Trial Outcomes & Findings for Bevacizumab With or Without Cyclophosphamide and Methotrexate: A Pilot Study in Women With Operable Breast Cancer (NCT NCT00121134)

NCT ID: NCT00121134

Last Updated: 2013-12-24

Results Overview

Recruitment status

COMPLETED

Study phase

NA

Target enrollment

164 participants

Primary outcome timeframe

1 year

Results posted on

2013-12-24

Participant Flow

This sequential cohort phase II study was performed in the outpatient setting at four institutions between 2005 and 2008.

A total of 164 participants were registered to enroll in the trial , but only 162 participants initiated treatment. So the evaluable population is 162 participants.

Participant milestones

Participant milestones
Measure
Group A- Bevacizumab Alone
Bevacizumab 15 mg/kg every 3 wks for 1 year
Group B-Bevacizumab+Cyclophosphamide+Methotrexate
Bevacizumab 15 mg/kg every 3 weeks for 1 year +Cyclophosphamide 50 mg orally daily for 6 months +methotrexate 2.5mg orally on day 1-2 each week for 6 months.
Group C-Bevacizumab + Capcitabine(18 Wks)
capecitabine 2000 mg/m2/day 14 days on/7 days off for 18 weeks, and bevacizumab 15 mg/kg every 3 weeks for 1 year
Group D-bevacizumab + Capecitibine (24wks)
capecitabine 2000 mg orally twice per day for 7 days on/7 days off for 24 weeks, and bevacizumab 15 mg/kg every 3 weeks for 1 year.
Overall Study
STARTED
40
41
41
40
Overall Study
COMPLETED
24
26
20
31
Overall Study
NOT COMPLETED
16
15
21
9

Reasons for withdrawal

Reasons for withdrawal
Measure
Group A- Bevacizumab Alone
Bevacizumab 15 mg/kg every 3 wks for 1 year
Group B-Bevacizumab+Cyclophosphamide+Methotrexate
Bevacizumab 15 mg/kg every 3 weeks for 1 year +Cyclophosphamide 50 mg orally daily for 6 months +methotrexate 2.5mg orally on day 1-2 each week for 6 months.
Group C-Bevacizumab + Capcitabine(18 Wks)
capecitabine 2000 mg/m2/day 14 days on/7 days off for 18 weeks, and bevacizumab 15 mg/kg every 3 weeks for 1 year
Group D-bevacizumab + Capecitibine (24wks)
capecitabine 2000 mg orally twice per day for 7 days on/7 days off for 24 weeks, and bevacizumab 15 mg/kg every 3 weeks for 1 year.
Overall Study
Progression of Disease
5
3
4
2
Overall Study
Toxicity
4
7
13
5
Overall Study
Physician Decision
6
4
4
1
Overall Study
Treatment Delay
1
0
0
0
Overall Study
Intercurrent Illness
0
0
0
1
Overall Study
Patient Personal Reasons
0
1
0
0

Baseline Characteristics

Bevacizumab With or Without Cyclophosphamide and Methotrexate: A Pilot Study in Women With Operable Breast Cancer

Baseline characteristics by cohort

Baseline characteristics by cohort
Measure
Group A- Bevacizumab Alone
n=40 Participants
Bevacizumab 15 mg/kg every 3 wks for 1 year
Group B-Bevacizumab+Cyclophosphamide+Methotrexate
n=41 Participants
Bevacizumab 15 mg/kg every 3 weeks for 1 year +Cyclophosphamide 50 mg orally daily for 6 months +methotrexate 2.5mg orally on day 1-2 each week for 6 months.
Group C-Bevacizumab + Capcitabine(18 Wks)
n=41 Participants
capecitabine 2000 mg/m2/day 14 days on/7 days off for 18 weeks, and bevacizumab 15 mg/kg every 3 weeks for 1 year
Group D-bevacizumab + Capecitibine (24wks)
n=40 Participants
capecitabine 2000 mg orally twice per day for 7 days on/7 days off for 24 weeks, and bevacizumab 15 mg/kg every 3 weeks for 1 year.
Total
n=162 Participants
Total of all reporting groups
Age, Continuous
49.05 years
STANDARD_DEVIATION 10.04 • n=5 Participants
48.83 years
STANDARD_DEVIATION 10.34 • n=7 Participants
48.71 years
STANDARD_DEVIATION 10.34 • n=5 Participants
49.55 years
STANDARD_DEVIATION 9.09 • n=4 Participants
49.03 years
STANDARD_DEVIATION 9.88 • n=21 Participants
Sex: Female, Male
Female
40 Participants
n=5 Participants
41 Participants
n=7 Participants
41 Participants
n=5 Participants
40 Participants
n=4 Participants
162 Participants
n=21 Participants
Sex: Female, Male
Male
0 Participants
n=5 Participants
0 Participants
n=7 Participants
0 Participants
n=5 Participants
0 Participants
n=4 Participants
0 Participants
n=21 Participants
Region of Enrollment
United States
40 participants
n=5 Participants
41 participants
n=7 Participants
41 participants
n=5 Participants
40 participants
n=4 Participants
162 participants
n=21 Participants

