Trial Outcomes & Findings for Randomized, Placebo-Controlled Study of Leptin for the Treatment of HIV Lipodystrophy and Metabolic Syndrome (NCT NCT00140244)

NCT ID: NCT00140244

Last Updated: 2017-05-11

Results Overview

Recruitment status

COMPLETED

Study phase

PHASE2

Target enrollment

7 participants

Primary outcome timeframe

At the end of each two month intervention

Results posted on

2017-05-11

Participant Flow

Participant milestones

Participant milestones
Measure
r-MetHuLeptin First, Then Placebo
r-MetHuLeptin subcutaneously once daily first, then Placebo both at a dose of 0.04 mg/kg/day divided into two equal doses, which were self-administered by sc injection at 0800 and 2000 h daily for 2 months.
Placebo First, Then r-metHuLeptin
Subcutaneously once daily Placebo first, then r-metHuLeptin both at a dose of 0.04 mg/kg/day divided into two equal doses, which were self-administered by sc injection at 0800 and 2000 h daily for 2 months.
Intervention 1
STARTED
3
4
Intervention 1
COMPLETED
3
4
Intervention 1
NOT COMPLETED
0
0
Washout
STARTED
3
4
Washout
COMPLETED
3
4
Washout
NOT COMPLETED
0
0
Intervention 2
STARTED
3
4
Intervention 2
COMPLETED
3
2
Intervention 2
NOT COMPLETED
0
2

Reasons for withdrawal

Withdrawal data not reported

Baseline Characteristics

Randomized, Placebo-Controlled Study of Leptin for the Treatment of HIV Lipodystrophy and Metabolic Syndrome

Baseline characteristics by cohort

Baseline characteristics by cohort
Measure
All Study Participants
n=7 Participants
r-MetHuLeptin SubQ once daily r-metHuLeptin/placebo then placebo/r-metHuLeptin
Age, Categorical
<=18 years
0 Participants
n=5 Participants
Age, Categorical
Between 18 and 65 years
7 Participants
n=5 Participants
Age, Categorical
>=65 years
0 Participants
n=5 Participants
Age, Continuous
45.8 years
STANDARD_DEVIATION 2 • n=5 Participants
Sex: Female, Male
Female
0 Participants
n=5 Participants
Sex: Female, Male
Male
7 Participants
n=5 Participants
Region of Enrollment
United States
7 participants
n=5 Participants
Body mass index
22.2 kg/m^2
STANDARD_DEVIATION 0.83 • n=5 Participants
Fasting leptin concentration
1.34 ng/ml
STANDARD_DEVIATION 0.2 • n=5 Participants
triglycerides
530 mg/dl
STANDARD_DEVIATION 53.8 • n=5 Participants
insulin
11.5 micro international units(μIU)/ml
STANDARD_DEVIATION 2.7 • n=5 Participants
glucose
81.1 mg/dl
STANDARD_DEVIATION 6.7 • n=5 Participants
hemoglobin A1c
5.1 %
STANDARD_DEVIATION 0.3 • n=5 Participants
CD4 count
454 cells/μl
STANDARD_DEVIATION 94 • n=5 Participants
HIV viral load
24524 copies/ml
STANDARD_DEVIATION 13693 • n=5 Participants

PRIMARY outcome

Timeframe: At the end of each two month intervention

Outcome measures

Outcome measures
Measure
r-MetHuLeptin
n=5 Participants
r-MetHuLeptin at a dose of 0.04 mg/kg/day divided into two equal doses, which were self-administered by sc injection at 0800 and 2000 h daily for 2 months.
Placebo
n=7 Participants
Placebo at a dose of 0.04 mg/kg/day divided into two equal doses, which were self-administered by sc injection at 0800 and 2000 h daily for 2 months.
Serum Lipid Levels
total cholesterol
228.8 mg/dl
Standard Error 13.3
219.7 mg/dl
Standard Error 13.1
Serum Lipid Levels
low density lipoprotein cholesterol
113.0 mg/dl
Standard Error 12.7
105.7 mg/dl
Standard Error 3.33
Serum Lipid Levels
triglycerides
409.0 mg/dl
Standard Error 88.8
520.5 mg/dl
Standard Error 91.1
Serum Lipid Levels
high density lipoprotein cholesterols
35 mg/dl
Standard Error 2.23
29.96 mg/dl
Standard Error 2.25
Serum Lipid Levels
Free fatty acids
0.45 mg/dl
Standard Error 0.07
0.61 mg/dl
Standard Error 0.09

