Comparison of Two Different Doses of STI571 in Treating Patients With Metastatic or Unresectable Gastrointestinal Stromal Tumor

NCT ID: NCT00009906

Last Updated: 2014-12-23

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

TERMINATED

Clinical Phase

PHASE3

Total Enrollment

748 participants

Study Classification

INTERVENTIONAL

Study Start Date

2000-12-31

Study Completion Date

2014-11-30

Brief Summary

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Randomized phase III trial to compare the effectiveness of two different doses of STI571 in treating patients who have metastatic or unresectable gastrointestinal stromal tumor. STI571 may interfere with the growth of tumor cells and may be an effective treatment for cancer. It is not yet known which dose of STI571 is more effective in treating gastrointestinal stromal tumors.

Detailed Description

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PRIMARY OBJECTIVES:

I. Compare the overall and progression-free survival of patients with CD117-expressing metastatic or unresectable gastrointestinal stromal tumor treated with two different doses of imatinib mesylate.

II. Compare the confirmed, unconfirmed, complete, and partial response rates in patients treated with these regimens.

III. Compare the toxic effects of these regimens in these patients.

OUTLINE: This is a randomized study. Patients are randomized to one of two treatment arms.

Arm I: Patients receive oral imatinib mesylate once daily.

Arm II: Patients receive oral imatinib mesylate twice daily.

Treatment continues in the absence of disease progression or unacceptable toxicity.

Patients in arm I with progressive disease may cross over to arm II and receive treatment in the absence of further disease progression.

Patients are followed every 3 months for 1 year, every 6 months for 2 years, and then annually thereafter.

PROJECTED ACCRUAL: A total of 600 patients will be accrued for this study within 24 months.

Conditions

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Gastrointestinal Stromal Tumor

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

DOUBLE

Participants Investigators

Study Groups

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Arm I (imatinib mesylate)

Patients receive oral imatinib mesylate once daily.

Group Type EXPERIMENTAL

Imatinib Mesylate

Intervention Type DRUG

Given orally

Arm II (imatinib mesylate)

Patients receive oral imatinib mesylate twice daily.

Group Type EXPERIMENTAL

Imatinib Mesylate

Intervention Type DRUG

Given orally

Interventions

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Imatinib Mesylate

Given orally

Intervention Type DRUG

Eligibility Criteria

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Inclusion Criteria

* Patient must have a biopsy proven diagnosis of gastrointestinal stromal tumor (GIST) which is distantly metastatic or unresectable; tumors must meet BOTH of the following criteria:

* The primary must be of visceral or intra-abdominal origin
* All patients must have immunohistochemical documentation of KIT (CD117) expression by tumor documented by DAKO antibody staining for suggested methodology) Material must be submitted to the CALGB Pathology Coordinating Center for pathology review; it is strongly recommended that snap-frozen tissue biopsy and sera be stored for future submission whenever possible
* Patient must have measurable or non-measurable disease by conventional scan imaging (CT or MRI) or physical examination; tests used to assess disease must have been performed within 28 days prior to registration; if a target lesion has been previously embolized or irradiated, there must be objective evidence of progression to be considered for response assessment
* Patient must have an identified team (including a medical oncologist and a surgeon) to provide care
* Patient must not have known brain metastasis
* Patient must have a Zubrod performance status of 0 - 3
* Patient must have resolution of transient toxicities from any prior therapy to =\< grade 1 (NCI-CTC version 2.0)
* The patient must not have received chemotherapy, biologic therapy or any other investigational drug for any reason within 28 days prior to registration; patients must not have had a major surgery within 14 days prior to registration
* If day 14 or 28 falls on a weekend or holiday, the limit may be extended to the next working day

* In calculating days of tests and measurements, the day a test or measurement is done is considered day 0; therefore, if a test is done on a Monday, the Monday two weeks later would be considered day 14; this allows for efficient patient scheduling without exceeding the guidelines
* No other prior malignancy is allowed except for the following: adequately treated basal cell or squamous cell skin cancer, in situ cervical cancer, adequately treated stage I or II cancer from which the patient is currently in complete remission, or any other cancer from which the patient has been disease-free for 5 years
* All patients must be informed of the investigational nature of this study and must sign and give written informed consent in accordance with institutional and federal guidelines
* At the time of patient registration, the treating institution's name and ID number must be provided to the Data Operations Center in Seattle in order to ensure that the current (within 365 days) date of institutional review board approval for this study has been entered into the data base
* Patients on lower dose arm (Arm 1) will be allowed to increase the daily dose of STI-571 in the case of disease progression; if there is questionable disease progression, the treating investigator should contact the primary Study Coordinator, Dr. George Demetri at 617/632-3985 to review progression information and discuss treatment options
Minimum Eligible Age

15 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Eastern Cooperative Oncology Group

