Vitamin E in Aging Persons With Down Syndrome

NCT ID: NCT00056329

Last Updated: 2012-05-04

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

UNKNOWN

Clinical Phase

PHASE3

Total Enrollment

350 participants

Study Classification

INTERVENTIONAL

Study Start Date

2002-04-30

Study Completion Date

2012-05-31

Brief Summary

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The goal of this study is to determine the safety and efficacy of the administration of vitamin E, which has been shown to delay the progression of Alzheimer's disease, in slowing the rate of cognitive/functional decline in older persons with Down syndrome.

Detailed Description

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The growing success of therapeutic interventions (including the antioxidant Vitamin E) for Alzheimer's disease in the general population requires a solution to the methodological problems so that therapeutic trials can be conducted in the aging population with Down syndrome which will ultimately improve their quality of life as well as that of their families and caregivers. The experience gained in this trial will be useful to the design of appropriate cognitive measures of Alzheimer's disease in persons with Down syndrome in subsequent trials.

The goal of this international three-year study is to determine whether the administration of vitamin E, which has been shown to delay the progression of Alzheimer's disease, will slow the rate of cognitive/functional decline in persons age 50 or older with Down syndrome. Persons with Down syndrome functioning at all levels of intellectual disability will be eligible. Men and women of approximately equal numbers and people from minorities and ethnic groups other than Caucasian will be included. A total of 350 individuals with Down syndrome, 50 years of age and older, have been recruited at approximately 21 trial sites. The study is a randomized, double-blind, placebo-controlled, parallel group design with stratification by geographic site and presence of Alzheimer disease according to DSM-IV (American Psychiatric Association) criteria for diagnosing this disease.

Apolipoprotein E (Apo E) genotype will be determined at the screening visit to allow secondary analyses of the impact of Apo E genotype (that may influence Alzheimer's disease risk) on outcome measures and the response to treatment. DNA specimens will also be stored for possible future genetic analyses, with trial sites allowing for non-participation in this procedure. Visits will occur at baseline and then at 6 monthly intervals, with each visit including interval medical history, current and interval medications, side effects checklist, adverse events, pill count, institutionalization status, cognitive, functional, and behavioral measures, and DSM-IV diagnostic assessment for Alzheimer's disease.

Conditions

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Down Syndrome Alzheimer Disease

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

QUADRUPLE

Participants Caregivers Investigators Outcome Assessors

Study Groups

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1

vitamin E plus multivitamin

Group Type EXPERIMENTAL

Vitamin E

Intervention Type DRUG

1,000 international units twice daily for three years

multivitamin

Intervention Type DRUG

once daily for three years

2

placebo with multivitamin

Group Type PLACEBO_COMPARATOR

multivitamin

Intervention Type DRUG

once daily for three years

Placebo

Intervention Type DRUG

Placebo twice daily for three years

Interventions

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Vitamin E

1,000 international units twice daily for three years

Intervention Type DRUG

multivitamin

once daily for three years

Intervention Type DRUG

Placebo

Placebo twice daily for three years

Intervention Type DRUG

Other Intervention Names

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tocopherol

Eligibility Criteria

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Inclusion Criteria

* Presence of clinically determined Down syndrome (karyotypes optional).
* Medically stable.
* Medications stable over 3 months.
* Appropriately signed and witnessed consent form.
* Involvement/cooperation of informant/caregiver.

Exclusion Criteria

* Medical/neurological condition (other than Alzheimer's disease) associated with dementia.
* Brief Praxis Test score \<20.
* Modified Hachinski score \>4.
* Major depression within 3 months.
* History of any disorder of blood coagulation (inherited or acquired).
* Current use of anti-coagulants.
* Use of experimental medications within 3 months.
* Regular use of vitamin E greater than 50 units per day during the previous 6 months.
Minimum Eligible Age

50 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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National Institute on Aging (NIA)

NIH

Sponsor Role collaborator

Eunice Kennedy Shriver National Institute of Child Health and Human Development (NICHD)

NIH

Sponsor Role collaborator

National Center for Complementary and Integrative Health (NCCIH)

