Study of High-Dose Melphalan and Autologous Stem Cell Transplantation in Patients With Primary Light Chain Amyloidosis

NCT ID: NCT00017680

Last Updated: 2008-06-09

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

Get a concise snapshot of the trial, including recruitment status, study phase, enrollment targets, and key timeline milestones.

Recruitment Status

COMPLETED

Clinical Phase

PHASE2

Total Enrollment

25 participants

Study Classification

INTERVENTIONAL

Study Start Date

1999-07-31

Study Completion Date

2004-04-30

Brief Summary

Review the sponsor-provided synopsis that highlights what the study is about and why it is being conducted.

OBJECTIVES: I. Determine the response, disease-free survival, and overall survival of patients with primary light chain amyloidosis treated with high-dose melphalan and autologous stem cell transplantation.

II. Determine the toxicity of this regimen in these patients.

Detailed Description

Dive into the extended narrative that explains the scientific background, objectives, and procedures in greater depth.

PROTOCOL OUTLINE: Patients may receive induction chemotherapy before study entry. Patients then receive filgrastim (G-CSF) or another growth factor for 4-6 days as peripheral blood stem cell (PBSC) mobilization. PBSC (or bone marrow) is harvested over 2-3 days.

Patients receive high-dose melphalan IV over 30 minutes twice daily on days -2 and -1. PBSC and/or bone marrow is reinfused on day 0. Patients receive G-CSF beginning on day 0 and continuing until blood counts recover. This course may be repeated 4-12 weeks later.

Patients are followed every 3 months for 1 year and then annually for 5 years.

Conditions

See the medical conditions and disease areas that this research is targeting or investigating.

Amyloidosis

Keywords

Explore important study keywords that can help with search, categorization, and topic discovery.

amyloidosis arthritis & connective tissue diseases genetic diseases and dysmorphic syndromes hematopoietic/lymphoid cancer oncologic disorders plasma cell neoplasm primary systemic amyloidosis rare disease

Study Design

Understand how the trial is structured, including allocation methods, masking strategies, primary purpose, and other design elements.

Allocation Method

NON_RANDOMIZED

Intervention Model

SINGLE_GROUP

Primary Study Purpose

TREATMENT

Blinding Strategy

NONE

Interventions

Learn about the drugs, procedures, or behavioral strategies being tested and how they are applied within this trial.

Melphalan

100 mg/m2 twice a day from Days -2 and -1 as induction therapy

Intervention Type DRUG

Autologous Stem Cell Transplantation

Bone marrow and peripheral blood stem cells harvested

Intervention Type PROCEDURE

Eligibility Criteria

Check the participation requirements, including inclusion and exclusion rules, age limits, and whether healthy volunteers are accepted.

Inclusion Criteria

Prior/Concurrent Therapy

* Biologic therapy: Concurrent participation in gene therapy trials allowed
* Chemotherapy: Prior chemotherapy allowed No other concurrent chemotherapy
* Endocrine therapy: No concurrent steroids unless given with amphotericin B, for adrenal failure, or for septic shock No concurrent hormones except for non-disease-related conditions (e.g., insulin for diabetes)
* Other: No concurrent barbiturates or acetaminophen Concurrent participation in supportive care trials allowed

Patient Characteristics

* Performance status: ECOG 0-3
* Hepatic: Bilirubin less than 2 times normal
* Renal: Creatinine less than 2.5 mg/dL OR On stable hemodialysis
* Pulmonary: DLCO at least 60% predicted OR Clearance by pulmonologist
* Other: HIV negative
Minimum Eligible Age

18 Years

Maximum Eligible Age

70 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

Meet the organizations funding or collaborating on the study and learn about their roles.

Herbert Irving Comprehensive Cancer Center

OTHER

Sponsor Role lead

Responsible Party

Identify the individual or organization who holds primary responsibility for the study information submitted to regulators.

Columbia University

Principal Investigators

Learn about the lead researchers overseeing the trial and their institutional affiliations.

Charles S. Hesdorffer

Role: STUDY_CHAIR

Herbert Irving Comprehensive Cancer Center

Locations

Explore where the study is taking place and check the recruitment status at each participating site.

Herbert Irving Comprehensive Cancer Center

New York, New York, United States

Site Status

Countries

Review the countries where the study has at least one active or historical site.

United States

Other Identifiers

Review additional registry numbers or institutional identifiers associated with this trial.

CPMC-IRB-9041

Identifier Type: -

Identifier Source: secondary_id

CPMC-CAMP-009A

Identifier Type: -

Identifier Source: secondary_id

199/15927

Identifier Type: -

Identifier Source: org_study_id