Trial Outcomes & Findings for UARK 98-026 TT II: Multiple Myeloma Evaluating Anti-Angiogenesis With Thalidomide and Post-Transplant Consolidation Chemotherapy (NCT NCT00083551)

NCT ID: NCT00083551

Last Updated: 2015-11-23

Results Overview

Overall Survival at six years after initiating protocol therapy

Recruitment status

COMPLETED

Study phase

PHASE3

Target enrollment

668 participants

Primary outcome timeframe

6 Years

Results posted on

2015-11-23

Participant Flow

Participant milestones

Participant milestones
Measure
Thalidomide
Thalidomide 400 QD during induction, 100 mg QD between transplants, 200 mg QD post transplant, 100 mg QD during year one of maintenance, and 50 mg QD during second year of maintenance.
No Thalidomide
Patient received no thalidomide during induction, consolidation, and maintenance therapy.
Overall Study
STARTED
323
345
Overall Study
COMPLETED
323
345
Overall Study
NOT COMPLETED
0
0

Reasons for withdrawal

Withdrawal data not reported

Baseline Characteristics

UARK 98-026 TT II: Multiple Myeloma Evaluating Anti-Angiogenesis With Thalidomide and Post-Transplant Consolidation Chemotherapy

Baseline characteristics by cohort

Baseline characteristics by cohort
Measure
Thalidomide
n=323 Participants
Thalidomide 400 QD during induction, 100 mg QD between transplants, 200 mg QD post transplant, 100 mg QD during year one of maintenance, and 50 mg QD during second year of maintenance.
No Thalidomide
n=345 Participants
Patient received no thalidomide during induction, consolidation, and maintenance therapy.
Total
n=668 Participants
Total of all reporting groups
Age, Customized
>/= 60 to < 65 years
130 participants
n=5 Participants
129 participants
n=7 Participants
259 participants
n=5 Participants
Age, Customized
>/= 65 years
64 participants
n=5 Participants
72 participants
n=7 Participants
136 participants
n=5 Participants
Age, Customized
< 60 years
129 participants
n=5 Participants
144 participants
n=7 Participants
273 participants
n=5 Participants
Sex: Female, Male
Female
137 Participants
n=5 Participants
135 Participants
n=7 Participants
272 Participants
n=5 Participants
Sex: Female, Male
Male
186 Participants
n=5 Participants
210 Participants
n=7 Participants
396 Participants
n=5 Participants

PRIMARY outcome

Timeframe: 6 Years

Overall Survival at six years after initiating protocol therapy

Outcome measures

Outcome measures
Measure
Thalidomide
n=323 Participants
Thalidomide 400 QD during induction, 100 mg QD between transplants, 200 mg QD post transplant, 100 mg QD during year one of maintenance, and 50 mg QD during second year of maintenance.
No Thalidomide
n=345 Participants
Patient received no thalidomide during induction, consolidation, and maintenance therapy.
Overall Survival
65 percentage of participants
58 percentage of participants

Adverse Events

Thalidomide

Serious events: 323 serious events
Other events: 323 other events
Deaths: 0 deaths

No Thalidomide

Serious events: 345 serious events
Other events: 345 other events
Deaths: 0 deaths