PRIMARY outcome

Timeframe: 1 year

Outcome measures

Outcome measures
Measure
Group A- Bevacizumab Alone
n=40 Participants
Bevacizumab 15 mg/kg every 3 wks for 1 year
Group B-Bevacizumab+Cyclophosphamide+Methotrexate
n=41 Participants
Bevacizumab 15 mg/kg every 3 weeks for 1 year +Cyclophosphamide 50 mg orally daily for 6 months +methotrexate 2.5mg orally on day 1-2 each week for 6 months.
Group C-Bevacizumab + Capcitabine(18 Wks)
n=41 Participants
capecitabine 2000 mg/m2/day 14 days on/7 days off for 18 weeks, and bevacizumab 15 mg/kg every 3 weeks for 1 year
Group D-bevacizumab + Capecitibine (24wks)
n=40 Participants
capecitabine 2000 mg orally twice per day for 7 days on/7 days off for 24 weeks, and bevacizumab 15 mg/kg every 3 weeks for 1 year.
The Completion Rate of 1 Year of Bevacizumab Therapy for All Four Cohorts
60 percentage of participants
58 percentage of participants
49 percentage of participants
76 percentage of participants

Adverse Events

Group A- Bevacizumab Alone

Serious events: 1 serious events
Other events: 40 other events
Deaths: 0 deaths

Group B-Bevacizumab+Cyclophosphamide+Methotrexate

Serious events: 3 serious events
Other events: 41 other events
Deaths: 0 deaths

Group C-Bevacizumab + Capcitabine(18 Wks)

Serious events: 1 serious events
Other events: 41 other events
Deaths: 0 deaths

Group D-bevacizumab + Capecitibine (24wks)

Serious events: 1 serious events
Other events: 40 other events
Deaths: 0 deaths

Serious adverse events

Serious adverse events
Measure
Group A- Bevacizumab Alone
n=40 participants at risk
Bevacizumab 15 mg/kg every 3 wks for 1 year
Group B-Bevacizumab+Cyclophosphamide+Methotrexate
n=41 participants at risk
Bevacizumab 15 mg/kg every 3 weeks for 1 year +Cyclophosphamide 50 mg orally daily for 6 months +methotrexate 2.5mg orally on day 1-2 each week for 6 months.
Group C-Bevacizumab + Capcitabine(18 Wks)
n=41 participants at risk
capecitabine 2000 mg/m2/day 14 days on/7 days off for 18 weeks, and bevacizumab 15 mg/kg every 3 weeks for 1 year
Group D-bevacizumab + Capecitibine (24wks)
n=40 participants at risk
capecitabine 2000 mg orally twice per day for 7 days on/7 days off for 24 weeks, and bevacizumab 15 mg/kg every 3 weeks for 1 year.
General disorders
Death
0.00%
0/40
0.00%
0/41
0.00%
0/41
2.5%
1/40 • Number of events 1
Respiratory, thoracic and mediastinal disorders
Dyspnea
0.00%
0/40
0.00%
0/41
2.4%
1/41 • Number of events 1
0.00%
0/40
Nervous system disorders
Headache
0.00%
0/40
0.00%
0/41
2.4%
1/41 • Number of events 1
0.00%
0/40
Blood and lymphatic system disorders
Hypertension
0.00%
0/40
2.4%
1/41 • Number of events 1
0.00%
0/41
0.00%
0/40
Skin and subcutaneous tissue disorders
Wound Dehiscence
0.00%
0/40
2.4%
1/41 • Number of events 2
0.00%
0/41
0.00%
0/40
Respiratory, thoracic and mediastinal disorders
Sinusitis
0.00%
0/40
2.4%
1/41 • Number of events 2
0.00%
0/41
0.00%
0/40
Gastrointestinal disorders
Lower GI bleed
2.5%
1/40 • Number of events 1
0.00%
0/41
0.00%
0/41
0.00%
0/40

