Trial Outcomes & Findings for Comparative Efficacy of Three Preparations of Botox-A in Treating Spasticity (NCT NCT00178646)

NCT ID: NCT00178646

Last Updated: 2021-01-22

Results Overview

The Ashworth Scale measures resistance during passive soft-tissue stretching and is used as a simple measure of spasticity. Score on the Ashworth scores ranges from 0-4, with 4 being the worst: 0 - No increase in muscle tone 1. \- Slight increase in muscle tone, manifested by a catch and release or by minimal resistance at the end of the range of motion when the affected part(s) is moved in flexion or extension 2. \- More marked increase in muscle tone through most of the range of motion, but affected limb easily flexed 3. \- Considerable increase in muscle tone, passive movement difficult 4. \- Limb in flexion or extension

Recruitment status

COMPLETED

Study phase

PHASE4

Target enrollment

33 participants

Primary outcome timeframe

Baseline

Results posted on

2021-01-22

Participant Flow

33 were enrolled but 32 started, and this is because one participant who enrolled decided not to start the study.

Participant milestones

Participant milestones
Measure
Low Volume, High Dose
Botox, 150 units prepared as 100 units/ml Botox: Botox 75-150 units, single treatment only
High Volume, High Dose
Botox 150 units, prepared as 50 units/ml. Botox: Botox 75-150 units, single treatment only
High Volume, Low Dose
Botox 75 units, prepared as 25 units/ml. Botox: Botox 75-150 units, single treatment only
Overall Study
STARTED
12
9
11
Overall Study
COMPLETED
12
8
10
Overall Study
NOT COMPLETED
0
1
1

Reasons for withdrawal

Withdrawal data not reported

Baseline Characteristics

Race and Ethnicity were not collected from any participant.

Baseline characteristics by cohort

Baseline characteristics by cohort
Measure
Low Volume, High Dose
n=12 Participants
Botox, 150 units prepared as 100 units/ml Botox: Botox 75-150 units, single treatment only
High Volume, High Dose
n=9 Participants
Botox 150 units, prepared as 50 units/ml. Botox: Botox 75-150 units, single treatment only
Low Volume, Low Dose
n=11 Participants
Botox 75 units, prepared as 25 units/ml. Botox: Botox 75-150 units, single treatment only
Total
n=32 Participants
Total of all reporting groups
Age, Categorical
<=18 years
0 Participants
n=12 Participants
0 Participants
n=9 Participants
0 Participants
n=11 Participants
0 Participants
n=32 Participants
Age, Categorical
Between 18 and 65 years
12 Participants
n=12 Participants
9 Participants
n=9 Participants
11 Participants
n=11 Participants
32 Participants
n=32 Participants
Age, Categorical
>=65 years
0 Participants
n=12 Participants
0 Participants
n=9 Participants
0 Participants
n=11 Participants
0 Participants
n=32 Participants
Sex: Female, Male
Female
2 Participants
n=12 Participants
4 Participants
n=9 Participants
3 Participants
n=11 Participants
9 Participants
n=32 Participants
Sex: Female, Male
Male
10 Participants
n=12 Participants
5 Participants
n=9 Participants
8 Participants
n=11 Participants
23 Participants
n=32 Participants
Race and Ethnicity Not Collected
0 Participants
Race and Ethnicity were not collected from any participant.