Serious adverse events

Serious adverse events
Measure
Thalidomide
n=323 participants at risk
Thalidomide 400 QD during induction, 100 mg QD between transplants, 200 mg QD post transplant, 100 mg QD during year one of maintenance, and 50 mg QD during second year of maintenance.
No Thalidomide
n=345 participants at risk
Patient received no thalidomide during induction, consolidation, and maintenance therapy.
Nervous system disorders
Grade4 Tremor
0.62%
2/323
0.29%
1/345
Nervous system disorders
Grade 3 Weakness (motor neuropathy)
17.0%
55/323
10.4%
36/345
Nervous system disorders
Grade 4 Weakness (motor neuropathy)
0.93%
3/323
1.4%
5/345
General disorders
Grade 3 Abdominal pain/cramping
3.1%
10/323
2.3%
8/345
General disorders
Grade 4 Abdominal pain/cramping
0.00%
0/323
0.29%
1/345
Cardiac disorders
Grade 3 Arrhythmia, NOS
3.7%
12/323
6.1%
21/345
Cardiac disorders
Grade 4 Arrhythmia, NOS
0.62%
2/323
0.58%
2/345
Cardiac disorders
Grade 3 Cardiac ischemia/infarction
0.93%
3/323
0.58%
2/345
Cardiac disorders
Grade 4 Cardiac ischemia/infarction
0.62%
2/323
0.29%
1/345
Cardiac disorders
Grade 3 Cardiovascular-other
2.2%
7/323
0.29%
1/345
Cardiac disorders
Grade 4 Cardiovascular-other
0.00%
0/323
0.29%
1/345
Cardiac disorders
Grade 3 Cerebrovascular ischemia
2.2%
7/323
0.58%
2/345
Cardiac disorders
Grade 4 Cerebrovascular ischemia
0.31%
1/323
0.00%
0/345
Cardiac disorders
Grade 3 Conduction abnormality/block
0.00%
0/323
0.29%
1/345
Cardiac disorders
Grade 4 Conduction abnormality/block
0.00%
0/323
0.29%
1/345
Cardiac disorders
Grade 3 Edema
1.9%
6/323
1.2%
4/345
Cardiac disorders
Grade 3 Hypertension
2.2%
7/323
2.0%
7/345
Cardiac disorders
Grade 3 Hypotension
2.5%
8/323
2.3%
8/345
Cardiac disorders
Grade 4 Hypotension
1.5%
5/323
0.00%
0/345
Cardiac disorders
Grade 3 LVEF decrease/CHF
0.00%
0/323
0.58%
2/345
Cardiac disorders
Grade 3 Nodal/junctional dysrhythmia
0.31%
1/323
0.00%
0/345
Cardiac disorders
Grade 3 Sinus bradycardia
1.9%
6/323
0.58%
2/345
Cardiac disorders
Grade 4 Sinus bradycardia
0.31%
1/323
0.00%
0/345
Cardiac disorders
Grade 3 Sinus tachycardia
0.93%
3/323
0.58%
2/345
Cardiac disorders
Grade 3 Supraventricular arrhythmia
2.2%
7/323
2.0%
7/345
Cardiac disorders
Grade 4 Supraventricular arrhythmia
0.00%
0/323
0.29%
1/345
Cardiac disorders
Grade 3 Surgery-injury of vein/artery
0.00%
0/323
0.29%
1/345
Cardiac disorders
Grade 3 Syncope
9.6%
31/323
3.5%
12/345
Cardiac disorders
Grade 3 Thrombosis/embolism
21.4%
69/323
13.6%
47/345
Cardiac disorders
Grade 4 Thrombosis/embolism
3.4%
11/323
0.87%
3/345
Cardiac disorders
Grade 3 Valvular heart disease
0.31%
1/323
0.00%
0/345
Cardiac disorders
Grade 3 Vasovagal episode
0.31%
1/323
0.00%
0/345
Cardiac disorders
Grade 3 Ventricular arrhythmia
0.62%
2/323
0.87%
3/345
Cardiac disorders
Grade 4 Ventricular arrhythmia
0.31%
1/323
0.00%
0/345
Cardiac disorders
Grade 3 Supra Arrhyth: Atrial Fib.
0.31%
1/323
0.00%
0/345
Blood and lymphatic system disorders
Grade 3 Clotting-other
0.31%
1/323
0.00%
0/345
Blood and lymphatic system disorders
Grade 3 Prothrombin time increase
0.31%
1/323
0.00%
0/345
Blood and lymphatic system disorders
Grade 3 Thrombotic microangiopathy
0.31%
1/323
0.00%
0/345
Ear and labyrinth disorders
Grade 3 Hearing
0.31%
1/323
0.29%
1/345
Ear and labyrinth disorders
Grade 3 Inner ear - hearing loss
2.5%
8/323
0.00%
0/345
Ear and labyrinth disorders
Grade 3 Middle ear - hearing loss/otitis
0.62%
2/323
0.29%
1/345
Endocrine disorders
Grade 3 Diabetes
0.31%
1/323
0.29%
1/345
Endocrine disorders
Grade 3 Endocrine - other
0.31%
1/323
0.00%
0/345
Endocrine disorders
Grade 3 SIADH
0.00%
0/323
0.29%
1/345
Eye disorders
Grade 3 Blurred vision
0.93%
3/323
0.58%
2/345
Eye disorders
Grade 3 Cataract
3.1%
10/323
1.2%
4/345
Eye disorders
Grade 3 Double vision
0.00%
0/323
0.29%
1/345
Eye disorders
Grade 3 Eye - other
0.62%
2/323
0.29%
1/345
Eye disorders
Grade 3 Keratitis
0.00%
0/323
0.29%
1/345
Eye disorders
Grade 3 Photophobia
0.00%
0/323
0.29%
1/345
Eye disorders
Grade 4 Retinopathy
0.31%
1/323
0.00%
0/345
General disorders
Grade 3 Fatigue/malaise/lethargy
40.2%
130/323
40.3%
139/345
General disorders
Grade 4 Fatigue/malaise/lethargy
12.4%
40/323
15.1%
52/345
General disorders
Grade 3 Fever without neutropenia
0.62%
2/323
2.3%
8/345
General disorders
Grade 4 Fever without neutropenia
0.00%
0/323
0.29%
1/345
General disorders
Grade 3 Fever, NOS
9.0%
29/323
7.2%
25/345
General disorders
Grade 4 Fever, NOS