NETWORK

Sponsor Role collaborator

SWOG Cancer Research Network

NETWORK

Sponsor Role collaborator

NCIC Clinical Trials Group

NETWORK

Sponsor Role collaborator

National Cancer Institute (NCI)

NIH

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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George Demetri

Role: PRINCIPAL_INVESTIGATOR

SWOG Cancer Research Network

Locations

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Western Regional CCOP

Phoenix, Arizona, United States

Site Status

University of Arizona Health Sciences Center

Tucson, Arizona, United States

Site Status

University of Arkansas for Medical Sciences

Little Rock, Arkansas, United States

Site Status

Highlands Oncology Group-Rogers

Rogers, Arkansas, United States

Site Status

City of Hope Comprehensive Cancer Center

Duarte, California, United States

Site Status

Long Beach Community Hospital

Long Beach, California, United States

Site Status

University of Southern California/Norris Cancer Center

Los Angeles, California, United States

Site Status

University of California at Los Angeles Health System

Los Angeles, California, United States

Site Status

Sutter Cancer Research Consortium

Novato, California, United States

Site Status

University of California Davis Comprehensive Cancer Center

Sacramento, California, United States

Site Status

Kaiser Permanente - Sacramento

Sacramento, California, United States

Site Status

University of California San Diego

San Diego, California, United States

Site Status

UCSF Medical Center-Mount Zion

San Francisco, California, United States

Site Status

Santa Rosa Memorial Hospital

Sana Rosa, California, United States

Site Status

Stanford University Hospitals and Clinics

Stanford, California, United States

Site Status

Presbyterian - Saint Lukes Medical Center - Health One

Denver, Colorado, United States

Site Status

Rose Medical Center

Denver, Colorado, United States

Site Status

Swedish Medical Center

Englewood, Colorado, United States

Site Status

Poudre Valley Hospital

Fort Collins, Colorado, United States

Site Status

Saint Mary Corwin Medical Center

Pueblo, Colorado, United States

Site Status

Middlesex Hospital

Middletown, Connecticut, United States

Site Status

MedStar Oncology Network

Washington D.C., District of Columbia, United States

Site Status

Mayo Clinic in Florida

Jacksonville, Florida, United States

Site Status

Hematology Oncology Associates

Lake Worth, Florida, United States

Site Status

Florida Hospital Orlando

Orlando, Florida, United States

Site Status

Moffitt Cancer Center

Tampa, Florida, United States

Site Status

Phoebe Putney Memorial Hospital

Albany, Georgia, United States

Site Status

Emory University/Winship Cancer Institute

Atlanta, Georgia, United States

Site Status

Atlanta Regional CCOP

Atlanta, Georgia, United States

Site Status

Medical Center of Central Georgia

Macon, Georgia, United States

Site Status

University of Hawaii Cancer Center

Honolulu, Hawaii, United States

Site Status

Hematology and Oncology Associates

Chicago, Illinois, United States

Site Status

Northwestern University

Chicago, Illinois, United States

Site Status

Jesse Brown Veterans Affairs Medical Center

Chicago, Illinois, United States

Site Status

Rush University Medical Center

Chicago, Illinois, United States

Site Status

University of Illinois

Chicago, Illinois, United States

Site Status

University of Chicago Comprehensive Cancer Center

Chicago, Illinois, United States

Site Status

Central Illinois CCOP

Decatur, Illinois, United States

Site Status

Alexian Brothers Medical and Cancer Center

Elk Grove Village, Illinois, United States

Site Status

NorthShore University HealthSystem-Evanston Hospital

Evanston, Illinois, United States

Site Status

Loyola University Medical Center

Maywood, Illinois, United States

Site Status

Mid-Illinois Hematology Oncology Associates

Normal, Illinois, United States

Site Status

Advocate Lutheran General Hospital.

Park Ridge, Illinois, United States

Site Status

Carle Cancer Center

Urbana, Illinois, United States

Site Status

Indiana University/Melvin and Bren Simon Cancer Center

Indianapolis, Indiana, United States

Site Status

IU Health Methodist Hospital

Indianapolis, Indiana, United States

Site Status

McFarland Clinic PC-William R Bliss Cancer Center

Ames, Iowa, United States

Site Status

University of Kansas Medical Center

Kansas City, Kansas, United States

Site Status

Kansas City CCOP

Prairie Village, Kansas, United States

Site Status

Stormont-Vail Regional Health Center

Topeka, Kansas, United States

Site Status

Our Lady Bellefonte Hospital

Ashland, Kentucky, United States

Site Status

Louisiana State University Health Science Center

New Orleans, Louisiana, United States

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Sinai Hospital of Baltimore

Baltimore, Maryland, United States

Site Status

Johns Hopkins University/Sidney Kimmel Comprehensive Cancer Center

Baltimore, Maryland, United States

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Massachusetts General Hospital Cancer Center

