A Study of Combination Thalidomide Plus Dexamethasone Therapy vs. Dexamethasone Therapy Alone in Previously Untreated Subjects With Multiple Myeloma

NCT ID: NCT00057564

Last Updated: 2015-09-11

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE3

Total Enrollment

470 participants

Study Classification

INTERVENTIONAL

Study Start Date

2003-02-28

Study Completion Date

2013-08-31

Brief Summary

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To compare the efficacy of combination oral thalidomide plus oral dexamethasone treatment to that of oral dexamethasone-alone treatments as induction (first-line) therapy for subjects with active multiple myeloma

Detailed Description

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Conditions

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Multiple Myeloma

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

DOUBLE

Participants Investigators

Study Groups

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A (Thalidomide & Dexamethasone)

Thalidomide 50mg/day + Dexamethasone 40mg

Group Type EXPERIMENTAL

A (Thalidomide + Dexamethasone)

Intervention Type DRUG

Thalidomide 50mg/day + Dexamethasone 40mg

B (Dexamethasone and placebo)

Dexamethasone and placebo

Group Type PLACEBO_COMPARATOR

B (Placebo + Dexamethasone)

Intervention Type DRUG

Placebo + Dexamethasone 40mg

Interventions

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A (Thalidomide + Dexamethasone)

Thalidomide 50mg/day + Dexamethasone 40mg

Intervention Type DRUG

B (Placebo + Dexamethasone)

Placebo + Dexamethasone 40mg

Intervention Type DRUG

Other Intervention Names

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Thalidomide Dexamethasone placebo

Eligibility Criteria

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Inclusion Criteria

* Active Multiple Myeloma Stage II or III Durie Salmon
* Measurable levels of myeloma paraprotein in serum (≥1.0g/dL) or urine (≥ 0.2g excreted in a 24-hour collection sample)
* Eastern Cooperative Oncology Group (ECOG) performance status of 0, 1, 2
* Women of child bearing potential must agree to abstain for heterosexual intercourse or use 2 methods of contraception, one effective (for example hormonal or tubal ligation) and one barrier (for example latex condom, diaphragm)
* Males must agree to use barrier contraception (latex condoms) when engaging in reproductive activity

Exclusion Criteria

* Pregnant or lactating females
* Peripheral neuropathy ≥ to grade 2 of the NCI CTC.
* Prior history of malignancy unless subject has been free of disease for ≥ 3 years
* Lab abnormality: Absolute neutrophil count (ANC) \<1,000 cells/mm\^3 (1.0 x 10\^9/L)
* Lab abnormality: Platelet count \<50,000/mm\^3 (50.0 x 10\^9/L)
* Lab abnormality: Serum creatinine \>3.0 mg/dL (265 µmol/L)
* Lab abnormality: Serum glutamic oxaloacetic transaminase (SGOT) /Aspartate aminotransferase (AST) or Serum glutamic pyruvic transaminase (SGPT)/Alanine transaminase (ALT) \>3.0 x upper limit of normal (ULN)
* Lab abnormality: Serum total bilirubin \> 2.0 mg/dL (34 µmol/L)
Minimum Eligible Age

18 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Celgene Corporation

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Robert Knight, MD

Role: STUDY_DIRECTOR

Celgene Corporation

Locations

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Clinical Research Consultants, Inc.