0.62%
2/323
0.87%
3/345
General disorders
Grade 3 Flu-like symptoms-other
0.93%
3/323
1.2%
4/345
General disorders
Grade 3 Insomnia
0.31%
1/323
0.00%
0/345
General disorders
Grade 3 Obesity
0.00%
0/323
0.29%
1/345
General disorders
Grade 3 Rigors/chills
0.00%
0/323
0.29%
1/345
General disorders
Grade 4 Sweating
0.00%
0/323
0.29%
1/345
General disorders
Grade 3 Weight loss
0.31%
1/323
0.29%
1/345
Gastrointestinal disorders
Grade 3 Anal incontinence
0.31%
1/323
0.00%
0/345
Gastrointestinal disorders
Grade 3 Anorexia
29.1%
94/323
28.7%
99/345
Gastrointestinal disorders
Grade 4 Anorexia
1.9%
6/323
1.7%
6/345
Gastrointestinal disorders
Grade 3 Colitis
2.5%
8/323
1.4%
5/345
Gastrointestinal disorders
Grade 4 Colitis
0.31%
1/323
2.0%
7/345
Gastrointestinal disorders
Grade 3 Constipation/bowel obstruction
9.6%
31/323
4.9%
17/345
Gastrointestinal disorders
Grade 4 Constipation/bowel obstruction
1.9%
6/323
2.3%
8/345
Gastrointestinal disorders
Grade 3 Dehydration
1.2%
4/323
1.4%
5/345
Gastrointestinal disorders
Grade 3 Diarrhea with colostomy
0.31%
1/323
1.2%
4/345
Gastrointestinal disorders
Grade 3 Diarrhea without colostomy
18.9%
61/323
23.2%
80/345
Gastrointestinal disorders
Grade 4 Diarrhea without colostomy
2.5%
8/323
2.0%
7/345
Gastrointestinal disorders
Grade 3 Dyspepsia/heartburn
0.93%
3/323
0.58%
2/345
Gastrointestinal disorders
Grade 3 Esophagitis/dysphagia
8.0%
26/323
10.1%
35/345
Gastrointestinal disorders
Grade 4 Esophagitis/dysphagia
3.1%
10/323
2.0%
7/345
Gastrointestinal disorders
Grade 3 Dysphagia
0.31%
1/323
0.00%
0/345
Gastrointestinal disorders
Grade 3 GI Mucositis, NOS
6.2%
20/323
2.9%
10/345
Gastrointestinal disorders
Grade 4 GI Mucositis, NOS
0.00%
0/323
0.29%
1/345
Gastrointestinal disorders
Grade 3 GI-other
0.62%
2/323
1.7%
6/345
Gastrointestinal disorders
Grade 4 GI-other
0.62%
2/323
0.29%
1/345
Gastrointestinal disorders
Grade 3 Ileus
0.00%
0/323
0.58%
2/345
Gastrointestinal disorders
Grade 3 Mouth Dryness
2.2%
7/323
1.4%
5/345
Gastrointestinal disorders
Grade 4 Mouth Dryness
0.00%
0/323
0.29%
1/345
Gastrointestinal disorders
Grade 3 Nausea
36.2%
117/323
34.2%
118/345
Gastrointestinal disorders
Grade 4 Nausea
0.93%
3/323
1.2%
4/345
Gastrointestinal disorders
Grade 3 Pancreatitis
0.31%
1/323
0.00%
0/345
Gastrointestinal disorders
Grade 3 Periodontal
0.31%
1/323
0.00%
0/345
Gastrointestinal disorders
Grade 3 RT-GI mucositis, NOS
0.31%
1/323
0.00%
0/345
Gastrointestinal disorders
Grade 3 Stomatitis/pharyngitis
18.6%
60/323
11.9%
41/345
Gastrointestinal disorders
Grade 4 Stomatitis/pharyngitis
2.2%
7/323
3.5%
12/345
Gastrointestinal disorders
Grade 3 Vomiting
11.5%
37/323
12.2%
42/345
Gastrointestinal disorders
Grade 4 Vomiting
1.9%
6/323
2.3%
8/345
Renal and urinary disorders
Grade 3 Bladder Spasms
1.2%
4/323
0.58%
2/345
Renal and urinary disorders
Grade 4 Bladder Spasms
0.31%
1/323
0.29%
1/345
Renal and urinary disorders
Grade 3 Creatinine increase
3.7%
12/323
2.3%
8/345
Renal and urinary disorders
Grade 4 Creatinine increase
5.0%
16/323
4.3%
15/345
Renal and urinary disorders
Grade 3 GU-other
0.62%
2/323
0.29%
1/345
Renal and urinary disorders
Grade 3 incontinence
0.00%
0/323
0.29%
1/345
Renal and urinary disorders
Grade 3 Renal failure
1.9%
6/323
1.7%
6/345
Renal and urinary disorders
Grade 4 Renal failure
2.5%
8/323
1.4%
5/345
Renal and urinary disorders
Grade 3 Urinary frequency/urgency
0.00%
0/323
0.58%
2/345
Renal and urinary disorders
Grade 3 Urinary retention
0.31%
1/323
0.00%
0/345
Blood and lymphatic system disorders
Grade 4 Anemia (HGB)
8.4%
27/323
9.9%
34/345
Blood and lymphatic system disorders
Grade 4 Neutropenia/granulocytopenia
74.9%
242/323
75.1%
259/345
Blood and lymphatic system disorders
Grade 4 Platelet transfusion
0.31%
1/323
0.00%
0/345
Blood and lymphatic system disorders
Grade 4 Thrombocytopenia (PLT)
49.2%
159/323
48.7%
168/345
Blood and lymphatic system disorders
Grade 4 Leukopenia (WBC)
79.6%
257/323
80.9%
279/345
Blood and lymphatic system disorders
Grade 3 Hematuria
1.5%
5/323
1.2%
4/345
Blood and lymphatic system disorders
Grade 4 Hematuria
0.00%
0/323
0.29%
1/345
Blood and lymphatic system disorders
Grade 3 Hemorrhage w/3-4 thrombocytopenia
11.8%
38/323
10.7%
37/345
Blood and lymphatic system disorders
Grade 4 Hemorrhage w/3-4 thrombocytopenia
1.9%
6/323
2.9%
10/345
Blood and lymphatic system disorders
Grade 3 Hemorrhage w/o 3-4 thrombocytopenia
0.00%
0/323
0.29%
1/345
