Trial Outcomes & Findings for Phase II Trial of Peginterferon Alpha-2b and Thalidomide in Adults With Recurrent Gliomas (NCT NCT00047879)

NCT ID: NCT00047879

Last Updated: 2011-10-26

Results Overview

Progression free survival is defined as the percent of patients that are progression free and alive 6 months after initiating therapy. Progression of disease by \> 50% increase in the size of the tumor compared to baseline after the first cycle only, and then \>25% increase in the size of the tumor for all subsequent cycles.

Recruitment status

COMPLETED

Study phase

PHASE2

Target enrollment

7 participants

Primary outcome timeframe

6 months

Results posted on

2011-10-26

Participant Flow

We planned to accrue 32 patients to the GBM stratum and 32 patients to the AG stratum. The accrual ceiling was 64 patients on this trial. We anticipated accruing these patients within one year of opening this study.

Participant milestones

Participant milestones
Measure
Glioblastoma Multiforme Stratum
Glioblastoma multiforme is one of the most common and aggressive types of brain tumor.
Anaplastic Glioma Stratum
Anaplastic glioma is a type of brain tumor that develops from star-shaped glial cells that support nerve cells. Anaplastic oligodendroglioma is a malignant type of brain tumor sensitive to treatment with chemotherapy and radiotherapy.
Overall Study
STARTED
4
3
Overall Study
COMPLETED
0
0
Overall Study
NOT COMPLETED
4
3

Reasons for withdrawal

Reasons for withdrawal
Measure
Glioblastoma Multiforme Stratum
Glioblastoma multiforme is one of the most common and aggressive types of brain tumor.
Anaplastic Glioma Stratum
Anaplastic glioma is a type of brain tumor that develops from star-shaped glial cells that support nerve cells. Anaplastic oligodendroglioma is a malignant type of brain tumor sensitive to treatment with chemotherapy and radiotherapy.
Overall Study
Progressive disease
4
3

Baseline Characteristics

Phase II Trial of Peginterferon Alpha-2b and Thalidomide in Adults With Recurrent Gliomas

Baseline characteristics by cohort

Baseline characteristics by cohort
Measure
Glioblastoma Multiforme Stratum
n=4 Participants
Glioblastoma multiforme is one of the most common and aggressive types of brain tumor.
Anaplastic Glioma Stratum
n=3 Participants
Anaplastic glioma is a type of brain tumor that develops from star-shaped glial cells that support nerve cells. Anaplastic oligodendroglioma is a malignant type of brain tumor sensitive to treatment with chemotherapy and radiotherapy.
Total
n=7 Participants
Total of all reporting groups
Age, Categorical
<=18 years
0 Participants
n=5 Participants
0 Participants
n=7 Participants
0 Participants
n=5 Participants
Age, Categorical
Between 18 and 65 years
4 Participants
n=5 Participants
1 Participants
n=7 Participants
5 Participants
n=5 Participants
Age, Categorical
>=65 years
0 Participants
n=5 Participants
2 Participants
n=7 Participants
2 Participants
n=5 Participants
Age Continuous
55.5 years
STANDARD_DEVIATION 10.85 • n=5 Participants
53.67 years
STANDARD_DEVIATION 11.93 • n=7 Participants
54.71 years
STANDARD_DEVIATION 10.36 • n=5 Participants
Sex: Female, Male
Female
0 Participants
n=5 Participants
1 Participants
n=7 Participants
1 Participants
n=5 Participants
Sex: Female, Male
Male
4 Participants
n=5 Participants
2 Participants
n=7 Participants
6 Participants
n=5 Participants
Region of Enrollment
United States
4 participants
n=5 Participants
3 participants
n=7 Participants
7 participants
n=5 Participants

PRIMARY outcome

Timeframe: 6 months

Population: The primary objective was not met. Only registered 7 out of 64 participants and they all came off the study for progressive disease around 3-4 months after starting the study. None of the participants were evaluated for progression-free survival at 6 months because the study was stopped at 4 months due to progressive disease.

Progression free survival is defined as the percent of patients that are progression free and alive 6 months after initiating therapy. Progression of disease by \> 50% increase in the size of the tumor compared to baseline after the first cycle only, and then \>25% increase in the size of the tumor for all subsequent cycles.

Outcome measures

Outcome data not reported

SECONDARY outcome

Timeframe: 6 months

Population: Registered 7 out of 64 participants and they came off study for progressive disease around 3-4 months after starting the study.

Response is defined per RECIST criteria. Measurable disease is defined as bidimensionally measurable lesions with clearly defined margins by CT or MRI scan. Evaluable disease is defined as unidimensionally measurable lesions, masses with margins not clearly defined, or lesions with a multiple cystic component. Complete response (CR) is complete disappearance of all measurable and evaluable disease. Partial response (PR) is greater than or equal to 50% decrease under baseline in the sum of products or perpendicular diameters of all measurable lesions.

Outcome measures

Outcome data not reported

SECONDARY outcome

Timeframe: 4 months

Here are the total number of participants with adverse events. For the detailed list of adverse events see the adverse event module.