Other adverse events

Other adverse events
Measure
Group A- Bevacizumab Alone
n=40 participants at risk
Bevacizumab 15 mg/kg every 3 wks for 1 year
Group B-Bevacizumab+Cyclophosphamide+Methotrexate
n=41 participants at risk
Bevacizumab 15 mg/kg every 3 weeks for 1 year +Cyclophosphamide 50 mg orally daily for 6 months +methotrexate 2.5mg orally on day 1-2 each week for 6 months.
Group C-Bevacizumab + Capcitabine(18 Wks)
n=41 participants at risk
capecitabine 2000 mg/m2/day 14 days on/7 days off for 18 weeks, and bevacizumab 15 mg/kg every 3 weeks for 1 year
Group D-bevacizumab + Capecitibine (24wks)
n=40 participants at risk
capecitabine 2000 mg orally twice per day for 7 days on/7 days off for 24 weeks, and bevacizumab 15 mg/kg every 3 weeks for 1 year.
Hepatobiliary disorders
ALT, SGPT
7.5%
3/40 • Number of events 6
17.1%
7/41 • Number of events 8
4.9%
2/41 • Number of events 2
7.5%
3/40 • Number of events 7
Hepatobiliary disorders
AST, SGOT
20.0%
8/40 • Number of events 17
29.3%
12/41 • Number of events 42
17.1%
7/41 • Number of events 12
7.5%
3/40 • Number of events 9
Gastrointestinal disorders
Abdomen, pain
20.0%
8/40 • Number of events 10
4.9%
2/41 • Number of events 3
14.6%
6/41 • Number of events 15
2.5%
1/40 • Number of events 1
Hepatobiliary disorders
Alkaline phosphatase
7.5%
3/40 • Number of events 12
4.9%
2/41 • Number of events 10
4.9%
2/41 • Number of events 2
5.0%
2/40 • Number of events 2
Respiratory, thoracic and mediastinal disorders
Allergic rhinitis
12.5%
5/40 • Number of events 17
0.00%
0/41
4.9%
2/41 • Number of events 2
7.5%
3/40 • Number of events 4
Psychiatric disorders
Agitation
0.00%
0/40
2.4%
1/41 • Number of events 4
0.00%
0/41
5.0%
2/40 • Number of events 2
Immune system disorders
Allergic Reaction
0.00%
0/40
2.4%
1/41 • Number of events 1
2.4%
1/41 • Number of events 1
5.0%
2/40 • Number of events 2
Skin and subcutaneous tissue disorders
Alopecia
2.5%
1/40 • Number of events 1
4.9%
2/41 • Number of events 9
7.3%
3/41 • Number of events 6
5.0%
2/40 • Number of events 5
Gastrointestinal disorders
Anorexia
15.0%
6/40 • Number of events 12
9.8%
4/41 • Number of events 12
19.5%
8/41 • Number of events 14
12.5%
5/40 • Number of events 15
Psychiatric disorders
Anxiety
25.0%
10/40 • Number of events 33
19.5%
8/41 • Number of events 20
19.5%
8/41 • Number of events 34
17.5%
7/40 • Number of events 15
Musculoskeletal and connective tissue disorders
Arthritis
0.00%
0/40
2.4%
1/41 • Number of events 7
0.00%
0/41
10.0%
4/40 • Number of events 9
Musculoskeletal and connective tissue disorders
back,pain
22.5%
9/40 • Number of events 16
26.8%
11/41 • Number of events 31
22.0%
9/41 • Number of events 34
15.0%
6/40 • Number of events 13
Metabolism and nutrition disorders
bicarbonate
0.00%
0/40
9.8%
4/41 • Number of events 11
2.4%
1/41 • Number of events 1
2.5%
1/40 • Number of events 1
Metabolism and nutrition disorders
bilirubin
5.0%
2/40 • Number of events 3
0.00%
0/41
4.9%
2/41 • Number of events 3
2.5%
1/40 • Number of events 2
Musculoskeletal and connective tissue disorders
bone, pain
7.5%
3/40 • Number of events 7
4.9%
2/41 • Number of events 3
7.3%
3/41 • Number of events 12
5.0%
2/40 • Number of events 2
Musculoskeletal and connective tissue disorders
breast,pain
15.0%
6/40 • Number of events 12
7.3%
