Treatment of Von Hippel-Lindau (VHL)-Related Hemangioblastoma With PTK787/ZK 222584

NCT ID: NCT00052013

Last Updated: 2017-03-06

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE2

Total Enrollment

11 participants

Study Classification

INTERVENTIONAL

Study Start Date

2003-02-28

Brief Summary

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The purpose of this study is to determine whether PTK787/ZK 222584 is effective in treating hemangioblastoma of the brain and/or retina in patients with von Hippel-Lindau disease. The study will also assess safety and tolerability of PTK787/ZK 222584, and changes in markers of angiogenesis (new blood vessel growth).

Detailed Description

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Conditions

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Von Hippel-Lindau Disease CNS Hemangioblastoma Retinal Hemangioblastoma

Study Design

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Allocation Method

NON_RANDOMIZED

Intervention Model

SINGLE_GROUP

Primary Study Purpose

TREATMENT

Blinding Strategy

NONE

Study Groups

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PTK787/ZK 222584

Group Type EXPERIMENTAL

PTK787/ZK 222584

Intervention Type DRUG

Interventions

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PTK787/ZK 222584

Intervention Type DRUG

Eligibility Criteria

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Inclusion Criteria

* Confirmed diagnosis of VHL disease
* One or more measurable CNS hemangioblastoma, if symptomatic, must be refractory or not amenable to standard therapy, if asymptomatic, must have had at least one prior neurosurgical treatment/ procedure; and/or: at least one untreatable or treatment-refractory retinal hemangioblastoma that is causing impaired visual function
* Karnofsky Performance Status \>=60
* Life expectancy \> 3 months
* Able to sign informed consent
* Adequate hematologic status, liver and kidney function

Exclusion Criteria

* Patients with other VHL-related tumors requiring or amenable to standard treatment
* Severe or uncontrolled concurrent illnesses that could compromise participation in the study
* Total urinary protein in 24 hour collection \> 500 mg
* Pregnant or breast feeding females, adults of reproductive potential not using effective contraception (hormonal methods not considered effective due to possible decreased effectiveness secondary to drug interaction with PTK787). Women of childbearing potential must have negative serum pregnancy test prior to initiation of treatment.
* Acute or chronic liver disease
* Diagnosis of HIV infection
* GI function that may alter absorption of PTK787
* Patients taking coumadin (warfarin sodium)
* Prior therapies (investigational drugs, chemotherapy) within 4 weeks prior to study entry
* Prior therapies (biologic, hormonal, immunotherapy, radiation therapy, surgery) within two weeks prior to study entry.
* Patients unwilling or unable to comply with protocol requirements
* Patients with concurrent, non VHL-related malignancies other than non-melanoma skin cancer
* Patients with contraindication to MRI imaging
Minimum Eligible Age

18 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Novartis Pharmaceuticals

INDUSTRY

Sponsor Role lead

Responsible Party

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Novartis Pharmaceuticals

Principal Investigators

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Novartis

Role: STUDY_CHAIR

Novartis

Locations

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Dana Farber Cancer Institute

Boston, Massachusetts, United States

Site Status

Duke University Medical Center

Durham, North Carolina, United States

Site Status

Countries

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United States

Other Identifiers

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CPTK787 0144

Identifier Type: -

Identifier Source: org_study_id

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