Outcome measures

Outcome measures
Measure
Glioblastoma Multiforme Stratum
n=4 Participants
Glioblastoma multiforme is one of the most common and aggressive types of brain tumor.
Anaplastic Glioma Stratum
n=3 Participants
Anaplastic glioma is a type of brain tumor that develops from star-shaped glial cells that support nerve cells. Anaplastic oligodendroglioma is a malignant type of brain tumor sensitive to treatment with chemotherapy and radiotherapy.
The Number of Participants With Adverse Events
4 Participants
2 Participants

Adverse Events

Glioblastoma Multiforme Stratum

Serious events: 3 serious events
Other events: 4 other events
Deaths: 0 deaths

Anaplastic Glioma Stratum

Serious events: 2 serious events
Other events: 2 other events
Deaths: 0 deaths

Serious adverse events

Serious adverse events
Measure
Glioblastoma Multiforme Stratum
n=4 participants at risk
Glioblastoma multiforme is one of the most common and aggressive types of brain tumor.
Anaplastic Glioma Stratum
n=3 participants at risk
Anaplastic glioma is a type of brain tumor that develops from star-shaped glial cells that support nerve cells. Anaplastic oligodendroglioma is a malignant type of brain tumor sensitive to treatment with chemotherapy and radiotherapy.
Gastrointestinal disorders
Nausea
0.00%
0/4 • 4 months
33.3%
1/3 • Number of events 1 • 4 months
Gastrointestinal disorders
Vomiting
0.00%
0/4 • 4 months
33.3%
1/3 • Number of events 1 • 4 months
Nervous system disorders
Headache
0.00%
0/4 • 4 months
33.3%
1/3 • Number of events 1 • 4 months
Musculoskeletal and connective tissue disorders
Muscle weakness
0.00%
0/4 • 4 months
33.3%
1/3 • Number of events 1 • 4 months
Investigations
Thrombocytopenia
0.00%
0/4 • 4 months
33.3%
1/3 • Number of events 1 • 4 months
Metabolism and nutrition disorders
Metabolic, hyperglycemia
25.0%
1/4 • Number of events 1 • 4 months
0.00%
0/3 • 4 months
Nervous system disorders
Seizure
25.0%
1/4 • Number of events 1 • 4 months
0.00%
0/3 • 4 months
Investigations
Elevated AST
25.0%
1/4 • Number of events 1 • 4 months
0.00%
0/3 • 4 months

Other adverse events

Other adverse events
Measure
Glioblastoma Multiforme Stratum
n=4 participants at risk
Glioblastoma multiforme is one of the most common and aggressive types of brain tumor.
Anaplastic Glioma Stratum
n=3 participants at risk
Anaplastic glioma is a type of brain tumor that develops from star-shaped glial cells that support nerve cells. Anaplastic oligodendroglioma is a malignant type of brain tumor sensitive to treatment with chemotherapy and radiotherapy.
General disorders
edema: limb right upper extremity
0.00%
0/4 • 4 months
33.3%
1/3 • Number of events 1 • 4 months
Investigations
Thrombocytopenia
0.00%
0/4 • 4 months
33.3%
1/3 • Number of events 1 • 4 months
General disorders
Fatigue
50.0%
2/4 • Number of events 3 • 4 months
0.00%
0/3 • 4 months
Nervous system disorders
Dizziness
25.0%
1/4 • Number of events 1 • 4 months
0.00%
0/3 • 4 months
Infections and infestations
Infection
25.0%
1/4 • Number of events 1 • 4 months
0.00%
0/3 • 4 months
Investigations
Metabolic, ALT elevated
25.0%
1/4 • Number of events 1 • 4 months
0.00%
0/3 • 4 months
Nervous system disorders
Pain, skin
25.0%
1/4 • Number of events 1 • 4 months
0.00%
0/3 • 4 months
Psychiatric disorders
Mood alteration
25.0%
1/4 • Number of events 1 • 4 months
0.00%
0/3 • 4 months
Psychiatric disorders
Confusion
25.0%
1/4 • Number of events 1 • 4 months
0.00%
0/3 • 4 months
Skin and subcutaneous tissue disorders
Dry skin
25.0%
1/4 • Number of events 1 • 4 months
0.00%
0/3 • 4 months
General disorders
Fever
25.0%
1/4 • Number of events 1 • 4 months
0.00%
0/3 • 4 months
Investigations
AST
25.0%
1/4 • Number of events 1 • 4 months
0.00%
0/3 • 4 months
Investigations
Glucose
25.0%
1/4 • Number of events 1 • 4 months
0.00%
0/3 • 4 months
Investigations
Elevated AST
25.0%
1/4 • Number of events 1 • 4 months
0.00%
0/3 • 4 months
Investigations
Elevated bilirubin
25.0%
1/4 • Number of events 1 • 4 months
0.00%
0/3 • 4 months
Gastrointestinal disorders
Nausea
25.0%
1/4 • Number of events 1 • 4 months
0.00%
0/3 • 4 months
Nervous system disorders
Neurology, somnolence
25.0%
1/4 • Number of events 1 • 4 months
0.00%
0/3 • 4 months
Skin and subcutaneous tissue disorders
Rash
25.0%
1/4 • Number of events 1 • 4 months
0.00%
0/3 • 4 months
Musculoskeletal and connective tissue disorders
Musculoskeletal, other leg/foot cramp
25.0%
1/4 • Number of events 1 • 4 months
0.00%
0/3 • 4 months

Additional Information

Howard A. Fine, M.D.

National Cancer Institute, National Institutes of Health

Phone: 301-402-6383

Results disclosure agreements

  • Principal investigator is a sponsor employee
  • Publication restrictions are in place