Blood and lymphatic system disorders
Grade 3 Hemorrhage-other
0.31%
1/323
0.00%
0/345
Blood and lymphatic system disorders
Grade 4 Vaginal bleeding
0.31%
1/323
0.00%
0/345
Blood and lymphatic system disorders
Grade 3 Petechiae/purpura
0.00%
0/323
0.29%
1/345
Blood and lymphatic system disorders
Grade 3 Melena/GI bleeding
1.9%
6/323
2.6%
9/345
Blood and lymphatic system disorders
Grade 4 Melena/GI bleeding
0.62%
2/323
0.58%
2/345
Immune system disorders
Grade 3 Allergic/hypersensitivity
0.00%
0/323
0.29%
1/345
Immune system disorders
Grade 3 Autoimmune reaction
1.2%
4/323
0.29%
1/345
Immune system disorders
Grade 4 Autoimmune reaction
1.2%
4/323
0.00%
0/345
Infections and infestations
Grade 3 Catheter related infection
3.4%
11/323
5.2%
18/345
Infections and infestations
Grade 3 Ear infection ANC mid ear
0.00%
0/323
0.29%
1/345
Infections and infestations
Grade 3 Febrile neutropenia
19.2%
62/323
23.2%
80/345
Infections and infestations
Grade 4 Febrile neutropenia
0.00%
0/323
0.58%
2/345
Infections and infestations
Grade 3 GI infection 3-4 ANC abdomen
0.00%
0/323
0.29%
1/345
Infections and infestations
Grade 3 GI infection 3-4 ANC appendix
0.00%
0/323
0.29%
1/345
Infections and infestations
Grade 3 GI Infection 3-4 ANC tooth
0.00%
0/323
0.29%
1/345
Infections and infestations
Grade 3 GI infection ANC abdomen
0.00%
0/323
0.29%
1/345
Infections and infestations
Grade 3 GU infection ABC UTI
0.31%
1/323
0.00%
0/345
Infections and infestations
Grade 3 Infection w/grade 3 or 4 Neutrophils
0.93%
3/323
0.29%
1/345
Infections and infestations
Grade 3 Infection w/o 3-4 Neutropenia
9.0%
29/323
11.0%
38/345
Infections and infestations
Grade 4 Infection w/o 3-4 Neutropenia
0.31%
1/323
0.29%
1/345
Infections and infestations
Grade 3 Infection w/3-4 Neutropenia
8.7%
28/323
7.8%
27/345
Infections and infestations
Grade 4 Infection w/3-4 Neutropenia
0.00%
0/323
0.29%
1/345
Infections and infestations
Grade 3 Infection ANC
8.4%
27/323
7.2%
25/345
Infections and infestations
Grade 4 Infection ANC
0.31%
1/323
0.00%
0/345
Infections and infestations
Grade 3 Lung infection 3-4 ANC
0.31%
1/323
0.00%
0/345
Infections and infestations
Grade 3 Lung Infection ANC Bronchus
0.31%
1/323
0.00%
0/345
Infections and infestations
Grade 3 Lung Infection ANC Lung
0.31%
1/323
0.00%
0/345
Infections and infestations
Grade 3 Lung Infection ANC Pharynx
0.31%
1/323
0.00%
0/345
Infections and infestations
Grade 3 Moderate
0.31%
1/323
0.58%
2/345
Infections and infestations
Grade 3 Respiratory infect w/neutrop
1.2%
4/323
0.58%
2/345
Infections and infestations
Grade 3 Muscle infection ANC Bone
0.31%
1/323
0.00%
0/345
Infections and infestations
Grade 3 Respiratory infection w/o neutrop
5.3%
17/323
2.9%
10/345
Infections and infestations
Grade 4 Respiratory infection w/o neutrop
0.31%
1/323
0.29%
1/345
Infections and infestations
Grade 3 Respiratory infection ANC
5.6%
18/323
3.2%
11/345
Infections and infestations
Grade 3 Skin infection 3-4 ANC lip/perior
0.31%
1/323
0.00%
0/345
Infections and infestations
Grade 3 Surgery-wound infection
0.62%
2/323
0.00%
0/345
Infections and infestations
Grade 4 Surgery -wound infection
0.31%
1/323
0.00%
0/345
Infections and infestations
Grade 3 Urinary tract infectiob w/neutrop
0.00%
0/323
0.29%
1/345
Infections and infestations
Grade 3 Uninary tract infection w/o neutrop
0.31%
1/323
0.58%
2/345
Infections and infestations
Grade 4 Urinary tract infection w/o neutrop
0.00%
0/323
0.29%
1/345
Infections and infestations
Grade 3 Urinary tract infection ANC
0.62%
2/323
0.87%
3/345
Hepatobiliary disorders
Grade 3 Alkaline phosphatase increase
0.93%
3/323
1.2%
4/345
Hepatobiliary disorders
Grade 3 Bilirubin increase
2.5%
8/323
2.6%
9/345
Hepatobiliary disorders
Grade 4 Bilirnbin increase
1.2%
4/323
0.58%
2/345
Hepatobiliary disorders
Grade 3 Hypoalbuminemia
5.0%
16/323
5.2%
18/345
Hepatobiliary disorders
Grade 3 Liver enlargement
0.00%
0/323
0.29%
1/345
Hepatobiliary disorders
Grade 3 SGOT (AST) increase
2.8%
9/323
2.0%
7/345
Hepatobiliary disorders
Grade 4 SGOT (AST) increase
0.00%
0/323
0.87%
3/345
Hepatobiliary disorders
Grade 3 SGPT (ALT) increase
5.6%
18/323
5.5%
19/345
Hepatobiliary disorders
Grade 4 SGPT (ALT) increase
0.31%
1/323
0.29%
1/345
Respiratory, thoracic and mediastinal disorders
Grade 4 Acute respiratory distress syndrome
0.31%
1/323
0.29%
1/345
Nervous system disorders
Grade 3 Apnea
0.62%
2/323
0.00%
0/345
Nervous system disorders
Grade 4 Apnea
0.31%
1/323
