Phase II Study of Dietary Cholesterol for Smith-Lemli-Opitz Syndrome

NCT ID: NCT00004347

Last Updated: 2005-06-24

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

UNKNOWN

Clinical Phase

PHASE2

Total Enrollment

5 participants

Study Classification

INTERVENTIONAL

Study Start Date

1995-11-30

Brief Summary

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OBJECTIVES: I. Examine the intestinal absorption of dietary cholesterol in patients with Smith-Lemli-Opitz syndrome.

II. Measure the effect of dietary cholesterol on plasma sterol composition. III. Quantify basal cholesterol synthesis, turnover of cholesterol and 7-dehydrocholesterol, and the effects of dietary cholesterol on these parameters.

IV. Identify fecal bile acid excretion quantitatively and qualitatively in these patients.

V. Compare the incorporation of deuterated water into plasma cholesterol, 7-dehydrocholesterol, and other intermediates, and assess the effect of dietary cholesterol on this incorporation.

Detailed Description

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PROTOCOL OUTLINE:

Patients are treated with 2 dietary regimens for 1 to 3 weeks: high cholesterol and cholesterol-free. Cholesterol is provided in the form of egg yolk. The absorption and metabolism of cholesterol are evaluated with plasma and fecal studies. Deuterated water is given to patients followed by analysis of deuterium in plasma cholesterol and other intermediates, including 7-dehydrocholesterol.

Conditions

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Smith-Lemli-Opitz Syndrome

Study Design

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Primary Study Purpose

TREATMENT

Interventions

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diet

Intervention Type BEHAVIORAL

Eligibility Criteria

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Inclusion Criteria

PROTOCOL ENTRY CRITERIA:

Smith-Lemli-Opitz syndrome
Minimum Eligible Age

0 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Oregon Health and Science University

OTHER

Sponsor Role collaborator

National Center for Research Resources (NCRR)

NIH

Sponsor Role lead

Principal Investigators

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William Connor

Role: STUDY_CHAIR

Oregon Health and Science University

Locations

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Oregon Health and Science University

Portland, Oregon, United States

Site Status RECRUITING

Countries

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United States

Facility Contacts

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Sonja Connor

Role: primary

503-494-7775

Jennifer Penfield

Role: backup

503-494-7944

Other Identifiers

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OHSU-4019

Identifier Type: -

Identifier Source: secondary_id

NCRR-M01RR00334-0068

Identifier Type: -

Identifier Source: org_study_id