SECONDARY outcome

Timeframe: At the end of each two month intervention

Outcome measures

Outcome measures
Measure
r-MetHuLeptin
n=5 Participants
r-MetHuLeptin at a dose of 0.04 mg/kg/day divided into two equal doses, which were self-administered by sc injection at 0800 and 2000 h daily for 2 months.
Placebo
n=7 Participants
Placebo at a dose of 0.04 mg/kg/day divided into two equal doses, which were self-administered by sc injection at 0800 and 2000 h daily for 2 months.
Insulin Resistance (as Assessed by HOMA-IR)
2.52 units on a scale
Standard Error 0.91
4.56 units on a scale
Standard Error 1.43

SECONDARY outcome

Timeframe: At the end of each two month intervention

Outcome measures

Outcome measures
Measure
r-MetHuLeptin
n=5 Participants
r-MetHuLeptin at a dose of 0.04 mg/kg/day divided into two equal doses, which were self-administered by sc injection at 0800 and 2000 h daily for 2 months.
Placebo
n=7 Participants
Placebo at a dose of 0.04 mg/kg/day divided into two equal doses, which were self-administered by sc injection at 0800 and 2000 h daily for 2 months.
Glycemia (as Assessed by Fasting Glucose)
91 mg/dl
Standard Error 2.28
95.6 mg/dl
Standard Error 2.8

SECONDARY outcome

Timeframe: At the end of each two month intervention

Outcome measures

Outcome measures
Measure
r-MetHuLeptin
n=5 Participants
r-MetHuLeptin at a dose of 0.04 mg/kg/day divided into two equal doses, which were self-administered by sc injection at 0800 and 2000 h daily for 2 months.
Placebo
n=7 Participants
Placebo at a dose of 0.04 mg/kg/day divided into two equal doses, which were self-administered by sc injection at 0800 and 2000 h daily for 2 months.
Low Density Lipoprotein (LDL) Cholesterol Levels
113 mg/dl
Standard Error 12.7
105.7 mg/dl
Standard Error 3.33

SECONDARY outcome

Timeframe: At the end of each two month intervention

Outcome measures

Outcome measures
Measure
r-MetHuLeptin
n=5 Participants
r-MetHuLeptin at a dose of 0.04 mg/kg/day divided into two equal doses, which were self-administered by sc injection at 0800 and 2000 h daily for 2 months.
Placebo
n=7 Participants
Placebo at a dose of 0.04 mg/kg/day divided into two equal doses, which were self-administered by sc injection at 0800 and 2000 h daily for 2 months.
Free Fatty Acid (FFA) Levels
0.45 mEq/liter
Standard Error 0.07
0.61 mEq/liter
Standard Error 0.09

SECONDARY outcome

Timeframe: At the end of each two month intervention

percent change in mean blood pressure

Outcome measures

Outcome measures
Measure
r-MetHuLeptin
n=5 Participants
r-MetHuLeptin at a dose of 0.04 mg/kg/day divided into two equal doses, which were self-administered by sc injection at 0800 and 2000 h daily for 2 months.
Placebo
n=7 Participants
Placebo at a dose of 0.04 mg/kg/day divided into two equal doses, which were self-administered by sc injection at 0800 and 2000 h daily for 2 months.
Blood Pressure
3.2 percentage change of mean blood pressure
Standard Error 5.7
-6.7 percentage change of mean blood pressure
Standard Error 6.4

SECONDARY outcome

Timeframe: At the end of each two month intervention

Fibrinogen

Outcome measures

Outcome measures
Measure
r-MetHuLeptin
n=5 Participants
r-MetHuLeptin at a dose of 0.04 mg/kg/day divided into two equal doses, which were self-administered by sc injection at 0800 and 2000 h daily for 2 months.
Placebo
n=7 Participants
Placebo at a dose of 0.04 mg/kg/day divided into two equal doses, which were self-administered by sc injection at 0800 and 2000 h daily for 2 months.
Fibrinogen
252.2 mg/dL
Standard Error 16.3
294.4 mg/dL
Standard Error 14.58

