Genetic Study of Sitosterolemia

NCT ID: NCT00004481

Last Updated: 2005-06-24

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

COMPLETED

Study Classification

OBSERVATIONAL

Study Start Date

1999-11-30

Brief Summary

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OBJECTIVES:

I. Identify the genetic defect and fine map the gene that causes sitosterolemia.

Detailed Description

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PROTOCOL OUTLINE: Patients, family members, and normal volunteers provide blood samples for genetic studies and may fill out a general health and medication history.

Linkage analysis and microsatellite screening is performed on genomic DNA, especially chromosome 2p21, between microsatellite markers D2S1788 and D2S1352.

Positive results may be reported to the patient and may influence future treatment.

Conditions

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Lipid Metabolism, Inborn Errors Sitosterolemia

Study Design

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Observational Model Type

NATURAL_HISTORY

Interventions

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genetic testing

Intervention Type PROCEDURE

Eligibility Criteria

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Inclusion Criteria

PROTOCOL ENTRY CRITERIA:

--Disease Characteristics--

* Diagnosis of sitosterolemia Presence of tendon and tuberous xanthomas Premature atherosclerotic disease No family history of premature coronary artery disease Normal or elevated plasma cholesterol levels

OR

* Family member of patient with sitosterolemia

OR

* Normal volunteer
Minimum Eligible Age

0 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

Yes

Sponsors

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Medical University of South Carolina

OTHER

Sponsor Role collaborator

National Center for Research Resources (NCRR)

NIH

Sponsor Role lead

Principal Investigators

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Shailesh B. Patel

Role: STUDY_CHAIR

Medical University of South Carolina

Locations

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Medical University of South Carolina

Charleston, South Carolina, United States

Site Status

Countries

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United States

Other Identifiers

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MUSC-HR-8022

Identifier Type: -

Identifier Source: secondary_id

NCRR-M01RR01070-0470

Identifier Type: -

Identifier Source: org_study_id