Interleukin-2 Plus Histamine Dihydrochloride in Treating Patients With Acute Myeloid Leukemia

NCT ID: NCT00003991

Last Updated: 2013-11-06

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE3

Total Enrollment

360 participants

Study Classification

INTERVENTIONAL

Study Start Date

1998-07-31

Study Completion Date

2011-08-31

Brief Summary

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RATIONALE: Interleukin-2 may stimulate a person's white blood cells to kill acute myeloid leukemia cells. Histamine dihydrochloride may prolong remission and reduce the risk of relapse in patients with acute myeloid leukemia in remission.

PURPOSE: Randomized phase III trial to determine the effectiveness of interleukin-2 plus histamine dihydrochloride in treating patients who have acute myeloid leukemia that is in remission following previous therapy.

Detailed Description

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OBJECTIVES: I. Compare the efficacy of interleukin-2 plus histamine dihydrochloride (Maxamine) vs no further therapy in prolonging the leukemia free survival in patients with acute myeloid leukemia in first or subsequent complete remission (CR) following consolidation therapy. II. Compare the relapse rate, overall survival, and quality of life in this patient population treated with interleukin-2 plus Maxamine vs no further therapy. III. Compare the remission inversion rate in patients in subsequent CR with this treatment regimen vs no further therapy.

OUTLINE: This is a randomized, open label, parallel, multicenter study. Patients are stratified according to complete remission (first vs subsequent). Patients are randomized to one of two treatment arms. Arm I: Following consolidation chemotherapy or autologous stem cell transplantation, patients receive interleukin-2 subcutaneously followed by histamine dihydrochloride subcutaneously over 5-7 minutes twice daily on days 1-21. Treatment repeats every 6 weeks for 3 courses and then every 9 weeks for 7 courses in the absence of disease relapse or unacceptable toxicity. Arm II: Patients receive no further therapy following consolidation chemotherapy or autologous stem cell transplantation. Quality of life is assessed prior to study, and at visits 6, 7, 10, 11, 16, 17, and 22. Patients are followed for relapse and survival every 3 months for 2.5 years.

PROJECTED ACCRUAL: A total of 360 patients will be accrued for this study.

Conditions

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Leukemia

Keywords

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adult acute myeloid leukemia in remission

Study Design

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Allocation Method

RANDOMIZED

Primary Study Purpose

TREATMENT

Interventions

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aldesleukin

Intervention Type BIOLOGICAL

histamine dihydrochloride

Intervention Type DRUG

Eligibility Criteria

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Inclusion Criteria

DISEASE CHARACTERISTICS: Cytologically confirmed acute myeloid leukemia (AML) in first complete remission (CR) or subsequent CR Less than 5% blasts in normal bone marrow Less than 3 months since last dose of chemotherapy OR Less than 6 months since achieving CR

PATIENT CHARACTERISTICS: Age: 18 and over Performance status: WHO 0-1 OR Karnofsky 70-100% Life expectancy: Greater than 3 months Hematopoietic: WBC at least 1,500/mm3 Platelet count at least 75,000/mm3 Hepatic: PTT normal Bilirubin no greater than 2 times upper limit of normal (ULN) SGOT and SGPT no greater than 2 times ULN Renal: Creatinine no greater than 1.5 times ULN Cardiovascular: No class III or IV heart disease No hypotension, severe hypertension, or serious or uncontrolled cardiac dysrhythmia (e.g., ventricular arrhythmias) No acute myocardial infarction within the past 12 months No active uncontrolled angina pectoris No symptomatic arteriosclerotic blood vessel disease Pulmonary: No history of asthma within the past 5 years Other: No other active malignancies except localized basal or squamous cell skin cancer or carcinoma in situ of the cervix HIV negative No prior or active peptic or esophageal ulcer disease No history of hypersensitivity to histamine or histamine products, or severe allergies Not pregnant or nursing

PRIOR CONCURRENT THERAPY: Biologic therapy: Prior autologous stem cell transplantation allowed No prior allogeneic stem cell transplantation No other concurrent immunomodulating agents Chemotherapy: See Disease Characteristics Prior induction or consolidation therapy allowed No concurrent chemotherapy Endocrine therapy: At least 24 hours since prior corticosteroids No concurrent steroids Radiotherapy: Not specified Surgery: Not specified Other: No concurrent alternative therapy (e.g., laetrile, Brudzinski's treatment, etc.)
Minimum Eligible Age

18 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Maxim Pharmaceuticals

INDUSTRY

Sponsor Role lead

Principal Investigators

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Barbara Berryhill

Role: STUDY_CHAIR

Maxim Pharmaceuticals

Locations

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University of Alabama Comprehensive Cancer Center

