Trial Outcomes & Findings for Neurotropin to Treat Chronic Neuropathic Pain (NCT NCT00006289)

NCT ID: NCT00006289

Last Updated: 2017-08-22

Results Overview

Assessments of pain severity by the patient using a visual analogue scale ranging from 0 to 100 (mm), with 0 = no pain and 100 = maximal pain level. When it is difficult to recruit the patients, the interim analysis using these data is performed after completion of the study of first 16 patients (target number is 30). The data from 16 patients was analyzed while investigators were blinded to the treatment code (Drug A and B) provided by the NIH pharmacy. Only after the analysis was completed was the code unblinded. Placebo or Neurotropin" in place of "drug A or drug B.

Recruitment status

TERMINATED

Study phase

PHASE2

Target enrollment

21 participants

Primary outcome timeframe

VAS of each patient is measured after each 5-week treatment interval with placebo or Neurotropin.

Results posted on

2017-08-22

Participant Flow

Most patients are recruited by direct physician referral or through the Patient Recruitment and Public Liaison (PRPL) office. Potential subjects are determined to be qualified by screening at Clinical Center, NIH in the US.

Patients who have abnormal results from routine laboratory test or are positive for HIV are excluded. Women who are pregnant or positive for pregnancy test are excluded. Also patients who have non-traumatic pain disorders or are obviously have impaired mental capacity are excluded.

Participant milestones

Participant milestones
Measure
Placebo First, Then Neurotropin
Receive the placebo b.i.d. for 5 weeks and then Neurotropin b.i.d. for 5 weeks (after at least 1 week washout period)
Neurotropin First, Then Placebo
Receive Neurotropin b.i.d. for 5 weeks and then the placebo b.i.d. for 5 weeks (after at least 1 week washout period)
First Intervention (5 Weeks)
STARTED
11
10
First Intervention (5 Weeks)
COMPLETED
10
10
First Intervention (5 Weeks)
NOT COMPLETED
1
0
Washout (>= 1 Week)
STARTED
10
10
Washout (>= 1 Week)
COMPLETED
10
10
Washout (>= 1 Week)
NOT COMPLETED
0
0
Second Intervention (5 Weeks)
STARTED
10
10
Second Intervention (5 Weeks)
COMPLETED
9
9
Second Intervention (5 Weeks)
NOT COMPLETED
1
1

Reasons for withdrawal

Reasons for withdrawal
Measure
Placebo First, Then Neurotropin
Receive the placebo b.i.d. for 5 weeks and then Neurotropin b.i.d. for 5 weeks (after at least 1 week washout period)
Neurotropin First, Then Placebo
Receive Neurotropin b.i.d. for 5 weeks and then the placebo b.i.d. for 5 weeks (after at least 1 week washout period)
First Intervention (5 Weeks)
Adverse Event
1
0
Second Intervention (5 Weeks)
Protocol Violation
1
1

Baseline Characteristics

Neurotropin to Treat Chronic Neuropathic Pain

Baseline characteristics by cohort

Baseline characteristics by cohort
Measure
Placebo First, Then Neurotropin
n=11 Participants
Receive Placebo 4 tabs b.i.d. for 5 weeks and then Neurotropin 4 tabs b.i.d. for 5 weeks (after at least 1 week washout period)
Neurotropin First, Then Placebo
n=10 Participants
Receive Neurotropin 4 tabs b.i.d. for 5 weeks and then Placebo 4 tabs b.i.d. for 5 weeks (after at least 1 week washout period)
Total
n=21 Participants
Total of all reporting groups
Age, Categorical
<=18 years
2 Participants
n=5 Participants
0 Participants
n=7 Participants
2 Participants
n=5 Participants
Age, Categorical
Between 18 and 65 years
9 Participants
n=5 Participants
9 Participants
n=7 Participants
18 Participants
n=5 Participants
Age, Categorical
>=65 years
0 Participants
n=5 Participants
1 Participants
n=7 Participants
1 Participants
n=5 Participants
Age, Continuous
37.3 years
STANDARD_DEVIATION 13.2 • n=5 Participants
46.5 years
STANDARD_DEVIATION 13.2 • n=7 Participants
41.7 years
STANDARD_DEVIATION 13.7 • n=5 Participants
Sex: Female, Male
Female
10 Participants
n=5 Participants
5 Participants
n=7 Participants
15 Participants
n=5 Participants
Sex: Female, Male
Male
1 Participants
n=5 Participants
5 Participants
n=7 Participants
6 Participants
n=5 Participants
Region of Enrollment
United States
11 participants
n=5 Participants
10 participants
n=7 Participants
21 participants
n=5 Participants