Boston, Massachusetts, United States

Site Status

Dana-Farber Cancer Institute

Boston, Massachusetts, United States

Site Status

Beth Israel Deaconess Medical Center

Boston, Massachusetts, United States

Site Status

Michigan Cancer Research Consortium Community Clinical Oncology Program

Ann Arbor, Michigan, United States

Site Status

University of Michigan University Hospital

Ann Arbor, Michigan, United States

Site Status

Oakwood Hospital and Medical Center

Dearborn, Michigan, United States

Site Status

Wayne State University/Karmanos Cancer Institute

Detroit, Michigan, United States

Site Status

Henry Ford Hospital

Detroit, Michigan, United States

Site Status

Grand Rapids Clinical Oncology Program

Grand Rapids, Michigan, United States

Site Status

West Michigan Cancer Center

Kalamazoo, Michigan, United States

Site Status

Marquette General Hospital

Marquette, Michigan, United States

Site Status

Unity Hospital

Fridley, Minnesota, United States

Site Status

University of Minnesota Medical Center-Fairview

Minneapolis, Minnesota, United States

Site Status

North Memorial Medical Health Center

Robbinsdale, Minnesota, United States

Site Status

Mayo Clinic

Rochester, Minnesota, United States

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Park Nicollet Clinic - Saint Louis Park

Saint Louis Park, Minnesota, United States

Site Status

Regions Hospital

Saint Paul, Minnesota, United States

Site Status

University of Mississippi Medical Center

Jackson, Mississippi, United States

Site Status

Saint Joseph's Health Center

Saint Charles, Missouri, United States

Site Status

Ozark Health Ventures LLC-Cancer Research for The Ozarks Springfield

Springfield, Missouri, United States

Site Status

Saint Louis Cancer and Breast Institute-South City

St Louis, Missouri, United States

Site Status

Barnes-Jewish Hospital

St Louis, Missouri, United States

Site Status

Missouri Baptist Medical Center

St Louis, Missouri, United States

Site Status

Alegent Health Immanuel Medical Center

Omaha, Nebraska, United States

Site Status

Dartmouth Hitchcock Medical Center

Lebanon, New Hampshire, United States

Site Status

Hackensack University Medical CCOP

Hackensack, New Jersey, United States

Site Status

Saint Barnabas Medical Center

Livingston, New Jersey, United States

Site Status

Rutgers Cancer Institute of New Jersey

New Brunswick, New Jersey, United States

Site Status

University of New Mexico

Albuquerque, New Mexico, United States

Site Status

Roswell Park Cancer Institute

Buffalo, New York, United States

Site Status

Winthrop University Hospital

Mineola, New York, United States

Site Status

Beth Israel Medical Center

New York, New York, United States

Site Status

New York University Langone Medical Center

New York, New York, United States

Site Status

Columbia University Medical Center

New York, New York, United States

Site Status

Memorial Sloan-Kettering Cancer Center

New York, New York, United States

Site Status

Albert Einstein College of Medicine

The Bronx, New York, United States

Site Status

Montefiore Medical Center - Moses Campus

The Bronx, New York, United States

Site Status

University of North Carolina

Chapel Hill, North Carolina, United States

Site Status

Duke University Medical Center

Durham, North Carolina, United States

Site Status

Southeast Cancer Control Consortium CCOP

Winston-Salem, North Carolina, United States

Site Status

Wake Forest University Health Sciences

Winston-Salem, North Carolina, United States

Site Status

Roger Maris Cancer Center

Fargo, North Dakota, United States

Site Status

Case Western Reserve University

Cleveland, Ohio, United States

Site Status

Cleveland Clinic Foundation

Cleveland, Ohio, United States

Site Status

Ohio State University Comprehensive Cancer Center

Columbus, Ohio, United States

Site Status

Columbus CCOP

Columbus, Ohio, United States

Site Status

Dayton CCOP

Dayton, Ohio, United States

Site Status

Saint Rita's Medical Center

Lima, Ohio, United States

Site Status

University of Oklahoma Health Sciences Center

Oklahoma City, Oklahoma, United States

Site Status

Sky Lakes Medical Center - Cancer Treatment Center

Klamath Falls, Oregon, United States

Site Status

Western Oncology Research Consortium

Portland, Oregon, United States

Site Status

Oregon Health and Science University

Portland, Oregon, United States

Site Status

Salem Hospital

Salem, Oregon, United States

Site Status

Geisinger Medical Center

Danville, Pennsylvania, United States

Site Status

Mercy Fitzgerald Hospital

Darby, Pennsylvania, United States

Site Status

Delaware County Memorial Hospital

Drexel Hill, Pennsylvania, United States

Site Status

University of Pennsylvania/Abramson Cancer Center

Philadelphia, Pennsylvania, United States

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Thomas Jefferson University Hospital