Hoover, Alabama, United States

Site Status

Arizona Clinical Research Center

Tucson, Arizona, United States

Site Status

UCLA School of Medicine

Los Angeles, California, United States

Site Status

James Berenson

West Hollywood, California, United States

Site Status

Mayo Clinic

Jacksonville, Florida, United States

Site Status

Melbourne Internal Medicine Associates Oncology

Melbourne, Florida, United States

Site Status

Jackson Memorial Hospital and Clinics

Miami, Florida, United States

Site Status

University of Miami Miller School/Jackson Memorial Hospital

Miami, Florida, United States

Site Status

University of Miami

Miami, Florida, United States

Site Status

Oncology Hematology Group of South Florida

Miami, Florida, United States

Site Status

Medical College of Georgia

Augusta, Georgia, United States

Site Status

Southern Illinois Hematology /Oncology

Centralia, Illinois, United States

Site Status

Rush Cancer Institute Section of Hematology

Chicago, Illinois, United States

Site Status

University of Iowa Hospital of Clinic

Iowa City, Iowa, United States

Site Status

Ocshner Clinic Foundation

New Orleans, Louisiana, United States

Site Status

University of Michigan Comprehensive Cancer Center

Ann Arbor, Michigan, United States

Site Status

Mayo Clinic Cancer Center

Rochester, Minnesota, United States

Site Status

Hackensack University Hospital

Hackensack, New Jersey, United States

Site Status

SUNY Upstate Medical University

Syracuse, New York, United States

Site Status

Wake Forest University School of Medicine

Winston-Salem, North Carolina, United States

Site Status

Cleveland Clinic- Taussig Cancer Center

Cleveland, Ohio, United States

Site Status

University of Pittsburgh

Pittsburgh, Pennsylvania, United States

Site Status

South Carolina Oncology Group

West Columbia, South Carolina, United States

Site Status

The Family Centre, PLLC

Collierville, Tennessee, United States

Site Status

East Tennessee Oncology/Hematology Associates

Knoxville, Tennessee, United States

Site Status

Medical College of Wisconsin

Milwaukee, Wisconsin, United States

Site Status

Royal Brisbane Hospital

Herston, Queensland, Australia

Site Status

Haematology Princess Alexandra Hospital

Woolloongabba, Queensland, Australia

Site Status

Frankston Hospital

Frankston, Victoria, Australia

Site Status

Peter MacCallum Cancer Institute

Melbourne, Victoria, Australia

Site Status

The Alfred Hospital

Melbourne, Victoria, Australia

Site Status

Bone Marrow Transplant Service Dept of Clinical Haematology and Medical Oncology

Parkville, Victoria, Australia

Site Status

Institut Jules Bordet Dep't of Clinical Haematology

Brussels, , Belgium

Site Status

Dept. Of Haematology Academisch Ziekenhuis VUB

Brussels, , Belgium

Site Status

University Hospital Ghent Dep't of Haematology

Ghent, , Belgium

Site Status

UMHAT Alexandrovska

Alexandrovska, , Bulgaria

Site Status

National Center of Haematology and Transfusiology

Sofia, , Bulgaria

Site Status

Military Medical Academy

Sofia, , Bulgaria

Site Status

Dalhousie University

Halifax, Nova Scotia, Canada

Site Status

Princess Margaret Hospital

Toronto, Ontario, Canada

Site Status

University Health Network Princess Margaret Hospital

Toronto, Ontario, Canada

Site Status

Centre Hopitalier Universitaire de Sherbrooke Hospital Fleurimont

Fleurimont, Quebec, Canada

Site Status

McGill University

Montreal, Quebec, Canada

Site Status

Saskatoon Cancer Centre University of Saskatoon

Saskatoon, Saskatchewan, Canada

Site Status

Universitaetsklinikum Dusseldorf Klinik fuer Haematologie

Düsseldorf, , Germany

Site Status

St. Laszlo Hoszpital

Budapest, , Hungary

Site Status

Petz Aladar County Hospital

Győr, , Hungary

Site Status

MidWestern Regional Hospital Haematology Dpt.

Dooradoyle, Limerick, Ireland

Site Status

Hope Directorate Dep't. Haematology St. James's Hospital

Dublin, , Ireland

Site Status

Hadassah University Hospital Hematology Dep't

‘En Kerem, Jerusalem, Israel

Site Status

Rambam Medical Center Dep't. Of Hematology

Haifa, , Israel

Site Status

Tel Aviv Sourasky Medical Center Hematology Institute

Tel Aviv, , Israel

Site Status

Director of Hematology Division BMT and CBB The Chaim Sheba Medical Center

Tel Litwinsky, , Israel

Site Status

Universita di Bari Dipartimento di Scienze Umana Sezione de Medicina Interna e Oncologia Medica Policlinico

Bari, , Italy

Site Status

Istituto di Ematologia e Oncologia Medica "L. e. A. Seragnoli"

Bologna, , Italy

Site Status

Azienda Ospedaliera San Martino

Genova, , Italy

Site Status

Ospedale Niguarda Ca Granda

Milan, , Italy

Site Status

Policlinico San Matteo

Pavia, , Italy

Site Status

Università La Sapienza Dipartimento di Biotecnologie Cellulari ed Ematologia

Roma, , Italy

Site Status

Clinica Ematologica Policlinico Universitario

Udine, , Italy

Site Status

Medical Academy of Bialystok

Bialystok, , Poland

Site Status

Institute of Internal Diseases University of Medicine

Gdansk, , Poland

Site Status

Jagiellonian University Collegium Medicum Department of Hematology

Krakow, , Poland

Site Status

Medical University of Lodz

Lodz, , Poland

Site Status

Private Medical Practice Centre of Clinical Laboratory of Densitometry At 'Officers of Professors'

Lublin, , Poland

Site Status

Medical University of Warsaw Dep't of Hematology, Oncology and Internal Diseases

Warsaw, , Poland

Site Status

Chelyabinsk Regional Clinical Hospital Hematology Dpt

Chelyabinsk, , Russia

Site Status

Republican Clinical Hospital #1 Hematology Dpt.