Birmingham, Alabama, United States

Site Status

Arizona Cancer Center

Tucson, Arizona, United States

Site Status

Scripps Clinic

La Jolla, California, United States

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Cedars-Sinai Medical Center

Los Angeles, California, United States

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Kaiser Permanente-Southern California Permanente Medical Group

San Diego, California, United States

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Sidney Kimmel Cancer Center

San Diego, California, United States

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Pacific Hematology/Oncology

San Francisco, California, United States

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Bethesda Bone Marrow Stem Cell Transplant Institute

Boynton Beach, Florida, United States

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University of Florida Health Science Center - Jacksonville

Jacksonville, Florida, United States

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Emory University Hospital - Atlanta

Atlanta, Georgia, United States

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University of Kansas Medical Center

Kansas City, Kansas, United States

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Oncology and Hematology Associates

Westwood, Kansas, United States

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Maine Center for Cancer Medicine and Blood Disorders

Scarborough, Maine, United States

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Henry Ford Hospital

Detroit, Michigan, United States

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Providence Hospital Cancer Center

Southfield, Michigan, United States

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Washington University School of Medicine

St Louis, Missouri, United States

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Nevada Cancer Center

Las Vegas, Nevada, United States

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Nevada Medical Group-Internal Medicine

Reno, Nevada, United States

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University of New Mexico Cancer Research & Treatment Center

Albuquerque, New Mexico, United States

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New York Presbyterian Hospital - Cornell Campus

New York, New York, United States

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University of Rochester Cancer Center

Rochester, New York, United States

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Our Lady of Mercy Medical Center

The Bronx, New York, United States

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New York Medical College

Valhalla, New York, United States

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Ireland Cancer Center

Cleveland, Ohio, United States

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University of Oklahoma Health Sciences Center

Oklahoma City, Oklahoma, United States

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University of Pennsylvania Cancer Center

Philadelphia, Pennsylvania, United States

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Western Pennsylvania Hospital

Pittsburgh, Pennsylvania, United States

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West Clinic, P.C.

Memphis, Tennessee, United States

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Boston Cancer Group

Memphis, Tennessee, United States

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Baylor University Medical Center

Dallas, Texas, United States

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Cancer Care Institute of South Texas

San Antonio, Texas, United States

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South Texas Cancer Institute

San Antonio, Texas, United States

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Liverpool Hospital

Liverpool, New South Wales, Australia

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Newcastle Mater Misericordiae Hospital

Newcastle, New South Wales, Australia

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Royal North Shore Hospital

St Leonards, New South Wales, Australia

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St. Vincent's Hospital

Sydney, New South Wales, Australia

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NSW Breast Cancer Institute

Westmead, New South Wales, Australia

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Wesley Clinic for Hematology/Oncology

Auchenflower, Queensland, Australia

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Royal Brisbane Hospital

Brisbane, Queensland, Australia

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Princess Alexandra Hospital

Brisbane, Queensland, Australia

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Mater Public Hospital

South Brisbane, Queensland, Australia

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Hanson Center for Cancer Research

Adelaide, South Australia, Australia

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Queen Elizabeth Hospital

Adelaide, South Australia, Australia

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Monash Medical Center

East Bentleigh, Victoria, Australia

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Peter MacCallum Cancer Institute

East Melbourne, Victoria, Australia

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Royal Melbourne Hospital

Parkville, Victoria, Australia

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Royal Perth Hospital

Perth, Western Australia, Australia

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Fremantle Hospital

Fremantle, , Australia

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Vancouver General Hospital

Vancouver, British Columbia, Canada

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Queen Elizabeth II Health Science Center

Halifax, Nova Scotia, Canada

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London Health Sciences Centre

London, Ontario, Canada

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Ottawa Regional Cancer Center - General Division

Ottawa, Ontario, Canada

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Seaforth Medical Centre

Montreal, Quebec, Canada

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Hopital Du Sacre-Coeur de Montreal

Montreal, Quebec, Canada

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Centre Hospitalier Universitaire de Quebec, Pavillion de Quebec

Québec, Quebec, Canada

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Royal University Hospital

Saskatoon, Saskatchewan, Canada

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Aalborg Hospital

Aalborg, , Denmark

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Odense University Hospital

Odense, , Denmark

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Tallinn Central Hospital

Tallinn, , Estonia

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University of Tartu

Tartu, , Estonia

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Helsinki University Central Hospital

Helsinki, , Finland

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Kuopio University Hospital

Kuopio, , Finland

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Tampere University Hospital

Tampere, , Finland

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Turku University Central Hospital

Turku, , Finland

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Centre Hospitalier Regional et Universitaire d'Angers

Angers, , France

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CHR de Besancon - Hopital Jean Minjoz