3/41 • Number of events 22
7.3%
3/41 • Number of events 14
2.5%
1/40 • Number of events 1
Blood and lymphatic system disorders
bruising
15.0%
6/40 • Number of events 12
7.3%
3/41 • Number of events 4
7.3%
3/41 • Number of events 11
2.5%
1/40 • Number of events 2
Musculoskeletal and connective tissue disorders
buttock, pain
0.00%
0/40
0.00%
0/41
0.00%
0/41
5.0%
2/40 • Number of events 8
Skin and subcutaneous tissue disorders
Chelitis
0.00%
0/40
0.00%
0/41
7.3%
3/41 • Number of events 3
0.00%
0/40
Musculoskeletal and connective tissue disorders
chest wall, pain
10.0%
4/40 • Number of events 13
4.9%
2/41 • Number of events 6
2.4%
1/41 • Number of events 1
2.5%
1/40 • Number of events 1
Musculoskeletal and connective tissue disorders
Chest/thoracic pain NOS
2.5%
1/40 • Number of events 1
7.3%
3/41 • Number of events 5
4.9%
2/41 • Number of events 4
7.5%
3/40 • Number of events 3
Gastrointestinal disorders
Constipation
25.0%
10/40 • Number of events 25
12.2%
5/41 • Number of events 17
29.3%
12/41 • Number of events 31
32.5%
13/40 • Number of events 55
General disorders
Constitutional, other
5.0%
2/40 • Number of events 5
2.4%
1/41 • Number of events 1
7.3%
3/41 • Number of events 3
10.0%
4/40 • Number of events 6
Respiratory, thoracic and mediastinal disorders
Cough
37.5%
15/40 • Number of events 34
26.8%
11/41 • Number of events 27
26.8%
11/41 • Number of events 23
30.0%
12/40 • Number of events 22
Hepatobiliary disorders
creatinine
2.5%
1/40 • Number of events 4
12.2%
5/41 • Number of events 8
0.00%
0/41
20.0%
8/40 • Number of events 21
Psychiatric disorders
Depression
7.5%
3/40 • Number of events 18
9.8%
4/41 • Number of events 15
7.3%
3/41 • Number of events 12
32.5%
13/40 • Number of events 28
Gastrointestinal disorders
Diarrhea w/o prior colostomy
30.0%
12/40 • Number of events 31
29.3%
12/41 • Number of events 30
48.8%
20/41 • Number of events 58
35.0%
14/40 • Number of events 32
Nervous system disorders
Dizziness
15.0%
6/40 • Number of events 7
12.2%
5/41 • Number of events 6
7.3%
3/41 • Number of events 6
12.5%
5/40 • Number of events 5
Eye disorders
Dry Eye Syndrome
0.00%
0/40
2.4%
1/41 • Number of events 8
4.9%
2/41 • Number of events 9
5.0%
2/40 • Number of events 5
Skin and subcutaneous tissue disorders
Dry Mouth
0.00%
0/40
2.4%
1/41 • Number of events 1
0.00%
0/41
5.0%
2/40 • Number of events 11
Skin and subcutaneous tissue disorders
Dry Skin
7.5%
3/40 • Number of events 5
0.00%
0/41
9.8%
4/41 • Number of events 10
5.0%
2/40 • Number of events 4
Respiratory, thoracic and mediastinal disorders
Dyspnea
15.0%
6/40 • Number of events 28
17.1%
7/41 • Number of events 26
19.5%
8/41 • Number of events 33
12.5%
5/40 • Number of events 11
Gastrointestinal disorders
Dyspepsia
22.5%
9/40 • Number of events 28
12.2%
5/41 • Number of events 16
7.3%
3/41 • Number of events 17
17.5%
7/40 • Number of events 30
Blood and lymphatic system disorders
Edema limb
12.5%
5/40 • Number of events 15
17.1%
7/41 • Number of events 29
12.2%
5/41 • Number of events 17
12.5%
5/40 • Number of events 11
Skin and subcutaneous tissue disorders
Erythema multiforme
7.5%
3/40 • Number of events 6
2.4%
1/41 • Number of events 1
0.00%
0/41
7.5%
3/40 • Number of events 5
Musculoskeletal and connective tissue disorders
Extrapyramidal movement
5.0%
2/40 • Number of events 6
0.00%