Philadelphia, Pennsylvania, United States

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Fox Chase Cancer Center

Philadelphia, Pennsylvania, United States

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Aria Health-Torresdale Campus

Philadelphia, Pennsylvania, United States

Site Status

Albert Einstein Medical Center

Philadelphia, Pennsylvania, United States

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Rhode Island Hospital

Providence, Rhode Island, United States

Site Status

Upstate Carolina CCOP

Spartanburg, South Carolina, United States

Site Status

Baptist Memorial Hospital and Cancer Center-Memphis

Memphis, Tennessee, United States

Site Status

Vanderbilt-Ingram Cancer Center

Nashville, Tennessee, United States

Site Status

M D Anderson Cancer Center

Houston, Texas, United States

Site Status

Huntsman Cancer Institute/University of Utah

Salt Lake City, Utah, United States

Site Status

Central Vermont Medical Center

Barre, Vermont, United States

Site Status

Central Vermont Medical Center/National Life Cancer Treatment

Berlin Corners, Vermont, United States

Site Status

Rutland Regional Medical Center

Rutland, Vermont, United States

Site Status

Virginia Oncology Associates-Hampton

Hampton, Virginia, United States

Site Status

Virginia Mason CCOP

Seattle, Washington, United States

Site Status

Group Health

Seattle, Washington, United States

Site Status

Cancer Care Northwest - Spokane South

Spokane, Washington, United States

Site Status

Northwest CCOP

Tacoma, Washington, United States

Site Status

Saint Vincent Hospital

Green Bay, Wisconsin, United States

Site Status

University of Wisconsin Hospital and Clinics

Madison, Wisconsin, United States

Site Status

Marshfield Clinic

Marshfield, Wisconsin, United States

Site Status

Tom Baker Cancer Centre

Calgary, Alberta, Canada

Site Status

Cross Cancer Institute

Edmonton, Alberta, Canada

Site Status

BCCA-Vancouver Cancer Centre

Vancouver, British Columbia, Canada

Site Status

Hamilton and District Urology Association McMaster Institute

Hamilton, Ontario, Canada

Site Status

Juravinski Cancer Centre at Hamilton Health Sciences

Hamilton, Ontario, Canada

Site Status

London Regional Cancer Program

London, Ontario, Canada

Site Status

Ottawa Health Research Institute-General Division

Ottawa, Ontario, Canada

Site Status

Mount Sinai Hospital

Toronto, Ontario, Canada

Site Status

CHUM - Hopital Notre-Dame

Montreal, Quebec, Canada

Site Status

McGill University Department of Oncology

Montreal, Quebec, Canada

Site Status

San Juan Veterans Affairs Medical Center

San Juan, , Puerto Rico

Site Status

San Juan City Hospital

San Juan, , Puerto Rico

Site Status

Countries

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Australia Belgium Denmark France Germany Italy Netherlands New Zealand Slovakia Spain Sweden Switzerland United Kingdom United States Canada Puerto Rico

References

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Heinrich MC, Rankin C, Blanke CD, Demetri GD, Borden EC, Ryan CW, von Mehren M, Blackstein ME, Priebat DA, Tap WD, Maki RG, Corless CL, Fletcher JA, Owzar K, Crowley JJ, Benjamin RS, Baker LH. Correlation of Long-term Results of Imatinib in Advanced Gastrointestinal Stromal Tumors With Next-Generation Sequencing Results: Analysis of Phase 3 SWOG Intergroup Trial S0033. JAMA Oncol. 2017 Jul 1;3(7):944-952. doi: 10.1001/jamaoncol.2016.6728.

Reference Type DERIVED
PMID: 28196207 (View on PubMed)

Other Identifiers

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NCI-2012-02372

Identifier Type: REGISTRY

Identifier Source: secondary_id

S0033

Identifier Type: -

Identifier Source: secondary_id

INT-S0033

Identifier Type: -

Identifier Source: secondary_id

CDR0000068422

Identifier Type: -

Identifier Source: secondary_id

CAN-NCIC-S0033

Identifier Type: -

Identifier Source: secondary_id

CLB-80004

Identifier Type: -

Identifier Source: secondary_id

SWOG-S0033

Identifier Type: -

Identifier Source: secondary_id

E-S0033

Identifier Type: -

Identifier Source: secondary_id

S0033

Identifier Type: OTHER

Identifier Source: secondary_id

S0033

Identifier Type: OTHER

Identifier Source: secondary_id

U10CA180888

Identifier Type: NIH

Identifier Source: secondary_id

View Link

U10CA032102

Identifier Type: NIH

Identifier Source: secondary_id

View Link

N01CM17003

Identifier Type: NIH

Identifier Source: secondary_id

View Link

NCI-2012-02372

Identifier Type: -

Identifier Source: org_study_id