A Comparison of Zidovudine Plus Lamivudine Versus ddI Used Alone or in Combination With Zidovudine in HIV-1 Infected Children

NCT ID: NCT00001066

Last Updated: 2011-03-02

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE2

Total Enrollment

740 participants

Study Classification

INTERVENTIONAL

Brief Summary

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To compare the efficacy of lamivudine (3TC) and zidovudine (AZT) in combination versus the better of didanosine (ddI) monotherapy or ddI/AZT combination, in symptomatic HIV-1 infected children who received less than 56 days of prior antiretroviral therapy. To evaluate the safety and tolerance of 3TC/AZT in this patient population. To determine other measures of diseases in response to the study regimens.

Currently, none of the potential treatments for HIV-1 infection has proven to be both nontoxic and effective in long-term use. However, previous studies in both adults and children have shown that 3TC combined with AZT reduced HIV load in blood and increased white blood cells. Additionally, 3TC has demonstrated a favorable safety profile.

Detailed Description

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Currently, none of the potential treatments for HIV-1 infection has proven to be both nontoxic and effective in long-term use. However, previous studies in both adults and children have shown that 3TC combined with AZT reduced HIV load in blood and increased white blood cells. Additionally, 3TC has demonstrated a favorable safety profile.

Patients are randomized to receive oral 3TC/AZT, ddI/AZT, or ddI alone for at least 24 months. PER AMENDMENT 4/29/96: NOTE: Randomization to ZDV+ddI arm was terminated in Spring of 1996 based upon the results of ACTG 152. Patients on that arm will continue on blinded study drug and will be followed until the end of the study.

Conditions

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HIV Infections

Study Design

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Primary Study Purpose

TREATMENT

Blinding Strategy

DOUBLE

Interventions

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Lamivudine

Intervention Type DRUG

Zidovudine

Intervention Type DRUG

Didanosine

Intervention Type DRUG

Eligibility Criteria

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Inclusion Criteria

Concurrent Medication:

Allowed:

* IVIG.
* Prophylaxis for opportunistic infection.
* EPO.
* G-CSF or GM-CSF.

Patients must have:

* Symptomatic HIV infection.
* Less than 56 days of prior antiretroviral therapy.
* Consent of parent or guardian.

NOTE:

* Co-enrollment on ACTG 219, ACTG 220, and certain ACTG opportunistic infection protocols is permitted.

Prior Medication:

Allowed:

* Up to 56 days of prior antiretroviral therapy.
* Prior immunomodulator therapy.

Exclusion Criteria

Co-existing Condition:

Patients with the following symptoms or conditions are excluded:

* Malignancy.
* Hypersensitivity to a nucleoside analog.
* Current grade 2 or higher amylase/lipase toxicity or grade 3 or 4 other toxicity.

PER AMENDMENT 4/29/96:

* Active opportunistic infection and/or serious bacterial infection at the time of entry.

Concurrent Medication:

Excluded:

* Any other anti-HIV therapy.
* Megestrol acetate ( Megace ).
* Probenecid.
* IV pentamidine.
* Human growth hormone ( hGH ).
* Systemic corticosteroids for more than 2 weeks.

Prior Medication:

Excluded:

* Investigational drug therapy within 14 days prior to study entry.
Minimum Eligible Age

3 Months

Maximum Eligible Age

15 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Bristol-Myers Squibb

INDUSTRY

Sponsor Role collaborator

Glaxo Wellcome

INDUSTRY

Sponsor Role collaborator

National Institute of Allergy and Infectious Diseases (NIAID)

NIH

Sponsor Role lead

Principal Investigators

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McKinney RE

Role: STUDY_CHAIR

Johnson GM

Role: STUDY_CHAIR

Locations

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Univ of Alabama at Birmingham Schl of Med / Pediatrics

Birmingham, Alabama, United States

Site Status

Arkansas Children's Hosp

Little Rock, Arkansas, United States

Site Status

UCSD Med Ctr / Pediatrics / Clinical Sciences

La Jolla, California, United States

Site Status

Long Beach Memorial (Pediatric)