PRIMARY outcome

Timeframe: Baseline

The Ashworth Scale measures resistance during passive soft-tissue stretching and is used as a simple measure of spasticity. Score on the Ashworth scores ranges from 0-4, with 4 being the worst: 0 - No increase in muscle tone 1. \- Slight increase in muscle tone, manifested by a catch and release or by minimal resistance at the end of the range of motion when the affected part(s) is moved in flexion or extension 2. \- More marked increase in muscle tone through most of the range of motion, but affected limb easily flexed 3. \- Considerable increase in muscle tone, passive movement difficult 4. \- Limb in flexion or extension

Outcome measures

Outcome measures
Measure
Low Volume, High Dose
n=12 Participants
Botox, 150 units prepared as 100 units/ml Botox: Botox 75-150 units, single treatment only
High Volume, High Dose
n=9 Participants
Botox 150 units, prepared as 50 units/ml. Botox: Botox 75-150 units, single treatment only
High Volume, Low Dose
n=11 Participants
Botox 75 units, prepared as 25 units/ml. Botox: Botox 75-150 units, single treatment only
Spastic Hypertonia as Measured by the Ashworth Scale
2.4 score on a scale
Interval 2.0 to 3.0
2.33 score on a scale
Interval 2.0 to 3.0
2.36 score on a scale
Interval 1.0 to 3.0

PRIMARY outcome

Timeframe: Four weeks

The Ashworth Scale measures resistance during passive soft-tissue stretching and is used as a simple measure of spasticity. Score on the Ashworth scores ranges from 0-4, with 4 being the worst: 0: No increase in muscle tone 1. Slight increase in muscle tone, manifested by a catch and release or by minimal resistance at the end of the range of motion when the affected part(s) is moved in flexion or extension 2. More marked increase in muscle tone through most of the range of motion, but affected limb easily flexed 3. Considerable increase in muscle tone, passive movement difficult 4. Limb in flexion or extension

Outcome measures

Outcome measures
Measure
Low Volume, High Dose
n=12 Participants
Botox, 150 units prepared as 100 units/ml Botox: Botox 75-150 units, single treatment only
High Volume, High Dose
n=9 Participants
Botox 150 units, prepared as 50 units/ml. Botox: Botox 75-150 units, single treatment only
High Volume, Low Dose
n=11 Participants
Botox 75 units, prepared as 25 units/ml. Botox: Botox 75-150 units, single treatment only
Spastic Hypertonia as Measured by the Ashworth Scale
2.42 score on a scale
Interval 2.0 to 3.0
2.56 score on a scale
Interval 2.0 to 3.0
2.36 score on a scale
Interval 1.0 to 3.0

PRIMARY outcome

Timeframe: Eight Weeks

The Ashworth Scale measures resistance during passive soft-tissue stretching and is used as a simple measure of spasticity. Score on the Ashworth scores ranges from 0-4, with 4 being the worst: 0: No increase in muscle tone 1. Slight increase in muscle tone, manifested by a catch and release or by minimal resistance at the end of the range of motion when the affected part(s) is moved in flexion or extension 2. More marked increase in muscle tone through most of the range of motion, but affected limb easily flexed 3. Considerable increase in muscle tone, passive movement difficult 4. Limb in flexion or extension

Outcome measures

Outcome measures
Measure
Low Volume, High Dose
n=12 Participants
Botox, 150 units prepared as 100 units/ml Botox: Botox 75-150 units, single treatment only
High Volume, High Dose
n=9 Participants
Botox 150 units, prepared as 50 units/ml. Botox: Botox 75-150 units, single treatment only
High Volume, Low Dose
n=11 Participants
Botox 75 units, prepared as 25 units/ml. Botox: Botox 75-150 units, single treatment only
Spastic Hypertonia as Measured by the Ashworth Scale
1.42 score on a scale
Interval 0.0 to 3.0
0.77 score on a scale
Interval 0.0 to 2.0
1 score on a scale
Interval 0.0 to 2.0

PRIMARY outcome

Timeframe: Twelve Weeks

Population: Data for this outcome measure were not collected for 2 in the Low volume High Dose arm, 1 in the High volume High Dose arm, and 1 in the High Volume Low Dose arm.