0/41
0.00%
0/41
0.00%
0/40
Musculoskeletal and connective tissue disorders
Extremity-limb, pain
35.0%
14/40 • Number of events 43
22.0%
9/41 • Number of events 53
19.5%
8/41 • Number of events 34
15.0%
6/40 • Number of events 18
General disorders
fatigue
52.5%
21/40 • Number of events 117
70.7%
29/41 • Number of events 147
70.7%
29/41 • Number of events 149
72.5%
29/40 • Number of events 182
Blood and lymphatic system disorders
febrile neutropenia
0.00%
0/40
2.4%
1/41 • Number of events 1
2.4%
1/41 • Number of events 1
5.0%
2/40 • Number of events 2
General disorders
fever w/o neutropenia
12.5%
5/40 • Number of events 6
17.1%
7/41 • Number of events 13
7.3%
3/41 • Number of events 3
10.0%
4/40 • Number of events 4
Gastrointestinal disorders
flatulence
5.0%
2/40 • Number of events 3
0.00%
0/41
0.00%
0/41
5.0%
2/40 • Number of events 5
Gastrointestinal disorders
Gastrointestinal-other
2.5%
1/40 • Number of events 1
4.9%
2/41 • Number of events 2
12.2%
5/41 • Number of events 7
7.5%
3/40 • Number of events 5
Skin and subcutaneous tissue disorders
Hand-foot reaction
0.00%
0/40
2.4%
1/41 • Number of events 1
90.2%
37/41 • Number of events 170
95.0%
38/40 • Number of events 191
Nervous system disorders
Head/headache
77.5%
31/40 • Number of events 121
68.3%
28/41 • Number of events 99
56.1%
23/41 • Number of events 106
65.0%
26/40 • Number of events 113
Blood and lymphatic system disorders
hematologic-other
7.5%
3/40 • Number of events 13
22.0%
9/41 • Number of events 108
9.8%
4/41 • Number of events 14
25.0%
10/40 • Number of events 51
Blood and lymphatic system disorders
hemoglobin
2.5%
1/40 • Number of events 1
22.0%
9/41 • Number of events 58
7.3%
3/41 • Number of events 8
12.5%
5/40 • Number of events 12
Blood and lymphatic system disorders
hemorrhage-other
5.0%
2/40 • Number of events 7
4.9%
2/41 • Number of events 2
0.00%
0/41
5.0%
2/40 • Number of events 2
Skin and subcutaneous tissue disorders
hemorrhoids
5.0%
2/40 • Number of events 2
0.00%
0/41
4.9%
2/41 • Number of events 4
0.00%
0/40
General disorders
Hot flashes
40.0%
16/40 • Number of events 89
24.4%
10/41 • Number of events 78
26.8%
11/41 • Number of events 58
45.0%
18/40 • Number of events 72
Metabolism and nutrition disorders
hypercalcemia
7.5%
3/40 • Number of events 13
2.4%
1/41 • Number of events 1
0.00%
0/41
0.00%
0/40
Endocrine disorders
Hyperglycemia
30.0%
12/40 • Number of events 28
22.0%
9/41 • Number of events 23
17.1%
7/41 • Number of events 12
25.0%
10/40 • Number of events 39
Metabolism and nutrition disorders
Hyperkalemia
5.0%
2/40 • Number of events 2
4.9%
2/41 • Number of events 5
0.00%
0/41
5.0%
2/40 • Number of events 2
Metabolism and nutrition disorders
Hypernatremia
2.5%
1/40 • Number of events 1
9.8%
4/41 • Number of events 9
9.8%
4/41 • Number of events 5
5.0%
2/40 • Number of events 3
Skin and subcutaneous tissue disorders
Hyperpigmentation
2.5%
1/40 • Number of events 7
2.4%
1/41 • Number of events 4
9.8%
4/41 • Number of events 24
5.0%
2/40 • Number of events 6
Blood and lymphatic system disorders
Hypertension
55.0%
22/40 • Number of events 50
39.0%
16/41 • Number of events 66
34.1%
14/41 • Number of events 54
35.0%
14/40 • Number of events 44
Metabolism and nutrition disorders
Hypoalbuminemia
10.0%
4/40 • Number of events 17
0.00%
0/41
0.00%
0/41
