measures
Measure
Imatinib Mesylate
n=17 Participants
Imatinib mesylate 600 or 800 mg/day PO + zoledronate 4 mg IV over 15 min every 3 weeks for 6 months. Glivec
Percentage of Participants With a Reduction of BCR-ABL Transcript Level > 4.5 Log From the Start of From Initiation of Treatment
0 percentage of participants
Interval 0.0 to 0.0

Adverse Events

Imatinib Mesylate

Serious events: 1 serious events
Other events: 0 other events
Deaths: 0 deaths

Serious adverse events

Serious adverse events
Measure
Imatinib Mesylate
n=17 participants at risk
Imatinib mesylate 600 or 800 mg/day PO + zoledronate 4 mg IV over 15 min every 3 weeks for 6 months. Glivec
Respiratory, thoracic and mediastinal disorders
Pulmonary edema
5.9%
1/17 • Number of events 1
Only serious adverse events were monitored. Adverse events (non-serious) were not assessed/monitored during the study.

Other adverse events

Adverse event data not reported

Additional Information

Dr Gabriel Etienne

Institut Bergonie

Results disclosure agreements

  • Principal investigator is a sponsor employee
  • Publication restrictions are in place