Izhevsk, , Russia

Site Status

Burdenko Central Military Clinical Hospital Hematology Center

Moscow, , Russia

Site Status

Russian Academy of Medical Sciences Scientific Center of Hematology

Moscow, , Russia

Site Status

Novosibirsk State Regional Clinical Hospital Hematology Centre

Novosibirsk, , Russia

Site Status

Research Institute of Hematology and Blood Transfusion,Clinical Department of Hematology with Bone Marrow Transplantation Unit

Saint Petersburg, , Russia

Site Status

St. Petersburg Pavlov State Medical University Bone Marrow Transplantation Clinic

Saint Petersburg, , Russia

Site Status

Clinical Hospital #31 Dpt of Bone Marrow Transplantation and Chemotherapy of Patients with Myeloproliferative Disorders

Saint Petersburg, , Russia

Site Status

Samara Regional Clinical Hospital Dep't. of Hematology and Bone Marrow Transplantation

Samara, , Russia

Site Status

Blokhin Cancer Research Center Dpt of Myeloproliferative Disorders Chemotherapy

Shosse, , Russia

Site Status

Nizhny Novgorod Clinical Hospital

Veliky Novgorod, , Russia

Site Status

Ekaterinburg 1st Regional Clinical Hospital Regional Hematology Centre

Yekaterinburg, , Russia

Site Status

Hospital Clinic

Barcelona, , Spain

Site Status

Hospital Universitario de la Princessa

Madrid, , Spain

Site Status

Hospital Doce de Octubre

Madrid, , Spain

Site Status

Clinica Universitaria de Navarra

Pamplona, , Spain

Site Status

Hospital Universitario de Salamanca

Salamanca, , Spain

Site Status

Hospital Universitario Marques de Valdecilla

Santander, , Spain

Site Status

Universitatsspital Zurich

Zurich, , Switzerland

Site Status

Cherkassy Regional Oncology Center

Cherkassy, , Ukraine

Site Status

Dnepropetrovsk City Clinical Hospital #4 Regional Hematology Centre

Dnipro, , Ukraine

Site Status

Ivano-Frankovsk Regional Clinical Hospital - Hospital Therapy Department

Ivano-Frankivsk, , Ukraine

Site Status

Kharkov Regional Clinical Oncology Center Dep't of Oncology and Pediatric Oncology

Kharkiv, , Ukraine

Site Status

Kiev Institute of Oncology of the UAMS Systemic Malignancies Department

Kiev, , Ukraine

Site Status

Kiev Bone Marrow Transplantation Center Bone Marrow Transplantation Department

Kiev, , Ukraine

Site Status

Institute of Hematology and Transfusiology of the UAMS Department of Blood Diseases with Clinical Biochemistry Group

Kiev, , Ukraine

Site Status

Institute of Blood Pathology and Transfusion Medicine of the UAMS

Lviv, , Ukraine

Site Status

Odessa Regional Clinical Hospital Hematology Dep't

Odesa, , Ukraine

Site Status

Zaporozhje Regional Clinical Hospital Hematology Dpt

Zaporizhzhya, , Ukraine

Site Status

Zhitomir Regional Clinical Hospital Hematology Centre

Zhytomyr, , Ukraine

Site Status

Belfast City Hospital Haematology Dpt.

Belfast, , United Kingdom

Site Status

Guys Hospital

London, , United Kingdom

Site Status

Guys Hospital

London, , United Kingdom

Site Status

Countries

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United States Australia Belgium Bulgaria Canada Germany Hungary Ireland Israel Italy Poland Russia Spain Switzerland Ukraine United Kingdom

References

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Rajkumar SV, Rosinol L, Hussein M, Catalano J, Jedrzejczak W, Lucy L, Olesnyckyj M, Yu Z, Knight R, Zeldis JB, Blade J. Multicenter, randomized, double-blind, placebo-controlled study of thalidomide plus dexamethasone compared with dexamethasone as initial therapy for newly diagnosed multiple myeloma. J Clin Oncol. 2008 May 1;26(13):2171-7. doi: 10.1200/JCO.2007.14.1853. Epub 2008 Mar 24.

Reference Type RESULT
PMID: 18362366 (View on PubMed)

Other Identifiers

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THAL-MM-003

Identifier Type: -

Identifier Source: org_study_id

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