0.00%
0/345
Respiratory, thoracic and mediastinal disorders
Grade 3 Cough
1.9%
6/323
0.87%
3/345
Respiratory, thoracic and mediastinal disorders
Grade 3 Dyspnea
5.6%
18/323
3.5%
12/345
Respiratory, thoracic and mediastinal disorders
Grade 4 Dyspnea
0.93%
3/323
0.29%
1/345
Respiratory, thoracic and mediastinal disorders
Grade 3 Hiccoughs
0.62%
2/323
0.58%
2/345
Respiratory, thoracic and mediastinal disorders
Grade 3 Hypoxia
10.2%
33/323
10.7%
37/345
Respiratory, thoracic and mediastinal disorders
Grade 4 Hypoxia
2.2%
7/323
0.87%
3/345
Respiratory, thoracic and mediastinal disorders
Grade 3 Lung Fistula
0.31%
1/323
0.00%
0/345
Respiratory, thoracic and mediastinal disorders
Grade 3 Lung-other
1.9%
6/323
1.7%
6/345
Respiratory, thoracic and mediastinal disorders
Grade 4 Lung-other
0.31%
1/323
0.00%
0/345
Respiratory, thoracic and mediastinal disorders
Grade 3 Pleural effusions
1.2%
4/323
0.87%
3/345
Respiratory, thoracic and mediastinal disorders
Grade 3 Pneumonitis/infilitrates
10.8%
35/323
8.7%
30/345
Respiratory, thoracic and mediastinal disorders
Grade 4 Pneumonitis/infiltrates
0.31%
1/323
1.2%
4/345
Respiratory, thoracic and mediastinal disorders
Grade 3 Pneumothorax
1.5%
5/323
0.00%
0/345
Respiratory, thoracic and mediastinal disorders
Grade 3 Pulmonary edema
0.31%
1/323
0.29%
1/345
Respiratory, thoracic and mediastinal disorders
Grade 3 Voice charge /stridor/larynx
0.00%
0/323
0.29%
1/345
Metabolism and nutrition disorders
Grade 3 Bicarbonate decrease
2.5%
8/323
1.4%
5/345
Metabolism and nutrition disorders
Grade 4 Bicarbonate decrease
0.31%
1/323
0.29%
1/345
Metabolism and nutrition disorders
Grade 3 Hypercalcemia
0.62%
2/323
1.2%
4/345
Metabolism and nutrition disorders
Grade 4 Hypercalcemia
1.9%
6/323
0.58%
2/345
Metabolism and nutrition disorders
Grade 3 Hyperglycemia
17.6%
57/323
24.3%
84/345
Metabolism and nutrition disorders
Grade 4 Hyperglycemia
3.1%
10/323
2.9%
10/345
Metabolism and nutrition disorders
Grade 3 Hyperkalemia
3.4%
11/323
5.2%
18/345
Metabolism and nutrition disorders
Grade 4 Hyperkalemia
1.5%
5/323
0.87%
3/345
Metabolism and nutrition disorders
Grade 3 Hypermagnesemia
4.3%
14/323
6.1%
21/345
Metabolism and nutrition disorders
Grade 4 Hypermagnesemia
0.31%
1/323
0.29%
1/345
Metabolism and nutrition disorders
Grade 3 Hypermatremia
0.00%
0/323
0.58%
2/345
Metabolism and nutrition disorders
Grade 4 Hyperuricemia
0.31%
1/323
0.00%
0/345
Metabolism and nutrition disorders
Grade 3 Hypocalcemia
18.9%
61/323
21.7%
75/345
Metabolism and nutrition disorders
Grade 4 Hypocalcemia
6.2%
20/323
4.9%
17/345
Metabolism and nutrition disorders
Grade 3 Hypokalemia
22.3%
72/323
25.8%
89/345
Metabolism and nutrition disorders
Grade 4 Hypokalemia
1.9%
6/323
0.87%
3/345
Metabolism and nutrition disorders
Grade 3 Hypomagnesemia
0.00%
0/323
2.9%
10/345
Metabolism and nutrition disorders
Grade 4 Hypomagnesemia
0.62%
2/323
0.00%
0/345
Metabolism and nutrition disorders
Grade 3 Hyponatremia
31.3%
101/323
27.5%
95/345
Metabolism and nutrition disorders
Grade 4 Hyponatremia
4.3%
14/323
2.3%
8/345
Metabolism and nutrition disorders
Grade 3 Hypophosphatemia
56.7%
183/323
62.0%
214/345
Metabolism and nutrition disorders
Grade 4 Hypophosphatemia
0.00%
0/323
0.87%
3/345
Musculoskeletal and connective tissue disorders
Grade 3 Fracture
0.00%
0/323
0.29%
1/345
Musculoskeletal and connective tissue disorders
Grade 2 Gait/Walking
0.93%
3/323
0.00%
0/345
Musculoskeletal and connective tissue disorders
Grade 4 Gait/Walking
0.31%
1/323
0.00%
0/345
Musculoskeletal and connective tissue disorders
Grade 3 Joint, muscle, bone
5.9%
19/323
1.7%
6/345
Musculoskeletal and connective tissue disorders
Grade 3 Muscle weakness
1.9%
6/323
1.4%
5/345
Musculoskeletal and connective tissue disorders
Grade 3 Osteonecrosis
0.62%
2/323
0.58%
2/345
Nervous system disorders
Grade 3 Anxiety/agitation
2.5%
8/323
4.6%
16/345
Nervous system disorders
Grade 4 Anxiety/agitation
0.93%
3/323
1.4%
5/345
Nervous system disorders
Grade 3 Ataxia
3.1%
10/323
1.7%
6/345
Nervous system disorders
Grade 4 CNS ischemia
0.31%
1/323
0.00%
0/345
Nervous system disorders
Grade 3 Confusion
7.7%
25/323
6.7%
23/345
Nervous system disorders
Grade 4 Confusion
1.5%
5/323
2.3%
8/345
Nervous system disorders
Grade 3 Depression
9.9%
32/323
8.1%
28/345
Nervous system disorders
Grade 4 Depression
1.9%
6/323
1.7%
6/345
Nervous system disorders
Grade 3 Dizziness/light headedness
10.8%
35/323
4.3%
15/345
