Trial Outcomes & Findings for 2nd Autologous Stem Cell Transplant in Patients With Persistent/Recurrent (AL) Amyloidosis (NCT NCT00075608)

NCT ID: NCT00075608

Last Updated: 2017-01-27

Results Overview

Feasibility and tolerability will be evaluated based on participants completing second transplant with tolerable adverse events

Recruitment status

TERMINATED

Study phase

PHASE2

Target enrollment

12 participants

Primary outcome timeframe

3 months after treatment and annually

Results posted on

2017-01-27

Participant Flow

Participants were recruited from March 2003 through July 2008 through the transplant clinic and amyloid clinic.

Participant milestones

Participant milestones
Measure
Second Transplant
Participants underwent a second treatment with high dose chemotherapy and stem cell transplant
Overall Study
STARTED
12
Overall Study
COMPLETED
12
Overall Study
NOT COMPLETED
0

Reasons for withdrawal

Withdrawal data not reported

Baseline Characteristics

2nd Autologous Stem Cell Transplant in Patients With Persistent/Recurrent (AL) Amyloidosis

Baseline characteristics by cohort

Baseline characteristics by cohort
Measure
Second Transplant
n=12 Participants
Participants underwent a second treatment with high dose chemotherapy and stem cell transplant
Age, Categorical
<=18 years
0 Participants
n=5 Participants
Age, Categorical
Between 18 and 65 years
12 Participants
n=5 Participants
Age, Categorical
>=65 years
0 Participants
n=5 Participants
Age, Continuous
54.25 years
STANDARD_DEVIATION 1 • n=5 Participants
Gender
Female
5 Participants
n=5 Participants
Gender
Male
7 Participants
n=5 Participants
Region of Enrollment
United States
12 participants
n=5 Participants

PRIMARY outcome

Timeframe: 3 months after treatment and annually

Population: No data were collected or analyzed due to study termination

Feasibility and tolerability will be evaluated based on participants completing second transplant with tolerable adverse events

Outcome measures

Outcome data not reported

PRIMARY outcome

Timeframe: 3 months after treatment and annually

Population: No data were collected or analyzed due to study termination

Response and durability of response will be based on hematologic Complete Response or Partial Response and date of relapse or death

Outcome measures

Outcome data not reported

PRIMARY outcome

Timeframe: 3 months after treatment and annually

Population: No data were collected or analyzed due to study termination

Evaluate immune reconstitution based on time to engraftment

Outcome measures

Outcome data not reported

Adverse Events

Second Transplant

Serious events: 12 serious events
Other events: 12 other events
Deaths: 0 deaths

Serious adverse events

Serious adverse events
Measure
Second Transplant
n=12 participants at risk
Participants who received a second transplant
Blood and lymphatic system disorders
Sepsis
16.7%
2/12 • Number of events 3 • 1 year
Adverse events were assessed for up to 1 year.
Infections and infestations
febrile neutropenia
66.7%
8/12 • Number of events 8 • 1 year
Adverse events were assessed for up to 1 year.
Renal and urinary disorders
Acute renal failure
16.7%
2/12 • Number of events 2 • 1 year
Adverse events were assessed for up to 1 year.
General disorders
fatigue
66.7%
8/12 • Number of events 8 • 1 year
Adverse events were assessed for up to 1 year.
Gastrointestinal disorders
nausea
25.0%
3/12 • Number of events 3 • 1 year
Adverse events were assessed for up to 1 year.
Gastrointestinal disorders
diarrhea
41.7%
5/12 • Number of events 5 • 1 year
Adverse events were assessed for up to 1 year.
Cardiac disorders
hypotension
41.7%
5/12 • Number of events 5 • 1 year
Adverse events were assessed for up to 1 year.
Cardiac disorders
arrhythmia
16.7%
2/12 • Number of events 2 • 1 year
Adverse events were assessed for up to 1 year.

Other adverse events

Other adverse events
Measure
Second Transplant
n=12 participants at risk
Participants who received a second transplant
Gastrointestinal disorders
nausea
75.0%
9/12 • Number of events 13 • 1 year
Adverse events were assessed for up to 1 year.
Gastrointestinal disorders
diarrhea
41.7%
5/12 • Number of events 6 • 1 year
Adverse events were assessed for up to 1 year.
Blood and lymphatic system disorders
peripheral edema
16.7%
2/12 • Number of events 2 • 1 year
Adverse events were assessed for up to 1 year.
Respiratory, thoracic and mediastinal disorders
dyspnea
25.0%
3/12 • Number of events 3 • 1 year
Adverse events were assessed for up to 1 year.
Investigations
hypocalcemia
16.7%
2/12 • Number of events 2 • 1 year
Adverse events were assessed for up to 1 year.
Investigations
hypoalbuminemia
25.0%
3/12 • Number of events 3 • 1 year
Adverse events were assessed for up to 1 year.

Additional Information

Principal Investigator

Boston Medical Center

Phone: 617-638-8261

Results disclosure agreements

  • Principal investigator is a sponsor employee
  • Publication restrictions are in place