SECONDARY outcome

Timeframe: At the end of each two month intervention

Outcome measures

Outcome measures
Measure
r-MetHuLeptin
n=5 Participants
r-MetHuLeptin at a dose of 0.04 mg/kg/day divided into two equal doses, which were self-administered by sc injection at 0800 and 2000 h daily for 2 months.
Placebo
n=7 Participants
Placebo at a dose of 0.04 mg/kg/day divided into two equal doses, which were self-administered by sc injection at 0800 and 2000 h daily for 2 months.
Insulin Levels
11.6 mcIU/ml
Standard Error 4.46
20.3 mcIU/ml
Standard Error 7.04

SECONDARY outcome

Timeframe: At the end of each two month intervention

lean body mass

Outcome measures

Outcome measures
Measure
r-MetHuLeptin
n=5 Participants
r-MetHuLeptin at a dose of 0.04 mg/kg/day divided into two equal doses, which were self-administered by sc injection at 0800 and 2000 h daily for 2 months.
Placebo
n=7 Participants
Placebo at a dose of 0.04 mg/kg/day divided into two equal doses, which were self-administered by sc injection at 0800 and 2000 h daily for 2 months.
Lean Body Mass
58.6 kg
Standard Error 4.41
61.6 kg
Standard Error 4.26

SECONDARY outcome

Timeframe: At the end of each two month intervention

Outcome measures

Outcome measures
Measure
r-MetHuLeptin
n=5 Participants
r-MetHuLeptin at a dose of 0.04 mg/kg/day divided into two equal doses, which were self-administered by sc injection at 0800 and 2000 h daily for 2 months.
Placebo
n=7 Participants
Placebo at a dose of 0.04 mg/kg/day divided into two equal doses, which were self-administered by sc injection at 0800 and 2000 h daily for 2 months.
Viral Load
11345 copies/ml
Standard Error 10596
12367 copies/ml
Standard Error 11861

SECONDARY outcome

Timeframe: At the end of each two month intervention

Outcome measures

Outcome measures
Measure
r-MetHuLeptin
n=5 Participants
r-MetHuLeptin at a dose of 0.04 mg/kg/day divided into two equal doses, which were self-administered by sc injection at 0800 and 2000 h daily for 2 months.
Placebo
n=7 Participants
Placebo at a dose of 0.04 mg/kg/day divided into two equal doses, which were self-administered by sc injection at 0800 and 2000 h daily for 2 months.
CD4+ Lymphocytes
556.6 cells/mcl
Standard Error 135
637.2 cells/mcl
Standard Error 158.4

SECONDARY outcome

Timeframe: At the end of each two month intervention

Outcome measures

Outcome measures
Measure
r-MetHuLeptin
n=5 Participants
r-MetHuLeptin at a dose of 0.04 mg/kg/day divided into two equal doses, which were self-administered by sc injection at 0800 and 2000 h daily for 2 months.
Placebo
n=7 Participants
Placebo at a dose of 0.04 mg/kg/day divided into two equal doses, which were self-administered by sc injection at 0800 and 2000 h daily for 2 months.
Interleukin-6 (IL-6) Levels
1.65 pg/ml
Standard Error 0.38
2.14 pg/ml
Standard Error 0.53

SECONDARY outcome

Timeframe: At the end of each two month intervention

Outcome measures

Outcome measures
Measure
r-MetHuLeptin
n=5 Participants
r-MetHuLeptin at a dose of 0.04 mg/kg/day divided into two equal doses, which were self-administered by sc injection at 0800 and 2000 h daily for 2 months.
Placebo
n=7 Participants
Placebo at a dose of 0.04 mg/kg/day divided into two equal doses, which were self-administered by sc injection at 0800 and 2000 h daily for 2 months.
Hepatic Fat Content
4.02 percentage of liver volume
Standard Error 3.15
4.01 percentage of liver volume
Standard Error 2.65

Adverse Events

r-MetHuLeptin

Serious events: 0 serious events
Other events: 0 other events
Deaths: 0 deaths

Placebo

Serious events: 0 serious events
Other events: 0 other events
Deaths: 0 deaths

Serious adverse events

Adverse event data not reported

Other adverse events

Adverse event data not reported

Additional Information

Dr. Christos Mantzoros

BIDMC

Phone: 617-667-8630

Results disclosure agreements

  • Principal investigator is a sponsor employee
  • Publication restrictions are in place