Long Beach, California, United States

Site Status

Children's Hosp of Los Angeles/UCLA Med Ctr

Los Angeles, California, United States

Site Status

Los Angeles County - USC Med Ctr

Los Angeles, California, United States

Site Status

UCLA Med Ctr / Pediatric

Los Angeles, California, United States

Site Status

Harbor - UCLA Med Ctr / UCLA School of Medicine

Los Angeles, California, United States

Site Status

Children's Hosp of Oakland

Oakland, California, United States

Site Status

Univ of California / Davis

Sacramento, California, United States

Site Status

UCSF / Moffitt Hosp - Pediatric

San Francisco, California, United States

Site Status

Stanford Univ School of Medicine

Stanford, California, United States

Site Status

Children's Hosp of Denver

Denver, Colorado, United States

Site Status

Univ of Connecticut / Farmington

Farmington, Connecticut, United States

Site Status

Yale Univ Med School

New Haven, Connecticut, United States

Site Status

Children's Hosp of Washington DC

Washington D.C., District of Columbia, United States

Site Status

Howard Univ Hosp

Washington D.C., District of Columbia, United States

Site Status

Children's Diagnostic and Treatment Ctr of South Florida

Fort Lauderdale, Florida, United States

Site Status

Univ of Florida

Gainesville, Florida, United States

Site Status

Univ of Florida Health Science Ctr / Pediatrics

Jacksonville, Florida, United States

Site Status

Univ of Miami (Pediatric)