2.5%
1/40 • Number of events 1
Metabolism and nutrition disorders
Hypocalcemia
17.5%
7/40 • Number of events 14
9.8%
4/41 • Number of events 5
2.4%
1/41 • Number of events 1
12.5%
5/40 • Number of events 6
Endocrine disorders
Hypoglycemia
7.5%
3/40 • Number of events 3
9.8%
4/41 • Number of events 6
4.9%
2/41 • Number of events 2
7.5%
3/40 • Number of events 5
Metabolism and nutrition disorders
Hypokalemia
15.0%
6/40 • Number of events 14
2.4%
1/41 • Number of events 1
0.00%
0/41
5.0%
2/40 • Number of events 5
Metabolism and nutrition disorders
Hyponatremia
7.5%
3/40 • Number of events 11
14.6%
6/41 • Number of events 10
0.00%
0/41
5.0%
2/40 • Number of events 10
Infections and infestations
Infection Gr0-2 neut, bronchus
7.5%
3/40 • Number of events 4
0.00%
0/41
2.4%
1/41 • Number of events 1
0.00%
0/40
Infections and infestations
Infection Gr0-2 neut, sinus
10.0%
4/40 • Number of events 7
7.3%
3/41 • Number of events 3
12.2%
5/41 • Number of events 10
7.5%
3/40 • Number of events 4
Infections and infestations
Infection Gr0-2 neut, skin
2.5%
1/40 • Number of events 1
4.9%
2/41 • Number of events 3
0.00%
0/41
5.0%
2/40 • Number of events 2
Infections and infestations
Infection Gr0-2 neut, upper airway
12.5%
5/40 • Number of events 5
7.3%
3/41 • Number of events 4
14.6%
6/41 • Number of events 11
2.5%
1/40 • Number of events 1
Infections and infestations
Infection Gr0-2 neut, urinary tract
5.0%
2/40 • Number of events 3
2.4%
1/41 • Number of events 2
4.9%
2/41 • Number of events 4
2.5%
1/40 • Number of events 1
Infections and infestations
Infection w/unk ANC upper airway NOS
2.5%
1/40 • Number of events 1
0.00%
0/41
0.00%
0/41
5.0%
2/40 • Number of events 3
Infections and infestations
Infection-other
20.0%
8/40 • Number of events 9
9.8%
4/41 • Number of events 4
2.4%
1/41 • Number of events 2
10.0%
4/40 • Number of events 6
General disorders
Insomnia
20.0%
8/40 • Number of events 48
14.6%
6/41 • Number of events 19
22.0%
9/41 • Number of events 45
25.0%
10/40 • Number of events 44
Reproductive system and breast disorders
irregular menses
5.0%
2/40 • Number of events 8
0.00%
0/41
2.4%
1/41 • Number of events 5
5.0%
2/40 • Number of events 3
Musculoskeletal and connective tissue disorders
joint, pain
77.5%
31/40 • Number of events 156
43.9%
18/41 • Number of events 110
56.1%
23/41 • Number of events 111
60.0%
24/40 • Number of events 103
Musculoskeletal and connective tissue disorders
joint-function
0.00%
0/40
2.4%
1/41 • Number of events 1
2.4%
1/41 • Number of events 1
5.0%
2/40 • Number of events 5
Blood and lymphatic system disorders
Leukocytes
22.5%
9/40 • Number of events 23
26.8%
11/41 • Number of events 34
9.8%
4/41 • Number of events 6
17.5%
7/40 • Number of events 19
Nervous system disorders
Memory impairment
2.5%
1/40 • Number of events 1
2.4%
1/41 • Number of events 3
0.00%
0/41
5.0%
2/40 • Number of events 3
Metabolism and nutrition disorders
Metabolic/laboratory-other
30.0%
12/40 • Number of events 42
29.3%
12/41 • Number of events 67
9.8%
4/41 • Number of events 7
12.5%
5/40 • Number of events 11
Infections and infestations
Muco/stomatitis(symptom) oral cavity
22.5%
9/40 • Number of events 29
24.4%
10/41 • Number of events 43
48.8%
20/41 • Number of events 56
35.0%
14/40 • Number of events 36
Infections and infestations