Nervous system disorders
Grade 4 Dizziness/light headedness
1.2%
4/323
0.87%
3/345
Nervous system disorders
Grade 3 Dizziness/vertigo
0.31%
1/323
0.00%
0/345
Nervous system disorders
Grade 3 Hallucinations
1.2%
4/323
0.58%
2/345
Nervous system disorders
Grade 3 Headache
3.4%
11/323
5.5%
19/345
Nervous system disorders
Grade 3 Insomnia
1.2%
4/323
1.2%
4/345
Nervous system disorders
Grade 3 Involuntary movement/restlessnes
0.31%
1/323
0.00%
0/345
Nervous system disorders
Grade 3 Mood/consciousness change
7.1%
23/323
4.9%
17/345
Nervous system disorders
Grade 4 Mood/consciousness change
0.62%
2/323
0.87%
3/345
Nervous system disorders
Grade 3 Neuro-other
0.93%
3/323
0.87%
3/345
Nervous system disorders
Grade 4 Neuro-other
0.00%
0/323
0.29%
1/345
Nervous system disorders
Grade 3 Seizures
0.62%
2/323
0.29%
1/345
Nervous system disorders
Grade 4 Seizures
0.00%
0/323
0.87%
3/345
Nervous system disorders
Grade 3 Sensory/neuropathy
14.2%
46/323
3.8%
13/345
Nervous system disorders
Grade 4 Sensory/neuropathy
0.31%
1/323
0.00%
0/345
Nervous system disorders
Grade 3 Somnolence/consciousness loss
12.4%
40/323
9.3%
32/345
Nervous system disorders
Grade 4 Somnolence/consciousness loss
1.2%
4/323
1.2%
4/345
Nervous system disorders
Grade 3 Speech impairment
0.00%
0/323
0.29%
1/345
Nervous system disorders
Grade 3 Tremor
9.9%
32/323
4.3%
15/345
General disorders
Grade 3 Arthralgia
1.9%
6/323
2.3%
8/345
General disorders
Grade 4 Arthralgia
0.00%
0/323
0.29%
1/345
General disorders
Grade 3 Bone pain
7.4%
24/323
5.2%
18/345
General disorders
Grade 4 Bone pain
1.2%
4/323
1.2%
4/345
Cardiac disorders
Grade 3 Cardiac/heart
0.31%
1/323
0.00%
0/345
Cardiac disorders
Grade 3 Chest/thorax
0.00%
0/323
0.29%
1/345
General disorders
Grade 3 Chest pain/not cardio or pleural
0.62%
2/323
1.2%
4/345
Ear and labyrinth disorders
Grade 3 Earache
0.62%
2/323
0.00%
0/345
General disorders
Grade 3 Extremity/limb
0.31%
1/323
0.58%
2/345
Eye disorders
Grade 3 Eye
0.00%
0/323
0.29%
1/345
General disorders
Grade 3 Hepatic pain
0.00%
0/323
0.29%
1/345
General disorders
Grade 3 Hip-left
0.31%
1/323
0.00%
0/345
General disorders
Grade 3 Lower back
0.31%
1/323
0.87%
3/345
Musculoskeletal and connective tissue disorders
Grade 3 Muscle
0.00%
0/323
0.29%
1/345
Musculoskeletal and connective tissue disorders
Grade 3 Myalgia
1.5%
5/323
0.58%
2/345
Musculoskeletal and connective tissue disorders
Grade 3 Myalgia/arthralgia
0.00%
0/323
0.87%
3/345
General disorders
Grade 3 Neuropathic pain
0.00%
0/323
0.87%
3/345
General disorders
Grade 3 Pain NOS
0.00%
0/323
0.29%
1/345
General disorders
Grade 3 Pain/other
16.4%
53/323
13.6%
47/345
General disorders
Grade 4 Pain/other
1.2%
4/323
0.00%
0/345
General disorders
Grade 3 Pelvic
0.00%
0/323
0.29%
1/345
General disorders
Grade 3 Pleuritic pain
0.62%
2/323
0.00%
0/345
General disorders
Grade 3 Rectal/perirectal pain
0.31%
1/323
0.29%
1/345
General disorders
Grade 3 Rib
0.00%
0/323
0.29%
1/345
General disorders
Grade 3 Tumor pain
0.00%
0/323
0.29%
1/345
General disorders
Grade 3 Upper Back
1.9%
6/323
1.2%
4/345
Neoplasms benign, malignant and unspecified (incl cysts and polyps)
Grade 4 Second primary
1.9%
6/323
1.7%
6/345
Reproductive system and breast disorders
Grade 3 Erectile impotence
0.31%
1/323
0.00%
0/345
Reproductive system and breast disorders
Grade 3 Female sterility
0.31%
1/323
0.00%
0/345
Reproductive system and breast disorders
Grade 3 Menses changes
0.31%
1/323
0.00%
0/345
Skin and subcutaneous tissue disorders
Grade 3 Decubitus
0.31%
1/323
0.00%
0/345
Skin and subcutaneous tissue disorders
Grade 3 Erythema multifrme/blistering
0.31%
1/323
0.00%
0/345
Skin and subcutaneous tissue disorders
Grade 3 Erythema/rash/eruption/desquamation
1.9%
6/323
1.7%
6/345
Skin and subcutaneous tissue disorders
Grade 3 Pruritis
0.31%
1/323
0.58%
2/345
Skin and subcutaneous tissue disorders
Grade 3 Rash/desquamation
10.5%
34/323
10.4%
36/345
Skin and subcutaneous tissue disorders
Grade 4 Rash/desquamation
2.5%
8/323
1.4%
5/345
Skin and subcutaneous tissue disorders
Grade 3 Skin/other
1.2%
4/323
1.2%
4/345
General disorders
Grade 3 Failure to engraft
0.31%
1/323
0.58%
2/345
General disorders
Grade 3 Stem cell infusion complication
0.00%
0/323
0.58%
2/345
General disorders
Grade 4 Stem cell infusion complication
0.31%
1/323
0.58%
2/345
General disorders
Grade 3 Syndrome/other
0.31%
1/323
0.00%
0/345
General disorders
Grade 3 Thrombosis/embolism
0.31%
1/323
0.58%
2/345