The Ashworth Scale measures resistance during passive soft-tissue stretching and is used as a simple measure of spasticity. Score on the Ashworth scores ranges from 0-4, with 4 being the worst: 0: No increase in muscle tone 1. Slight increase in muscle tone, manifested by a catch and release or by minimal resistance at the end of the range of motion when the affected part(s) is moved in flexion or extension 2. More marked increase in muscle tone through most of the range of motion, but affected limb easily flexed 3. Considerable increase in muscle tone, passive movement difficult 4. Limb in flexion or extension

Outcome measures

Outcome measures
Measure
Low Volume, High Dose
n=10 Participants
Botox, 150 units prepared as 100 units/ml Botox: Botox 75-150 units, single treatment only
High Volume, High Dose
n=8 Participants
Botox 150 units, prepared as 50 units/ml. Botox: Botox 75-150 units, single treatment only
High Volume, Low Dose
n=10 Participants
Botox 75 units, prepared as 25 units/ml. Botox: Botox 75-150 units, single treatment only
Spastic Hypertonia as Measured by the Ashworth Scale
1.3 score on a scale
Interval 0.0 to 2.0
1 score on a scale
Interval 0.0 to 2.0
1.7 score on a scale
Interval 1.0 to 3.0

PRIMARY outcome

Timeframe: Sixteen Weeks

Population: Data for this outcome measure were not collected for 1 in the High volume High Dose arm and 1 in the High Volume Low Dose arm.

The Ashworth Scale measures resistance during passive soft-tissue stretching and is used as a simple measure of spasticity. Score on the Ashworth scores ranges from 0-4, with 4 being the worst: 0: No increase in muscle tone 1. Slight increase in muscle tone, manifested by a catch and release or by minimal resistance at the end of the range of motion when the affected part(s) is moved in flexion or extension 2. More marked increase in muscle tone through most of the range of motion, but affected limb easily flexed 3. Considerable increase in muscle tone, passive movement difficult 4. Limb in flexion or extension

Outcome measures

Outcome measures
Measure
Low Volume, High Dose
n=12 Participants
Botox, 150 units prepared as 100 units/ml Botox: Botox 75-150 units, single treatment only
High Volume, High Dose
n=8 Participants
Botox 150 units, prepared as 50 units/ml. Botox: Botox 75-150 units, single treatment only
High Volume, Low Dose
n=10 Participants
Botox 75 units, prepared as 25 units/ml. Botox: Botox 75-150 units, single treatment only
Spastic Hypertonia as Measured by the Ashworth Scale
1.42 score on a scale
Interval 0.0 to 2.0
1.13 score on a scale
Interval 1.0 to 2.0
1.1 score on a scale
Interval 0.0 to 2.0

SECONDARY outcome

Timeframe: Baseline

This outcome reports the angle formed during ankle dorsiflexion by an imaginary line drawn on the outer side of the leg with an imaginary line drawn on the outside of the foot. The angle changes as the ankle is curled up (dorsiflexed) or down (plantarflexed). Many people with stroke develop muscle tightness (a condition called spasticity) or contracture, which leads to ankle plantarflexion and results in a "foot drop" appearance and limits range of motion. When the ankle is neutral and the foot is flat, the angle between the leg and the foot is roughly a right angle, and this neutral position is indicated as 0 degrees from the neutral position. If the foot is below the neutral position during maximum ankle dorsiflexion, then the angle reported is the number of degrees below the neutral position (reported as a negative value). If the foot is above the neutral position, then the angle reported is the number of degrees above the neutral position (positive value).

Outcome measures

Outcome measures
Measure
Low Volume, High Dose
n=12 Participants
Botox, 150 units prepared as 100 units/ml Botox: Botox 75-150 units, single treatment only
High Volume, High Dose
n=9 Participants
Botox 150 units, prepared as 50 units/ml. Botox: Botox 75-150 units, single treatment only
High Volume, Low Dose
n=11 Participants
Botox 75 units, prepared as 25 units/ml. Botox: Botox 75-150 units, single treatment only
Range of Motion as Measured by Goniometry
-9.42 degrees
Standard Deviation 5.42
-6.56 degrees
Standard Deviation 9.96
-19.64 degrees
Standard Deviation 13.90

SECONDARY outcome

Timeframe: 8 weeks

Population: Data were not collected for on in the Low volume, High Dose arm, one in the High volume, High Dose arm, and one in the High Volume, Low Dose arm.