Muco/stomatitis by exam, oral cavity
2.5%
1/40 • Number of events 1
12.2%
5/41 • Number of events 22
19.5%
8/41 • Number of events 13
17.5%
7/40 • Number of events 9
Musculoskeletal and connective tissue disorders
Muscle, pain
25.0%
10/40 • Number of events 28
9.8%
4/41 • Number of events 11
14.6%
6/41 • Number of events 13
10.0%
4/40 • Number of events 20
Musculoskeletal and connective tissue disorders
Musculoskeletal/soft tissue-other
7.5%
3/40 • Number of events 3
17.1%
7/41 • Number of events 29
14.6%
6/41 • Number of events 16
12.5%
5/40 • Number of events 8
Skin and subcutaneous tissue disorders
Nail changes
0.00%
0/40
7.3%
3/41 • Number of events 12
2.4%
1/41 • Number of events 2
5.0%
2/40 • Number of events 8
Respiratory, thoracic and mediastinal disorders
Nasal cavity/paranasal sinus reaction
0.00%
0/40
4.9%
2/41 • Number of events 2
4.9%
2/41 • Number of events 3
12.5%
5/40 • Number of events 23
Gastrointestinal disorders
Nausea
25.0%
10/40 • Number of events 23
46.3%
19/41 • Number of events 37
31.7%
13/41 • Number of events 27
42.5%
17/40 • Number of events 41
Musculoskeletal and connective tissue disorders
Neck,pain
20.0%
8/40 • Number of events 14
2.4%
1/41 • Number of events 1
7.3%
3/41 • Number of events 4
10.0%
4/40 • Number of events 8
Nervous system disorders
Neuropathy-sensory
25.0%
10/40 • Number of events 48
26.8%
11/41 • Number of events 47
26.8%
11/41 • Number of events 45
37.5%
15/40 • Number of events 58
Blood and lymphatic system disorders
Neutrophils
15.0%
6/40 • Number of events 12
31.7%
13/41 • Number of events 26
9.8%
4/41 • Number of events 4
17.5%
7/40 • Number of events 17
General disorders
Nonneuropathic generalized weakness
5.0%
2/40 • Number of events 11
0.00%
0/41
0.00%
0/41
2.5%
1/40 • Number of events 1
Blood and lymphatic system disorders
Nose, hemorrhage
40.0%
16/40 • Number of events 45
46.3%
19/41 • Number of events 54
29.3%
12/41 • Number of events 28
35.0%
14/40 • Number of events 40
Blood and lymphatic system disorders
Oral cavity, hemorrhage
2.5%
1/40 • Number of events 1
2.4%
1/41 • Number of events 2
2.4%
1/41 • Number of events 3
7.5%
3/40 • Number of events 4
General disorders
Oral gums, pain
2.5%
1/40 • Number of events 1
0.00%
0/41
0.00%
0/41
5.0%
2/40 • Number of events 3
Nervous system disorders
Pain NOS
5.0%
2/40 • Number of events 9
0.00%
0/41
0.00%
0/41
0.00%
0/40
Nervous system disorders
Pain-other
15.0%
6/40 • Number of events 15
22.0%
9/41 • Number of events 16
14.6%
6/41 • Number of events 12
17.5%
7/40 • Number of events 10
Cardiac disorders
Palpitations
5.0%
2/40 • Number of events 5
4.9%
2/41 • Number of events 7
0.00%
0/41
0.00%
0/40
Blood and lymphatic system disorders
Platelets
5.0%
2/40 • Number of events 9
9.8%
4/41 • Number of events 14
9.8%
4/41 • Number of events 8
12.5%
5/40 • Number of events 22
Renal and urinary disorders
Proteinuria
52.5%
21/40 • Number of events 61
68.3%
28/41 • Number of events 89
61.0%
25/41 • Number of events 77
52.5%
21/40 • Number of events 71
Skin and subcutaneous tissue disorders
Pruritus/itching
15.0%
6/40 • Number of events 8
4.9%
2/41 • Number of events 3
4.9%
2/41 • Number of events 5
12.5%
5/40 • Number of events 7
Respiratory, thoracic and mediastinal disorders
Pulmonary/upper respiratory-other
17.5%
7/40 • Number of events 11