Other adverse events

Other adverse events
Measure
Thalidomide
n=323 participants at risk
Thalidomide 400 QD during induction, 100 mg QD between transplants, 200 mg QD post transplant, 100 mg QD during year one of maintenance, and 50 mg QD during second year of maintenance.
No Thalidomide
n=345 participants at risk
Patient received no thalidomide during induction, consolidation, and maintenance therapy.
Cardiac disorders
Grade 1 Arrythmia, NOS
21.7%
70/323
25.5%
88/345
Cardiac disorders
Grade 2 Arrythmia, NOS
6.5%
21/323
8.4%
29/345
Cardiac disorders
Grade 1 Edema
31.3%
101/323
24.1%
83/345
Cardiac disorders
Grade 2 Edema
10.2%
33/323
8.1%
28/345
Cardiac disorders
Grade 1 Sinus tachycardia
0.00%
0/323
4.6%
16/345
Cardiac disorders
Grade 2 Thrombosis/embolism
5.3%
17/323
6.1%
21/345
Endocrine disorders
Grade 1 Hypothyroidism
6.8%
22/323
6.1%
21/345
Endocrine disorders
Grade 2 Hypothyroidism
9.3%
30/323
0.00%
0/345
Eye disorders
Grade 2 Blurred vision
16.4%
53/323
13.6%
47/345
Eye disorders
Grade 1 Eye - other
7.4%
24/323
0.00%
0/345
Eye disorders
Grade 1 Vision, NOS
5.0%
16/323
0.00%
0/345
General disorders
Grade 2 Fatigue/malaise/lethargy
24.5%
79/323
22.0%
76/345
General disorders
Grade 1 Fever without neutropenia
14.9%
48/323
13.0%
45/345
General disorders
Grade 2 Fever without neutropenia
9.9%
32/323
6.1%
21/345
General disorders
Grade 1 Fever, NOS
29.1%
94/323
32.5%
112/345
General disorders
Grade 2 Fever, NOS
22.3%
72/323
17.1%
59/345
General disorders
Grade 1 Flu-like symptoms-other
10.8%
35/323
7.8%
27/345
General disorders
Grade 1 Insomnia
6.5%
21/323
0.00%
0/345
General disorders
Grade 1 Rigors/chills
9.0%
29/323
4.1%
14/345
General disorders
Grade 1 sweating
11.5%
37/323
9.0%
31/345
General disorders
Grade 2 sweating
10.5%
34/323
10.4%
36/345
General disorders
Grade 1 Weight gain
11.1%
36/323
9.0%
31/345
General disorders
Grade 1 Weight loss
10.8%
35/323
10.7%
37/345
Gastrointestinal disorders
Grade 1 Anorexia
15.5%
50/323
18.0%
62/345
Gastrointestinal disorders
Grade 2 Anorexia
13.0%
42/323
12.8%
44/345
Gastrointestinal disorders
Grade 2 Colitis
0.00%
0/323
7.0%
24/345
Gastrointestinal disorders
Grade 1 Constipation/bowel obstruction
17.0%
55/323
20.0%
69/345
Gastrointestinal disorders
Grade 2 Constipation/bowel obstruction
44.3%
143/323
32.5%
112/345
Gastrointestinal disorders
Grade 1 Diarrhea without colostomy
15.5%
50/323
14.8%
51/345
Gastrointestinal disorders
Grade 2 Diarrhea without colostomy
36.8%
119/323
36.8%
127/345
Gastrointestinal disorders
Grade 1 Dyspepsia/heartburn
8.4%
27/323
5.5%
19/345
Gastrointestinal disorders
Grade 1 Esophagitis/dysphagia
21.7%
70/323
16.2%
56/345
Gastrointestinal disorders
Grade 2 Esophagitis/dysphagia
16.7%
54/323
23.5%
81/345
Gastrointestinal disorders
Grade 1 Mouth Dryness
16.1%
52/323
13.3%
46/345
Gastrointestinal disorders
Grade 2 Mouth Dryness
22.6%
73/323
13.9%
48/345
Gastrointestinal disorders
Grade 1 Nausea
14.2%
46/323
10.7%
37/345
Gastrointestinal disorders
Grade 2 Nausea
25.7%
83/323
34.2%
118/345
Gastrointestinal disorders
Grade 1 Stomatitis/pharyngitis
19.5%
63/323
19.1%
66/345
Gastrointestinal disorders
Grade 2 Stomatitis/pharyngitis
22.6%
73/323
26.1%
90/345
Gastrointestinal disorders
Grade 1 Taste Disturbance
0.00%
0/323
4.9%
17/345
Gastrointestinal disorders
Grade 1 Vomiting
18.0%
58/323
18.8%
65/345
Gastrointestinal disorders
Grade 2 Vomiting
32.5%
105/323
35.4%
122/345
Renal and urinary disorders
Grade 1 Bladder Spasms
0.00%
0/323
6.1%
21/345
Renal and urinary disorders
Grade 1 Creatinine increase
23.8%
77/323
26.4%
91/345
Renal and urinary disorders
Grade 2 Creatinine increase
16.4%
53/323
18.0%
62/345
Renal and urinary disorders
Grade 1 Urinary frequency/urgency
9.9%
32/323
6.4%
22/345
Blood and lymphatic system disorders
Grade 2 Anemia (HGB)
21.7%
70/323
22.0%
76/345
Blood and lymphatic system disorders
Grade 3 Anemia (HGB)
49.8%
161/323
50.4%
174/345
Blood and lymphatic system disorders
Grade 3 Neutropenia/ granulocytopenia
5.0%
16/323
5.8%
20/345
Blood and lymphatic system disorders
Grade 3 PRBC transfusion
7.7%
25/323
0.00%
0/345
Blood and lymphatic system disorders
Grade 3 Platelet Transfusion
5.0%
16/323
0.00%
0/345
Blood and lymphatic system disorders
Grade 3 Thrombocytopenia (PLT)
30.7%
99/323
32.5%
112/345
Blood and lymphatic system disorders
Grade 2 Hematuria
0.00%
0/323
4.6%
16/345
Blood and lymphatic system disorders
Grade 1 Hemorrhage w/3-4 thrombocytopenia
12.4%
40/323
18.3%
63/345
Immune system disorders
Grade 1 Allergic rhinitis
16.7%
54/323
12.2%
42/345
Immune system disorders
Grade 1 Autoimmune reaction
7.7%
25/323
8.1%
28/345
Infections and infestations
Grade 2 Infection w/Grade 3 or 4 Neutrophils
6.5%
21/323
0.00%
0/345
Infections and infestations
Grade 2 Infection w/o 3-4 Neutropenia
10.5%
34/323
9.6%
33/345
Infections and infestations
Grade 2 Lung Infection ANC Bronchus
6.2%
20/323
4.3%
15/345
Infections and infestations
Grade 2 Respiratory infection w/o neutrop
10.2%
33/323
13.3%
46/345
Infections and infestations
Grade 1 Respiratory infection w/o neutrop
5.3%
17/323
0.00%
0/345
Hepatobiliary disorders
Grade 1 Alkaline phosphatase increase
43.0%
139/323
43.2%
149/345
Hepatobiliary disorders
Grade 2 Alkaline phosphatase increase
5.3%
17/323
6.1%
21/345
Hepatobiliary disorders
Grade 1 Bilirubin increase
16.1%
52/323
18.0%
62/345
Hepatobiliary disorders
Grade 2 Bilirubin increase
8.7%
28/323
7.0%
24/345
Hepatobiliary disorders
Grade 1 Hypoalbuminemia
26.6%
86/323
27.0%
93/345
Hepatobiliary disorders
Grade 2 Hypoalbuminemia
48.0%
155/323
51.9%
179/345
Hepatobiliary disorders
Grade 1 SGOT (AST) increase
34.4%
111/323
35.9%
124/345
Hepatobiliary disorders
Grade 2 SGOT (AST) increase
7.7%
25/323
8.7%
30/345
Hepatobiliary disorders
Grade 1 SGPT (ALT) increase
40.6%
131/323
40.6%
140/345
Hepatobiliary disorders
Grade 2 SGPT (ALT) increase
12.1%
39/323
16.5%
57/345
Respiratory, thoracic and mediastinal disorders
Grade 1 Cough
35.0%
113/323
29.9%