PRIMARY outcome

Timeframe: VAS of each patient is measured after each 5-week treatment interval with placebo or Neurotropin.

Assessments of pain severity by the patient using a visual analogue scale ranging from 0 to 100 (mm), with 0 = no pain and 100 = maximal pain level. When it is difficult to recruit the patients, the interim analysis using these data is performed after completion of the study of first 16 patients (target number is 30). The data from 16 patients was analyzed while investigators were blinded to the treatment code (Drug A and B) provided by the NIH pharmacy. Only after the analysis was completed was the code unblinded. Placebo or Neurotropin" in place of "drug A or drug B.

Outcome measures

Outcome measures
Measure
VAS After Placebo Treatment First in G-1
n=7 Participants
This group received placebo 4 tabs b.i.d. for 5 weeks first. VAS was determined at the end of the 5 week-treatment.
VAS After Neurotropin Treatment Second in G-1
n=7 Participants
This group received Neurotropin 4 tabs b.i.d. for 5 weeks after at least 1 week "washout" period following the first 5 week interval on placebo. VAS was determined at the end of the 5 week-treatment of Neurotropin.
VAS After Neurotropin Treatment First in G-2
n=9 Participants
This group received Neurotropin 4 tabs b.i.d. for 5 weeks first. VAS was determined at the end of the 5 week-treatment.
VAS After Placebo Treatment Second in G-2
n=9 Participants
This group received placebo 4 tabs b.i.d. for 5 weeks after at least 1 week "washout" period following the first 5 week interval on Neurotropin. VAS was determined at the end of the 5 week-treatment of placebo.
Visual Analogue Scale (VAS) of Pain Scores After Administration of Test Drugs (Placebo or Neurotropin )
33.6 mm
Standard Error 11.1
38.3 mm
Standard Error 8.8
36.0 mm
Standard Error 7.6
31.1 mm
Standard Error 7.7

PRIMARY outcome

Timeframe: NRS of each patient is measured after each five-week treatment interval with placebo or Neurotropin.

Assessments of pain severity by the patient using a numeric rating scale ranging from 0 to 10 as a verbal response where 0 = no pain and 10 =maximal pain. When it is difficult to recruit the patients, the interim analysis using these data is performed after completion of the study of first 16 patients (target number is 30). The data from 16 patients was analyzed while the investigators are blinded to the treatment code (Drug A or B) provided by the NIH pharmacy. Only after the analysis was completed was the code unblinded. Placebo or Neurotropin" in place of "drug A or drug B.

Outcome measures

Outcome measures
Measure
VAS After Placebo Treatment First in G-1
n=7 Participants
This group received placebo 4 tabs b.i.d. for 5 weeks first. VAS was determined at the end of the 5 week-treatment.
VAS After Neurotropin Treatment Second in G-1
n=7 Participants
This group received Neurotropin 4 tabs b.i.d. for 5 weeks after at least 1 week "washout" period following the first 5 week interval on placebo. VAS was determined at the end of the 5 week-treatment of Neurotropin.
VAS After Neurotropin Treatment First in G-2
n=9 Participants
This group received Neurotropin 4 tabs b.i.d. for 5 weeks first. VAS was determined at the end of the 5 week-treatment.
VAS After Placebo Treatment Second in G-2
n=9 Participants
This group received placebo 4 tabs b.i.d. for 5 weeks after at least 1 week "washout" period following the first 5 week interval on Neurotropin. VAS was determined at the end of the 5 week-treatment of placebo.
Numeric Rating Scale (NRS) of Pain Scores After Administration of Test Drugs (Neurotropin or Placebo)
3.0 units on a scale
Standard Deviation 1.1
3.3 units on a scale
Standard Deviation 0.9
4.0 units on a scale
Standard Deviation 0.8
3.1 units on a scale
Standard Deviation 0.8

PRIMARY outcome

Timeframe: MPQ of each patient is measured after each five-week treatment interval with drug A or drug B.