29.3%
12/41 • Number of events 43
24.4%
10/41 • Number of events 26
40.0%
16/40 • Number of events 44
Skin and subcutaneous tissue disorders
Radiation dermatitis
5.0%
2/40 • Number of events 2
0.00%
0/41
0.00%
0/41
0.00%
0/40
Skin and subcutaneous tissue disorders
Rash/desquamation
17.5%
7/40 • Number of events 12
19.5%
8/41 • Number of events 12
12.2%
5/41 • Number of events 9
7.5%
3/40 • Number of events 5
Skin and subcutaneous tissue disorders
Rash: acne/acneiform
2.5%
1/40 • Number of events 1
2.4%
1/41 • Number of events 1
4.9%
2/41 • Number of events 5
20.0%
8/40 • Number of events 12
Gastrointestinal disorders
Rectum, hemorrhage
10.0%
4/40 • Number of events 9
0.00%
0/41
2.4%
1/41 • Number of events 1
0.00%
0/40
Musculoskeletal and connective tissue disorders
Rigors/chills
5.0%
2/40 • Number of events 3
4.9%
2/41 • Number of events 2
4.9%
2/41 • Number of events 3
0.00%
0/40
Skin and subcutaneous tissue disorders
Skin-other
10.0%
4/40 • Number of events 5
4.9%
2/41 • Number of events 2
14.6%
6/41 • Number of events 12
17.5%
7/40 • Number of events 13
Skin and subcutaneous tissue disorders
Sweating
7.5%
3/40 • Number of events 4
9.8%
4/41 • Number of events 12
0.00%
0/41
2.5%
1/40 • Number of events 1
General disorders
Taste disturbance
17.5%
7/40 • Number of events 27
9.8%
4/41 • Number of events 15
17.1%
7/41 • Number of events 36
20.0%
8/40 • Number of events 29
Eye disorders
Tearing
2.5%
1/40 • Number of events 1
0.00%
0/41
0.00%
0/41
5.0%
2/40 • Number of events 3
General disorders
Throat/Pharynx/larynx,pain
5.0%
2/40 • Number of events 3
2.4%
1/41 • Number of events 1
2.4%
1/41 • Number of events 1
5.0%
2/40 • Number of events 2
Reproductive system and breast disorders
Vagina, hemorrhage
0.00%
0/40
2.4%
1/41 • Number of events 2
0.00%
0/41
5.0%
2/40 • Number of events 4
Reproductive system and breast disorders
Vaginal discharge (non-infectious)
5.0%
2/40 • Number of events 3
4.9%
2/41 • Number of events 3
2.4%
1/41 • Number of events 2
0.00%
0/40
Reproductive system and breast disorders
Vaginal dryness
15.0%
6/40 • Number of events 19
2.4%
1/41 • Number of events 1
2.4%
1/41 • Number of events 1
5.0%
2/40 • Number of events 2
Eye disorders
Vision-blurred
2.5%
1/40 • Number of events 1
4.9%
2/41 • Number of events 3
7.3%
3/41 • Number of events 5
2.5%
1/40 • Number of events 1
General disorders
Voice changes/dysarthria
10.0%
4/40 • Number of events 14
12.2%
5/41 • Number of events 36
7.3%
3/41 • Number of events 8
5.0%
2/40 • Number of events 13
Gastrointestinal disorders
Vomiting
17.5%
7/40 • Number of events 12
7.3%
3/41 • Number of events 6
14.6%
6/41 • Number of events 7
22.5%
9/40 • Number of events 13
General disorders
Weight Gain
2.5%
1/40 • Number of events 2
0.00%
0/41
0.00%
0/41
7.5%
3/40 • Number of events 6
Skin and subcutaneous tissue disorders
Wound-non-infectious
2.5%
1/40 • Number of events 1
2.4%
1/41 • Number of events 1
0.00%
0/41
5.0%
2/40 • Number of events 2
Cardiac disorders
Cardiac-other
2.5%
1/40 • Number of events 3
7.3%
3/41 • Number of events 7
7.3%
3/41 • Number of events 4
5.0%
2/40 • Number of events 4

Additional Information

Dr Harold J. Burstein

DFCI

Phone: 617-632-3800

Results disclosure agreements

  • Principal investigator is a sponsor employee
  • Publication restrictions are in place