103/345
Respiratory, thoracic and mediastinal disorders
Grade 2 Cough
13.9%
45/323
9.0%
31/345
Respiratory, thoracic and mediastinal disorders
Grade 2 Dyspnea
30.0%
97/323
26.7%
92/345
Respiratory, thoracic and mediastinal disorders
Grade 2 Hypoxia
7.4%
24/323
7.0%
24/345
Respiratory, thoracic and mediastinal disorders
Grade 2 Pneumonitis/infiltrates
6.2%
20/323
6.4%
22/345
General disorders
Grade 1 Edema-limb
6.8%
22/323
0.00%
0/345
General disorders
Grade 1 Lymphedema
5.0%
16/323
0.00%
0/345
Metabolism and nutrition disorders
Grade 1 Bicarbonate decrease
60.1%
194/323
62.9%
217/345
Metabolism and nutrition disorders
Grade 2 Bicarbonate decrease
8.7%
28/323
11.9%
41/345
Metabolism and nutrition disorders
Grade 1 Hypercalcemia
10.5%
34/323
10.7%
37/345
Metabolism and nutrition disorders
Grade 1 Hyperglycemia
14.9%
48/323
13.9%
48/345
Metabolism and nutrition disorders
Grade 2 Hyperglycemia
47.1%
152/323
43.8%
151/345
Metabolism and nutrition disorders
Grade 1 Hyperkalemia
24.1%
78/323
23.8%
82/345
Metabolism and nutrition disorders
Grade 2 Hyperkalemia
9.0%
29/323
4.3%
15/345
Metabolism and nutrition disorders
Grade 1 Hypermagnesemia
18.6%
60/323
15.1%
52/345
Metabolism and nutrition disorders
Grade 1 Hypematremia
24.8%
80/323
21.4%
74/345
Metabolism and nutrition disorders
Grade 1 Hypocalcemia
10.8%
35/323
11.9%
41/345
Metabolism and nutrition disorders
Grade 2 Hypocalcemia
45.2%
146/323
46.4%
160/345
Metabolism and nutrition disorders
Grade 1 Hypokalemia
54.2%
175/323
52.8%
182/345
Metabolism and nutrition disorders
Grade 1 Hypomagnesemia
44.0%
142/323
45.8%
158/345
Metabolism and nutrition disorders
Grade 2 Hypomagnesemia
36.8%
119/323
33.6%
116/345
Metabolism and nutrition disorders
Grade 1 Hyponatremia
43.7%
141/323
51.9%
179/345
Metabolism and nutrition disorders
Grade 2 Hypophosphatemia
23.2%
75/323
18.8%
65/345
Metabolism and nutrition disorders
Grade 1 Joint, muscle, bone
13.6%
44/323
11.6%
40/345
Musculoskeletal and connective tissue disorders
Grade 2 Joint, muscle, bone
6.8%
22/323
0.00%
0/345
Musculoskeletal and connective tissue disorders
Grade 1 Muscle weakness
10.5%
34/323
6.4%
22/345
Musculoskeletal and connective tissue disorders
Grade 2 Muscle weakness
4.0%
13/323
5.8%
20/345
Nervous system disorders
Grade 1 Anxiety/agitation
24.5%
79/323
27.0%
93/345
Nervous system disorders
Grade 2 Anxiety/agitation
17.0%
55/323
12.8%
44/345
Nervous system disorders
Grade 1 Ataxia
13.9%
45/323
7.8%
27/345
Nervous system disorders
Grade 2 Ataxia
8.4%
27/323
0.00%
0/345
Nervous system disorders
Grade 1 Confusion
26.0%
84/323
26.7%
92/345
Nervous system disorders
Grade 2 Confusion
13.0%
42/323
10.1%
35/345
Nervous system disorders
Grade 1 Depression
26.3%
85/323
29.3%
101/345
Nervous system disorders
Grade 2 Depression
27.6%
89/323
27.2%
94/345
Nervous system disorders
Grade 1 Dizziness/light headedness
23.5%
76/323
22.0%
76/345
Nervous system disorders
Grade 2 Dizziness/light headedness
16.4%
53/323
11.9%
41/345
Nervous system disorders
Grade 1 Headache
14.9%
48/323
14.8%
51/345
Nervous system disorders
Grade 2 Headache
11.5%
37/323
8.4%
29/345
Nervous system disorders
Grade 1 Insomnia
14.2%
46/323
12.2%
42/345
Nervous system disorders
Grade 2 Insomnia
4.6%
15/323
0.00%
0/345
Nervous system disorders
Grade 1 Memory loss
6.2%
20/323
0.00%
0/345
Nervous system disorders
Grade 1 Mood/consciousness change
15.8%
51/323
10.4%
36/345
Nervous system disorders
Grade 2 Mood/consciousness change
10.8%
35/323
9.0%
31/345
Nervous system disorders
Grade 1 Sensory neuropathy
22.3%
72/323
38.8%
134/345
Nervous system disorders
Grade 2 Sensory/neuropathy
35.6%
115/323
18.0%
62/345
Nervous system disorders
Grade 1 Somnolence/consciousness loss
23.2%
75/323
22.6%
78/345
Nervous system disorders
Grade 2 Somnolence/consciousness loss
16.1%
52/323
9.9%
34/345
Nervous system disorders
Grade 1 Tremor
19.8%
64/323
14.8%
51/345
Nervous system disorders
Grade 2 Tremor
13.9%
45/323
9.3%
32/345
Nervous system disorders
Grade 1 Weakness (motor neuropathy)
13.9%
45/323
15.1%
52/345
Nervous system disorders
Grade 2 Weakness (motor neuropathy)
23.8%
77/323
15.7%
54/345
General disorders
Grade 1 Abdominal pain/cramping
6.2%
20/323
7.5%
26/345
General disorders
Grade 1 Arthralgia
18.6%
60/323
17.1%
59/345
General disorders
Grade 2 Arthralgia
7.1%
23/323
7.8%
27/345
General disorders
Grade 1 Bone pain
23.8%
77/323
20.3%
70/345
General disorders
Grade 2 Bone pain
17.0%
55/323
18.8%
65/345
Musculoskeletal and connective tissue disorders
Grade 1 Myalgia
12.4%
40/323
15.4%
53/345
Musculoskeletal and connective tissue disorders
Grade 2 Myalgia
8.0%
26/323
4.1%
14/345
General disorders
Grade 1 Pain/other
16.4%
53/323
22.3%
77/345
General disorders
Grade 2 Pain/other
22.9%
74/323
18.0%
62/345
General disorders
Grade 1 Upper back
12.4%
40/323
7.8%
27/345
General disorders
Grade 2 Upper back
10.8%
35/323
5.5%
19/345
Skin and subcutaneous tissue disorders
Grade 2 Alopecia
22.6%
73/323
22.9%
79/345
Skin and subcutaneous tissue disorders
Grade 1 Bruising
7.7%
25/323
7.8%
27/345
Skin and subcutaneous tissue disorders
Grade 1 Dry skin
18.6%
60/323
12.5%
43/345
Skin and subcutaneous tissue disorders
Grade 2 Dry skin
5.9%
19/323
0.00%
0/345
Skin and subcutaneous tissue disorders
Erythema/rash/eruption/desquamation
11.5%
37/323
10.7%
37/345
Skin and subcutaneous tissue disorders
Grade 2 Erythema/rash/eruption/desquamation
5.6%
18/323
3.5%
12/345
Skin and subcutaneous tissue disorders
Grade 1 Rash/desquamation
22.6%
73/323
24.9%
86/345
Skin and subcutaneous tissue disorders
Grade 2 Rash/desquamation
25.4%
82/323
27.0%
93/345
Skin and subcutaneous tissue disorders
Grade 4 Skin/other
6.5%
21/323
4.9%
17/345
General disorders
Grade 1 Stem cell infusion complication
0.00%
0/323
4.9%
17/345

Additional Information

Bart Barlogie

UAMS Myeloma Institute

Phone: 501-526-6990

Results disclosure agreements

  • Principal investigator is a sponsor employee
  • Publication restrictions are in place