This outcome reports the angle formed during ankle dorsiflexion by an imaginary line drawn on the outer side of the leg with an imaginary line drawn on the outside of the foot. The angle changes as the ankle is curled up (dorsiflexed) or down (plantarflexed). Many people with stroke develop muscle tightness (a condition called spasticity) or contracture, which leads to ankle plantarflexion and results in a "foot drop" appearance and limits range of motion. When the ankle is neutral and the foot is flat, the angle between the leg and the foot is roughly a right angle, and this neutral position is indicated as 0 degrees from the neutral position. If the foot is below the neutral position during maximum ankle dorsiflexion, then the angle reported is the number of degrees below the neutral position (reported as a negative value). If the foot is above the neutral position, then the angle reported is the number of degrees above the neutral position (positive value).

Outcome measures

Outcome measures
Measure
Low Volume, High Dose
n=11 Participants
Botox, 150 units prepared as 100 units/ml Botox: Botox 75-150 units, single treatment only
High Volume, High Dose
n=8 Participants
Botox 150 units, prepared as 50 units/ml. Botox: Botox 75-150 units, single treatment only
High Volume, Low Dose
n=10 Participants
Botox 75 units, prepared as 25 units/ml. Botox: Botox 75-150 units, single treatment only
Range of Motion as Measured by Goniometry
-1.82 degrees
Standard Deviation 6.82
2.25 degrees
Standard Deviation 8.08
-2.30 degrees
Standard Deviation 6.57

Adverse Events

Low Volume, High Dose

Serious events: 0 serious events
Other events: 1 other events
Deaths: 0 deaths

High Volume, High Dose

Serious events: 0 serious events
Other events: 2 other events
Deaths: 0 deaths

Low Volume, Low Dose

Serious events: 0 serious events
Other events: 0 other events
Deaths: 0 deaths

Serious adverse events

Adverse event data not reported

Other adverse events

Other adverse events
Measure
Low Volume, High Dose
n=12 participants at risk
Botox, 150 units prepared as 100 units/ml Botox: Botox 75-150 units, single treatment only
High Volume, High Dose
n=9 participants at risk
Botox 150 units, prepared as 50 units/ml. Botox: Botox 75-150 units, single treatment only
Low Volume, Low Dose
n=11 participants at risk
Botox 75 units, prepared as 25 units/ml. Botox: Botox 75-150 units, single treatment only
Eye disorders
Visual Change
0.00%
0/12 • Four months
11.1%
1/9 • Number of events 1 • Four months
0.00%
0/11 • Four months
Respiratory, thoracic and mediastinal disorders
Cough
0.00%
0/12 • Four months
11.1%
1/9 • Number of events 1 • Four months
0.00%
0/11 • Four months
Nervous system disorders
Altered Mental Status
0.00%
0/12 • Four months
11.1%
1/9 • Number of events 1 • Four months
0.00%
0/11 • Four months
Musculoskeletal and connective tissue disorders
Foot pain
8.3%
1/12 • Number of events 1 • Four months
0.00%
0/9 • Four months
0.00%
0/11 • Four months
Gastrointestinal disorders
Bowel urgency
0.00%
0/12 • Four months
11.1%
1/9 • Number of events 1 • Four months
0.00%
0/11 • Four months
General disorders
Increased Salivation
0.00%
0/12 • Four months
11.1%
1/9 • Number of events 1 • Four months
0.00%
0/11 • Four months

Additional Information

Gerard E. Francisco

UTHealth

Phone: 7137975246

Results disclosure agreements

  • Principal investigator is a sponsor employee
  • Publication restrictions are in place