NIH

Sponsor Role collaborator

New York State Institute for Basic Research

OTHER_GOV

Sponsor Role lead

Responsible Party

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Arthur Dalton

Deputy Director

Responsibility Role PRINCIPAL_INVESTIGATOR

Principal Investigators

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Arthur J Dalton, PhD

Role: PRINCIPAL_INVESTIGATOR

New York State Institute for Basic Research in Developmental Disabilities

Paul S Aisen, MD

Role: STUDY_DIRECTOR

Georgetown University

Mary C Sano, PhD

Role: STUDY_DIRECTOR

Icahn School of Medicine at Mount Sinai

Locations

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University of Connecticut Health Center

Farmington, Connecticut, United States

Site Status

Roskamp Institute Memory Clinic

Tampa, Florida, United States

Site Status

Institute for the Study of Disadvantage and Disability

Atlanta, Georgia, United States

Site Status

May South, Inc.

Atlanta, Georgia, United States

Site Status

University of Illinois at Chicago

Chicago, Illinois, United States

Site Status

Southern Illinois University School of Medicine

Springfield, Illinois, United States

Site Status

Third Age, Inc.

Lexington, Kentucky, United States

Site Status

McLean Hospital

Belmont, Massachusetts, United States

Site Status

Clinical Research Center of New Jersey

Voorhees Township, New Jersey, United States

Site Status

University at Albany, SUNY

Albany, New York, United States

Site Status

Nathan Kline Institute

Orangeburg, New York, United States

Site Status

George Jervis Clinic

Staten Island, New York, United States

Site Status

Westchester Institute for Human Development

Valhalla, New York, United States

Site Status

University Memory and Aging Center, Case Western Reserve University

Cleveland, Ohio, United States

Site Status

Centre for Developmental Disabilities Studies

Ryde, New South Wales, Australia

Site Status

Down Syndrome Research Foundation

Port Coquitlam, British Columbia, Canada

Site Status

Surrey Place Centre

Toronto, Ontario, Canada

Site Status

Saskatoon City Hospital

Saskatoon, Saskatchewan, Canada

Site Status

University of Cambridge

Cambridge, England, United Kingdom

Site Status

Greenfields Monyhull Hospital

Kings Norton, Birmingham, England, United Kingdom

Site Status

Kings College: London

London, England, United Kingdom

Site Status

Mercer Institute for Research on Ageing, St. James Hospital

Dublin, Ireland, United Kingdom

Site Status

Countries

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United States Australia Canada United Kingdom

References

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Sano M, Ernesto C, Thomas RG, Klauber MR, Schafer K, Grundman M, Woodbury P, Growdon J, Cotman CW, Pfeiffer E, Schneider LS, Thal LJ. A controlled trial of selegiline, alpha-tocopherol, or both as treatment for Alzheimer's disease. The Alzheimer's Disease Cooperative Study. N Engl J Med. 1997 Apr 24;336(17):1216-22. doi: 10.1056/NEJM199704243361704.

Reference Type BACKGROUND
PMID: 9110909 (View on PubMed)

Aisen PS, Davis KL. The search for disease-modifying treatment for Alzheimer's disease. Neurology. 1997 May;48(5 Suppl 6):S35-41. doi: 10.1212/wnl.48.5_suppl_6.35s.

Reference Type BACKGROUND
PMID: 9153159 (View on PubMed)

Aylward EH, Burt DB, Thorpe LU, Lai F, Dalton A. Diagnosis of dementia in individuals with intellectual disability. J Intellect Disabil Res. 1997 Apr;41 ( Pt 2):152-64. doi: 10.1111/j.1365-2788.1997.tb00692.x.

Reference Type BACKGROUND
PMID: 9161927 (View on PubMed)

Dalton, AJ, Mehta, PD, Fedor, BL, Patti, PJ: Cognitive changes in memory precede those in praxis in aging persons with Down syndrome. Journal of Intellectual and Developmental Disability 24(2):169-187,1999.

Reference Type BACKGROUND

Sano M, Aisen PS, Dalton AJ, Andrews HF, Tsai W-Y, and the International Down Syndrome Alzheimer Disease Consortium. Assessment of aging individuals with Down syndrome in clinical trials: results of baseline measures. Journal of Policy and Practice in Intellectual Disabilities. 2005 2(2):126-138.

Reference Type RESULT

Other Identifiers

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R01AG016381

Identifier Type: NIH

Identifier Source: secondary_id

View Link

NIA Grant AG16381

Identifier Type: -

Identifier Source: secondary_id

IA0039

Identifier Type: -

Identifier Source: org_study_id

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