Effects of CX516 on Functioning in Fragile X Syndrome and Autism

NCT ID: NCT00054730

Last Updated: 2005-06-24

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE2

Study Classification

INTERVENTIONAL

Study Start Date

2002-06-30

Brief Summary

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This study will investigate whether CX516 can improve attention, memory, language, or behavior in adults with Fragile X Syndrome and/or Autism.

CX516 is an AMPAKINE® compound. AMPAKINE compounds enhance synaptic strength. There is evidence to suggest that the synapses in the brain of an individual with fragile X syndrome are immature and abnormal. It is possible CX516 may partially correct this synaptic transmission defect and lead to improvement in cognitive and behavioral functioning.

There is also reason to believe that these changes caused by CX516 could be helpful in managing cognitive and behavioral symptoms in patients with autistic disorder.

Involvement for each participant will last 28 days. Participants will be given study medication, a physical exam, and a variety of cognitive assessment tests to study potential drug effectiveness at improving disease symptoms.

Detailed Description

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Conditions

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Fragile X Syndrome Autism

Keywords

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Fragile X Syndrome Autism

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

DOUBLE

Interventions

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CX516 (Ampalex®)

Intervention Type DRUG

Eligibility Criteria

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Inclusion Criteria

Fragile X group

* DNA-based diagnosis of Fragile X syndrome

Autism group

* Documented diagnosis with ADOS; ADI-R; CARS and GARS

Both groups

* 18-50 years
* Measured IQ below 85
* Measured IQ \>20
* Mental age \>30 months
* Stable medication regimen for past 8 weeks
* Normal hearing
* Vision corrected to at least 20/50
* All females of childbearing age must have a negative pregnancy test at enrollment

Exclusion Criteria

* Recent history of seizure, epilepsy, or blackouts
* Unresolved medical issue impacting performance
* Behavioral dysfunction to the point that subject cannot cooperate for testing
* History of drug-induced neutropenia
* Uncontrolled hypertension
Minimum Eligible Age

18 Years

Maximum Eligible Age

50 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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FRAXA Research Foundation

OTHER

Sponsor Role collaborator

RespireRx

INDUSTRY

Sponsor Role lead

Locations

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UC Davis-MIND Institute

Sacramento, California, United States

Site Status

RUSH-Presbyterian-St. Luke's Medical Center

Chicago, Illinois, United States

Site Status

Countries

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United States

Related Links

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http://www.fraxa.org

Fraxa is a research foundation whose mission is to support research aimed at treatment for Fragile X syndrome.

Other Identifiers

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CORX-CX516-013

Identifier Type: -

Identifier Source: org_study_id