Assessments of pain severity by the patient using a McGill Pain Questionnaire which consists of 3 major classes of word descriptors-sensory, affective and evaluative - that are used by patients to specify subjective pain experience. Each word chosen from descriptor responses to 20 questions is given a value and the sum of the values of the responses provides a score which is an index of the pain severity with a minimum value of 20 and a maximal value of 78. When it is difficult to recruit the patients, the interim analysis using these data is performed after completion of the study of first 16 patients (target number is 30). The data from 16 patients was analyzed while investigators are blinded to the treatment code (drug A or B) provided by the NIH pharmacy. Only after the analysis was completed was the code unblinded. Placebo or Neurotropin" in place of "drug A or drug B.

Outcome measures

Outcome measures
Measure
VAS After Placebo Treatment First in G-1
n=7 Participants
This group received placebo 4 tabs b.i.d. for 5 weeks first. VAS was determined at the end of the 5 week-treatment.
VAS After Neurotropin Treatment Second in G-1
n=7 Participants
This group received Neurotropin 4 tabs b.i.d. for 5 weeks after at least 1 week "washout" period following the first 5 week interval on placebo. VAS was determined at the end of the 5 week-treatment of Neurotropin.
VAS After Neurotropin Treatment First in G-2
n=9 Participants
This group received Neurotropin 4 tabs b.i.d. for 5 weeks first. VAS was determined at the end of the 5 week-treatment.
VAS After Placebo Treatment Second in G-2
n=9 Participants
This group received placebo 4 tabs b.i.d. for 5 weeks after at least 1 week "washout" period following the first 5 week interval on Neurotropin. VAS was determined at the end of the 5 week-treatment of placebo.
McGill Pain Questionnaire (MPQ) of Scores After Administration of Test Drugs (Neurotropin or Placebo)
22.4 units on a scale
Standard Error 5.9
33.1 units on a scale
Standard Error 4.0
25.4 units on a scale
Standard Error 4.9
27.1 units on a scale
Standard Error 5.7

Adverse Events

Placebo First, Then Neurotropin

Serious events: 0 serious events
Other events: 1 other events
Deaths: 0 deaths

Neurotropin First, Then Placebo

Serious events: 0 serious events
Other events: 0 other events
Deaths: 0 deaths

Serious adverse events

Adverse event data not reported

Other adverse events

Other adverse events
Measure
Placebo First, Then Neurotropin
n=11 participants at risk
Receive the placebo b.i.d. for 5 weeks and then Neurotropin b.i.d. for 5 weeks (after at least 1 week washout period)
Neurotropin First, Then Placebo
n=10 participants at risk
Receive Neurotropin b.i.d. for 5 weeks and then the placebo b.i.d. for 5 weeks (after at least 1 week washout period)
Nervous system disorders
worsening of pain
9.1%
1/11 • Number of events 1 • Adverse event information will be collected during the treatments and 5 weeks after the completion of study.
Advese event information will be collected by blood test, weekly questionnaire, and self-report of patients.
0.00%
0/10 • Adverse event information will be collected during the treatments and 5 weeks after the completion of study.
Advese event information will be collected by blood test, weekly questionnaire, and self-report of patients.

Additional Information

Dr. Leorey Saligan (Principal Investigator, former PI: Dr. Raymond Dioone)

National Institute of Nursing Research

Phone: 301-451-1685

Results disclosure agreements

  • Principal investigator is a sponsor employee
  • Publication restrictions are in place