A Thyroid Hormone Analog to Fight Heart Failure: Phase II Trial (DITPA)

NCT ID: NCT00032643

Last Updated: 2013-11-05

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

TERMINATED

Clinical Phase

PHASE2

Total Enrollment

150 participants

Study Classification

INTERVENTIONAL

Study Start Date

2004-06-30

Study Completion Date

2006-12-31

Brief Summary

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Congestive heart failure (CHF) affects 4-5 million Americans, and its prevalence is predicted to increase over the next few decades. Thyroid hormone has unique actions which make it a novel and potentially useful agent for treatment of CHF. Due to possible adverse affects of thyroid hormone, there is interest in developing analogs with fewer undesirable side effects. 3,5- diiodothyropropionic acid (DITPA) has been shown to improve diastolic function in both animal models and a recently completed double-blind placebo controlled trial in 19 humans.

The goal of the proposed Phase II study is to show safety and demonstrate a medication of efficacy of DITPA needed in patients with CHF. This study is a prerequisite for a larger Phase III trial which would determine whether mortality is improved with DITPA. To better define the appropriate doses, prior to the Phase II study we will conduct an initial pharmacokinetic study.

Detailed Description

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Intervention: After enrollment, patients receive a clinical assessment, echocardiogram and laboratory studies. Then, each patient receives treatment with one of two doses of 3,5-diiodothyropropionic acid (DITPA) or placebo for six months.

Primary hypothesis: DITPA will improve cardiovascular function and clinical status in patients with moderately severe heart failure and be similar to placebo on safety measures.

Secondary hypothesis:

Primary Outcomes: 1. Composite endpoint composed of cardiovascular mortality/morbidity, change in NYHA class and change in global assessment, and 2. safety.

Study Abstract: Congestive heart failure (CHF) affects 4-5 million Americans, and its prevalence is predicted to increase over the next few decades. Thyroid hormone has unique actions which make it a novel and potentially useful agent for treatment of CHF. Due to possible adverse effects of thyroid hormone, there is interest in developing analogs with fewer undesirable side effects. DITPA has been shown to improve diastolic function in both animal models and a recently completed double-blind placebo controlled trial in 19 humans.

The goal of the proposed Phase II study is to define the dose of DITPA needed to achieve hemodynamic improvement in patients with CHF. This study is a prerequisite for a larger Phase III trial which would determine whether mortality is improved with DITPA. To better define the appropriate doses, prior to the Phase II study we will conduct an initial pharmacokinetic study.

Conditions

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Congestive Heart Failure

Study Design

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Blinding Strategy

DOUBLE

Study Groups

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Arm 1

Group Type OTHER

DITPA

Intervention Type DRUG

Interventions

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DITPA

Intervention Type DRUG

Eligibility Criteria

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Inclusion Criteria

INCLUSION

To be enrolled, patients must:

1. be veterans,
2. have moderately severe CHF (NYHA class II, III or IV),
3. be 18 or older,
4. not have clinically important renal, hepatic or hematological disorders or clinically significant abnormal laboratory findings,
5. not have a pre-existing thyroid disease,
6. not have anemia (hematocrit less than 30%),
7. not have chronic pulmonary disease that limits exercise tolerance or requires use of chronic bronchodilator therapy or steroids,
8. be able to walk on the level for 6 minutes,
9. not have hemodynamically significant pericardial disease,
10. not have angina pectoris severe enough to require frequent administration of sublingual nitroglycerin,
11. not have acute myocardial infarction within 6 months of screening,
12. not have inoperable aortic stenosis,
13. not have symptomatic ventricular arrhythmias or ventricular arrhythmia requiring pharmacological therapy,
14. not have implanted cardioverter defibrillator,
15. not be taking amiodarone,
16. not have demonstrated non-compliance with prior medical regimes;
17. not be on an investigational drug,
18. not have a medical condition that, in the investigator's opinion, would make the patient ineligible,
19. not have an allergy to iodine or shellfish,
20. not be in sinus rhythm,
21. not be of childbearing potential,
22. have an ejection fraction greater than 40%.
Minimum Eligible Age

18 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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US Department of Veterans Affairs

FED

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Steven Goldman, MD

Role: STUDY_CHAIR

Southern Arizona VA Health Care System

Locations

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Southern Arizona VA Health Care System

Tucson, Arizona, United States

Site Status

VA Greater Los Angeles Healthcare System, West LA

West Los Angeles, California, United States

Site Status

VA Eastern Colorado Health Care System, Denver

Denver, Colorado, United States

Site Status

VA Medical Center, Minneapolis

Minneapolis, Minnesota, United States

Site Status

VA Medical Center, Cleveland

Cleveland, Ohio, United States

Site Status

Ralph H Johnson VA Medical Center, Charleston

Charleston, South Carolina, United States

Site Status

VA South Texas Health Care System, San Antonio

San Antonio, Texas, United States

Site Status

Countries

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United States

Other Identifiers

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526

Identifier Type: -

Identifier Source: org_study_id