Miami, Florida, United States

Site Status

Arnold Palmer Hosp for Children & Women

Orlando, Florida, United States

Site Status

All Children's Hosp

St. Petersburg, Florida, United States

Site Status

Univ of South Florida

Tampa, Florida, United States

Site Status

Saint Joseph's Hosp

Tampa, Florida, United States

Site Status

HRS Palm Beach County Public Health Unit

West Palm Beach, Florida, United States

Site Status

Emory Univ Hosp / Pediatrics

Atlanta, Georgia, United States

Site Status

Med College of Georgia

Augusta, Georgia, United States

Site Status

Mem Children's Hosp

Savannah, Georgia, United States

Site Status

Mount Sinai Hosp Med Ctr

Chicago, Illinois, United States

Site Status

Cook County Hosp

Chicago, Illinois, United States

Site Status

Univ of Illinois College of Medicine / Pediatrics

Chicago, Illinois, United States

Site Status

Chicago Children's Memorial Hosp

Chicago, Illinois, United States

Site Status

Univ of Chicago Children's Hosp

Chicago, Illinois, United States

Site Status

Tulane Univ / Charity Hosp of New Orleans

New Orleans, Louisiana, United States

Site Status

Univ of Maryland at Baltimore / Univ Med Ctr

Baltimore, Maryland, United States

Site Status

Johns Hopkins Hosp - Pediatric

Baltimore, Maryland, United States

Site Status

Children's Hosp of Boston

Boston, Massachusetts, United States

Site Status

Boston City Hosp / Pediatrics

Boston, Massachusetts, United States

Site Status

Baystate Med Ctr of Springfield

Springfield, Massachusetts, United States

Site Status

Univ of Massachusetts Med School

Worcester, Massachusetts, United States

Site Status

Children's Hosp of Michigan

Detroit, Michigan, United States

Site Status

Univ of Minnesota Med School

Minneapolis, Minnesota, United States

Site Status

Univ of Mississippi Med Ctr

Jackson, Mississippi, United States

Site Status

St Louis Children's Hosp

St Louis, Missouri, United States

Site Status

UMDNJ - Robert Wood Johnson Med School / Pediatrics

New Brunswick, New Jersey, United States

Site Status

Univ of Medicine & Dentistry of New Jersey / Univ Hosp

Newark, New Jersey, United States

Site Status

Saint Joseph's Hosp and Med Ctr/UMDNJ - New Jersey Med Schl

Newark, New Jersey, United States

Site Status

Children's Hosp of New Jersey / UMDNJ - New Jersey Med Schl

Newark, New Jersey, United States

Site Status

Children's Hosp at Albany Med Ctr

Albany, New York, United States

Site Status

King's County Hosp Ctr / Pediatrics

Brooklyn, New York, United States

Site Status

SUNY - Brooklyn

Brooklyn, New York, United States

Site Status

Children's Hosp of Buffalo

Buffalo, New York, United States

Site Status

North Shore Univ Hosp

Great Neck, New York, United States

Site Status

Schneider Children's Hosp

New Hyde Park, New York, United States

Site Status

Beth Israel Med Ctr / Pediatrics

New York, New York, United States

Site Status

Bellevue Hosp / New York Univ Med Ctr

New York, New York, United States

Site Status

Saint Luke's - Roosevelt Hosp Ctr

New York, New York, United States

Site Status

Metropolitan Hosp Ctr

New York, New York, United States

Site Status

Mount Sinai Med Ctr / Pediatrics

New York, New York, United States

Site Status

Columbia Presbyterian Med Ctr

New York, New York, United States

Site Status

Harlem Hosp Ctr

New York, New York, United States

Site Status

Univ of Rochester Medical Center

Rochester, New York, United States

Site Status

State Univ of New York at Stony Brook

Stony Brook, New York, United States

Site Status

SUNY Health Sciences Ctr at Syracuse / Pediatrics

Syracuse, New York, United States

Site Status

Bronx Lebanon Hosp Ctr

The Bronx, New York, United States

Site Status

Westchester Hosp

Valhalla, New York, United States

Site Status

Duke Univ Med Ctr

Durham, North Carolina, United States

Site Status

Univ of North Carolina at Chapel Hill / Duke Univ Med Ctr

Durham, North Carolina, United States

Site Status

Cincinnati Children's Hosp / Univ Hosp

Cincinnati, Ohio, United States

Site Status

Case Western Reserve Univ - Pediatric

Cleveland, Ohio, United States

Site Status

Columbus Children's Hosp

Columbus, Ohio, United States

Site Status

Children's Med Ctr

Dayton, Ohio, United States

Site Status

Children's Hosp of Philadelphia

Philadelphia, Pennsylvania, United States

Site Status

Saint Christopher's Hosp for Children

Philadelphia, Pennsylvania, United States

Site Status

Rhode Island Hosp / Brown Univ

Providence, Rhode Island, United States

Site Status

Med Univ of South Carolina

Charleston, South Carolina, United States

Site Status

Univ of South Carolina School of Med

Columbia, South Carolina, United States

Site Status

Saint Jude Children's Research Hosp of Memphis

Memphis, Tennessee, United States

Site Status

Children's Med Ctr of Dallas

Dallas, Texas, United States

Site Status

Cook - Fort Worth Children's Med Ctr

Fort Worth, Texas, United States

Site Status

Hermann Hosp / Univ Texas Health Science Ctr

Houston, Texas, United States

Site Status

Texas Children's Hosp / Baylor Univ

Houston, Texas, United States

Site Status

Univ of Texas Health Science Ctr

San Antonio, Texas, United States

Site Status

Senetara Norfolk Gen Hosp

Norfolk, Virginia, United States

Site Status

Virginia Commonwealth Univ

Richmond, Virginia, United States

Site Status

Children's Hospital & Medical Center / Seattle ACTU

Seattle, Washington, United States

Site Status

Ramon Ruiz Arnau Univ Hosp / Pediatrics

Bayamón, , Puerto Rico

Site Status

Mayaguez Med Ctr

Mayagüez, , Puerto Rico

Site Status

Univ of Puerto Rico / Univ Children's Hosp AIDS

San Juan, , Puerto Rico

Site Status

San Juan City Hosp

San Juan, , Puerto Rico

Site Status

Countries

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United States Puerto Rico

References

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Combination therapies improve outlook for children with HIV disease. NIAID AIDS Agenda. 1997 Aug:10.

Reference Type BACKGROUND
PMID: 11364606 (View on PubMed)

McKinney RE Jr. Ongoing and future trials of antiretroviral therapy in the pediatric AIDS clinical trials group (PACTG). Conf Retroviruses Opportunistic Infect. 1996 Jan 28-Feb 1;3rd:173

Reference Type BACKGROUND

James JS. Major pediatric study stopped early: combination treatment better. AIDS Treat News. 1997 Jul 4;(No 274):5-6.

Reference Type BACKGROUND
PMID: 11364462 (View on PubMed)

Perrier M, Schwarz T, Gonzalez O, Brounts S. Squamous cell carcinoma invading the right temporomandibular joint in a Belgian mare. Can Vet J. 2010 Aug;51(8):885-7.

Reference Type BACKGROUND
PMID: 21037891 (View on PubMed)

Benjamin DK Jr, Miller WC, Benjamin DK, Ryder RW, Weber DJ, Walter E, McKinney RE. A comparison of height and weight velocity as a part of the composite endpoint in pediatric HIV. AIDS. 2003 Nov 7;17(16):2331-6. doi: 10.1097/00002030-200311070-00007.

Reference Type BACKGROUND
PMID: 14571184 (View on PubMed)

Other Identifiers

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ACTG 300

Identifier Type: -

Identifier Source: org_study_id

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