Besançon, , France

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Hopital Beaujon

Clichy, , France

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Hopital Andre Mignot

Le Chesnay, , France

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Centre Hospitalier Regional de Lille

Lille, , France

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Hopital Edouard Herriot

Lyon, , France

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CHR Hotel Dieu

Nantes, , France

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Centre Henri Becquerel

Rouen, , France

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Zentralklinikum Augsburg

Augsburg, , Germany

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Universitaetsklinikum Charite

Berlin, , Germany

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Evang. Diakonissenanstalt

Bremen, , Germany

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Medizinische Klinik I

Dresden, , Germany

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Universitaetsklinik und Strahlenklinik - Essen

Essen, , Germany

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Klinikum der J.W. Goethe Universitaet

Frankfurt, , Germany

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Martin Luther Universitaet

Halle, , Germany

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Universitats-Krankenhaus Eppendorf

Hamburg, , Germany

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Medizinische Hochschule Hannover

Hanover, , Germany

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Medizinische Klinik und Poliklinik

Heidelberg, , Germany

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Staedtische Kliniken Osnabruek

Osnabrück, , Germany

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Universitat Rostock

Rostock, , Germany

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Caritasklinik St. Theresa

Saarbrücken, , Germany

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Universitaetsklinikum Tuebingen

Tübingen, , Germany

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Klinikum der Universitaet Ulm

Ulm, , Germany

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Medizinische Poliklinik der Universitat

Würzburg, , Germany

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Rambam Medical Center

Haifa, , Israel

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Hadassah University Hospital

Jerusalem, , Israel

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Rabin Medical Center

Petah Tikva, , Israel

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Sheba Medical Center

Ramat Gan, , Israel

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Kaplan Hospital

Rehovot, , Israel

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Tel-Aviv Medical Center-Ichilov Hospital

Tel Aviv, , Israel

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University of Auckland School of Medicine

Auckland, , New Zealand

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Canterbury Health Laboratories

Christchurch, , New Zealand

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Waikato Hospital

Hamilton, , New Zealand

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Palmerston North Hospital

Palmerston North, , New Zealand

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Wellington Hospital

Wellington, , New Zealand

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County Hospital (Malar Hospital)

Eskilstuna, , Sweden

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Sahlgrenska University Hospital

Gothenburg (Goteborg), , Sweden

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County Hospital/Kalmar

Kalmar, , Sweden

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Central Hospital

Karlstad, , Sweden

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University Hospital of Linkoping

Linköping, , Sweden

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Lund University Hospital

Lund, , Sweden

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Malmo University Hospital

Malmo, , Sweden

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Regional Hospital

Örebro, , Sweden

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County Hospital (Karnsjukhuset)

Skövde, , Sweden

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Huddinge Hospital

Stockholm, , Sweden

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Karolinska Hospital

Stockholm, , Sweden

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County Hospital/Sundsvall

Sundsvall, , Sweden

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County Hospital/Uddevalla

Uddevalla, , Sweden

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Umea Universitet

Umeå, , Sweden

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University Hospital - Uppsala

Uppsala, , Sweden

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County Hospital/Vasteras

Västerås, , Sweden

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Birmingham Heartlands and Solihull NHS Trust (Teaching)

Birmingham, England, United Kingdom

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Leeds Teaching Hospital Trust

Leeds, England, United Kingdom

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Manchester Royal Infirmary

Manchester, England, United Kingdom

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Countries

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United States Australia Canada Denmark Estonia Finland France Germany Israel New Zealand Sweden United Kingdom

References

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Buyse M, Michiels S, Squifflet P, Lucchesi KJ, Hellstrand K, Brune ML, Castaigne S, Rowe JM. Leukemia-free survival as a surrogate end point for overall survival in the evaluation of maintenance therapy for patients with acute myeloid leukemia in complete remission. Haematologica. 2011 Aug;96(8):1106-12. doi: 10.3324/haematol.2010.039131. Epub 2011 May 5.

Reference Type RESULT
PMID: 21546500 (View on PubMed)

Buyse M, Squifflet P, Lucchesi KJ, Brune ML, Castaigne S, Rowe JM. Assessment of the consistency and robustness of results from a multicenter trial of remission maintenance therapy for acute myeloid leukemia. Trials. 2011 Mar 23;12:86. doi: 10.1186/1745-6215-12-86.

Reference Type RESULT
PMID: 21429214 (View on PubMed)

Other Identifiers

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MAXIM-MP-MA-0201

Identifier Type: -

Identifier Source: secondary_id

CWRU-MAXI-1998

Identifier Type: -

Identifier Source: secondary_id

CDR0000067196

Identifier Type: -

Identifier Source: org_study_id